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Clinical Trials on Glykogenová skladovací choroba typu 1A
Total 137 results
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Oregon Health and Science UniversityAlaska Department of Health and Social ServicesCompletedCarnitine Palmitoyl Transferase Type 1A (CPT1A) DeficiencyUnited States
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Connecticut Children's Medical CenterJohns Hopkins University; Eunice Kennedy Shriver National Institute of Child... and other collaboratorsRecruitingAlbright Hereditary Osteodystrophy | Pseudopseudohypoparathyroidism | Pseudohypoparathyroidism Type 1AUnited States
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Children's Hospital of PhiladelphiaTerminatedAlbright Hereditary Osteodystrophy | Pseudohypoparathyroidism Type 1AUnited States
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Jonsson Comprehensive Cancer CenterBristol-Myers SquibbCompletedChordoma | Metastatic Chordoma | Unresectable Chordoma | Locally Advanced ChordomaUnited States
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M.D. Anderson Cancer CenterRecruitingChordoma | Metastatic Chordoma | Unresectable ChordomaUnited States
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University Hospital, Clermont-FerrandActive, not recruitingCharcot-Marie-Tooth Type 1A NeuropathyFrance
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University Hospital, Clermont-FerrandCompletedCharcot-Marie-Tooth Type 1A NeuropathyFrance
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Institut CurieActive, not recruitingSkull Base Chordoma | Vertebral ChordomaFrance
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Heidelberg UniversityActive, not recruiting
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Huashan HospitalBoehringer IngelheimNot yet recruiting
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Xuanwu Hospital, BeijingRecruiting
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CNAO National Center of Oncological HadrontherapyDept. of Electronics, Informatics, Bioengineering, Politecnico di Milano,...Recruiting
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ModernaTX, Inc.RecruitingGlycogen Storage DiseaseUnited States, Canada
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Massachusetts General HospitalM.D. Anderson Cancer Center; National Cancer Institute (NCI)Active, not recruitingChordoma of Sacrum | Chordoma of Spine | Chordoma of Base of Skull | Chondrosarcoma of the Spine | Chondrosarcoma of the SacrumUnited States
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Vanderbilt University Medical CenterRecruitingPseudohypoparathyroidism Type 1a | Albright Hereditary Osteodystrophy | PseudohypoparathyroidismUnited States
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Ashley ShoemakerEnrolling by invitationPseudohypoparathyroidism Type 1a | Albright Hereditary Osteodystrophy | PseudohypoparathyroidismUnited States
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Vanderbilt University Medical CenterMassachusetts General HospitalCompletedPseudohypoparathyroidism Type 1a | Albright Hereditary OsteodystrophyUnited States
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National Cancer Institute (NCI)RecruitingGenes | Sporadic ChordomaUnited States
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Weill Medical College of Cornell UniversityRecruitingChoroid Plexus Carcinoma | Atypical Choroid Plexus PapillomaUnited States
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Iconic Therapeutics, Inc.CompletedUveal Melanoma | Choroid NeoplasmUnited States
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M.D. Anderson Cancer CenterActive, not recruiting
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University Hospital HeidelbergCompleted
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Italian Sarcoma GroupRecruitingChordomaItaly, Spain, Netherlands, Austria, Germany, Hungary, Japan, Norway, Poland, United Kingdom
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Massachusetts General HospitalActive, not recruiting
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Saint John's Cancer InstituteEli Lilly and Company; Chordoma FoundationCompleted
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Leiden University Medical CenterBoehringer Ingelheim; Chordoma FoundationActive, not recruiting
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Novartis PharmaceuticalsCompleted
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NantCell, Inc.National Cancer Institute (NCI)Completed
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Centre Hospitalier Universitaire de Saint EtienneCompleted
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Barts & The London NHS TrustRoyal Marsden NHS Foundation Trust; Guy's and St Thomas' NHS Foundation Trust; Case Western Reserve University and other collaboratorsCompletedEndometrial Cancer | Surgically Staged Endometrial and Cervical Carcinoma | Cervical Cancer: Invasive Disease, FIGO Stage 1B1 or Higher | Stage 1A With Myometrial Invasion or Any Higher Stage and Grade 3 | Stage 1A With Myometrial Invasion or Any Other Higher Stage and Serous Papillary or... and other conditionsUnited Kingdom
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Xuanwu Hospital, BeijingRecruitingChordoma | Chemotherapy EffectChina
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Hospices Civils de LyonRecruitingMalignant Tumors as Chordoma, Adenoid Cystic Carcinoma and SarcomaFrance
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Heidelberg UniversityRecruitingChordoma | Tumor | TreatmentGermany
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National Cancer Institute (NCI)Completed
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ImmunityBio, Inc.WithdrawnChordoma | Unresectable Malignant NeoplasmUnited States
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Deric M Park MDUnknown
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Sidney Kimmel Comprehensive Cancer Center at Johns...Bristol-Myers Squibb; National Cancer Institute (NCI); Chordoma FoundationActive, not recruiting
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Tasly GeneNet Pharmaceuticals Co., LtdRecruitingCharcot-Marie-Tooth Type 1AChina
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Nationwide Children's HospitalSuspendedCharcot-Marie-Tooth Neuropathy Type 1AUnited States
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Pharnext S.C.A.Premier Research Group plc; Eurofins Optimed; Synteract HCR (Syneos Health); Gr... and other collaboratorsActive, not recruitingCharcot-Marie-Tooth Disease, Type IAUnited States, Belgium, Canada, France, Netherlands, Spain, United Kingdom
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Freeman-Sheldon Research Group, Inc.TerminatedCraniofacial Abnormalities | Arthrogryposis | Freeman-Sheldon Syndrome | Arthrogryposis Distal Type 2A | Whistling Face Syndrome | Craniocarpotarsal Dysplasia | Craniocarpotarsal Dystrophy | Freeman-Sheldon Syndrome Variant | Sheldon-Hall Syndrome | Arthrogryposis Distal Type 2B | Gordon Syndrome | Arthrogryposis... and other conditionsUnited States
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University of GenovaUnknownCharcot-Marie-Tooth Disease | Charcot-Marie-Tooth Disease Type 1AItaly
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ENCellRecruitingCharcot-Marie-Tooth Disease Type 1AKorea, Republic of
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Pharnext SACompletedPhase III Trial Assessing the Efficacy and Safety of PXT3003 in CMT1A Patients (PLEO-CMT) (PLEO-CMT)Charcot-Marie-Tooth Disease Type 1AUnited States, United Kingdom, Belgium, Canada, France, Netherlands, Spain, Germany
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Massachusetts General HospitalNational Cancer Institute (NCI)Completed
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Assistance Publique Hopitaux De MarseilleRecruitingCharcot-Marie-Tooth Disease Type 1AFrance
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Washington University School of MedicineWithdrawnUveal Neoplasms | Choroid Neoplasms | Iris NeoplasmsUnited States