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Search clinical trials for: hereditary retinoblastoma,
Total 2869 results
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Swedish Orphan BiovitrumRecruitingHereditary Tyrosinemia, Type IChina
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Nanjing University School of MedicineRecruiting
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Lassen Therapeutics Inc.RecruitingEye Diseases | Endocrine System Diseases | Thyroid Eye Disease | Graves Ophthalmopathy | Orbital Diseases | Thyroid Associated Ophthalmopathy | Graves Orbitopathy | ProptosisUnited States, United Kingdom, Spain
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bluebird bioCenter for International Blood and Marrow Transplant ResearchRecruitingCerebral Adrenoleukodystrophy (CALD)United States
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University College, LondonNot yet recruiting
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National Cancer Institute (NCI)Not yet recruitingNeurofibromatosis 1 | Nerve Sheath NeoplasmsUnited States
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Samsung Medical CenterNot yet recruitingCharcot-Marie-Tooth Disease, Type 1
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Tampere University HospitalTampere UniversityRecruitingLynch Syndrome | Urothelial CarcinomaCanada, Finland
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Hospital Universitari Vall d'Hebron Research InstituteErasme University Hospital; Cyprus Institute of Neurology and Genetics; EuroBloodNet...RecruitingIron Metabolism Disorders | Sickle Cell Disease | Thalassemia | Hemolytic; Anemia, Hereditary, Due to Enzyme Disorder | Anemia Due to Membrane Defect | CDA | Sideroblastic Anemia | Constitutional Aplastic Anemia | Hereditary AnemiaSpain
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Foundation For Rare Disease ResearchInstitute for Asthma & Allergy; Virant Diagnostics, Inc.; MedBio Reference Laboratories...Not yet recruitingAngioedema | Urticaria | C1 Inhibitor Deficiency | Angioedemas, Hereditary | Mastocytosis | Indolent Systemic Mastocytosis | Systemic Mastocytoses | ACE Inhibitor-Induced Angioedema
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New York Stem Cell Foundation Research InstituteCharcot-Marie-Tooth AssociationRecruitingHealthy | Charcot-Marie-Tooth DiseaseUnited States
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Johns Hopkins UniversityRecruitingGranular Dystrophy, CornealUnited States
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Baylor College of MedicineCenter for Cell and Gene Therapy, Baylor College of MedicineNot yet recruitingHepatocellular Carcinoma | Liposarcoma | Rhabdomyosarcoma | Wilms Tumor | Hepatoblastoma | Malignant Rhabdoid Tumor | Yolk Sac Tumor | Embryonal Sarcoma of LiverUnited States
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University of Alabama at BirminghamChildren's Hospital of Philadelphia; Congressionally Directed Medical Research...Not yet recruitingNeurofibromatosis 1 | Plexiform Neurofibroma
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Centre Hospitalier National d'Ophtalmologie des...Street LabNot yet recruitingRetinal Degeneration
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Rutgers, The State University of New JerseyRecruitingBreast Cancer | Colorectal Cancer | Ovarian Cancer | Fallopian Tube Cancer | Prostate Cancer | Endometrial Cancer | Pancreas Cancer | Peritoneal CancerUnited States
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Sixth Affiliated Hospital, Sun Yat-sen UniversityRecruitingHereditary DiseasesChina
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Oscar Gerardo Arrieta RodríguezRecruiting
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Viridian Therapeutics, Inc.Recruiting
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St. Joseph's Hospital and Medical Center, PhoenixTexas Tech UniversityNot yet recruitingCognitive Dysfunction | Neurodegenerative Disease, Hereditary | Cognitive Impairment, Mild | Amyloid Plaque | Inflammation, Brain
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Minoryx Therapeutics, S.L.RecruitingX-linked AdrenoleukodystrophyFrance
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AstraZenecaRecruitingNeurofibroma, PlexiformChina
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Royal Marsden NHS Foundation TrustRecruitingLynch Syndrome | Familial Adenomatous Polyposis | Hereditary Diffuse Gastric Cancer | Peutz-Jeghers Syndrome | Cowden Syndrome | Li Fraumeni Syndrome | MutYH-associated Polyposis | SMAD4 Gene MutationUnited Kingdom
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David M. RitterRecruitingTuberous Sclerosis Complex | LymphangioleiomyomatosisUnited States
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Karolinska InstitutetRecruitingCardiovascular Diseases | Dyslipidemias | Hereditary DiseasesSweden
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M.D. Anderson Cancer CenterRecruiting
