Neoadjuvant Trastuzumab, Pertuzumab and Zongertinib Without Chemotherapy in HER2-positive Breast Cancer: the TRAIN-5 Study (TRAIN-5)
This is a single-center, phase 1b study evaluating the safety, feasibility and initial efficacy of a neoadjuvant treatment with zongertinib, trastuzumab and pertuzumab in stage II-IIIA HER2-positive breast cancer.
調査の概要
状態
状態
条件
条件
介入・治療
介入・治療
詳細な説明
Neoadjuvant chemotherapy combined with dual HER2-targeted therapy results in high rates of pathological complete response (pCR) and excellent long-term survival outcomes in patients with HER2-positive breast cancer. However, this intensive treatment carries significant toxicity, leading to both acute and long-term side effects. Long-term and potentially irreversible toxicities such as neuropathy, persistent fatigue, and cognitive impairment frequently occur and may significantly impair long-term quality of life. Additionally, brain recurrence remains a well-documented, devastating complication in HER2-positive disease.
Previous studies have demonstrated that neoadjuvant treatment with dual HER2-targeted therapy consisting of trastuzumab and pertuzumab without chemotherapy can induce pCR in 11% to 47% of patients, while event-free survival appeared non-inferior. These findings suggest that omission of chemotherapy may be feasible in selected patients. Strategies to improve patient selection and to enhance HER2-directed therapy using novel highly selective agents may further increase pCR rates and expand the proportion of patients eligible for chemotherapy-free treatment. The use of agents with adequate central nervous system penetration may additionally reduce the risk of brain recurrence.
Zongertinib is an orally administered, highly selective, and irreversible HER2 tyrosine kinase inhibitor with minimal off-target toxicity. It has demonstrated robust preclinical and clinical activity against HER2-altered solid tumours, including efficacy in patients with brain metastases. Given its favourable pharmacologic profile and promising therapeutic potential, zongertinib is a strong candidate for incorporation into a chemotherapy-free neoadjuvant regimen for HER2-positive breast cancer.
研究の種類
研究の種類
入学 (推定)
入学
段階
段階
- フェーズ 1
連絡先と場所
研究場所
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-
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Amsterdam、オランダ
- Netherlands Cancer Institute
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コンタクト:
- Gabe Sonke, MD PhD
- 電話番号:0205129111
- メール:trainstudies@nki.nl
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主任研究者:
- Gabe Sonke, MD PhD
-
-
参加基準
適格基準
適格基準
就学可能な年齢
健康ボランティアの受け入れ
受講資格のある性別
説明
Inclusion Criteria:
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Signed written informed consent
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Pathologically confirmed primary invasive breast cancer
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Stage II - IIIA primary breast cancer according to TNM-staging (8th edition, AJCC); (largest tumour diameter DCE-MRI > 2cm (cT2-3) and/or cN1-2 confirmed with FNA or histology)
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Homogeneous HER2 overexpression (IHC 3+) on pre-treatment biopsy, with confirmatory HER2 amplification by in situ hybridization
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Known oestrogen- and progesterone-receptor expression of the invasive tumour
a. Hormone receptor negativity is defined as expression of both oestrogen and progesterone receptors being less than 10%
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WHO performance status of 0 or 1
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18 years of age or older
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LVEF ≥50% measured by echocardiography or MUGA
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Eligible for neoadjuvant treatment
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Laboratory requirements within 4 weeks prior to the start of study treatment:
- Adequate bone marrow function (ANC ≥1.5 x 109/l, platelets ≥100 x 109/l, haemoglobin ≥5.6 mmol/L (≥90 g/L); without the use of hematopoietic growth factors within 4 weeks prior to start of trial medication.
- Adequate hepatic function (ALT and AST ≤3 times upper limit of normal (ULN), Alkaline phosphatase <5 times ULN, Total bilirubin ≤1.5 times the ULN, except for patients with Gilbert's syndrome: total bilirubin ≤3 times ULN or direct bilirubin ≤1.5 times ULN);
- Adequate renal function: Estimated Glomerular Filtration Rate (eGFR) ≥30 mL/min/1.73m2 calculated using Chronic Kidney Disease Epidemiology (CKD-EPI) formula.
