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Search clinical trials for: Wolman syndrome
Total 37410 results
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Centre Hospitalier Universitaire de LiegeSanofi; Takeda; University of Liege; Orchard Therapeutics; Centre Hospitalier Régional... and other collaboratorsRecruitingCongenital Adrenal Hyperplasia | Hemophilia A | Hemophilia B | Mucopolysaccharidosis I | Mucopolysaccharidosis II | Cystic Fibrosis | Alpha 1-Antitrypsin Deficiency | Sickle Cell Disease | Fanconi Anemia | Chronic Granulomatous Disease | Wilson Disease | Severe Congenital Neutropenia | Ornithine Transcarbamylase... and other conditionsBelgium
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University of California, San FranciscoRecruitingMucopolysaccharidosis I | Mucopolysaccharidosis II | Mucopolysaccharidosis VI | Wolman Disease | Pompe Disease Infantile-Onset | Mucopolysaccharidosis IV A | Mucopolysaccharidosis VII | Neuronopathic Gaucher DiseaseUnited States
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RTI InternationalEunice Kennedy Shriver National Institute of Child Health and Human Development... and other collaboratorsEnrolling by invitationPrimary Hyperoxaluria Type 3 | Diabetes Mellitus | Hemophilia A | Hemophilia B | Hereditary Fructose Intolerance | Cystic Fibrosis | Factor VII Deficiency | Phenylketonurias | Sickle Cell Disease | Dravet Syndrome | Duchenne Muscular Dystrophy | Prader-Willi Syndrome | Fragile X Syndrome | Chronic Granulomatous Disease and other conditionsUnited States
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New York Medical CollegeCompletedMucopolysaccharidosis I | Myelodysplastic Syndrome | Acute Lymphocytic Leukemia | Acute Myelogenous Leukemia | Niemann-Pick Disease | Mucopolysaccharidosis VI | Wolman Disease | Adrenoleukodystrophy | Batten Disease | Metachromatic Leukodystrophy | Diamond-Blackfan Anemia | Severe Aplastic Anemia | Fucosidosis | Gaucher... and other conditionsUnited States
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Alexion PharmaceuticalsTerminatedLysosomal Acid Lipase DeficiencyUnited Kingdom, Finland, United States, Italy
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Masonic Cancer Center, University of MinnesotaCompletedWolman Disease | Adrenoleukodystrophy | Metachromatic Leukodystrophy | Sanfilippo Syndrome | GM1 Gangliosidosis | Globoid Cell Leukodystrophy | Tay Sachs Disease | Sandhoffs Disease | I-Cell DiseaseUnited States
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Alexion PharmaceuticalsCompletedWolman Disease | Lysosomal Acid Lipase DeficiencyUnited Kingdom, France, United States, Egypt, Ireland
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Masonic Cancer Center, University of MinnesotaTerminatedSphingolipidoses | Niemann-Pick Disease, Type C | Krabbe Disease | Sly Syndrome | Fucosidosis | Aspartylglucosaminuria | Alpha Mannosidosis | Hurler's Syndrome | Maroteaux-Lamy Syndrome | Wolman's Disease | Niemann-Pick Disease Type BUnited States
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Masonic Cancer Center, University of MinnesotaCompletedLysosomal Storage Disease | Peroxisomal DisorderUnited States
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Fairview University Medical CenterUnknownMucopolysaccharidosis I | Niemann-Pick Disease | Mucopolysaccharidosis VI | Wolman Disease | Adrenoleukodystrophy | Metachromatic Leukodystrophy | Pulmonary Complications | Fucosidosis | Globoid Cell Leukodystrophy | Gaucher's Disease | Mannosidosis | I Cell DiseaseUnited States
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IRCCS San RaffaeleNot yet recruitingMitral Valve Prolapse Syndrome | Arrhythmogenic Bileaflet Mitral Prolapse | Mitral Valve Disorder
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Sun Yat-Sen Memorial Hospital of Sun Yat-Sen UniversityRecruiting
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Xuanwu Hospital, BeijingNot yet recruitingEpilepsy, Drug ResistantChina
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University of Illinois at Urbana-ChampaignNot yet recruitingCognitive Change | Diet, Healthy | Metabolic Syndrome, Protection Against
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Parc Tauli Research and Innovation Institute FoundationNot yet recruiting
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Foundation University IslamabadRecruiting
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Faming ZhangNot yet recruitingIrritable Bowel SyndromeChina
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Inflammx Therapeutics IncRecruiting
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Beijing Tongren HospitalThe First Affiliated Hospital with Nanjing Medical UniversityNot yet recruitingReversal of Neuromuscular BlockadeChina
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argenxNot yet recruiting
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Peking University First HospitalPeking University Third Hospital; Peking University Cancer Hospital & InstituteRecruitingCutaneous T Cell Lymphoma | Cutaneous T-Cell Lymphoma/Mycosis FungoidesChina
