- ICH GCP
- US Clinical Trials Registry
- Search trials
Search clinical trials for: children with rare diseases
Total 405804 results
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University of VermontEunice Kennedy Shriver National Institute of Child Health and Human Development...Not yet recruitingEmergencies | Infant Conditions | Child, Only | Infant Morbidity | Chronic Condition | Children With Medical Complexity | Utilization, Health CareUnited States
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TakedaNot yet recruitingPouchitisBelgium, Spain, Czechia, Italy, Israel, Croatia, Greece, Poland
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Kirsehir Ahi Evran UniversitesiRecruiting
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Hospices Civils de LyonNot yet recruitingQuality of Life | Renal Insufficiency | Urinary Incontinence | End Stage Renal Disease | Chronic Renal Disease | Bladder Dysfunction | Posterior Urethral ValveFrance
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University of MalagaJorge Manuel Góngora RodríguezNot yet recruiting
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Union de Gestion des Etablissements des Caisses...RecruitingChildren With Cerebral PalsyFrance
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Opna Bio LLCNot yet recruitingRefractory Multiple Myeloma | Relapsed Multiple MyelomaUnited States
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Chia Tai Tianqing Pharmaceutical Group Co., Ltd.Not yet recruitingT-lymphoblastic Lymphoma | T-lymphoblastic LeukemiaChina
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Savara Inc.Not yet recruitingAutoimmune Pulmonary Alveolar ProteinosisUnited States
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Ascendis Pharma Growth Disorders A/SNot yet recruitingAchondroplasiaDenmark, Ireland, United Kingdom
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Omer AyhanRecruiting
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Universidad Nacional Andres BelloNot yet recruiting
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Vittore Buzzi Children's HospitalRecruitingBronchiolitis | Noninvasive VentilationItaly
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Sijia GuRecruitingChild, Only | Hematopoietic Stem Cell Transplantation | Graft-Versus-Host Disease | Haploidentical Hematopoietic Stem Cell TransplantationChina
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Case Comprehensive Cancer CenterNot yet recruitingAcute Leukemia | Acute Lymphoblastic Leukemia, Pediatric | Myeloproliferative Neoplasm | Acute Myeloid Leukemia in ChildrenUnited States
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University of St. Augustine for Health SciencesRecruitingSpina BifidaUnited States
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University of Colorado, DenverChildren's Hospital ColoradoNot yet recruitingMigraine | Migraine in AdolescenceUnited States
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Kite, A Gilead CompanyArcellx, Inc.Not yet recruiting
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Eli Lilly and CompanyNot yet recruiting
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SpinogenixAvance Clinical Pty Ltd.Not yet recruiting
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Children's Hospital Los AngelesNot yet recruitingCystic Fibrosis | Constipation Chronic IdiopathicUnited States
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University of South FloridaRecruitingOppositional Defiant Disorder | Insomnia ChronicUnited States
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QED Therapeutics, Inc.RecruitingHypochondroplasiaUnited States, Australia, Norway, Portugal, Singapore, Spain
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The First Affiliated Hospital of Soochow UniversityNot yet recruitingMultiple Myeloma | Newly Diagnosed | MRD | High Risk
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Riphah International UniversityNot yet recruiting
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Riphah International UniversityNot yet recruitingSpastic Cerebral PalsyPakistan
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University of CalgaryRecruitingPhysical Disability | Developmental Disability | CP (Cerebral Palsy)Canada
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Riphah International UniversityNot yet recruitingCerebral Palsy (CP)Pakistan
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Riphah International UniversityNot yet recruiting
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Ankara City Hospital BilkentRecruiting
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Hasan Kalyoncu UniversityNot yet recruiting
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Tisento TherapeuticsNot yet recruitingMitochondrial Encephalopathy, Lactic Acidosis and Stroke-Like Episodes (MELAS Syndrome)United States, Australia, Italy, Germany, Canada, United Kingdom
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Children's Oncology GroupNot yet recruitingStage I Kidney Wilms Tumor | Stage II Kidney Wilms Tumor | Stage III Kidney Wilms Tumor | Stage IV Kidney Wilms Tumor
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Ankara City Hospital BilkentRecruiting
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Children's National Research InstituteSteven & Alexandra Cohen Foundation; Clinical Trials Network for Lyme and Other...RecruitingPregnancy Complications | Parenting | Tick-Borne Diseases | Lyme Disease | Chronic Lyme Disease | Tick-Borne Infections | Post Treatment Lyme DiseaseUnited States
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McGill University Health Centre/Research Institute...Not yet recruiting
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Vanderbilt University Medical CenterAminu Kano Teaching Hospital; Murtala Muhammed Specialist HospitalNot yet recruitingMalnutrition | Sickle Cell Disease
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Universidade Norte do ParanáNot yet recruitingEffects of Photobiomodulation on the Innate Immune System of Neonates and Infants With BronchiolitisBronchiolitis | Virus Disease | VirusBrazil
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Nutricia FoundationRecruiting
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argenxNot yet recruitingGeneralized Myasthenia Gravis
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St. Jude Children's Research HospitalAbbVieNot yet recruitingT-cell Lymphoma | T-cell Acute Lymphoblastic Leukemia | Mixed Phenotype Acute LeukemiaUnited States
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GRIN Therapeutics, Inc.RecruitingTuberous Sclerosis Complex | Focal Cortical DysplasiaSpain, United Kingdom, Australia, Belgium, Canada, Italy, Poland
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Gazi UniversityNot yet recruitingLymphoma | Childhood Cancer | AML, Childhood | Solid Tumor, Childhood | ALL, ChildhoodTurkey
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Alliance for International Medical ActionInstitut National de la Santé Et de la Recherche Médicale, France; Programme... and other collaboratorsNot yet recruitingNutrition | Vaccination | Immunization CoverageNigeria
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Hospital Universiti Sains MalaysiaNot yet recruiting
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Inmunova S.A.Chemo Research; KLIXAR; Linical; CrovelisNot yet recruiting
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Seattle Children's HospitalUniversity of KentuckyNot yet recruitingPancreatitis | Chronic Pancreatitis | Acute Recurrent PancreatitisUnited States
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Murdoch Childrens Research InstituteNot yet recruitingHodgkin Lymphoma | Non Hodgkin LymphomaAustralia
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EpicentreEpicentre, Niger; National Nutrition Direction, Niger; Ministry of Public Health... and other collaboratorsRecruiting
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Daniel MorgensternThe Hospital for Sick ChildrenRecruiting