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Clinical Trials on GNE Myopathy
Total 1127 results
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Ruhr University of BochumNot yet recruitingOne Week Follow-up Assessment | Six Weeks Follow-up Assessment | Three Months Follow-up AssessmentGermany
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University Hospital, BrestUnknownBreast Neoplasms | HER-2 Gene AmplificationFrance
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Taiho Oncology, Inc.RecruitingAdvanced Cholangiocarcinoma | FGFR2 Fusions | Gene RearrangementUnited States, Korea, Republic of, Spain, Japan, Portugal, Italy, China, Argentina, Brazil, Poland, Australia
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Peking Union Medical CollegeUnknownBreast Cancer | HER2 Gene MutationChina
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Tel-Aviv Sourasky Medical CenterUnited States Department of DefenseRecruitingEvaluation of the Frequency and Severity of Sleep Abnormalities in Patients With Parkinson's DiseaseParkinson Disease | GBA Gene Mutation | Leucine-rich Repeat Kinase 2 (LRRK2) Gene MutationIsrael
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Centre Hospitalier Universitaire de Saint EtienneCompleted
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Spanish National Research CouncilHospital Beata María AnaCompletedHemiparesis/Hemiplegia (One Sided Weakness/Paralysis)Spain
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Chugai PharmaceuticalNot yet recruitingAntiphospholipid Syndrome (APS) | Immune Thrombocytopenia (ITP) | Dermatomyositis (DM) | Bullous Pemphigoid (BP) | Behçet's Syndrome (BS) | Immune-mediated Necrotizing Myopathy (IMNM)United States, Japan
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Assistance Publique - Hôpitaux de ParisAssociation Française contre les Myopathies (AFM), ParisUnknownRespiratory Insufficiency | Myopathy | Muscular WeaknessFrance
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National Taiwan University HospitalUnknownAcute Renal Failure | Neuroleptic Malignant Syndrome | Rhabdomyolysis | MyopathyTaiwan
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Masaryk UniversityPalacky UniversityRecruitingDegenerative Cervical Spinal Myelopathy | Cervical Spinal Cord CompressionCzechia
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Medtronic Spinal and BiologicsCompletedRadiculopathy | Myelopathy | Cervical Degenerative Disc DiseaseUnited States
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BayerRecruitingAdvanced or Recurrent Solid Tumor Harboring an NTRK Gene FusionJapan
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HutchmedRecruitingIsocitrate Dehydrogenase Gene MutationSpain, United States
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Institut Claudius RegaudRecruitingDDX41 Gene MutationFrance
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University of TriesteCompletedThoracic Surgery | One-lung Ventilation | Respiratory Mechanics | Artificial RespirationItaly
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Intergroupe Francophone de Cancerologie ThoraciquePfizerCompletedALK Gene Rearrangement Positive | Non-small Cell Lung Cancer Metastatic | ROS-1 Gene Rearrangement PositiveFrance
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Women's College HospitalCanadian Institutes of Health Research (CIHR); London Health Sciences Centre; H. Lee Moffitt Cancer Center and Research Institute and other collaboratorsUnknownBreast Cancer | Ovarian Cancer | BRCA1 Gene Mutation | BRCA2 Gene MutationCanada
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National Cancer Institute (NCI)Glaxosmithkline Biologicals S.A.TerminatedRenal Failure | Solid Neoplasm | BRAF Gene Mutation | Hepatic ComplicationUnited States, Canada
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Simons SearchlightBoston Children's Hospital; Geisinger Clinic; Simons FoundationRecruitingSMARCA4 Gene Mutation | DDX3X | 16P11.2 Deletion Syndrome | 16p11.2 Duplications | 1Q21.1 Deletion | 1Q21.1 Microduplication Syndrome (Disorder) | ACTL6B | ADNP | AHDC1 | ANK2 | ANKRD11 | ARID1B | ASH1L | BCL11A | CHAMP1 | CHD2 | CHD8 | CSNK2A1 | CTBP1 | CTNNB1 Gene Mutation | CUL3 | DNMT3A | DSCAM | DYRK1A | FOXP1 | GRIN2A | GRIN2B | HIVEP2-Related Intellectual... and other conditionsUnited States
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Duke UniversityGenzyme, a Sanofi CompanyCompletedNeuropathy | Myopathy | Glycogen Storage Disease Type II (Late-onset Pompe Disease)United States
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Baylor College of MedicineDoris Duke Charitable FoundationRecruitingRAI1 Gene 17P11.2 Deletion+DuplicationUnited States
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Pamukkale UniversityRecruitingHemiparesis/Hemiplegia (One Sided Weakness/Paralysis)Turkey
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Notal Vision Ltd.CompletedA. AMD Patients, Where at Least One Eye is With Active CNV, Presenting Retinal Fluid at the Enrolment Visit, Undergoing Active Anti-VEGF TreatmentIsrael
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Hospitales Universitarios Virgen del RocíoCompletedAcute Aortic Syndrome | Gene AbnormalitySpain
