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Clinical Trials on Hereditary Diseases
Total 378887 results
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ShireWithdrawnHereditary Angioedema (HAE)
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BioCryst PharmaceuticalsCompletedHereditary Angioedema (HAE)Austria, Denmark, France, Germany, Hungary, Israel, Italy, North Macedonia, Poland, Romania, Switzerland, United Kingdom
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ShireCompletedHereditary Angioedema (HAE)Germany, Spain, United Kingdom, France, Italy, Belgium
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CSL BehringChiltern International Inc.CompletedIncludes: Hereditary AngioedemaUnited States, Denmark, Germany, Switzerland
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Eye Hospital Pristina KosovoEnrolling by invitationMacular Corneal DystrophyKosovo
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Cornea Research Foundation of AmericaCompletedFuchs' Endothelial Dystrophy | Bullous KeratopathyUnited States
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Glostrup University Hospital, CopenhagenUnknownFuchs' Endothelial Dystrophy | Bullous KeratopathyDenmark
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Shanghai Vitalgen BioPharma Co., Ltd.Not yet recruitingBietti Crystalline DystrophyChina
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Beijing Tongren HospitalRecruitingBietti Crystalline DystrophyChina
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University Hospital, GrenobleRecruitingAngio Edema HereditaryFrance
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TakedaRecruitingHereditary Angioedema (HAE)Japan
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ShireTakeda Development Center Americas, Inc.Active, not recruitingHereditary Angioedema (HAE)Germany, Switzerland, Spain, Israel, Italy, Austria, Portugal, Kuwait
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ShireTakedaCompleted
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TakedaCompletedHereditary Angioedema (HAE)China
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BioCryst PharmaceuticalsCompletedHereditary Angioedema, HAEJapan
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ShireCompletedHereditary Angioedema (HAE)United States
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ShireCompletedHereditary Angioedema (HAE)United States, United Kingdom, Germany, Canada, Italy, Jordan, Puerto Rico
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ShireCompletedHereditary Angioedema (HAE)Spain, Israel, United States, Hungary, Germany, Canada, Romania
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ShireCompletedHereditary Angioedema (HAE)United States, Germany, Hungary
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ShireCompletedHereditary Angioedema (HAE)United States, Germany, Spain, Sweden
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ShireCompletedHereditary Angioedema (HAE)United States
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ShireCompletedHereditary Angioedema (HAE)Israel, Germany, Mexico, United States, Romania
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ShireCompletedHereditary Angioedema (HAE)Japan
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ShireCompletedHereditary Angioedema (HAE)United States, Jordan, Italy
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BioCryst PharmaceuticalsCompletedHereditary Angioedema (HAE)Canada, United Kingdom, Germany, Spain, Australia, Hungary, Italy, Austria, North Macedonia, Denmark, Switzerland
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Medical University of ViennaCompletedFuchs' Endothelial DystrophyAustria
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Centre Hospitalier Régional Metz-ThionvilleCompletedEndothelial Corneal Dystrophy
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Hôpital Necker-Enfants MaladesEuropean Georges Pompidou Hospital; CLAIROPCompletedSafety Issues | Efficacy, SelfFrance
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Centre Hospitalier National d'Ophtalmologie des...StreetlabCompletedRetinitis Pigmentosa | Leber's Hereditary Optic Neuropathy | Stargardt DiseaseFrance
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Santhera PharmaceuticalsCompletedLeber's Hereditary Optic NeuropathyCanada, Germany, United Kingdom
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OctapharmaRecruiting
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Hospital Universitari Vall d'Hebron Research InstituteHospital Universitario La PazNot yet recruitingHereditary Angioedema With C1 Esterase Inhibitor DeficiencySpain
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CSL BehringCompletedHereditary Angioedema Types I and IIBulgaria, Hungary, Poland, Romania
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CSL BehringCompletedHereditary Angioedema Types I and IIGermany
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Unity Health TorontoSunnybrook Health Sciences Centre; University of Pittsburgh; Duke University; Barrow... and other collaboratorsActive, not recruitingHereditary Hemorrhagic Telangiectasia (HHT)Canada
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Imperial College LondonCompletedHereditary Hemorrhagic Telangiectasia (HHT)United Kingdom
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University Hospital, EssenCompletedHereditary Haemorrhagic Telangiectasia (HHT)Germany
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Singapore Eye Research InstituteRecruitingThe Effects of Ripasudil in Patients With FED Undergoing Femtosecond Laser Assisted Cataract SurgeryCataract | Fuchs' Endothelial DystrophySingapore
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Massachusetts Eye and Ear InfirmaryCompletedCataract | Fuchs' Endothelial DystrophyUnited States
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Legacy Health SystemLions VisionGift Research; Optovue; Devers Eye InstituteTerminated
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First Affiliated Hospital of Fujian Medical UniversityRecruiting
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University Hospital, EssenCompleted
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Assistance Publique - Hôpitaux de ParisCompletedRhabdomyolysis Linked to a Hereditary Disease of MetabolismFrance
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Stanford UniversityUniversity of Pennsylvania; University of California, Davis; Oregon Health and... and other collaboratorsRecruitingFuchs' Endothelial Dystrophy | Fuchs Dystrophy | FuchsUnited States
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Michael D. Straiko, MDLions VisionGift Research; Eye Bank Association of AmericaRecruitingFuchs Endothelial DystrophyUnited States
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Trefoil Therapeutics, Inc.CompletedFuchs' Endothelial Dystrophy | Fuchs Dystrophy | FuchsUnited States
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University of SouthamptonUnknownKeratoconus | Fuchs Dystrophy | Corneal DiseaseUnited Kingdom
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Scripps HealthJ. Craig Venter InstituteCompletedLi-Fraumeni Syndrome | Hereditary Cancer Syndromes | TP53 Gene Germline Mutation CarrierUnited States
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Chigenovo Co., LtdRecruitingBietti's Crystalline DystrophyChina
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Oregon Health and Science UniversityRecruitingCorneal Opacity | Keratoconus | Corneal DystrophyUnited States