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Clinical Trials on Inherited Metabolic Disorders IMD
Total 38889 results
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Fondazione Don Carlo Gnocchi OnlusUniversity of Milano Bicocca; Università Carlo Cattaneo , CastellanzaUnknownChronic Obstructive Pulmonary Disease (COPD) | Chronic Heart Failure (CHF) | Parkinson Disease (PD)Italy
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Reha RheinfeldenWithdrawnStroke | Parkinson Disease | Traumatic Brain Injury | Guillain-Barre Syndrome
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First Affiliated Hospital Xi'an Jiaotong UniversityXi'an Gaoxin HospitalUnknownSepsis | Anemia | Vitamin D Deficiency | Vitamin A Deficiency | Bronchopulmonary Dysplasia | Very Low Birth Weight Infants | Vitamin E DeficiencyChina
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Clinique Romande de ReadaptationCompletedStroke | Multiple Sclerosis | Cerebral Palsy | Parkinson Disease | Spinal Cord Injuries | People With Impaired Lower Extremity FunctionSwitzerland
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Universität Duisburg-EssenWeinmann Geräte für Medizin GmbH + Co. KGCompletedDuchenne Muscular Dystrophy | Spinal Muscular Atrophy | Chronic Respiratory InsufficiencyGermany
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Thomas Jefferson UniversityRecruitingStroke | Cerebral Palsy | Amyotrophic Lateral Sclerosis | Muscular Dystrophies | Spinal Cord Injuries | Hemiparesis | Spinal Muscular Atrophy | Quadriplegia | Arthrogryposis | Neurologic Diseases | Charcot-Marie-Tooth | Weakness of Extremities as Sequela of Stroke | Weakness Due to Upper Motor Neuron Dysfunction | Arm ParalysisUnited States
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University of Dublin, Trinity CollegeMotor Neurone Disease Association, UK; Irish Research Council, IE; Thierry Latran... and other collaboratorsRecruitingMultiple Sclerosis | Primary Lateral Sclerosis | Postpoliomyelitis Syndrome | Motor Neuron Disease, Amyotrophic Lateral Sclerosis | Motor Neuron Disease Progressive Spinal Muscle AtrophyIreland
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M.D. Anderson Cancer CenterRecruitingBreast Cancer | Gynecologic Cancer | Pancreatic Cancer | Lynch Syndrome | Endometrial Cancer | Colon Cancer | Hereditary Breast and Ovarian Cancer Syndrome | Uterus Cancer | Ovary CancerUnited States
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University of BaselRecruitingLynch Syndrome | Hereditary Breast and Ovarian CancerSwitzerland
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Hereditary Neuropathy FoundationRecruitingCharcot-Marie-Tooth Disease | Charcot-Marie-Tooth Disease, Type IA | Charcot-Marie-Tooth Disease Type 2A | Charcot-Marie-Tooth | Charcot-Marie-Tooth Disease, Type IB | Charcot-Marie-Tooth Disease Type 2 | Charcot-Marie-Tooth Disease, Type 2C | Charcot-Marie-Tooth Disease Type 2A2B | Charcot-Marie-Tooth... and other conditionsUnited States
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Kun SunRecruitingSpinal Muscular Atrophy 1China
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Fondazione Policlinico Universitario Agostino Gemelli...RecruitingEnd Stage Renal Disease | Kidney Transplantation | Obesity, Morbid | Endoscopic Sleeve GastroplastyItaly
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Institut de Myologie, FranceRoche Pharma AGNot yet recruitingMuscular Atrophy, Spinal, Type II | Muscular Atrophy, Spinal, Type IIIFrance
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First Affiliated Hospital Xi'an Jiaotong UniversityRecruitingVitamin D Deficiency | Chronic Kidney Disease 5D | Secondary Hyperparathyroidism Due to Renal CausesChina
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Fudan UniversityNot yet recruitingMalnutrition | Sarcopenia | Non Small Cell Lung CancerChina
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Chinese University of Hong KongRecruitingObesity | Breast Cancer | Colorectal Cancer | Prostate CancerHong Kong
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Federal University of PiauiFoundation for Research Support of the State of PiauíCompletedDiabetic Foot | Diabetic Foot UlcerBrazil
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Rhythm Pharmaceuticals, Inc.CompletedBardet-Biedl Syndrome | POMC Deficiency Obesity | PCSK1 Deficiency Obesity | LEPR Deficiency ObesityUnited States, Australia, Spain, United Kingdom
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Hospital Galdakao-UsansoloCompletedInflammatory Bowel Diseases | Gastric Cancer | Colorectal Cancer | Pancreatic Cancer | Crohn Disease | Ulcerative Colitis | Pancreatitis, Acute | Esophagus CancerSpain
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Novartis Gene TherapiesCompletedSpinal Muscular Atrophy 1United States
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University of MinhoFoundation for Science and Technology, PortugalActive, not recruitingDiabetes Mellitus | Diabetic Foot UlcerPortugal
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Podimetrics, Inc.UnknownQuality of Life | Diabetic Foot | Diabetes Complications | Mental Health Wellness 1 | Ulcer FootUnited States
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Stanford UniversityCompletedMuscular Atrophy, SpinalUnited States
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Assistance Publique - Hôpitaux de ParisCompleted
