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Clinical Trials on Inherited Metabolic Disorders (IMD)
Total 39418 results
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University of PennsylvaniaRecruitingObesity | Chronic Obstructive Pulmonary Disease | Pulmonary Hypertension | Interstitial Lung Disease | Sarcoidosis, PulmonaryUnited States
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Drexel UniversityUniversity of Pennsylvania; Temple UniversityActive, not recruitingDiabetic Foot Ulcer | Venous UlcerUnited States
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UCSF Benioff Children's Hospital OaklandNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK); Medical... and other collaboratorsCompletedSickle Cell Disease | Thalassemia | Diamond-Blackfan AnemiaUnited States, United Kingdom, Germany
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Johns Hopkins UniversityUniversity of North Carolina, Chapel Hill; Children's Hospital Medical Center... and other collaboratorsTerminatedPneumonia | Malnutrition | Hypoxemia | Human Immunodeficiency Virus (HIV)Malawi
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Hoffmann-La RocheAssociation Française contre les Myopathies (AFM), ParisCompletedSpinal Muscular Atrophy Type II | Spinal Muscular Atrophy Type III Non AmbulantGermany, Italy, France, Belgium, Poland, Netherlands, United Kingdom
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The University of Texas Health Science Center at...Sanchez Cancer CenterTerminatedNeoplasm Metastasis | Lung Cancer | Bone Cancer | Prostate CancerUnited States
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Assiut UniversityNot yet recruitingVitamin B 12 Deficiency | End Stage Renal Disease on Dialysis
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Merve KurtRecruitingDuchenne Muscular Dystrophy | Virtual Reality | Spinal Muscular Atrophy | Neuromuscular Disease | BiofeedbackTurkey
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Novartis Gene TherapiesActive, not recruitingSMA | Spinal Muscular Atrophy Type II | Spinal Muscular Atrophy Type I | Spinal Muscular Atrophy Type IIIUnited States, Belgium, France, Japan, United Kingdom, Italy, Taiwan, Australia, Canada
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Columbia UniversityMuscular Dystrophy Association; Stevens Institute of TechnologyCompletedDuchenne Muscular Dystrophy | Spinal Muscular Atrophy Type 3United States
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Dionyssiotis, Yannis, M.D.University of Athens; University of PatrasCompletedStroke | Multiple Sclerosis | Traumatic Brain Injury | Spinal Cord Injuries | Sarcopenic ObesityGreece
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Global Healthy Living FoundationUniversity of Alabama at BirminghamRecruitingHeart Failure | Stroke | Epilepsy | Multiple Sclerosis | Obesity | Diabetes | Chronic Obstructive Pulmonary Disease | Osteoarthritis | Rheumatoid Arthritis | Parkinson Disease | Peripheral Arterial Disease | Inflammatory Bowel Diseases | Amyotrophic Lateral Sclerosis | Psoriasis | Asthma | Muscular Dystrophy | Fibromyalgia | Alzheimer... and other conditionsUnited States
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University of Alabama at BirminghamLakeshore Foundation; YMCA of Greater BirminghamActive, not recruitingStroke | Multiple Sclerosis | Cerebral Palsy | Parkinson Disease | Traumatic Brain Injury | Spinal Cord Injuries | Spina BifidaUnited States
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Bijan Najafi, PhDOrthotic Holdings, Inc.CompletedDiabetes | Cancer | Arthritis | Parkinson's Disease | Peripheral Arterial Disease | End Stage Renal Failure on Dialysis | Accidental Falls | Fall Due to Loss of Equilibrium | High Risk of Falls Due to Mobility LimitationUnited States
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Enzyvant Therapeutics GmBHNational Institute of Allergy and Infectious Diseases (NIAID); Eunice Kennedy... and other collaboratorsCompletedDiGeorge Syndrome | DiGeorge Anomaly | Complete DiGeorge Anomaly | Complete DiGeorge SyndromeUnited States
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Children's Hospital Medical Center, CincinnatiCompletedDuchenne Muscular Dystrophy | Spinal Muscular Atrophy | Congenital Muscular Dystrophy
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Assiut UniversityUnknownDiabetic Neuropathies | Carpal Tunnel Syndrome | Guillain-Barre Syndrome
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AstraZenecaCompletedBleeding ,Arrhythmias, Heart Failure, Acute Renal Failure, Acute Liver Failure, Dyspnoea, GoutSweden
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Mayo ClinicEnrolling by invitationAutoimmune Diseases | Diabetes | Chronic Kidney Diseases | Tobacco Use | Overweight or Obesity | Inflammatory Disease | MRSA | Infections Joint Prosthetic | MSSA ColonizationUnited States
