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Clinical Trials on Craniofacial Abnormalities in Japan
Total 552 results
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Boehringer IngelheimRecruitingNetherton SyndromeBelgium, United Kingdom, Australia, Germany, China, Malaysia, United States, Japan, France, Israel, Bulgaria, Italy, Switzerland, Austria, Netherlands, Portugal
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AstraZenecaIqvia Pty LtdActive, not recruitingRespiratory Syncytial Virus InfectionsJapan
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Medtronic EndovascularCompletedFistula | Arteriovenous Fistula | Arteriovenous Fistula Stenosis | Arteriovenous Fistula OcclusionNew Zealand, United States, Japan
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Eli Lilly and CompanyCompletedAdult Growth Hormone DeficiencyJapan
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Novartis PharmaceuticalsCompletedCushing's Syndrome | Ectopic Corticotropin Syndrome | Adrenal Adenoma | Adrenal Carcinoma | AIMAH | PPNADJapan
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BayerCompletedHemophilia A | Hemophilia BUkraine, United Kingdom, Bulgaria, Germany, Japan
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Kobe UniversityBoehringer IngelheimActive, not recruitingInsulin Resistance - Type A | Insulin Resistance - Type B | Lipoatrophic Diabetes Mellitus | Insulin Resistance SyndromeJapan
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Baxalta now part of ShireCompletedPrimary Immunodeficiency Diseases (PID)Japan
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TakedaCompleted
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Novo Nordisk A/SEnrolling by invitation
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Kobe UniversityBoehringer IngelheimActive, not recruitingInsulin Resistance - Type A | Insulin Resistance - Type B | Lipoatrophic Diabetes Mellitus | Insulin Resistance SyndromeJapan
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Boehringer IngelheimTerminatedDermatitis, AtopicUnited States, Japan, Canada
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Baxalta now part of ShireTakedaCompleted
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AstraZenecaArdea Biosciences, Inc.CompletedGout and HyperuricemiaJapan
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JCR Pharmaceuticals Co., Ltd.Completed
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TakedaCompletedHereditary AngioedemaJapan
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SanofiCompleted
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Eli Lilly and CompanyCompletedAtopic DermatitisUnited States, Japan
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KU LeuvenCompletedCongenital Heart DiseaseBotswana, United States, Korea, Republic of, Belgium, Sweden, France, Switzerland, Denmark, Pakistan, Norway, Taiwan, Malta, Brazil, Bulgaria, India, Austria, Argentina, Australia, Cameroon, Canada, Chile, Colombia, Ethiopia, Greece, Italy and more
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Translational Research Center for Medical Innovation...RecruitingNeutral Lipid Storage DiseaseChina, United States, France, Austria, Germany, Italy, Japan, Netherlands, United Kingdom
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PfizerTerminated
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BayerCompletedHemophilia AUnited States, Japan, United Kingdom, Spain
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Boston UniversityNational Institute of Neurological Disorders and Stroke (NINDS); Food and Drug...CompletedFamilial Amyloid Polyneuropathy | Familial AmyloidosisUnited States, Italy, Japan, Sweden, United Kingdom
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Novo Nordisk A/SCompletedCongenital Bleeding Disorder | Haemophilia AJapan
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JCR Pharmaceuticals Co., Ltd.Active, not recruitingMucopolysaccharidosis IIJapan
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Cooperative International Neuromuscular Research...United States Department of DefenseCompletedDuchenne Muscular Dystrophy | Becker Muscular Dystrophy | Limb Girdle Muscular DystrophyUnited States, Japan, Canada
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Dermavant Sciences GmbHCompleted
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Novartis PharmaceuticalsTerminatedSickle Cell DiseaseUnited Arab Emirates, Bahrain, Kuwait, Qatar, Saudi Arabia
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Calcilytix Therapeutics, Inc., a BridgeBio companyRecruitingAutosomal Dominant Hypocalcemia (ADH)United States, Australia, United Kingdom, Denmark, Italy, France, Japan, Taiwan, Canada, Czechia, Netherlands
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CSL BehringCompletedPrimary Immune DeficiencyJapan
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CSL BehringCompleted
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ShireCompletedMetachromatic Leukodystrophy (MLD)Australia, Denmark, Japan, France, Germany
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AbbVie (prior sponsor, Abbott)Eisai Co., Ltd.CompletedIntestinal Behçet's DiseaseJapan
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CSL BehringCompletedPrimary Immune Deficiency DisorderJapan
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Weill Medical College of Cornell UniversityBayer; University Hospital, BonnCompletedHemophilia A | Hemophilia BUnited States, Israel, Australia, Italy, Sweden, Germany, Japan, Netherlands, Taiwan
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Chiesi Farmaceutici S.p.A.ICON plcRecruiting
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ShireCompleted
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BioMarin PharmaceuticalRecruitingHypochondroplasiaUnited States, Spain, Canada, France, Japan, Australia, Italy, Argentina, Brazil, Germany, United Kingdom
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Amicus TherapeuticsCompletedFabry DiseaseJapan, Taiwan, Turkey, United States, Brazil
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Diurnal LimitedCompletedCongenital Adrenal HyperplasiaFrance, United States, Japan
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Calcilytix Therapeutics, Inc., a BridgeBio companyRecruitingAutosomal Dominant HypocalcemiaUnited States, France, Denmark, Australia, Japan, Belgium, Canada, Italy, Netherlands, United Kingdom, Portugal, Finland, Germany
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Diurnal LimitedEnrolling by invitationCongenital Adrenal HyperplasiaUnited States, France, Japan
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Bioverativ, a Sanofi companyCompletedHemophilia AUnited States, Japan
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BayerCompletedAtopic DermatitisUnited States, Japan
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Kyowa Kirin Co., Ltd.CompletedA Study of KRN23 in Adult and Pediatric Patients With X-linked Hypophosphatemic Rickets/OsteomalaciaXLHJapan, Korea, Republic of
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Genzyme, a Sanofi CompanyActive, not recruitingGaucher Disease Type 1 | Gaucher Disease Type 3Germany, United States, Japan, United Kingdom
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PfizerCompletedShort Stature Born Small for Gestational Age (SGA)Japan
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Hoffmann-La RocheChugai PharmaceuticalCompletedHemophilia AUnited States, Belgium, Spain, Japan, Poland, Australia
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BioMarin PharmaceuticalActive, not recruitingAchondroplasiaUnited States, Australia, Japan, United Kingdom
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Translational Research Center for Medical Innovation...Osaka University Graduate School of MedicineCompleted