- Either International Normalized Ratio (INR) or Prothrombin Time (PT) ≤1.5 times ULN unless on a stable dose of an anticoagulant with no unexplained elevation of INR
- Activated Partial Thromboplastin Time (aPTT) ≤ 1.5 times ULN unless on a stable dose of an anticoagulant with no unexplained elevation of INR
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Women of childbearing potential (WOCBP) must be ready and able to use dual highly effective methods of birth control per ICH M3 (R2) that result in a low failure rate of less than 1% per year when used consistently and correctly during study treatment and 7 months after last dose of trastuzumab
Exclusion Criteria:
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Inflammatory breast cancer, cT4 and/or cN3 tumours
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Occult breast cancer (cT0)
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Bilateral breast cancer
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Current pregnancy or breastfeeding. Women who are breastfeeding can be enrolled if they stop breastfeeding.
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Current or previous other malignancy unless treated without systemic therapy and more than five years ago
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HER2 heterogeneity on pre-treatment biopsy
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Psychological, familial, sociological, or geographical condition potentially hampering compliance with the study protocol and follow-up schedule
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History or presence of cardiovascular abnormalities such as uncontrolled hypertension, congestive heart failure NYHA classification of III or IV, unstable angina or poorly controlled arrhythmia which are considered as clinically relevant by the investigator. Myocardial infarction, stroke, or pulmonary embolism within 6 months prior to registration.
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Any clinically important abnormalities (as assessed by the investigator) in rhythm, conduction, or morphology of resting electrocardiograms
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Mean resting corrected QT interval (QTcF) >470 msec (females) or >450 msec (males) based on screening 12-lead ECG
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Patients with chronic HBV infection with active disease who meet the criteria for anti-HBV therapy (according to local / institutional standard) who have not been treated with suppressive antiviral therapy prior to initiation of study treatment
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Patients with a history of HCV infection who meet one or both of the following criteria:
- Currently receiving curative antiviral treatment
- HCV viral load is above the limit of quantification (HCV RNA positive)
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Patients with history of HIV infection who meet one or more of the following criteria;
- CD4+ count <350 cells/μL
- Viral load >400 copies/μL (local lab assessment)
- Not receiving antiretroviral therapy
- Receiving established antiretroviral therapy for less than 4 weeks prior to the start of trial treatment
- History of AIDS-defining opportunistic infections within 12 months prior to start of trial treatment
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Active or known or history of non-infectious interstitial lung disease/pneumonitis
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Any history or presence of uncontrolled gastrointestinal disorders that could affect the intake and/or absorption of the trial drug (e.g., nausea, vomiting, Crohn's disease, ulcerative colitis, chronic diarrhoea, malabsorption) in the opinion of the investigator
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Active infectious disease requiring systemic therapy, which puts the patient at increased risk in the opinion of the investigator.
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Patients with severe hepatic impairment (classified as Child-Pugh C or score 10-15)
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Known history of allergy to the trial drug(s) or any excipients of the trial drug(s) or contraindication to any of the trial drugs
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Contraindications for MRI or or non-evaluable MRI
研究計画
研究はどのように設計されていますか?
