- ICH GCP
- US Clinical Trials Registry
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Clinical Trials on Hurler Syndrome in United States
Total 14112 results
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Genzyme, a Sanofi CompanyBioMarin/Genzyme LLCCompletedMucopolysaccharidosis I | Hurler-Scheie Syndrome | Hurlers SyndromeUnited States, Canada, Germany
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Genzyme, a Sanofi CompanyBioMarin/Genzyme LLCCompletedMucopolysaccharidosis I | Hurler's Syndrome | Hurler-Scheie Syndrome | Scheie's SyndromeUnited States
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Genzyme, a Sanofi CompanyBioMarin/Genzyme LLCCompletedMucopolysaccharidosis I | Scheie Syndrome | Hurler's Syndrome | Hurler-Scheie SyndromeUnited States, Canada, United Kingdom, Brazil, Germany, Italy, Netherlands
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REGENXBIO Inc.Active, not recruitingHurler Syndrome | Hurler-Scheie Syndrome | Mucopolysaccharidosis Type I (MPS I)United States, Brazil, Israel
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Orchard TherapeuticsRecruitingMPS-IH (Hurler Syndrome)Netherlands, United States, Italy, United Kingdom
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Genzyme, a Sanofi CompanyBioMarin/Genzyme LLCCompletedMucopolysaccharidosis I | Scheie Syndrome | Hurler Syndrome | Hurler-Scheie SyndromeNetherlands, France, Germany, United Kingdom
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Talaris Therapeutics Inc.Duke UniversityTerminatedNiemann-Pick Disease | Alpha-mannosidosis | Tay Sachs Disease | Sandhoff Disease | Metachromatic Leukodystrophy (MLD) | Hurler-Scheie Syndrome | Hurler Syndrome (MPS I) | Hunter Syndrome (MPS II) | Sanfilippo Syndrome (MPS III) | Krabbe Disease (Globoid Leukodystrophy) | Adrenoleukodystrophy (ALD and AMN) | Pelizaeus...United States
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University of Colorado, DenverCompletedTurner Syndrome | Turner Syndrome Mosaicism, 45, X/46, XX or XY | Turner Syndrome Mosaicism 46,X,I(X)(Q10)/45,X | Turner Syndrome Karyotype 46,X With Abnormal Sex Chromosome , Except I(Xq)United States
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University of MinnesotaNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK); National... and other collaboratorsCompletedHurler Syndrome | Sanfilippo Syndrome Type A | Sanfilippo Syndrome Type BUnited States
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Denver Health and Hospital AuthorityUniversity of Colorado, DenverTerminated
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Masonic Cancer Center, University of MinnesotaCompleted
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Masonic Cancer Center, University of MinnesotaCompletedMucopolysaccharidosis I | Hurler SyndromeUnited States
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Stanford UniversityTerminatedCerebral Blood Flow | Horner Syndrome | Regional AnesthesiaUnited States
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Masonic Cancer Center, University of MinnesotaTerminatedHurler Syndrome | Mucopolysaccharidosis Type IH | MPS IUnited States
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Clinical Nutrition Research Center, Illinois Institute...Wm. Wrigley Jr. CompanyCompleted
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Procter and GambleCompleted
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Masonic Cancer Center, University of MinnesotaCompleted
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Temple UniversityInternational Life Sciences InstituteCompleted
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Pennington Biomedical Research CenterAmerican Egg BoardCompleted
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Pennington Biomedical Research CenterOmniActive Health TechnologiesCompletedEating | Hunger | Energy MetabolismUnited States
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Patricia I. Dickson, M.D.National Institute of Diabetes and Digestive and Kidney Diseases (NIDDK); University... and other collaboratorsCompletedMucopolysaccharidosis I | Scheie Syndrome | Lysosomal Storage Disease | Cognitive Decline | Hurler-Scheie SyndromeUnited States
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Arizona State UniversityArdent Mills, LLCCompletedBlood Glucose | Hunger | Dietary FiberUnited States
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Patricia I. Dickson, M.D.The Ryan FoundationTerminatedMucopolysaccharidosis I | Scheie Syndrome | Lysosomal Storage Disease | Spinal Cord Compression | Hurler-Scheie SyndromeFinland, United States
