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Clinical Trials on Congenital Factor VIII (FVIII) Deficiency
Total 542 results
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Fairview University Medical CenterCompleted
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Dana-Farber Cancer InstituteUnknownFanconi's AnemiaUnited States
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Novo Nordisk A/SCompletedTurner Syndrome | Growth Hormone Disorder | Growth Hormone Deficiency in Children | Genetic Disorder | Foetal Growth Problem | Small for Gestational Age | Growth Disorder | Idiopathic Short StatureGermany
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Bellicum PharmaceuticalsTerminatedHemoglobinopathies | Hemophagocytic Lymphohistiocytosis | Metabolic Disorders | Primary Immune Deficiency Disorders | Inherited Bone Marrow Failure SyndromeUnited States
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Damascus UniversityCompletedMalocclusion, Angle Class IIISyrian Arab Republic
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National Human Genome Research Institute (NHGRI)RecruitingMetabolic Disease | Purine-Pyrimidine Metabolism | AICDA, OMIM *605257, Immunodeficiency With Hyper-IgM, Type 2; HIGM2 | UNG, OMIM *191525, Hyper-IgM Syndrome 5 | NT5C3A<TAB>, OMIM *606224, Anemia, Hemolytic, Due to UMPH1 Deficiency | UMPS, OMIM *613891, Orotic Aciduria | DHODH, OMIM *126064,... and other conditionsUnited States
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Cairo UniversityRecruitingMalocclusion | Angle Class II | Mandible SmallEgypt
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Rio de Janeiro State UniversityRecruitingMalocclusion, Angle Class IIIBrazil
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University of Alberta, Graduate Orthodontic ProgramCompleted
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University of California, San FranciscoCompletedSickle Cell Disease | Hemoglobinopathies | Thalassemia | Hematologic Malignancies | Immunodeficiencies | Fanconi's Anemia | Nonmalignant Diseases | Genetic Inborn Errors of MetabolismUnited States
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McGill University Health Centre/Research Institute...RecruitingPeroxisome Biogenesis Disorder | Zellweger Spectrum Disorder | RCDP - Rhizomelic Chondrodysplasia Punctata | D-Bifunctional Protein Deficiency | Alpha-Methylacyl-CoA Racemase Deficiency | Peroxisomal Acyl-CoA Oxidase Deficiency | Peroxisomal Acyl-CoA Oxidase 2 Deficiency | ATP Binding Cassette Subfamily... and other conditionsCanada
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Assistance Publique - Hôpitaux de ParisNot yet recruiting
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University of California, San FranciscoCompletedSickle Cell Disease | Hemoglobinopathies | Thalassemia | Hematologic Malignancies | Immunodeficiencies | Fanconi's Anemia | Nonmalignant Diseases | Genetic Inborn Errors of MetabolismUnited States
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University of California, San FranciscoThrasher Research FundCompletedSickle Cell Disease | Hemoglobinopathies | Fanconi Anemia | Thalassemia | Hematologic Malignancies | Immunodeficiencies | Nonmalignant Diseases | Genetic Inborn Errors of MetabolismUnited States
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Ziekenhuis Oost-LimburgUnknownMaxillary Hypoplasia | Malocclusion, Angle Class IIIBelgium
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Bellicum PharmaceuticalsTerminatedLymphoma, Non-Hodgkin | Myelodysplastic Syndromes | Acute Lymphoblastic Leukemia | Primary Immunodeficiency | Anemia, Sickle Cell | Hemoglobinopathies | Fanconi Anemia | Anemia, Aplastic | Thalassemia | Cytopenia | Diamond Blackfan Anemia | Leukemia, Acute Myeloid (AML), ChildItaly
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Gary M Brittenham, MDCompletedVitamin D Deficiency | Asthma | Sickle Cell Disease | Acute Chest Syndrome | Respiratory InfectionsUnited States
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Fayoum UniversityCompleted
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Cairo UniversityUnknown
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Rocket Pharmaceuticals Inc.Active, not recruitingFanconi Anemia Complementation Group ASpain
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Joanne Kurtzberg, MDAldagenCompletedAnemia, Aplastic | MDS | Inborn Errors of Metabolism | Congenital Marrow Failure | Congenital Immunodeficiency SyndromeUnited States
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Ferring PharmaceuticalsTerminatedGrowth Hormone Deficiency | Turner's SyndromeFrance
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Rocket Pharmaceuticals Inc.UnknownFanconi Anemia Complementation Group AUnited States
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Children's Hospital Medical Center, CincinnatiAmgenCompleted
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Rocket Pharmaceuticals Inc.Enrolling by invitationFanconi Anemia | Fanconi Anemia Complementation Group ASpain
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University of New MexicoCompletedRetinitis Pigmentosa | Age Related Macular Degeneration | Congenital Stationary Night Blindness | ColorblindnessUnited States