デザインの詳細
- 主な目的:処理
- 割り当て:なし
- 介入モデル:単一グループの割り当て
- マスキング:なし(オープンラベル)
アーム数
武器と介入
参加者グループ / アーム参加者グループ / アーム |
介入・治療介入・治療 |
|---|---|
|
実験的:This is a single-arm, non-comparative, non-randomized, single-center phase 1b study
Eligible patients are adults (≥18 years) with pathologically confirmed primary stage II-IIIA HER2-positive breast cancer, defined as homogenous HER2 3+ on immunohistochemistry. Additional eligibility criteria include WHO performance status 0-1, left ventricular ejection fraction ≥50%, adequate hepatic, renal and bone marrow function, and absence of current or previous other malignancy unless treated without systemic therapy and disease-free for more than five years. |
All patients will receive neoadjuvant treatment with trastuzumab, pertuzumab and zongertinib. Patients with hormone receptor-positive tumours will additionally receive concurrent endocrine therapy with an aromatase inhibitor; premenopausal patients will also receive an LHRH antagonist. Breast MRI will be performed at baseline and after three cycles to assess functional tumour volume (FTV). Patients demonstrating ≥65% FTV reduction will continue the chemotherapy-free regimen for an additional three cycles. Patients with <65% FTV will switch to standard neoadjuvant chemotherapy for three cycles. Following completion of neoadjuvant therapy, patients will undergo surgery within six weeks. Those achieving pCR will continue adjuvant trastuzumab according to ESMO guidelines. Patients without pCR will receive adjuvant chemotherapy according to standard care. |
この研究は何を測定していますか?
主要な結果の測定
主要な結果の測定
結果測定 |
メジャーの説明 |
時間枠 |
|---|---|---|
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Safety
時間枠:Incidence and severity of adverse events (all grades) occuring during treatment and up to 30 days after last administration of study treatment.
|
The primary objective is to evaluate the safety of neoadjuvant chemotherapy-free regimen consisting of trastuzumab, pertuzumab and zongertinib in patients with stage II-IIIA HER2-positive breast cancer. |
Incidence and severity of adverse events (all grades) occuring during treatment and up to 30 days after last administration of study treatment.
|
二次結果の測定
二次結果の測定
結果測定 |
メジャーの説明 |
時間枠 |
|---|---|---|
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Progressive disease during neoadjuvant treatment
時間枠:Patients will participate in the study for approximately 24 weeks (including surgery), with a follow-up period of up to 10 years.
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Progressive disease during neoadjuvant treatment |
Patients will participate in the study for approximately 24 weeks (including surgery), with a follow-up period of up to 10 years.
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Pathological complete response
時間枠:Patients will participate in the study for approximately 24 weeks (including surgery), with a follow-up period of up to 10 years.
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Pathological complete response |
Patients will participate in the study for approximately 24 weeks (including surgery), with a follow-up period of up to 10 years.
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Residual cancer burden
時間枠:Patients will participate in the study for approximately 24 weeks (including surgery), with a follow-up period of up to 10 years.
|
Residual cancer burden |
Patients will participate in the study for approximately 24 weeks (including surgery), with a follow-up period of up to 10 years.
|
|
Radiological response
時間枠:Patients will participate in the study for approximately 24 weeks (including surgery), with a follow-up period of up to 10 years.
|
Radiological response |
Patients will participate in the study for approximately 24 weeks (including surgery), with a follow-up period of up to 10 years.
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Event-free survival
時間枠:Patients will participate in the study for approximately 24 weeks (including surgery), with a follow-up period of up to 10 years.
|
Event-free survival |
Patients will participate in the study for approximately 24 weeks (including surgery), with a follow-up period of up to 10 years.
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|
Overall survival
時間枠:Patients will participate in the study for approximately 24 weeks (including surgery), with a follow-up period of up to 10 years.
|
Overall survival |
Patients will participate in the study for approximately 24 weeks (including surgery), with a follow-up period of up to 10 years.
|
協力者と研究者
協力者
協力者
研究記録日
主要日程の研究
研究開始 (推定)
研究開始
一次修了 (推定)
一次修了
研究の完了 (推定)
研究の完了
試験登録日
最初に提出
最初に提出
QC基準を満たした最初の提出物
QC基準を満たした最初の提出物
最初の投稿 (実際)
最初の投稿
学習記録の更新
投稿された最後の更新 (実際)
投稿された最後の更新
QC基準を満たした最後の更新が送信されました
QC基準を満たした最後の更新が送信されました
最終確認日
最終確認日
詳しくは
本研究に関する用語
キーワード
その他の研究ID番号
その他の研究ID番号
- N25TRN
個々の参加者データ (IPD) の計画
個々の参加者データ (IPD) を共有する予定はありますか?
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