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Clinical Trials on Congenital Factor VIII (FVIII) Deficiency
Total 542 results
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Baylor College of MedicineShireActive, not recruiting
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University of UtahThe Hospital for Sick Children; Boston Children's HospitalCompletedAtherosclerosis | Down Syndrome | Cardiovascular Risk FactorUnited States
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McGill UniversityEthiopian Health and Nutrition Research Institute; Micronutrient InitiativeCompletedGoiter | Iodine Deficiency | CretinismCanada
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Future University in EgyptRecruitingBimaxillary Protrusion | Class III Malocclusion | Class II Division 1 Malocclusion | Crowding, ToothEgypt
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Cairo UniversityUnknownClass III Malocclusion | Class II Malocclusion
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Cairo UniversityUnknownClass II Division 1 Malocclusion
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Trakya UniversityIstanbul UniversityCompletedMaxillary Retrognathism | Rapid Maxillary Expansion | Face MaskTurkey
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Assistance Publique - Hôpitaux de ParisCompleted
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Al-Azhar UniversityEnrolling by invitationEffect of PowerScope Appliance in Treatment of Patients With Class 3 MalocclusionEgypt
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Future University in EgyptCompletedBimaxillary Protrusion | Class III Malocclusion | Crowding, Tooth | Class II MalocclusionEgypt
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Damascus UniversityHama UniversityCompletedCross Bite | Orthodontic Appliance Complication | Class III MalocclusionSyrian Arab Republic
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rEVO BiologicsCompletedAntithrombin III DeficiencyUnited States, France, United Kingdom, Germany, Canada, Austria, Australia, Italy
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Richard FryeAutism Discovery and Treatment FoundationRecruitingEpilepsy | Neurodevelopmental Disorders | Autism Spectrum Disorder | Down Syndrome | Mitochondrial Encephalomyopathies | Pediatric Acute-Onset Neuropsychiatric Syndrome | Cerebral Folate Deficiency | Pediatric Autoimmune Neuropsychiatric Disorder Associated With Streptococcal InfectionUnited States
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Universitair Ziekenhuis BrusselNot yet recruiting
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Memorial Sloan Kettering Cancer CenterBoston Children's Hospital; Fred Hutchinson Cancer Center; Children's Hospital... and other collaboratorsCompletedLeukemia | Myelodysplastic Syndrome | Aplastic AnemiaUnited States
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Massachusetts General HospitalEunice Kennedy Shriver National Institute of Child Health and Human Development... and other collaboratorsCompletedAdherence, Patient | Zika Virus InfectionPuerto Rico
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Fondazione Policlinico Universitario Agostino Gemelli...RecruitingNoonan Syndrome | Costello Syndrome | RASopathy | Cardio-Facio-Cutaneous SyndromeItaly
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Fondazione Policlinico Universitario Agostino Gemelli...RecruitingNoonan Syndrome | Costello Syndrome | RASopathy | Cardio-Facio-Cutaneous SyndromeItaly
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Hospital de Niños R. Gutierrez de Buenos AiresRecruitingChagas Disease | SyphilisArgentina
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Fondazione Policlinico Universitario Agostino Gemelli...RecruitingNoonan Syndrome | Costello Syndrome | RASopathy | Cardio-Facio-Cutaneous SyndromeItaly
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Pontifícia Universidade Católica de Minas GeraisUnknownCleft Lip and Palate | Class III Malocclusion | Palatal Expansion Technique | Skeletal MalocclusionBrazil
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Novo Nordisk A/SCompletedChronic Kidney Disease | Turner Syndrome | Noonan Syndrome | Chronic Renal Insufficiency | Growth Hormone Disorder | Growth Hormone Deficiency in Children | Adult Growth Hormone Deficiency | Genetic Disorder | Foetal Growth Problem | Small for Gestational AgeIsrael, Saudi Arabia, Spain, Argentina, Russian Federation, Germany, Netherlands, Italy, Belgium, United Kingdom, Slovenia, Ireland, Sweden, Denmark, Hungary, Finland, Norway, France, Czechia, Lithuania, Luxembourg, Serbia, Switzerland
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Wake Forest University Health SciencesCompletedCardiovascular Diseases | Diabetes | Metabolic Syndrome | Liver Fat | Cardiovascular Risk Factor | Diet Habit | Dietary Modification | High Cholesterol | Triglycerides High | Low-density-lipoprotein-type | HDL Cholesterol, Low Serum | High Blood Sugar | Intra-abdominal Fat | High Density Lipoprotein DeficiencyUnited States
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Assistance Publique - Hôpitaux de ParisEuroFancolenCompleted
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Masonic Cancer Center, University of MinnesotaCompleted
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Children's Hospital Medical Center, CincinnatiNational Heart, Lung, and Blood Institute (NHLBI)CompletedFanconi AnemiaUnited States
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Shenzhen Geno-Immune Medical InstituteUnknown
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Medical College of WisconsinMemorial Sloan Kettering Cancer CenterCompleted
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Neena Kapoor, M.D.Withdrawn
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National Heart, Lung, and Blood Institute (NHLBI)CompletedPancytopenia | Fanconi's AnemiaUnited States
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Boston Children's HospitalNational Heart, Lung, and Blood Institute (NHLBI); Children's Hospital Medical...Completed
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Fred Hutchinson Cancer CenterNational Cancer Institute (NCI)CompletedFanconi AnemiaUnited States, Brazil
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Children's Hospital Medical Center, CincinnatiFDA Office of Orphan Products DevelopmentCompleted
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Office of Rare Diseases (ORD)UnknownAdrenal Hyperplasia, CongenitalUnited States, Brazil, France
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University of MinnesotaUnknown
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Boston Children's HospitalCompleted
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Masonic Cancer Center, University of MinnesotaCompletedFanconi AnemiaUnited States
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Hospital Universitari Vall d'Hebron Research InstituteCIEMAT; CIBERERCompleted
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National Heart, Lung, and Blood Institute (NHLBI)Children's Hospital Medical Center, CincinnatiCompletedFanconi AnemiaUnited States
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Baylor College of MedicineCenter for Cell and Gene Therapy, Baylor College of Medicine; University of...TerminatedFANCONI ANEMIAUnited States
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University of MinnesotaCompleted
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Sun Yat-sen UniversityRecruitingColorectal Cancer Stage II | Colorectal Cancer Stage III | MSI-H | Mmr DeficiencyChina
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Grifols Biologicals, LLCActive, not recruitingAntithrombin III Deficiency
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Dr. Siyami Ersek Thoracic and Cardiovascular Surgery...CompletedExtracorporeal Membrane Oxygenation Complication | Antithrombin III DeficiencyTurkey
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Zagazig UniversityCompletedVitamin D Deficiency | Sickle Cell Disease | Bone Mineral Density | Health Related Quality of Life | Hand Grip StrengthEgypt
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Masonic Cancer Center, University of MinnesotaCompleted
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Masonic Cancer Center, University of MinnesotaTerminated
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OHSU Knight Cancer InstituteNational Cancer Institute (NCI)TerminatedFanconi AnemiaUnited States
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Memorial Sloan Kettering Cancer CenterNational Cancer Institute (NCI); Miltenyi Biotec, Inc.Completed
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Duke UniversityCompletedHemoglobinopathies | Thalassemia | Lysosomal Storage Disease | Immunodeficiencies | Inborn Errors of Metabolism | Sickle Cell | Non Malignant Disorders | Congenital Marrow FailuresUnited States