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Clinical Trials on Neuroaxonal Dystrophies
Total 1171 results
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Retrotope, Inc.CompletedNeuroaxonal Dystrophy, InfantileEgypt, China, Saudi Arabia, India, Tunisia
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Retrotope, Inc.Active, not recruitingInfantile Neuroaxonal DystrophyUnited States
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Retrotope, Inc.CompletedInfantile Neuroaxonal Dystrophy | INADUnited States
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Duke UniversityTerminatedInfantile Neuroaxonal DystrophyUnited States
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University Hospital, Clermont-FerrandEnrolling by invitationNeuroaxonal Dystrophy, AtypicalFrance
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ApoPharmaFood and Drug Administration (FDA)CompletedPantothenate Kinase-Associated NeurodegenerationUnited States, Germany, Italy, United Kingdom
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Oregon Health and Science UniversityEunice Kennedy Shriver National Institute of Child Health and Human Development... and other collaboratorsActive, not recruitingPantothenate Kinase-Associated NeurodegenerationUnited States
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Chiesi Canada CorpNo longer availablePantothenate Kinase-Associated Neurodegeneration
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Travere Therapeutics, Inc.TerminatedPantothenate Kinase-Associated NeurodegenerationUnited States, Canada, Czechia, France, Germany, Italy, Norway, Poland, Spain
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ApoPharmaCompletedPantothenate Kinase-Associated NeurodegenerationUnited States, Germany, Italy, United Kingdom
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Myotonic Dystrophy FoundationRecruitingMyotonic Dystrophy | Myotonic Dystrophy 1 | Steinert's Disease | Congenital Myotonic Dystrophy | PROMM (Proximal Myotonic Myopathy) | Steinert Disease | Dystrophia Myotonica 1 | Myotonic Dystrophy 2 | Dystrophia Myotonica | Dystrophia Myotonica 2 | Myotonia Dystrophica | Myotonic Dystrophy, Congenital | Myotonic... and other conditionsUnited States
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Susan J. HayflickOregon Health and Science UniversityRecruitingNeurodegeneration With Brain Iron Accumulation (NBIA)United States
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University Hospital, BordeauxInstitut National de la Santé Et de la Recherche Médicale, FranceCompletedNeurodegeneration With Brain Iron Accumulation (NBIA)France
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Susan J. HayflickOregon Health and Science University; Oregon Clinical and Translational Research...CompletedPantothenate Kinase-associated Neurodegeneration (PKAN)United States
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Castle Creek Biosciences, LLC.TerminatedEpidermolysis Bullosa Dystrophica, RecessiveUnited States
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Instituto de Investigación Hospital Universitario...Instituto de Salud Carlos III; Universidad Carlos III Madrid (TERMeG); St John... and other collaboratorsUnknownEpidermolysis Bullosa Dystrophica, RecessiveSpain
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Krystal Biotech, Inc.CompletedDystrophic Epidermolysis Bullosa | Recessive Dystrophic Epidermolysis Bullosa | Dominant Dystrophic Epidermolysis Bullosa | DEB - Dystrophic Epidermolysis BullosaUnited States
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Krystal Biotech, Inc.RecruitingDystrophic Epidermolysis Bullosa | Recessive Dystrophic Epidermolysis Bullosa | Dominant Dystrophic Epidermolysis BullosaUnited States
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Krystal Biotech, Inc.CompletedDystrophic Epidermolysis Bullosa | Recessive Dystrophic Epidermolysis Bullosa | Dominant Dystrophic Epidermolysis BullosaUnited States
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Ente Ospedaliero Ospedali GallieraActive, not recruitingIron Overload | Neurodegenerative DiseaseItaly
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Shanghai General Hospital, Shanghai Jiao Tong University...RecruitingInherited Retinal DystrophiesChina
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Fondation Ophtalmologique Adolphe de RothschildRecruitingHereditary Retinal DystrophiesFrance
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Abeona Therapeutics, IncNational Institute of Arthritis and Musculoskeletal and Skin Diseases (NIAMS) and other collaboratorsCompletedEpidermolysis Bullosa | Epidermolysis Bullosa DystrophicaUnited States
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Holostem Terapie Avanzate s.r.l.Paracelsus Medical UniversityTerminatedRecessive Dystrophic Epidermolysis BullosaAustria
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Columbia UniversityTerminatedEpidermolysis BullosaUnited States
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University of Southern CaliforniaCompletedRecessive Dystrophic Epidermolysis Bullosa
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University of Southern CaliforniaCompleted
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King's College LondonUnknownRecessive Dystrophic Epidermolysis BullosaUnited Kingdom
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Stanford UniversityTerminatedEpidermolysis Bullosa DystrophicaUnited States
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University of Southern CaliforniaRecruitingRecessive Dystrophic Epidermolysis BullosaUnited States
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Stanford UniversityRecruitingEpidermolysis Bullosa DystrophicaUnited States
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Phoenix Tissue Repair, Inc.CompletedRecessive Dystrophic Epidermolysis BullosaUnited States
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Phoenicis TherapeuticsNot yet recruitingDystrophic Epidermolysis BullosaUnited States
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Thomas Jefferson UniversityOnconova Therapeutics, Inc.RecruitingRecessive Dystrophic Epidermolysis BullosaUnited States
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Castle Creek Biosciences, LLC.Active, not recruitingRecessive Dystrophic Epidermolysis BullosaUnited States
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Phoenix Tissue Repair, Inc.Phoenix Tissue Repair, a BridgeBio companyCompletedRecessive Dystrophic Epidermolysis BullosaUnited States
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RHEACELL GmbH & Co. KGFGK Clinical Research GmbH; Ticeba GmbH; Granzer Regulatory Consulting & ServicesCompletedRecessive Dystrophic Epidermolysis BullosaUnited States, Austria, France, Germany, United Kingdom
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Phoenix Tissue Repair, Inc.CompletedRecessive Dystrophic Epidermolysis BullosaUnited States
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Gangnam Severance HospitalDaewoong Pharmaceutical Co. LTD.CompletedRecessive Dystrophic Epidermolysis BullosaKorea, Republic of
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King's College LondonUniversity College, LondonCompletedRecessive Dystrophic Epidermolysis BullosaUnited Kingdom
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Stanford UniversityCompletedEpidermolysis Bullosa DystrophicaUnited States
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Stanford UniversityRecruitingRecessive Dystrophic Epidermolysis BullosaUnited States
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Stanford UniversityCompletedEpidermolysis Bullosa | Epidermolysis Bullosa DystrophicaUnited States
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Institut National de la Santé Et de la Recherche...UnknownRecessive Dystrophic Epidermolysis BullosaFrance, United Kingdom
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Abeona Therapeutics, IncCompletedEpidermolysis Bullosa | Recessive Dystrophic Epidermolysis BullosaUnited States
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Krystal Biotech, Inc.Stanford UniversityWithdrawnDystrophic Epidermolysis Bullosa | DEB - Dystrophic Epidermolysis BullosaUnited States
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Goethe UniversityNot yet recruitingNeuroaxial Analgesia ProceduresGermany
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Abeona Therapeutics, IncRecruitingEpidermolysis Bullosa | Recessive Dystrophic Epidermolysis Bullosa | RDEBUnited States
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Fondation Ophtalmologique Adolphe de RothschildRecruitingVision Functional Brain Networks in Patients With Hereditary Retinal DystrophiesFrance
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Assistance Publique - Hôpitaux de ParisRecruitingLimb Girdle Muscular DystrophiesFrance