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Clinical Trials on Autosomal Recessive Degenerative and Progressive Cerebellar Ataxia
Total 610 results
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Otsuka Pharmaceutical Development & Commercialization...RecruitingAutosomal Recessive Polycystic Kidney Disease (ARPKD)United States, Belgium, Spain, Germany, United Kingdom, Poland
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Sheba Medical CenterEnrolling by invitationParkinson Disease | Cerebellar Ataxia | Dystonia | Multiple System Atrophy | Corticobasal Degeneration | Progressive Supranuclear Palsy | Essential Tremor | Dementia With Lewy Bodies | Normal Pressure HydrocephalusIsrael
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Rutgers, The State University of New JerseyRecruitingParkinson Disease | Movement Disorders | Huntington Disease | Essential Tremor | Spinocerebellar Ataxias | Dystonia, PrimaryUnited States
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Fondation Ophtalmologique Adolphe de RothschildTerminatedChoroidal NeovascularizationFrance
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Hospices Civils de LyonUnknownAutoimmune Encephalitis | Imbic Encephalitis | Autoimmune Cerebellar Ataxia | Stiff-person SyndromeFrance
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National Institute of Neurological Disorders and...CompletedHealthy | Celiac Disease | Cerebellar AtaxiaUnited States
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Lexeo TherapeuticsRecruitingFriedreich Ataxia | Cardiomyopathy, SecondaryUnited States, Canada
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MeddocRecruiting
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Kadmon Corporation, LLCCompletedPolycystic Kidney, Autosomal RecessiveUnited States
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University of FloridaNational Institutes of Health (NIH); National Institute on Deafness and Other...WithdrawnStroke | Dysphagia | Spinocerebellar Ataxia | Dysarthria | Cerebral Stroke
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Johann Wolfgang Goethe University HospitalCSL BehringCompletedInfections | Lung Disease | Immunodeficiency | Ataxia Telangiectasia
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Weill Medical College of Cornell UniversityNational Heart, Lung, and Blood Institute (NHLBI)RecruitingMyocardial Fibrosis | Cardiomyopathies | Friedreich Ataxia | Cardiac HypertrophyUnited States
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Cairo UniversityRecruitingMedulloblastoma | AtaxiaEgypt
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Instituto Universitario de Oftalmobiología Aplicada...Hospital del Río Hortega; Hospital Clínico Universitario de ValladolidCompletedMultiple Sclerosis | Eye Abnormalities | Parkinson Disease | Ataxia, Cerebellar | Injury BrainSpain
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Newcastle-upon-Tyne Hospitals NHS TrustRecruitingBethlem Myopathy | Ullrich Congenital Muscular Dystrophy 1, Digenic, Col6A1/Col6A2 | Ullrich Congenital Muscular Dystrophy 1, Autosomal Recessive | Ullrich Congenital Muscular Dystrophy 1, Autosomal Dominant | Bethlem Myopathy 1, Autosomal Recessive | UCMD | BTHLM1United Kingdom
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S. Andrea HospitalCompletedMultiple Sclerosis | Cerebellar Ataxia | Hereditary AtaxiaItaly
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Children's Hospital of PhiladelphiaNational Heart, Lung, and Blood Institute (NHLBI)Recruiting
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Mayo ClinicNational Institute on Deafness and Other Communication Disorders (NIDCD)RecruitingPrimary Progressive Aphasia | Apraxia of Speech | PPA | Non-fluent Aphasia | Primary Progressive Non-fluent AphasiaUnited States
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Ludwig-Maximilians - University of MunichCompletedInclusion Body Myositis, Sporadic | Inclusion Body Myopathy, Autosomal-recessive | Inclusion Body Myopathy, Autosomal-dominant | Congenital Cataracts, Facial Dysmorphism, And NeuropathyGermany
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University of California, Los AngelesNational Institute on Aging (NIA); University of Southern CaliforniaUnknownAlzheimer Disease | Corticobasal Degeneration | Primary Progressive Aphasia | Alzheimer Disease, Early Onset | Alzheimer Disease, Late Onset | Dementia, Alzheimer Type | Logopenic Progressive Aphasia | Visuospatial/Perceptual Abilities | Posterior Cortical Atrophy | Executive Dysfunction | Ideomotor ApraxiaUnited States
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Mayo ClinicCompletedPrimary Progressive Aphasia | Aphasia | Semantic Dementia | Apraxia of Speech | Primary Progressive Nonfluent Aphasia | PPA | Non-fluent Aphasia | Progressive AphasiaUnited States
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Larimar Therapeutics, Inc.Clinilabs, Inc.CompletedHealthy Volunteers | Friedreich AtaxiaUnited States
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The University of Texas at DallasEnrolling by invitationPrimary Progressive Aphasia | Apraxia of SpeechUnited States
