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Clinical Trials on Krabbe Disease
Total 376894 results
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State University of New York at BuffaloEunice Kennedy Shriver National Institute of Child Health and Human Development... and other collaboratorsRecruiting
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Passage Bio, Inc.SuspendedLeukodystrophy, Globoid CellUnited States, Brazil, Netherlands, United Kingdom, Canada, Israel
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Forge Biologics, IncRecruitingKrabbe DiseaseUnited States
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CENTOGENE GmbH RostockWithdrawnKrabbe DiseaseEgypt, Germany, India, Sri Lanka
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Forge Biologics, IncNot yet recruiting
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Forge Biologics, IncActive, not recruiting
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University of PittsburghNational Institute of Neurological Disorders and Stroke (NINDS)Active, not recruiting
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Talaris Therapeutics Inc.Duke UniversityTerminatedNiemann-Pick Disease | Alpha-mannosidosis | Tay Sachs Disease | Sandhoff Disease | Metachromatic Leukodystrophy (MLD) | Hurler-Scheie Syndrome | Hurler Syndrome (MPS I) | Hunter Syndrome (MPS II) | Sanfilippo Syndrome (MPS III) | Krabbe Disease (Globoid Leukodystrophy) | Adrenoleukodystrophy (ALD and AMN) | Pelizaeus...United States
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New York Medical CollegeCompletedMucopolysaccharidosis I | Myelodysplastic Syndrome | Acute Lymphocytic Leukemia | Acute Myelogenous Leukemia | Niemann-Pick Disease | Mucopolysaccharidosis VI | Wolman Disease | Adrenoleukodystrophy | Batten Disease | Metachromatic Leukodystrophy | Diamond-Blackfan Anemia | Severe Aplastic Anemia | Fucosidosis | Gaucher... and other conditionsUnited States
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University of ChicagoNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK); National... and other collaboratorsCompletedKrabbe Disease | Mucopolysaccharidosis Type II (MPS II) | Mucopolysaccharidosis Type I (MPS I) | Mucopolysaccharidosis Type III (MPS III) | Mucopolysaccharidosis Type VI (MPS VI)United States
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Masonic Cancer Center, University of MinnesotaCompletedMucopolysaccharidosis | Hurler Syndrome | Sphingolipidoses | Peroxisomal Disorders | Krabbe Disease | Adrenoleukodystrophy (ALD) | Hunter Syndrome | Sly Syndrome | Fucosidosis | Aspartylglucosaminuria | Alpha Mannosidosis | Metachromatic Leukodystrophy (MLD) | Maroteaux-Lamy SyndromeUnited States
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Masonic Cancer Center, University of MinnesotaTerminatedSphingolipidoses | Niemann-Pick Disease, Type C | Krabbe Disease | Sly Syndrome | Fucosidosis | Aspartylglucosaminuria | Alpha Mannosidosis | Hurler's Syndrome | Maroteaux-Lamy Syndrome | Wolman's Disease | Niemann-Pick Disease Type BUnited States
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University of PittsburghRecruitingLysosomal Storage Diseases | Leukodystrophy | Niemann-Pick Diseases | Batten Disease | Gaucher Disease | Krabbe Disease | Alpha-Mannosidosis | Osteopetrosis | Tay-Sachs Disease | Pelizaeus-Merzbacher Disease | Sandhoff Disease | GM1 Gangliosidoses | MPS I | MPS II | Vanishing White Matter Disease | Multiple Sulfatase Deficiency... and other conditionsUnited States
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Children's Hospital of PhiladelphiaEli Lilly and Company; University of Pennsylvania; Takeda; National Institute of... and other collaboratorsRecruitingMucopolysaccharidoses | Leukoencephalopathies | Leukodystrophy | Adrenoleukodystrophy | Adrenomyeloneuropathy | X-linked Adrenoleukodystrophy | Gangliosidoses | Metachromatic Leukodystrophy | Krabbe Disease | Refsum Disease | Cadasil | Sjogren-Larsson Syndrome | Allan-Herndon-Dudley Syndrome | White Matter Disease | GM2... and other conditionsUnited States
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Children's Hospital of PhiladelphiaIllumina, Inc.Active, not recruitingMucopolysaccharidoses | Leukodystrophy | Adrenoleukodystrophy | Adrenomyeloneuropathy | X-linked Adrenoleukodystrophy | Gangliosidoses | Metachromatic Leukodystrophy | Krabbe Disease | Refsum Disease | Cadasil | Sjogren-Larsson Syndrome | Allan-Herndon-Dudley Syndrome | White Matter Disease | GM2 Gangliosidosis | Zellweger... and other conditionsUnited States
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Gangnam Severance HospitalRecruitingPancretic Dissease (Benign/Malignancy) | BIle Duct Diseae(Benign/Malignancy) | Ampulla of Vater Disease (Benign/Malignancy)Korea, Republic of
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University of MichiganNational Institutes of Health (NIH); National Institute of Dental and Craniofacial...CompletedPeriodontal Disease | Non-diseased PatientsUnited States
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RTI InternationalEunice Kennedy Shriver National Institute of Child Health and Human Development... and other collaboratorsEnrolling by invitationPrimary Hyperoxaluria Type 3 | Diabetes Mellitus | Hemophilia A | Hemophilia B | Hereditary Fructose Intolerance | Cystic Fibrosis | Factor VII Deficiency | Phenylketonurias | Sickle Cell Disease | Dravet Syndrome | Duchenne Muscular Dystrophy | Prader-Willi Syndrome | Fragile X Syndrome | Chronic Granulomatous Disease and other conditionsUnited States
