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Clinical Trials on Pick's Disease
Total 378665 results
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Genzyme, a Sanofi CompanyCompletedSphingomyelin LipidosisUnited States, Belgium, Brazil, France, Germany, Italy, United Kingdom
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Genzyme, a Sanofi CompanyCompletedHuman Acid Sphingomyelinase DeficiencyUnited Kingdom, United States
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Mayo ClinicCompleted
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Hospital Sao DomingosCompleted
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St. Luke's-Roosevelt Hospital CenterCompletedCritically Ill Very Elderly Patients Admitted to ICU'sUnited States
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Chung-Hsing WangSanofiNot yet recruiting
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Chinese Medical AssociationRecruiting
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SanofiApproved for marketing
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Genzyme, a Sanofi CompanyCompletedSphingomyelin LipidosisBrazil, France, Italy, United States, Germany, United Kingdom
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National Institute of Neurological Disorders and...CompletedPick Disease of the BrainUnited States
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SanofiRecruitingAcid Sphingomyelinase Deficiency (ASMD)France
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SanofiCompletedSphingomyelin LipidosisItaly, Czechia, Belgium, France, Portugal, Turkey, United States, Argentina, Brazil, Chile, Germany, Romania, Spain
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Masonic Cancer Center, University of MinnesotaCompletedNiemann-Pick Disease | Wolman Disease | Adrenoleukodystrophy | Batten Disease | Metachromatic Leukodystrophy | GM1 Gangliosidosis | Fucosidosis | Globoid Cell Leukodystrophy | Gaucher's Disease | Tay Sachs Disease | Sandhoff DiseaseUnited States
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Joanne Kurtzberg, MDThe Marcus FoundationRecruitingMucopolysaccharidosis II | Brain Diseases, Metabolic, Inborn | Adrenoleukodystrophy | Batten Disease | Leukodystrophy, Metachromatic | Leukodystrophy, Globoid Cell | Alpha-Mannosidosis | Tay-Sachs Disease | Pelizaeus-Merzbacher Disease | Sandhoff Disease | Neimann Pick Disease | Sanfilippo MucopolysaccharidosesUnited States
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University of PittsburghRecruitingLysosomal Storage Diseases | Leukodystrophy | Niemann-Pick Diseases | Batten Disease | Gaucher Disease | Krabbe Disease | Alpha-Mannosidosis | Osteopetrosis | Tay-Sachs Disease | Pelizaeus-Merzbacher Disease | Sandhoff Disease | GM1 Gangliosidoses | MPS I | MPS II | Vanishing White Matter Disease | Multiple Sulfatase Deficiency... and other conditionsUnited States
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SanofiRecruitingAcid SphingoMyelinase Deficiency | Gaucher Disease, SplenomegalyFrance
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Radboud University Medical CenterRecruitingPost-Intensive Care Syndrome (PICS)Netherlands
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Otto-von-Guericke University MagdeburgUniversity Hospital Regensburg; University of RegensburgCompletedCritical Illness | Post Intensive Care Syndrome | PICSGermany
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GAAD Medical Research Institute Inc.UnknownPick Disease of the BrainCanada
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Fairview University Medical CenterUnknownMucopolysaccharidosis I | Niemann-Pick Disease | Mucopolysaccharidosis VI | Wolman Disease | Adrenoleukodystrophy | Metachromatic Leukodystrophy | Pulmonary Complications | Fucosidosis | Globoid Cell Leukodystrophy | Gaucher's Disease | Mannosidosis | I Cell DiseaseUnited States
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Johnson & Johnson Pharmaceutical Research & Development...CompletedFrontotemporal Dementia | Pick Complex
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Albert Einstein College of MedicineEunice Kennedy Shriver National Institute of Child Health and Human Development... and other collaboratorsEnrolling by invitationMucopolysaccharidosis II | Fabry Disease | Niemann-Pick Disease, Type C | Mucopolysaccharidosis VI | Lysosomal Acid Lipase Deficiency | Metachromatic Leukodystrophy | Gaucher Disease | Cerebrotendinous Xanthomatosis | Mucopolysaccharidosis IV A | GM1 Gangliosidosis | Mucopolysaccharidosis VII | Acid Sphingomyelinase... and other conditionsUnited States
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Children's Hospital Los AngelesCompletedGranuloma | Anemia | Thrombocytopenia | Neutropenia | Sickle Cell Disease | Thalassemia | Niemann-Pick Disease | Wiskott-Aldrich Syndrome | Osteopetrosis | Fucosidosis | Chediak Higashi Syndrome | Hurler DiseaseUnited States
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University of North Carolina, Chapel HillNational Institute of Mental Health (NIMH); Psychiatric Center BallerupRecruitingEating Disorders | ARFID | Eating Disorders in Children | Eating, PickyUnited States