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University of Southern CaliforniaNational Cancer Institute (NCI)WithdrawnStage I Breast Cancer | Cancer Survivor | Stage II Breast Cancer | Stage IIIA Breast Cancer | Stage IIIB Breast Cancer | Stage IA Breast Cancer | Stage IB Breast Cancer | Stage IIA Breast Cancer | Stage IIB Breast Cancer | Stage IIIC Breast Cancer | Estrogen Receptor Positive | Progesterone Receptor Positive | Stage... and other conditionsUnited States
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OHSU Knight Cancer InstituteNational Cancer Institute (NCI); Oregon Health and Science UniversityRecruitingMalignant Solid Neoplasm | Lynch Syndrome | Hematopoietic and Lymphoid System Neoplasm | Breast Ductal Carcinoma In Situ | Hereditary Neoplastic Syndrome | BRCA1/2-Associated Hereditary Breast and Ovarian Cancer SyndromeUnited States
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Ilya PharmaEuropean CommissionRecruitingDiabetic Foot Ulcer | Wound Heal | Wound Healing Disorder | Wound Healing Delayed | Wound Healing Disturbance of | Diabetic Foot Ulcer MixedSweden
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Foundation For Rare Disease ResearchInstitute for Asthma & Allergy; Virant Diagnostics, Inc.; MedBio Reference Laboratories...Not yet recruitingAngioedema | Urticaria | C1 Inhibitor Deficiency | Angioedemas, Hereditary | Mastocytosis | Indolent Systemic Mastocytosis | Systemic Mastocytoses | ACE Inhibitor-Induced Angioedema
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McMaster UniversityCanadian Institutes of Health Research (CIHR)RecruitingDiabetes Mellitus | Chronic Kidney Diseases | Chronic Obstructive Pulmonary Disease | Osteoarthritis | Dementia | Congestive Heart Failure | Depression, AnxietyCanada
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OPKO Health, Inc.RecruitingSecondary Hyperparathyroidism | Chronic Kidney Disease stage4 | Chronic Kidney Disease stage3 | Vitamin d DeficiencyUnited States
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Enzyvant Therapeutics GmBHNational Institute of Allergy and Infectious Diseases (NIAID); Eunice Kennedy... and other collaboratorsCompletedDiGeorge Anomaly | Complete DiGeorge Anomaly | Complete DiGeorge Syndrome | Complete Atypical DiGeorge Anomaly | Complete Atypical DiGeorge SyndromeUnited States
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Cloud DX Inc.CompletedPneumonia | Hypertension | Diabetes Mellitus | Atrial Fibrillation | Urinary Tract Infection | Healthy Volunteers | OSA | COPD | Leukocytosis | Acute Otitis Media | Iron Deficient AnemiaCanada
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University of WashingtonCompletedDiabetes Complications | Renal Insufficiency, Chronic | Dementia | Leukemia, Lymphocytic, Chronic, B-Cell | Peripheral Vascular Disease | Frail Elderly | Congestive Heart Failure | Malignant Neoplasm | Lung Disease Chronic | Liver Failures, ChronicUnited States
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University of ArkansasWithdrawnPancreatic Neoplasms | Colorectal Neoplasms, Hereditary Nonpolyposis | BRCA1 Gene Mutation | BRCA2 Gene Mutation | Hereditary Pancreatitis | Ataxia Telangiectasia | Peutz-Jegher's Syndrome | Familial Atypical Mole-Malignant Melanoma SyndromeUnited States
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EMD Serono Research & Development Institute, Inc.Merck KGaA, Darmstadt, GermanyNot yet recruitingOvarian CancerUnited States, Germany
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Medipol UniversityRecruitingScoliosis | Exercise | Pulmonary Rehabilitation | Spinal Muscular Atrophy Type I | Chest Deformities | Spinal OrthosisTurkey
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University of Miami Sylvester Comprehensive Cancer...The V Foundation for Cancer ResearchRecruitingObesity | Diet, Healthy | Cancer, Breast | Activity, Motor | Cancer, Uterus | Cancer, OvaryUnited States
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The University of Hong KongRecruitingCardiovascular Diseases | Hypertension | Diabetes Mellitus | Cancer | Kidney Disease, Chronic | Noncommunicable Diseases | Chronic Respiratory DiseaseChina
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Assistance Publique - Hôpitaux de ParisCompletedDuchenne Muscular Dystrophy | Spinal Muscular AtrophyFrance
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West China HospitalCompletedDiabetes | Chronic Kidney Diseases | Cardiovascular AbnormalitiesChina
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DePuy InternationalTerminatedOsteoarthritis | Avascular Necrosis | Post-traumatic Arthritis | Congenital Hip Dysplasia | Slipped Capital Femoral Epiphysis | Collagen DisordersGermany
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National Heart, Lung, and Blood Institute (NHLBI)CompletedHeart Diseases | Cardiovascular Diseases | Heart Failure | Coronary Disease | Hypertension | Diabetes Mellitus | Peripheral Vascular Diseases | Kidney Failure, Chronic | Cerebrovascular Accident