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University Hospital, Gentofte, CopenhagenRigshospitalet, Denmark; The Novo Nordic Foundation; Region Capital Denmark; VIVE... and other collaboratorsNot yet recruitingCross-sectorial Use of Patient-Reported Outcomes in Chronic Degenerative Shoulder Conditions (C-PRO)Shoulder Impingement Syndrome | Shoulder Osteoarthritis | Shoulder Capsulitis | Shoulder Impingement | Shoulder Bursitis | Shoulder Disease | Rotator Cuff Syndrome | Rotator Cuff Syndrome of Shoulder and Allied Disorders | Shoulder FrozenDenmark
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TCROSS Co., Ltd.Kaneka CorporationRecruitingStable Angina | Unstable Angina | Non-ST-elevation Acute Coronary SyndromeJapan
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Istanbul Medipol University HospitalRecruiting
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University of PennsylvaniaNot yet recruitingObstructive Sleep Apnea of AdultUnited States
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UCB Biopharma SRLNot yet recruiting
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Second Affiliated Hospital, School of Medicine,...Not yet recruiting
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The Second Hospital of Nanjing Medical UniversityRecruitingType A Aortic DissectionChina
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Universitätsklinikum Hamburg-EppendorfRecruitingFamilial Adenomatous Polyposis | Adenomatous Polyposis Coli | Duodenal AdenomaGermany
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Tanta UniversityNot yet recruitingPost Thoracotomy Pain | Thoracic Paravertebral Block | External Oblique Intercostal Plane BlockEgypt
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Hospices Civils de LyonNot yet recruitingCampylobacter InfectionsFrance
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Rijnstate HospitalRecruitingObesity | Obstructive Sleep Apnea | Bariatric Surgery CandidateNetherlands
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Distribuidora Biolife SA de CVRecruiting
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Assistance Publique - Hôpitaux de ParisNot yet recruitingIrritable Bowel SyndromeFrance
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Ionis Pharmaceuticals, Inc.Not yet recruitingMethyl CpG Binding Protein 2 (MECP2) Duplication Syndrome
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Hookipa Biotech GmbHNot yet recruitingHuman Immunodeficiency Virus (HIV) InfectionUnited States
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Centre Hospitalier Universitaire de NiceNot yet recruiting
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Etlik Zubeyde Hanım Women's Health Care, Training...Not yet recruitingPolycystic Ovary Syndrome | Diet Habit | Adolescent Behavior
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University of MichiganRecordati Rare DiseasesRecruitingAdrenal Insufficiency | Hypercortisolism | Endogenous Cushing SyndromeUnited States
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Zhongda HospitalRecruitingRespiratory Distress Syndrome | Mechanical Ventilation | Positive-Pressure RespirationChina
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Beijing Chao Yang HospitalRecruitingUsing Functional Lung MRI to Explore Pulmonary Perfusion Changes in Patients With Pulmonary Fibrosis and Emphysema SyndromeChina
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Kırıkkale UniversityTC Erciyes UniversityNot yet recruitingPostoperative Complications | Obstructive Sleep Apnea of Adult | Obstructive Sleep Apnea Risk Management | Dental Caries Under General Anesthesia
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Ain Shams UniversityNot yet recruitingCoenzyme Q10 Role in Prevention of Contrast Induced Nephropathy in Acute Coronary Syndrome Patients.Contrast-induced NephropathyEgypt
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Etlik Zubeyde Hanım Women's Health Care, Training...Not yet recruitingDepression | Sexual Dysfunction | Polycystic Ovary
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Shandong Qilu Stem Cells Engineering Co., Ltd.Qilu Children's Hospital of Shandong UniversityRecruitingBronchopulmonary Dysplasia | Hypoxic-Ischemic Encephalopathy | Short Bowel SyndromeChina
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Cambridge University Hospitals NHS Foundation TrustNot yet recruitingAcute Coronary SyndromesUnited Kingdom
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Essen BiotechRecruitingAutoimmune Diseases | Systemic Lupus Erythematosus | Sjogren's Syndrome | Systemic Lupus Erythematosus AcuteChina
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Taejoon Pharmaceutical Co., Ltd.RecruitingDry Eye | Dry Eye SyndromesKorea, Republic of
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Fundación Santiago Dexeus FontRegen Lab SANot yet recruitingGenitourinary Syndrome of MenopauseSpain