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Danish Head and Neck Cancer GroupRecruitingHypoxia | Head and Neck Squamous Cell Carcinoma | Radiotherapy | Hypoxic Modification | Gene Profile, Gene SignatureDenmark
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Ascenta TherapeuticsTerminatedLocally Advanced Esophageal or GE Junction CancerUnited States
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Stanford UniversityNovartis PharmaceuticalsCompletedAmeloblastoma | BRAF Gene MutationUnited States
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Diakonessenhuis, UtrechtAgendiaCompletedBreastcancer | Invasive Breast Carcinoma by Gene Expression ProfileNetherlands
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Universiti Putra MalaysiaCentral Sugars Refinery Sdn Bhd, MalaysiaTerminatedMetabolic Syndrome | Cardiometabolic Risk | Gene ExpressionMalaysia
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Samsung Medical CenterAsan Medical Center; Seoul National University Hospital; Korea University Guro... and other collaboratorsCompletedPostoperative Complications | Positive End Expiratory Pressure | Thoracic Surgery | Postoperative Pulmonary Complication | One-Lung Ventilation | Driving PressureKorea, Republic of
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Centre Chirurgical Marie LannelongueCompletedPatients Are Recruited From One Thoracic and Cardiac Surgery ICUFrance
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University of WashingtonActive, not recruitingBRCA1 Gene Mutation | BRCA2 Gene Mutation | Castration-Resistant Prostate Carcinoma | Homologous Recombination Deficiency | PSA Progression | Stage IV Prostate Adenocarcinoma AJCC v7 | Castration Levels of Testosterone | ATM Gene Mutation | Prostate Carcinoma Metastatic in the Bone | PSA Level Greater...United States
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Jordi Perez LopezHospital Vall d'HebronUnknown
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University of Wisconsin, MadisonRecruitingERα+ Breast Cancer | ESR1 Gene MutationUnited States
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UNICANCERCompletedKRAS Gene Mutation | Infiltrating Urothelial CarcinomaFrance
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Regeneron PharmaceuticalsRecruitingCongenital Hearing Loss Secondary to Biallelic Mutations in the Otoferlin Gene (OTOF) | Biallelic Mutations in the Gap Junction Beta 2 (GJB2) Gene | Digenic Mutations in GJB2/Gap Junction Beta 6 (GJB6) GenesUnited States
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Henan Cancer HospitalRecruitingDiffuse Large B Cell Lymphoma | CD79A Gene Mutation | CD79B Gene MutationChina
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Calithera Biosciences, IncTerminatedNon-Small Cell Lung Cancer | Non-squamous Non-small-cell Lung Cancer | Non-Squamous Non-Small Cell Neoplasm of Lung | KEAP1 Gene Mutation | NFE2L2 Gene Mutation | NRF2 MutationUnited States
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Jazz PharmaceuticalsRecruitingBiliary Tract Cancer | HER2 Gene MutationUnited States, Puerto Rico
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Ascletis Pharmaceuticals Co., Ltd.RecruitingHIV Infections | HIV-1-infection | PD-L1 Gene MutationChina
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Centre Hospitalier Universitaire, AmiensCompletedBacterial Infection With One or More Extended Spectrum Betalactamases Remaining Susceptible to TemocillinFrance
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Cumhuriyet UniversityCompletedLung Neoplasms | Gene, p53Turkey
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Rush University Medical CenterWithdrawnDegenerative Disc Disease | Radiculopathy | Myelopathy | Spondylosis | Stenosis | Herniated Nucleus Pulposus | MyeloradiculopathyUnited States
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Cairo UniversityUnknownAcute Renal Failure | Anuria | Obstructive Uropathy | Ureteric StonesEgypt
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University of Southern CaliforniaNational Cancer Institute (NCI)Active, not recruitingStage IIIA Non-Small Cell Lung Cancer | Stage IIIB Non-Small Cell Lung Cancer | Head and Neck Squamous Cell Carcinoma | Recurrent Head and Neck Carcinoma | Recurrent Non-Small Cell Lung Carcinoma | Stage IV Non-Small Cell Lung Cancer | ALK Gene Mutation | EGFR Gene Mutation | Metastatic Head and Neck... and other conditionsUnited States
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University of UtahNational Cancer Institute (NCI)TerminatedObstructive Sleep Apnea Syndrome | Polycythemia Vera | Essential Thrombocythemia | CALR Gene Mutation | JAK2 Gene Mutation | MPL Gene MutationUnited States
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Carolina Neurosurgery & Spine AssociatesTerminatedMyelopathy | Spinal Disease | Neurogenic Claudication | Spinal RadiculopathyUnited States
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Medtronic Spinal and BiologicsCompletedRadiculopathy | Myelopathy | Cervical Degenerative Disc DiseaseUnited States
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Khondrion BVJulius ClinicalCompletedMitochondrial Diseases | Mitochondrial Myopathies | MELAS Syndrome | Mitochondrial Encephalomyopathies | MIDDNetherlands, Denmark, Germany, United Kingdom