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Clinical Trials on Bone Marrow Failure Syndromes
Total 10221 results
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Northwell HealthCompletedPure Red Cell Aplasia | Diamond Blackfan Anemia | Blackfan Diamond Syndrome | DBA | Congenital Hypoplastic AnemiaUnited States
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Masonic Cancer Center, University of MinnesotaCompleted
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Masonic Cancer Center, University of MinnesotaTerminated
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OHSU Knight Cancer InstituteNational Cancer Institute (NCI)TerminatedFanconi AnemiaUnited States
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Memorial Sloan Kettering Cancer CenterNational Cancer Institute (NCI); Miltenyi Biotec, Inc.Completed
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Fairview University Medical CenterCompleted
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Dana-Farber Cancer InstituteUnknownFanconi's AnemiaUnited States
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National Cancer Institute (NCI)CompletedDyskeratosis Congenita | Telomere Biology DisordersUnited States
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Adrianna Vlachos, MDTerminatedPure Red Cell Aplasia | Diamond Blackfan AnemiaUnited States
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National Heart, Lung, and Blood Institute (NHLBI)CompletedAnemia, Aplastic | Red-Cell Aplasia, Pure | Anemia, Diamond-BlackfanUnited States
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National Heart, Lung, and Blood Institute (NHLBI)RecruitingSevere Aplastic Anemia | Single Lineage Cytopenias, T-LGL | Hypoplastic MDSUnited States
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University Hospital FreiburgCompletedMyelodysplastic Syndromes | Fanconi Anemia | Dyskeratosis Congenita | Pearson Marrow-pancreas Syndrome | Shwachman-diamond SyndromeSpain, Germany, Switzerland, Austria, Netherlands, Italy, Czech Republic, Belgium, Denmark, Ireland
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Merck Sharp & Dohme LLCTerminatedMyelodysplastic Syndromes | Blood Disease | Bone Marrow Disease
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Assistance Publique - Hôpitaux de ParisEuroFancolenCompleted
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Masonic Cancer Center, University of MinnesotaCompleted
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Children's Hospital Medical Center, CincinnatiNational Heart, Lung, and Blood Institute (NHLBI)CompletedFanconi AnemiaUnited States
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Shenzhen Geno-Immune Medical InstituteUnknown
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Medical College of WisconsinMemorial Sloan Kettering Cancer CenterCompleted
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Neena Kapoor, M.D.Withdrawn
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National Heart, Lung, and Blood Institute (NHLBI)CompletedPancytopenia | Fanconi's AnemiaUnited States
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Boston Children's HospitalNational Heart, Lung, and Blood Institute (NHLBI); Children's Hospital Medical...Completed
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Fred Hutchinson Cancer CenterNational Cancer Institute (NCI)CompletedFanconi AnemiaUnited States, Brazil
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University of MinnesotaUnknown
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Xiaofan ZhuAvailableFanconi Anemia | Autosomal or Sex Linked Recessive Genetic Disease | Bone Marrow Hematopoiesis Failure, Multiple Congenital Abnormalities, and Susceptibility to Neoplastic Diseases. | Hematopoiesis Maintainance.China
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Memorial Sloan Kettering Cancer CenterRecruitingAplastic Anemia | Cytopenia | Hypocellular MarrowUnited States
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Peking University People's HospitalUnknownAplastic Anemia | Stem Cell Transplant Complications | Engraft FailureChina
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St. Jude Children's Research HospitalBaylor College of Medicine; Children's Hospital of Philadelphia; Dana-Farber... and other collaboratorsRecruitingMyelodysplastic Syndromes | Sickle Cell Disease | Fanconi Anemia | Severe Congenital Neutropenia | Bone Marrow Failure Syndromes | Blood Coagulation Disorder | Erythrocyte Disorder | Leukocyte Disorder | Hemostasis | Dyskeratosis Congenita | Diamond-Blackfan Anemia | Congenital Thrombocytopenia | Myeloproliferative...United States
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Everett MeyerCompletedLeukemia, Myeloid | Myeloproliferative Disorders | Anemia | Neural Tube Defects | Myelodysplastic Syndromes (MDS) | Bone Marrow Transplant FailureUnited States
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Children's Hospital Medical Center, CincinnatiMemorial Sloan Kettering Cancer Center; Fred Hutchinson Cancer CenterRecruitingFanconi Anemia | Myelodysplastic Syndrome (MDS) | Acute Myelogenous Leukemia (AML) | Severe Marrow FailureUnited States
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M.D. Anderson Cancer CenterTerminatedLeukemia | Aplastic Anemia | Non Hodgkin's LymphomaUnited States
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Institute of Hematology & Blood Diseases Hospital...Fosun Pharmaceutical Distribution Jiangsu co., LimitedNot yet recruiting
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Rocket Pharmaceuticals Inc.UnknownFanconi Anemia Complementation Group AUnited States
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Children's Hospital Medical Center, CincinnatiAmgenCompleted
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Rocket Pharmaceuticals Inc.Enrolling by invitationFanconi Anemia | Fanconi Anemia Complementation Group ASpain
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Baylor College of MedicineThe Methodist Hospital Research Institute; Center for Cell and Gene Therapy...TerminatedFanconi Anemia | Severe Aplastic AnemiaUnited States
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Cystinosis Research FoundationUnknownCystinosis | Nephropathic Cystinosis | Renal Fanconi SyndromeUnited States
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Masonic Cancer Center, University of MinnesotaRecruitingAplastic Anemia | Dyskeratosis CongenitaUnited States
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Masonic Cancer Center, University of MinnesotaCompletedAplastic Anemia | Dyskeratosis CongenitaUnited States
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Memorial Sloan Kettering Cancer CenterPediatric Brain Tumor ConsortiumTerminatedFanconi Anemia | Myelodysplastic Syndrome (MDS) | Acute Myelogenous Leukemia (AML)United States
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Novartis PharmaceuticalsNot yet recruitingAplastic Anemia
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Peking Union Medical College HospitalRecruiting
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The First Affiliated Hospital of Soochow UniversityRecruiting
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European Society for Blood and Marrow TransplantationGenzyme, a Sanofi CompanyCompletedAplastic AnemiaSwitzerland, United Kingdom, Germany, Italy, France, Saudi Arabia
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Incyte CorporationNo longer available
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Novartis PharmaceuticalsCompleted
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National Heart, Lung, and Blood Institute (NHLBI)CompletedAplastic AnemiaUnited States
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University of Sao PauloCompleted
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Hospital Universitario Dr. Jose E. GonzalezWithdrawn
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Asan Medical CenterCompletedAplastic AnemiaKorea, Republic of
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Shenzhen Zhongxing Yangfan Biotech Co. Ltd.The 12th Guangzhou Municipal Hospital; Liu Hua Qiao HospitalUnknownAnemia, AplasticChina