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- US Clinical Trials Registry
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Clinical Trials on Ceroid Storage Disease
Total 379665 results
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National Institute of Arthritis and Musculoskeletal...CompletedMyositis | Dermatomyositis | Polymyositis | Glycogen Storage Disease Type II | Glycogen Storage Disease Type VIIUnited States
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Genzyme, a Sanofi CompanyRecruitingPompe Disease (Late-onset) | Glycogen Storage Disease Type II (GSD-II) | Glycogenesis 2 Acid Maltase DeficiencyCroatia, United States, Italy, Belgium, Czechia
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National Taiwan University HospitalRecruiting
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National Taiwan University HospitalRecruiting
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Amicus TherapeuticsActive, not recruitingPompe DiseaseUnited States, Netherlands, United Kingdom, Australia, Germany, New Zealand
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University of FloridaEunice Kennedy Shriver National Institute of Child Health and Human Development...Completed
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Asklepios Biopharmaceutical, Inc.Active, not recruiting
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University of FloridaLacerta TherapeuticsCompletedPompe DiseaseUnited States
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University of FloridaBioMarin PharmaceuticalCompleted
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LMU KlinikumGenzyme, a Sanofi CompanyCompletedPompe DiseaseGermany, Taiwan, Italy
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Amicus TherapeuticsCompleted
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National Taiwan University HospitalCompleted
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National Taiwan University HospitalUnknown
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Genzyme, a Sanofi CompanyCompletedGlycogen Storage Disease Type IIUnited States, France, Germany, Israel, Italy, Netherlands, Taiwan
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Fundació Institut de Recerca de l'Hospital de la...Genzyme, a Sanofi CompanyUnknown
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National Taiwan University HospitalCompleted
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Amicus TherapeuticsCompletedGlycogen Storage Disease Type II | Pompe DiseaseUnited States
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Sunnybrook Health Sciences CentreCanadian Institutes of Health Research (CIHR)UnknownAtherosclerosis | Carotid Artery DiseaseCanada
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Our Lady of the Lake HospitalLouisiana State University Health Sciences Center in New OrleansCompletedPost-Surgical Injection With Triamcinolone Versus Triamcinolone/Fluorouracil in Treatment of KeloidsKeloid | Keloid Scar Following SurgeryUnited States
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Dallas VA Medical CenterAmerican Heart AssociationTerminatedStroke | Carotid Artery DiseaseUnited States
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Genzyme, a Sanofi CompanyApproved for marketingGlycogen Storage Disease Type II (GSD-II) | Acid Maltase Deficiency Disease | Glycogenosis 2 | Pompe Disease (Late-Onset)United States
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Albert Einstein College of MedicineNational Heart, Lung, and Blood Institute (NHLBI)CompletedCarotid Artery Plaque
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Peking Union Medical College HospitalRecruiting
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IRCCS Policlinico S. DonatoUniversity of Pavia; Ministry of Health, ItalyCompleted
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Terumo Europe N.V.CompletedCarotid Artery StenosisBelgium, Spain, Czechia, France, Serbia, Netherlands, Germany, Hungary, North Macedonia, Latvia, Poland, Portugal, Slovakia
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Ziv HospitalUnknownCarotid Artery StenosisIsrael
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European Society for Blood and Marrow TransplantationMallinckrodtCompletedSteroid Refractory GVHDSpain, United Kingdom, Sweden, Italy, Israel, France, Denmark, Germany, Poland, Turkey, Romania, Belgium, Greece, Russian Federation
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Iconic Therapeutics, Inc.CompletedUveal Melanoma | Choroid NeoplasmUnited States
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University of FloridaPrometheus LaboratoriesCompletedInflammatory Bowel Disease | Glycogen Storage Disease Type IaUnited States
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Mr Ihab AliCompletedCarotid Artery Diseases | Peripheral Artery DiseaseEgypt
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Cedars-Sinai Medical CenterNational Heart, Lung, and Blood Institute (NHLBI); American Heart AssociationCompletedCarotid Artery DiseaseUnited States
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Canadian Atherosclerosis Imaging NetworkCanadian Institutes of Health Research (CIHR)Completed
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Assaf-Harofeh Medical CenterCompleted
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University Hospital OlomoucRecruitingStroke, Ischemic | Stenosis, CarotidCzechia
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University Hospital OstravaPalacky UniversityCompletedInternal Carotid Artery StenosisCzech Republic
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Huashan HospitalNot yet recruitingPompe Disease (Late-onset)China
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Rambam Health Care CampusRecruitingPompe Disease Infantile-OnsetIsrael
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Astellas Gene TherapiesRecruitingPompe Disease (Late-onset)United States, United Kingdom
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Amicus TherapeuticsRecruitingPompe Disease (Late-onset)United States, Taiwan, Japan, Australia, Canada
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Genzyme, a Sanofi CompanyRecruitingGlycogen Storage Disease Type II | Pompe DiseaseHungary, Croatia, Serbia, United States, Argentina, Australia, Belgium, Brazil, Bulgaria, Canada, Chile, China, Colombia, Denmark, France, Germany, Greece, Hong Kong, India, Indonesia, Israel, Italy, Japan, Jordan, Korea, Republic of, Kuwait and more
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Amicus TherapeuticsActive, not recruitingPompe Disease (Late-onset)United States, Germany, Taiwan, Belgium, Australia, Slovenia, Spain, Netherlands, Hungary, Japan, Austria, United Kingdom, France, Argentina, Canada, Sweden, Denmark, New Zealand, Greece, Korea, Republic of, Bosnia and Herzegovina, Ita... and more
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Duke UniversityGenzyme, a Sanofi CompanyActive, not recruitingPompe Disease (Late-onset) | Pompe Disease | GAA DeficiencyUnited States
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Amicus TherapeuticsAvailablePompe Disease Infantile-OnsetTaiwan, United States, Italy
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BioMarin PharmaceuticalTerminatedLate-onset Pompe DiseaseUnited States, United Kingdom
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Duke UniversityWithdrawnPompe Disease (Late-onset)United States
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Rambam Health Care CampusCompletedEnzyme Replacement Therapy in Pompe Disease
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Genzyme, a Sanofi CompanyCompletedGlycogen Storage Disease Type II | Pompe Disease Infantile-OnsetUnited States, France, South Africa
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Peking University Third HospitalCompletedCarotid Endarterectomy | Coronary Artery Bypass GraftingChina