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Yonsei UniversityActive, not recruitingCoronary Artery DiseasseKorea, Republic of
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McMaster Children's HospitalSt. Justine's HospitalCompletedInflammatory Bowel Diseases | Crohn Disease | Colitis | Pediatric Crohns DiseaseCanada
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First Affiliated Hospital of Wenzhou Medical UniversityCompletedLiver Diseases | Small Bowel Disease | Colorectal Disease | Gastric Diseases | Digestive Tract DiseasesChina
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Academisch Medisch Centrum - Universiteit van Amsterdam...CelltrionRecruitingBowel Disease | Inflammatory Disease | Disease CrohnNetherlands
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National Heart, Lung, and Blood Institute (NHLBI)CompletedHeart Diseases | Cardiovascular Diseases | Vascular Diseases | Raynaud's Disease
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The Second Hospital of Nanjing Medical UniversityAir Force Military Medical University, ChinaRecruitingInflammatory Bowel Disease | Crohn's DiseasesChina
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Facet BiotechCompletedCrohn's Disease | Colitis | Digestive System Disease | Gastrointestinal Disease | Intestinal DiseaseUnited States, Canada
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Central Hospital, Nancy, FranceInstitut Régional de Médecine Physique et de RéadaptationUnknownInterest of Hydrophysiotherapy Care in Parkinson Disease's Motor and Non-motor Symptoms (THERMAPARK)Interest of Hydrophysiotherapy Care in Parkinson Disease's Non-motor Symptoms
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Klinikum Westbrandenburg GmbHUnknown
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University of BernMerck Sharp & Dohme LLC; University Hospital, Basel, Switzerland; University... and other collaboratorsCompleted
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Children's Hospital Los AngelesCompleted
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Ryazan State Medical UniversityCompletedChronic Obstructive Pulmonary Disease | Peripheral Artery DiseaseRussian Federation
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Direct Biologics, LLCRecruitingInflammatory Bowel Diseases | Crohn DiseaseUnited States
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First Affiliated Hospital of Harbin Medical UniversityUnknownColon Disease; | Rectal DiseaseChina
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Fondazione IRCCS Policlinico San Matteo di PaviaUniversity of PaviaRecruitingCalcific Aortic Valve DiaseaseItaly
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First Affiliated Hospital of Harbin Medical UniversityUnknownColon Disease; | Rectal Disease;China
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Medtronic - MITGCompletedInflammatory Bowel Disease, Crohn DiseaseIsrael
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National Institutes of Health Clinical Center (CC)CompletedVascular Diseases | Cancer | Metabolic Bone Disease | Inflammatory DiseaseUnited States
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National Institute of Allergy and Infectious Diseases...RecruitingOccupational Accidents | Incubation Period, Infectious DiseseUnited States
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University of North Carolina, Chapel HillUniversity of Amsterdam; Crohn's and Colitis FoundationRecruitingCrohn Disease | Pediatric Crohns DiseaseNetherlands, United States, Canada, Israel
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Pharmbio Korea Co., Ltd.CompletedColonic Diseases | Digestive System Disease | Gastrointestinal Disease | Intestinal DiseaseKorea, Republic of
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Cedars-Sinai Medical CenterUnknownCrohn's Disease | Inflammatory Bowel DiseaseUnited States
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Dartmouth-Hitchcock Medical CenterAbbottCompletedCrohn's Disease | Inflammatory Bowel DiseaseUnited States
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Hospices Civils de LyonNot yet recruitingCrohn Disease | Pediatric Crohns DiseaseFrance
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Janssen-Cilag Ltd.RecruitingFistulizing Crohns Disease | Perianal Crohns DiseaseNetherlands, United States, Belgium, Korea, Republic of, Taiwan, Israel, Japan, Canada, Hungary, Germany, Greece, United Kingdom, Australia, Spain, Saudi Arabia, Poland, Turkey, Portugal, Czechia, Italy, Jordan, France
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Morphic Therapeutic, IncRecruitingInflammatory Bowel Diseases | Crohn's DiseaseUnited States
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Qu Biologics Inc.CompletedCrohn's Disease | Inflammatory Bowel DiseaseCanada
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Simon Fraser UniversityCanadian Institutes of Health Research (CIHR); Michael Smith Foundation for...CompletedHeart Failure | Diabetes | Chronic Obstructive Pulmonary Disease | Chronic Kidney Disease | Ischemic Heart DiseaseCanada
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University of LeicesterRecruitingHeart Failure | Chronic Obstructive Pulmonary Disease | Asthma | Type 2 Diabetes | Coronary Heart Disease | Interstitial Lung DiseaseUnited Kingdom
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New Aera, IncUnknownInterstitial Lung Disease | Chronic Obstructive Lung Disease
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University of NebraskaNot yet recruitingPeripheral Arterial Disease | Peripheral Vascular Diseases | Peripheral Arterial Occlusive Disease | Peripheral Artery DiseaseUnited States