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Duke UniversityNational Institute of Mental Health (NIMH)Active, not recruitingARFID | Picky Eating | Eating Disorders in ChildrenUnited States
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University of KentuckyCompletedCritical Illness | Muscle Weakness | Intensive Care (ICU) Myopathy | PICSUnited States
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Talaris Therapeutics Inc.Duke UniversityTerminatedNiemann-Pick Disease | Alpha-mannosidosis | Tay Sachs Disease | Sandhoff Disease | Metachromatic Leukodystrophy (MLD) | Hurler-Scheie Syndrome | Hurler Syndrome (MPS I) | Hunter Syndrome (MPS II) | Sanfilippo Syndrome (MPS III) | Krabbe Disease (Globoid Leukodystrophy) | Adrenoleukodystrophy (ALD and AMN) | Pelizaeus...United States
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New York Medical CollegeCompletedMucopolysaccharidosis I | Myelodysplastic Syndrome | Acute Lymphocytic Leukemia | Acute Myelogenous Leukemia | Niemann-Pick Disease | Mucopolysaccharidosis VI | Wolman Disease | Adrenoleukodystrophy | Batten Disease | Metachromatic Leukodystrophy | Diamond-Blackfan Anemia | Severe Aplastic Anemia | Fucosidosis | Gaucher... and other conditionsUnited States
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IBSA Farmaceutici Italia SrlDerming SRLCompletedAcne Scars - Mixed Atrophic and Hypertrophic | Ice Pick Scars | Rolling Scars | Boxcar ScarsItaly
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University of BarcelonaRecruitingDepression | Quality of Life | Stress | Anxiety | Intensive Care Unit | Family | Patient | PICS | Diary (Blank Journal)Spain
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University of UtahPrimary Children's Hospital; Walden University; Mesa State College: Grand Junction... and other collaboratorsCompletedCerebral Palsy | Sensory Processing Disorder | Developmental Coordination Disorder | NICU | Sensorimotor Deficits | Feeding Problems | Picky EatersUnited States
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Eline C. B. EskesRecruiting
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Uppsala UniversityCompletedDepression | PTSD | Anxiety Disorder | Postintensive Care Syndrome | PICS | Intensive Care Psychiatric Disorder
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Fundación Española de Hematología y HemoterapíaRecruitingGaucher Disease | Acid SphingoMyelinase DeficiencySpain
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Mayo ClinicRecruitingCOVID-19 | Critical Illness | Cognitive Impairment | Dysbiosis | Mental Health Impairment | Weakness, Muscle | PICSUnited States
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General Hospital GroeningeActive, not recruitingCOVID-19 | Mental Health | Critically Ill | Post Intensive Care Syndrome | PICSBelgium
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Duke UniversityEunice Kennedy Shriver National Institute of Child Health and Human Development... and other collaboratorsRecruitingCOVID-19 | Critical Illness | ICU Acquired Weakness | Cardiorespiratory Fitness | PICSUnited States
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University Hospital, LilleRecruiting
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Prevail TherapeuticsEli Lilly and CompanyRecruitingFrontotemporal DementiaUnited States, Australia, Belgium, Spain, United Kingdom, France
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Alector Inc.Active, not recruitingFrontotemporal DementiaCanada, United States, Germany, United Kingdom, Italy, Netherlands
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AI Therapeutics, Inc.No longer available
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National Institute of Neurological Disorders and...Completed
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Tiffany Chow, MDH. Lundbeck A/SCompletedFrontotemporal DementiaCanada
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University Hospital, CaenUniversity Hospital, Rouen; Rennes University HospitalRecruiting
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Nantes University HospitalRecruiting
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Georgetown UniversityJohns Hopkins University; National Institute on Aging (NIA); National Institute...Active, not recruitingAlzheimer Disease | Aphasia, Primary Progressive | AnomiaUnited States
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Norwegian Centre for Ageing and HealthKarolinska University Hospital; Zealand University Hospital; Oslo University... and other collaboratorsCompletedAlzheimer Disease | Frontotemporal DementiaNorway
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Avid RadiopharmaceuticalsCompletedFrontotemporal Dementia | Alzheimer's DiseaseUnited Kingdom
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Bastyr UniversityRecruitingParkinson's Disease | Parkinsonism | Corticobasal Degeneration | Shy-Drager Syndrome | Progressive Supranuclear Palsy | Dementia With Lewy Bodies | MSA - Multiple System Atrophy | Olivopontocerebellar Atrophies | Pick DiseaseUnited States
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University of Missouri-ColumbiaRecruiting