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Baylor College of MedicineThe Methodist Hospital Research Institute; Center for Cell and Gene Therapy...TerminatedFanconi Anemia | Severe Aplastic AnemiaUnited States
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Washington University School of MedicineRecruitingSevere Combined Immunodeficiency | Chronic Granulomatous Disease | DiGeorge Syndrome | Hemophagocytic Lymphohistiocytosis | Wiskott-Aldrich Syndrome | X-linked Lymphoproliferative Syndrome | X-linked Agammaglobulinemia | Chediak-Higashi Syndrome | IPEX | Autoimmune Lymphoproliferative Syndrome | Common Variable... and other conditionsUnited States
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First Affiliated Hospital Xi'an Jiaotong UniversitySimcere CompanyRecruitingCerebral Infarction | G6PD DeficiencyChina
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Imperial College LondonTerminatedHereditary Haemorrhagic TelangiectasiaUnited Kingdom
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Assistance Publique - Hôpitaux de ParisCompletedIntellectual Deficiency | Cerebral AbnormalityFrance
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University of California, San FranciscoNational Cancer Institute (NCI)CompletedLeukemia | Thrombocytopenia | Fanconi Anemia | Congenital Amegakaryocytic Thrombocytopenia | Severe Congenital Neutropenia | Diamond-blackfan AnemiaUnited States
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University of Sao PauloFundação de Amparo à Pesquisa do Estado de São Paulo; Coordenação de Aperfeiçoamento...CompletedMalocclusion, Angle Class III | Crossbite (Anterior) (Posterior)Brazil
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Advanced Osteotomy Tools (AOT) AGClinical Trial Unit, University Hospital Basel, SwitzerlandCompletedAbnormalities, Jaw | Malocclusion, Angle Class IIIGermany, Austria, Switzerland
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Makerere UniversityCompletedMalaria | Sickle Cell AnemiaUganda
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University Hospital, AngersUniversity of Angers, AngersUnknownIsolated Growth Hormone Deficiency | Turner Syndrome | Pediatrics | Social Cognition | Cognitive Functions
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Novo Nordisk A/SCompletedChronic Kidney Disease | Turner Syndrome | Chronic Renal Insufficiency | Growth Hormone Disorder | Growth Hormone Deficiency in Children | Genetic Disorder | Delivery Systems | Foetal Growth Problem | Small for Gestational AgeFrance
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Novo Nordisk A/SCompletedChronic Kidney Disease | Turner Syndrome | Chronic Renal Insufficiency | Growth Hormone Disorder | Growth Hormone Deficiency in Children | Genetic Disorder | Delivery Systems | Foetal Growth Problem | Small for Gestational AgeFrance
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Novo Nordisk A/SCompletedTurner Syndrome | Growth Hormone Disorder | Growth Hormone Deficiency in Children | Genetic DisorderJapan
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Novo Nordisk A/SCompletedTurner Syndrome | Growth Hormone Disorder | Growth Hormone Deficiency in Children | Genetic DisorderIsrael
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University of GaziantepCompletedMalocclusion, Angle Class IIITurkey
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Alexandria UniversityCompletedMalocclusion, Angle Class IIIEgypt
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University of OxfordMahidol University; Ministry of Health, ThailandRecruitingIron Deficiency AnemiaThailand
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University Hospital, EssenFederal Ministry of Education and Reserach (BMBF)CompletedDetection of Frequency, Severity and Progression of Cardiovascular Diseases in Patients With HIV-infection. | Effect on Cardiovascular Risk and Life Quality by Age, Gender, Classic Cardiovascular Risk Factors, | HIV-specific Cardiovascular Risk Factors, Cardiovascular Medication, Antiretroviral...Germany
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Baylor College of MedicineNational Institute of Arthritis and Musculoskeletal and Skin Diseases (NIAMS) and other collaboratorsCompletedRothmund-Thomson SyndromeUnited States
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Rhythm Pharmaceuticals, Inc.CompletedBardet-Biedl Syndrome | POMC DeficiencyNetherlands, United States, Germany, Canada, Puerto Rico, United Kingdom
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National Institute of Allergy and Infectious Diseases...Albert Einstein College of MedicineRecruitingInfections | Immune System Diseases | Pneumonia | Job Syndrome | STAT3 Transcription FactorUnited States
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Cairo UniversityActive, not recruitingMaxillofacial Abnormalities | Skeletal Malocclusion | Mandible PrognathismEgypt
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Ferring PharmaceuticalsTerminated
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Merck KGaA, Darmstadt, GermanyCompletedGrowth Hormon Deficiency | Turner Syndrome in Pre-pubertal Children