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Johns Hopkins UniversityNeurofibromatosis Therapeutic Acceleration ProgramRecruitingCutaneous Neurofibroma | NF1 | MonotherapyUnited States
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Elpida Therapeutics SPCNot yet recruitingNeuromuscular Diseases | Peripheral Neuropathy | Neuro-Degenerative Disease
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Ionis Pharmaceuticals, Inc.RecruitingPelizaeus-Merzbacher DiseaseFrance, Netherlands
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NYU Langone HealthNot yet recruitingFamilial DysautonomiaUnited States
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Assistance Publique - Hôpitaux de ParisNot yet recruitingHemophilia A | Hemophilia B | Cystic Fibrosis | Sickle Cell Disease | Muscular Dystrophy, Duchenne | Fragile X Syndrome | Huntington Disease | Myotonic Dystrophy | Autosomal Recessive Polycystic Kidney Disease | Neurofibromatosis-Noonan Syndrome | Muscular Dystrophy, Becker | Invasive PreNatal Diagnosis in a... and other conditionsFrance
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Ganzhou Hemay Pharmaceutical Co., LtdRecruitingBehçet's DiseaseChina
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PYC TherapeuticsNot yet recruitingOptic Atrophies, Hereditary | Autosomal Dominant Optic Atrophy | Optic Atrophy, Autosomal Dominant | Kjer Optic AtrophyAustralia
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Assistance Publique - Hôpitaux de ParisRecruiting
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Centre Hospitalier Universitaire de NiceRecruitingAllergic BronchiolitisFrance
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Massachusetts General HospitalJohns Hopkins UniversityRecruitingNeurofibromatosis 1United States
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NYU Langone HealthNot yet recruiting
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Intellia TherapeuticsRegeneron PharmaceuticalsRecruitingTransthyretin Amyloidosis (ATTR) With CardiomyopathyUnited States, Australia, United Kingdom, New Zealand, Canada
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Innovent Biologics (Suzhou) Co. Ltd.RecruitingThyroid Eye Disease, TEDChina
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Massachusetts General HospitalJohns Hopkins UniversityRecruitingNeurofibromatosis 1United States
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Motric BioRecruitingStroke | Multiple Sclerosis | Cerebral Palsy | Spinal Cord Injuries | Dystonia | Muscle Spasticity | Hereditary Spastic Paraplegia | Hypertonia, MuscleUnited States
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University College, LondonRecruitingHereditary Sensory Neuropathy Type IUnited Kingdom
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Sling Therapeutics, Inc.RecruitingEye Diseases | Endocrine System Diseases | Thyroid Diseases | Thyroid Eye Disease | Graves Ophthalmopathy | Exophthalmos | Orbital Diseases | Thyroid Associated Ophthalmopathy | Graves Orbitopathy | Proptosis | IGF1R | HashimotoUnited States
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The 923rd Hospital of Joint Logistics Support Force...Guangzhou Reforgene Medicine Co., Ltd.RecruitingHemoglobinopathies | Hereditary Diseases | Alpha Thalassemia Hemoglobin H Constant SpringChina
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University of North Carolina, Chapel HillUnited States Department of DefenseRecruiting
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Hoffmann-La RocheRecruitingThyroid Eye DiseaseKorea, Republic of, United Kingdom, United States, Canada, China, Israel, France, Spain
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Memorial Sloan Kettering Cancer CenterRecruitingSolid Tumor | Neuroblastoma | Solid Tumor, Adult | Primary Brain Tumor | Solid Carcinoma | Low-grade Glioma | Central Nervous System Tumor | Refractory Cancer | CNS Tumor, Adult | CNS Tumors | NF1 | Plexiform Neurofibroma | CNS Tumor, Childhood | Optic Pathway Gliomas | MAP Kinase Family Gene MutationUnited States
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Keratoplasty Alliance InternationalRecruitingCorneal Disease | Corneal Transplant Failure | Endothelial Corneal Dystrophy | Corneal Transplant RejectionUnited States
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Weill Medical College of Cornell UniversityNational Cancer Institute (NCI)RecruitingColorectal Cancer | Endometrial Cancer | Hereditary Cancer SyndromesUnited States
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National Human Genome Research Institute (NHGRI)RecruitingMetabolic Disease | Purine-Pyrimidine Metabolism | AICDA, OMIM *605257, Immunodeficiency With Hyper-IgM, Type 2; HIGM2 | UNG, OMIM *191525, Hyper-IgM Syndrome 5 | NT5C3A<TAB>, OMIM *606224, Anemia, Hemolytic, Due to UMPH1 Deficiency | UMPS, OMIM *613891, Orotic Aciduria | DHODH, OMIM *126064,... and other conditionsUnited States