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The University of Tennessee, KnoxvilleCompleted
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Purdue UniversityWake Forest University Health SciencesRecruitingDiet, Healthy | Food Habits | Nutrition, Healthy | HungerUnited States
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Swansea UniversityCompletedHungerUnited Kingdom
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National Cancer Institute (NCI)CompletedPreviously Treated Myelodysplastic Syndromes | Secondary Myelodysplastic Syndromes | de Novo Myelodysplastic SyndromesUnited States
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St Mary's University CollegeUnknownFood Preferences | HungerUnited Kingdom
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Fred Hutchinson Cancer CenterNational Cancer Institute (NCI)CompletedPreviously Treated Myelodysplastic Syndromes | Secondary Myelodysplastic Syndromes | de Novo Myelodysplastic SyndromesUnited States
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Masonic Cancer Center, University of MinnesotaCompletedMucopolysaccharidosis | Hurler Syndrome | Sphingolipidoses | Peroxisomal Disorders | Krabbe Disease | Adrenoleukodystrophy (ALD) | Hunter Syndrome | Sly Syndrome | Fucosidosis | Aspartylglucosaminuria | Alpha Mannosidosis | Metachromatic Leukodystrophy (MLD) | Maroteaux-Lamy SyndromeUnited States
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PersImmune, IncUniversity of California, San DiegoUnknown
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Zoe Global LimitedActive, not recruiting
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Benjamin TomlinsonRecruitingMyelodysplastic Syndromes | MDS/MPN Crossover SyndromesUnited States
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Dana-Farber Cancer InstituteCompletedMyelodysplastic Syndromes (MDS)United States
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Sequenom, Inc.Friends Research Institute, Inc.TerminatedDown Syndrome | Turner Syndrome | Edwards Syndrome | Patau SyndromeUnited States
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University of Colorado, DenverActive, not recruitingHigh Grade Myelodysplastic SyndromesUnited States
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The University of Texas Health Science Center,...RecruitingNeuropsychiatric SyndromesUnited States
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Brian JonasNational Cancer Institute (NCI); Celgene; Pharmacyclics LLC.CompletedPreviously Treated Myelodysplastic Syndrome | Myelodysplastic Syndrome | Therapy-Related Myelodysplastic Syndrome | Secondary Myelodysplastic Syndrome | Refractory High Risk Myelodysplastic SyndromeUnited States
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Imperial College LondonRecruitingMay-Thurner SyndromeUnited Kingdom
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PepsiCo Global R&DCompletedSelf Reported Ratings of HungerUnited Kingdom
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Mayo ClinicCompletedCongenital Myasthenic SyndromeUnited States
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Rockefeller UniversityCompleted
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Wake Forest University Health SciencesNational Cancer Institute (NCI)TerminatedPreviously Treated Myelodysplastic SyndromesUnited States
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National Pediatric Neuroinflammation Organization...CompletedOpsoclonus-myoclonus SyndromeUnited States
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University of FloridaCompletedSmall Intestinal Bacterial Overgrowth Syndrome (SIBO) | Small Bowel Bacterial Overgrowth Syndrome (SBBOS)United States
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National Pediatric Neuroinflammation Organization...Genentech, Inc.CompletedAtaxia | Myoclonus | Opsoclonus-myoclonus Syndrome | OpsoclonusUnited States
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AkesoRecruitingHigher-risk Myelodysplastic SyndromesUnited States, China
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Center for Hunger-Free CommunitiesCompletedChild Development | Hunger | Social IsolationUnited States
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Case Comprehensive Cancer CenterRecruitingMyelodysplastic Syndrome (MDS)United States
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Weill Medical College of Cornell UniversityNovartis PharmaceuticalsCompletedMyelodysplastic Syndrome (MDS)United States