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University of MinnesotaWithdrawnMild Cognitive Impairment (MCI) | Amyotrophic Lateral Sclerosis (ALS) | Dementia With Lewy Bodies (DLB) | Alzheimer Disease (AD) | Frontotemporal Lobar Degeneration (FTLD) | Parkinsons Disease With Dementia (PDD) | Transient Epileptic Amnesia (TEA) | Temporal Lobe Epilepsy (TLE) | Spinocerebellar Ataxias... and other conditionsUnited States
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Murdoch Childrens Research InstituteUniversity of Sydney; Sydney Children's Hospitals Network; Women's and Children... and other collaboratorsActive, not recruitingAutosomal Recessive Disorder | X-Linked Genetic DiseasesAustralia
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Mayo ClinicRecruitingPrimary Progressive Aphasia | Apraxia of Speech | Primary Progressive Nonfluent Aphasia | Non-fluent AphasiaUnited States
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Origin BiosciencesCompletedMolybdenum Cofactor Deficiency (MoCD) | Rare Autosomal Recessive Disorder | Deficiency of Activity of Molybdenum-dependent Enzymes (Sulfite Oxidase [SOX], Xanthine Dehydrogenase, and Aldehyde Oxidase)United States
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University of MiamiTerminatedApraxia SpeechUnited States
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CENTOGENE GmbH RostockEnrolling by invitationHereditary Diseases | FXN Gene | FRDALebanon
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Beijing Airdoc Technology Co., Ltd.Shanghai Children's Medical CenterRecruiting
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SightGlass Vision, Inc.University of WaterlooActive, not recruitingMyopia, ProgressiveCanada
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Ocumension (Hong Kong) LimitedORA, Inc.; Statistics & Data CorporationActive, not recruiting
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Jeff RabinWithdrawn
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Kyorin UniversityCompletedDisease Progression | Autosomal Dominant Polycystic Kidney DiseaseJapan
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Fundació Institut de Recerca de l'Hospital de la...CompletedCough | Gastroesophageal Reflux | Cerebellar AtaxiaSpain
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Erasmus Medical CenterZonMw: The Netherlands Organisation for Health Research and DevelopmentRecruiting
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Thomas A. Aller, ODSynergEyes, Inc.WithdrawnMyopia | Myopia, ProgressiveUnited States
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Laboratorios Sophia S.A de C.V.Not yet recruiting
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Beijing Airdoc Technology Co., Ltd.Eye & ENT Hospital of Fudan UniversityRecruiting
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Essilor InternationalActive, not recruitingMyopia | Myopia, ProgressiveSingapore
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Tianjin Eye HospitalCompleted
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Aller, Thomas A., ODVisioneering Technologies, IncUnknownMyopia | Myopia, ProgressiveUnited States
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Mayo ClinicNational Eye Institute (NEI)CompletedRetinal Disease | Best Vitelliform Macular Dystrophy | Bestrophinopathy | Adult Onset Vitelliform Macular Dystrophy | Autosomal Dominant VitreoretinalchoroidopathyUnited States
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University of California, San FranciscoNational Institutes of Health (NIH); National Institute on Aging (NIA)Active, not recruitingProgressive Supranuclear Palsy (PSP) | Corticobasal Degeneration (CBD) | Nonfluent Variant Primary Progressive Aphasia (nfvPPA) | Corticobasal Syndrome (CBS) | Cortical-basal Ganglionic Degeneration (CBGD) | Oligosymptomatic/Variant Progressive Supranuclear Palsy (o/vPSP)United States, Canada
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Menicon Co., Ltd.CompletedChildren, Only | Myopia, Progressive
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Imperial College LondonUnknown
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Menicon Co., Ltd.Universidad Europea de Madrid; Clinica novovisionCompletedChildren, Only | Myopia, Progressive
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Mei changlinUnknownHypertension | Autosomal Dominant Polycystic Kidney DiseaseChina
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Mayo ClinicNational Institute of Neurological Disorders and Stroke (NINDS); National Institute... and other collaboratorsRecruitingAmyotrophic Lateral Sclerosis | Progressive Supranuclear Palsy (PSP) | Corticobasal Degeneration (CBD) | GRN Related Frontotemporal Dementia | Behavioral Variant Frontotemporal Dementia (bvFTD) | Semantic Variant Primary Progressive Aphasia (svPPA) | Nonfluent Variant Primary Progressive Aphasia... and other conditionsUnited States, Canada
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Krystal Biotech, Inc.Not yet recruitingAutosomal Recessive IchthyosisUnited States