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State University of New York at BuffaloRecruitingFibrosis | Hepatitis B | Hepatitis C | Fatty Liver | Cirrhosis | Bariatric Surgery Candidate | Obesity, Childhood | Non-Alcoholic Steatohepatitis(NASH)United States
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Hospices Civils de LyonUnknownGenetic Syndrome | Taybi Linder SyndromeFrance
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Advice Pharma Group srlRecruitingDiabetes | Chronic Kidney Diseases | Tuberous Sclerosis | Albuminuria | Treatment Adherence | Arterial Hypertension | Treatment Adherence and Compliance | Nephronophthisis | Polycystic Kidney | Chronic Glomerulonephritis | Cystic Kidney Diseases | Cortical Cystic Disease | Cystic DiseasesItaly
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National Cancer Institute (NCI)RecruitingLynch Syndrome | Malignant Glioma | Recurrent Childhood Ependymoma | Recurrent Medulloblastoma | Refractory Ependymoma | Refractory Medulloblastoma | Recurrent Diffuse Intrinsic Pontine Glioma | Refractory Diffuse Intrinsic Pontine Glioma | Recurrent Brain Neoplasm | Refractory Brain Neoplasm | Constitutional...United States, Canada
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Okuvision GmbHCompletedPrimary Open Angle Glaucoma | Retinal Vein Occlusion | Retinitis Pigmentosa | Retinal Artery Occlusion | Dry Age Related Macular Degeneration | Hereditary Macular Degeneration | Macula Off | Treated Retina Detachment | Non-Arthritic-Anterior-Ischemic Optic-Neuropathy | Hereditary Autosomal Dominant Optic... and other conditions
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ConvaTec Inc.CompletedMultiple Sclerosis | Lower Urinary Tract Symptoms | Parkinson Disease | Spinal Cord Injuries | Bladder Outlet Obstruction | Cauda Equina Syndrome | Detrusor Underactivity | Enlarged Prostate With Lower Urinary Tract SymptomsUnited Kingdom, United States, France
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Kaiser PermanenteGarfield Memorial FundCompletedLiver Failure | Acquired Immunodeficiency Syndrome | Stroke | Pneumonia | Diabetes Mellitus | Cancer | Pulmonary Disease, Chronic Obstructive | Respiratory Failure | Renal Failure | Dementia | Kidney Failure, Chronic | Coronary Arteriosclerosis | Cerebrovascular Accident | Failure to Thrive | Heart Failure, CongestiveUnited States
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Daniel BernsteinCompletedSoft Tissue Sarcoma | Lymphoma, Non-Hodgkin | Leukemia | Breast Cancer | Myeloproliferative Disorders | Multiple Myeloma | Anemia | Pancreatic Cancer | Hodgkin Disease | Esophageal Cancer | Amyloidosis | Lung Cancer | Bone Cancer | Prostate Cancer | Neuroendocrine Tumors | Mesothelioma | Skin Cancer | Thyroid Cancer | Anal Cancer | Hepatobiliary Neoplasm and other conditionsUnited States
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Baylor College of MedicineThe Methodist Hospital Research Institute; Center for Cell and Gene Therapy...RecruitingHaploidentical Hematopoietic Cell Transplantation Using TCR Alpha/Beta and CD19 Depletion (HAPLOTAB)Myelodysplastic Syndromes | Primary Immunodeficiency Diseases | Hemoglobinopathies | Chronic Myeloid Leukemia | Cytopenia | Severe Aplastic Anemia | Bone Marrow Failure Syndrome | Acute Myeloid Leukemia in Remission | Hemophagocytic Lymphohistiocytoses | Acute Lymphoblastic Leukemia in Remission | Severe...United States
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University of HelsinkiRoyal Children's Hospital; Murdoch Childrens Research Institute; University of... and other collaboratorsActive, not recruitingLiver Diseases | Kidney Diseases | Diabetes | Rheumatic Diseases | Inflammatory Bowel Diseases | Neurologic Disorder | Congenital Heart Disease | TransitionAustralia, Finland
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University of Southern DenmarkZealand University Hospital; Holbaek Sygehus; Naestved Hospital; Nykøbing Falster... and other collaboratorsActive, not recruitingDepression | Heart Failure | Hypertension | Chronic Obstructive Pulmonary Disease | Osteoarthritis, Knee | Coronary Heart Disease | Osteoarthritis, Hip | Type2 DiabetesDenmark
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M.D. Anderson Cancer CenterNational Cancer Institute (NCI)Active, not recruitingObesity | Overweight | Ductal Breast Carcinoma In Situ | Deleterious BRCA1 Gene Mutation | Deleterious BRCA2 Gene Mutation | Premalignant LesionUnited States
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University of Southern CaliforniaNational Institute on Aging (NIA); Huntington HospitalCompletedDepression | Stroke | Hypertension | Diabetes | Cancer | Chronic Obstructive Pulmonary Disease | Asthma | Chronic Heart Failure | Heart Disease | Study Focus: 30-day Rehospitalizations Among At-risk Older Adults Randomized to a Social Work-driven Care Transitions InterventionUnited States