- ICH GCP
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Clinical Trials on Brain Diseases, Metabolic
Total 380587 results
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ISU Abxis Co., Ltd.Completed
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BioMarin PharmaceuticalRecruitingPhenylketonuria (PKU)United States, Germany, Italy
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Nutricia ResearchCompleted
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BioMarin PharmaceuticalActive, not recruiting
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BioMarin PharmaceuticalCompletedPhenylketonuria (PKU)United States, Turkey, Canada, France, Germany, Italy, United Kingdom
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Sutphin DrugsUnknownHereditary Tyrosinemia, Type IIndia
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Charite University, Berlin, GermanyJohannes Gutenberg University MainzCompletedPhenylketonuria | Endothelial Dysfunction
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Washington University School of MedicineUniversity of Missouri-Columbia; Northwestern University; Oregon Health and Science... and other collaboratorsTerminated
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SanofiCompletedGaucher's DiseaseUnited States
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ShireCompletedGaucher DiseaseUnited States, Spain, United Kingdom, Israel
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ShireCompletedGaucher DiseaseIsrael, Romania, Serbia
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ShireCompletedGaucher Disease, Type 3Egypt, India, Tunisia
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ISU Abxis Co., Ltd.CompletedGaucher Disease, Type 1
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Genzyme, a Sanofi CompanyCompletedGaucher Disease, Type 1United States, United Kingdom, Bulgaria, Canada, Colombia, India, Israel, Lebanon, Mexico, Russian Federation, Serbia, Tunisia
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Genzyme, a Sanofi CompanyCompletedGaucher Disease, Type 1United States, France, Germany, Italy, Brazil, Australia, Argentina, Canada, Egypt, Russian Federation, Spain, United Kingdom
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Genzyme, a Sanofi CompanyWithdrawnGaucher Disease, Type 1United States, India
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ISU Abxis Co., Ltd.Completed
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Amicus TherapeuticsTerminatedType 1 Gaucher DiseaseUnited States, United Kingdom
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PTC TherapeuticsAxio Research. LLCCompleted
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NYU Langone HealthGenzyme, a Sanofi CompanyCompleted
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Guy's and St Thomas' NHS Foundation TrustUnknownCardiovascular Diseases | PhenylketonuriasUnited Kingdom
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BioMarin PharmaceuticalRecruitingPhenylketonuria (PKU)United States
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PTC TherapeuticsCompletedBH4 Deficiency | HyperphenylalaninemiaUnited States
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Homology Medicines, IncTerminatedPhenylketonuria | Phenylketonurias | PAH DeficiencyUnited States
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Homology Medicines, IncTerminated
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Taipei Veterans General Hospital, TaiwanBioMarin PharmaceuticalUnknownPAH Deficiency | Pku Phenylketonuria
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Nutricia UK LtdCompletedPhenylketonurias | Hyperphenylalaninaemia, Type IUnited Kingdom
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University of Southern CaliforniaBioMarin PharmaceuticalCompleted
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Stanford UniversityBioMarin PharmaceuticalWithdrawnClassical Phenylketonuria(PKU)
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metaX Institut fuer Diatetik GmbHBirmingham Children's HospitalCompletedPhenylketonurias | Hyperphenylalaninaemia | Tetrahydrobiopterin DeficiencyUnited Kingdom
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BioMarin PharmaceuticalActive, not recruitingPhenylketonuria (PKU)United States, Germany
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Homology Medicines, IncEnrolling by invitationPhenylketonuria | PAH DeficiencyUnited States
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BioMarin PharmaceuticalCompletedPhenylketonuria (PKU)United States
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BioMarin PharmaceuticalCompletedPhenylketonuria (PKU)United States
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University of British ColumbiaRare Disease Foundation, Vancouver, CanadaCompleted
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University of GlasgowUnknownPhenylketonuria (PKU)United Kingdom
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University Hospital, ToursInstitut National de la Santé Et de la Recherche Médicale, FranceCompletedPKU | HyperphenylalaninemiaFrance
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Dr. Linda RandolphBioMarin PharmaceuticalTerminated
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Andrea GropmanEunice Kennedy Shriver National Institute of Child Health and Human Development... and other collaboratorsRecruitingBrain Diseases, Metabolic, Inborn | Amino Acid Metabolism, Inborn Errors | Urea Cycle DisordersUnited States, Canada, Germany, Switzerland
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National Institute of Neurological Disorders and...Completed
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Luca RonfaniUniversity of TriesteCompletedUrea Cycle Disorders, Inborn | Other Metabolic DiseasesItaly
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University of PisaCompletedTo Determine the Effect of GLP1 on Cognitive Function, Brain Glucose Metabolism and Neuroplasticity.Glucose Metabolism Disorders | Obesity | Degenerative Brain DisorderItaly
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University of MinnesotaRecruitingGaucher Disease, Type 3United States
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TakedaActive, not recruiting
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Shaare Zedek Medical CenterShireCompletedGaucher Disease, Type 1
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Shaare Zedek Medical CenterPfizerCompletedGaucher Disease, Type 1
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National Taiwan University HospitalSanofiCompleted
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ShireCompletedGaucher Disease, Type 1Israel, Paraguay, Argentina, Russian Federation, Tunisia
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ShireCompletedGaucher Disease, Type 1Spain, Israel, United States, India, Paraguay, United Kingdom, Russian Federation, Tunisia, Argentina
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PfizerWithdrawnType 1 Gaucher DiseaseUnited States