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Clinical Trials on Congenital Sucrase-isomaltase Deficiency (CSID)
Total 368 results
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Al-Azhar UniversityRecruitingMaxillary Deficiency | Maxillary RetrusionEgypt
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University of AlexandriaRecruiting
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Menzies School of Health ResearchPATH; Indonesia University; Institute of Tropical Medicine, Belgium; UNITAID; Burnet... and other collaboratorsRecruitingVivax Malaria | G6PD DeficiencyIndonesia
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Macfarlane Burnet Institute for Medical Research...PATH; UNITAID; University of Melbourne; Menzies School of Health Research; Medicines... and other collaboratorsRecruitingVivax Malaria | G6PD DeficiencyPapua New Guinea
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National Medical Research Center for Children's...RecruitingVitamin D Deficiency | Osteoporosis | Osteopenia | Phosphorus and Calcium Disorders | Bullosa EpidermolysisRussian Federation
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Universitas PadjadjaranHasan Sadikin General HospitalCompletedVitamin D Deficiency | Tuberculosis | ThalassemiaIndonesia
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Children's Hospital Los AngelesLucile Packard Children's HospitalTerminatedMetabolic Diseases | Stem Cell Transplantation | Chronic Granulomatous Disease | Bone Marrow Transplantation | Thalassemia | Wiskott-Aldrich Syndrome | Genetic Diseases | Peripheral Blood Stem Cell Transplantation | Pediatrics | Diamond-Blackfan Anemia | Allogeneic Transplantation | Combined Immune Deficiency | X-linked Lymphoproliferative Disease
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Columbia UniversityUnknownSevere Combined Immunodeficiency | Fanconi Anemia | Bone Marrow Failure | OsteopetrosisUnited States
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Dr. Prayuth SudathipMedicines for Malaria VentureCompletedMalaria, Vivax | G6PD DeficiencyThailand
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Ferring PharmaceuticalsCompletedTurner's Syndrome | Human Growth Hormone DeficiencyFrance
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Zhejiang UniversityUnknownPregnancy | Congenital Hypothyroidism | Iodine DeficiencyChina
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Federal Research Institute of Pediatric Hematology...Not yet recruitingSevere Congenital Neutropenia | GATA2 DeficiencyRussian Federation
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Lucas Otieno Tina, MD MScGlaxoSmithKline; Strathmore UniversityCompletedSickle Cell Disease | Zinc Deficiency | Infection
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McGill UniversityEthiopian Health and Nutrition Research Institute; Micronutrient InitiativeCompletedGoiter | Iodine Deficiency | CretinismCanada
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Indiana Hemophilia &Thrombosis Center, Inc.Genentech, Inc.Recruiting
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Cairo UniversityUnknownClass II Division 1 Malocclusion
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Assistance Publique - Hôpitaux de ParisCompleted
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Richard FryeAutism Discovery and Treatment FoundationRecruitingEpilepsy | Neurodevelopmental Disorders | Autism Spectrum Disorder | Down Syndrome | Mitochondrial Encephalomyopathies | Pediatric Acute-Onset Neuropsychiatric Syndrome | Cerebral Folate Deficiency | Pediatric Autoimmune Neuropsychiatric Disorder Associated With Streptococcal InfectionUnited States
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Baxalta now part of ShireCompletedHemophilia A | Congenital Factor VIII (FVIII) DeficiencyUnited Kingdom, France, Germany, Hungary
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Memorial Sloan Kettering Cancer CenterBoston Children's Hospital; Fred Hutchinson Cancer Center; Children's Hospital... and other collaboratorsCompletedLeukemia | Myelodysplastic Syndrome | Aplastic AnemiaUnited States
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Novo Nordisk A/SCompletedCongenital Bleeding Disorder | Acquired Bleeding Disorder | Acquired Haemophilia | Congenital FVII Deficiency | Glanzmann's DiseaseGermany
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Novo Nordisk A/SCompletedChronic Kidney Disease | Turner Syndrome | Noonan Syndrome | Chronic Renal Insufficiency | Growth Hormone Disorder | Growth Hormone Deficiency in Children | Adult Growth Hormone Deficiency | Genetic Disorder | Foetal Growth Problem | Small for Gestational AgeIsrael, Saudi Arabia, Spain, Argentina, Russian Federation, Germany, Netherlands, Italy, Belgium, United Kingdom, Slovenia, Ireland, Sweden, Denmark, Hungary, Finland, Norway, France, Czechia, Lithuania, Luxembourg, Serbia, Switzerland
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Boston Children's HospitalCompleted
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Masonic Cancer Center, University of MinnesotaCompletedFanconi AnemiaUnited States
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Hospital Universitari Vall d'Hebron Research InstituteCIEMAT; CIBERERCompleted
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National Heart, Lung, and Blood Institute (NHLBI)Children's Hospital Medical Center, CincinnatiCompletedFanconi AnemiaUnited States
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Baylor College of MedicineCenter for Cell and Gene Therapy, Baylor College of Medicine; University of...TerminatedFANCONI ANEMIAUnited States
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University of MinnesotaCompleted
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Assistance Publique - Hôpitaux de ParisEuroFancolenCompleted
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Masonic Cancer Center, University of MinnesotaCompleted
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Children's Hospital Medical Center, CincinnatiNational Heart, Lung, and Blood Institute (NHLBI)CompletedFanconi AnemiaUnited States
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Shenzhen Geno-Immune Medical InstituteUnknown
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Medical College of WisconsinMemorial Sloan Kettering Cancer CenterCompleted
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Neena Kapoor, M.D.Withdrawn
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National Heart, Lung, and Blood Institute (NHLBI)CompletedPancytopenia | Fanconi's AnemiaUnited States
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Boston Children's HospitalNational Heart, Lung, and Blood Institute (NHLBI); Children's Hospital Medical...Completed
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Fred Hutchinson Cancer CenterNational Cancer Institute (NCI)CompletedFanconi AnemiaUnited States, Brazil
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Children's Hospital Medical Center, CincinnatiFDA Office of Orphan Products DevelopmentCompleted
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Office of Rare Diseases (ORD)UnknownAdrenal Hyperplasia, CongenitalUnited States, Brazil, France
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University of MinnesotaUnknown
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Masonic Cancer Center, University of MinnesotaCompleted
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Masonic Cancer Center, University of MinnesotaTerminated
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OHSU Knight Cancer InstituteNational Cancer Institute (NCI)TerminatedFanconi AnemiaUnited States
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Memorial Sloan Kettering Cancer CenterNational Cancer Institute (NCI); Miltenyi Biotec, Inc.Completed
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Duke UniversityCompletedHemoglobinopathies | Thalassemia | Lysosomal Storage Disease | Immunodeficiencies | Inborn Errors of Metabolism | Sickle Cell | Non Malignant Disorders | Congenital Marrow FailuresUnited States
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Fairview University Medical CenterCompleted
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Dana-Farber Cancer InstituteUnknownFanconi's AnemiaUnited States
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Zagazig UniversityCompletedVitamin D Deficiency | Sickle Cell Disease | Bone Mineral Density | Health Related Quality of Life | Hand Grip StrengthEgypt
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Novo Nordisk A/SCompletedTurner Syndrome | Growth Hormone Disorder | Growth Hormone Deficiency in Children | Genetic Disorder | Foetal Growth Problem | Small for Gestational Age | Growth Disorder | Idiopathic Short StatureGermany