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UMC UtrechtCompletedSpinal Muscular Atrophy | SMA | Kugelberg-Welander DiseaseNetherlands
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Svendborg HospitalOdense University HospitalUnknownGiant Cell Arteritis | Polymyalgia RheumaticaDenmark
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Vanderbilt UniversityWestern Michigan UniversityCompletedMultiple System Atrophy | Pure Autonomic Failure | Parkinson's Plus SyndromesUnited States
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Instituto Nacional de Cancerologia de MexicoUnknownAnorexia | Non-Small Cell Lung Cancer | Cachexia | Weight LoseMexico
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Queensland Centre for Gynaecological CancerThe University of Queensland; Cancer Australia Priority-driven Collaborative...CompletedFallopian Tube Cancer | Epithelial Ovarian Cancer | Peritoneal CancerAustralia
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University Hospital, CataniaUnknownDepression | Anxiety | Hereditary AngioEdemaItaly
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Assistance Publique - Hôpitaux de ParisNot yet recruiting
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Korea University Ansan HospitalRecruitingSepsis | Shock | Trauma | Cardiac Arrest | Acute Respiratory Failure | Patients Who Visit Emergency DepartmentKorea, Republic of
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University Health Network, TorontoWomen's College Hospital; Markham Stouffville Hospital; William Osler Health... and other collaboratorsRecruitingHypertension | Diabetes Mellitus | Chronic Obstructive Pulmonary Disease | Heart Failure,Congestive | Mental Health (Depression)Canada
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Seoul National University HospitalRecruitingMultiple System AtrophyKorea, Republic of
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University Hospital, BordeauxFondation Francophone pour la Recherche sur le DiabeteRecruitingDiabetic Foot UlcerFrance, Martinique
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Duke UniversityNational Eye Institute (NEI)RecruitingHealthy | Diabetic Retinopathy | Cataract | Strabismus | Retinal Detachment | Epiretinal Membrane | Macular Holes | Retinal Disease | Preretinal Fibrosis | Ocular TumorUnited States
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TakedaRecruitingSpinal and Bulbar Muscular AtrophyJapan
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Vanderbilt University Medical CenterNational Heart, Lung, and Blood Institute (NHLBI)RecruitingMultiple System Atrophy | Orthostatic Hypotension | Pure Autonomic Failure | Autonomic FailureUnited States
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Virginia Commonwealth UniversityMuscular Dystrophy AssociationActive, not recruitingLGMD2E | LGMD2I | LGMD2A | LGMD2B | LGMD2C | LGMD1B | LGMD1C | LGMD1D | LGMD1E | LGMD1F | LGMD1G | LGMD1H | LGMD2D | LGMD2F | LGMD2G | LGMD2J | LGMD2K | LGMD2L | LGMD2M | LGMD2N | LGMD2O | LGMD2P | LGMD2Q | LGMD2S | LGMD2T | LGMD2U | LGMD2W | LGMD2X | LGMD2YUnited States
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King's College Hospital NHS TrustUniversity of Pennsylvania; Gilead Sciences; The Leeds Teaching Hospitals NHS... and other collaboratorsActive, not recruitingCardiovascular Diseases | Kidney Diseases | Obesity | Diabetes Mellitus | Genetic Predisposition to Disease | Kidney Injury | HIV NephropathyUnited Kingdom
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Centre Hospitalier Régional de la CitadelleCompletedSafety and Efficacy Study of Pyridostigmine on Patients With Spinal Muscular Atrophy Type 3 (EMOTAS)Spinal Muscular Atrophy Type 3Belgium
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National Taiwan University HospitalTerminatedMultiple System Atrophy | Ataxia, CerebellarTaiwan
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Novartis Gene TherapiesPRA Health SciencesCompletedSpinal Muscular Atrophy Type IKorea, Republic of, Taiwan, Japan
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Novartis PharmaceuticalsCompletedSpinal and Bulbar Muscular AtrophyUnited States, Germany, Italy, Denmark
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Stanford UniversityCompletedA Pilot Therapeutic Trial Using Hydroxyurea in Type II and Type III Spinal Muscular Atrophy PatientsMuscular Atrophy, SpinalUnited States
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Isfahan University of Medical SciencesUnknownVitamin D Deficiency Treatment Outcomes After Non-ST-Segment Elevation Myocardial Infarction (NAVID)Inflammation | Vitamin D Deficiency | Coronary Artery Disease With Myocardial Infarction | Non-ST Elevation Myocardial Infarction (nSTEMI)Iran, Islamic Republic of
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National Institute of Dental and Craniofacial Research...CompletedPrecocious Puberty | McCune Albright Syndrome | Polyostotic Fibrous DysplasiaUnited States
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Beth Israel Deaconess Medical CenterWithdrawnAcute Respiratory Distress Syndrome | Low Tidal Volume VentilationUnited States
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University of UtahLeadiant Biosciences, Inc.; Families of Spinal Muscular AtrophyCompletedSpinal Muscular Atrophy Type IUnited States, Canada, Germany