- ICH GCP
- US Clinical Trials Registry
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Clinical Trials on Sanfilippo A
Total 4798 results
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Jiangsu Gensciences lnc.RecruitingSevere Hemophilia AChina
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OctapharmaRecruitingSevere Hemophilia ASpain, Croatia, Italy, North Macedonia, Serbia
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Institute of Hematology & Blood Diseases Hospital...Sinocelltech Ltd.RecruitingHemophilia A With InhibitorChina
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Margaret RagniHealth Resources and Services Administration (HRSA)Terminated
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OctapharmaTerminatedSevere Hemophilia ABulgaria
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Children's Hospital Los AngelesTakedaActive, not recruitingHemophilia A With InhibitorUnited States
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City of Hope Medical CenterCSL Behring; Grifols Therapeutics LLC; Grifols Biologicals, LLC; Charta Foundation and other collaboratorsCompletedSevere Hemophilia AUnited States
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OctapharmaCompletedSevere Hemophilia ARussian Federation, Ukraine
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OctapharmaCompletedSevere Hemophilia AUnited States, France, Canada, United Kingdom, India, Georgia, Moldova, Republic of, Poland, Ukraine
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Bioverativ Therapeutics Inc.CompletedSevere Hemophilia AUnited States, United Kingdom, Australia
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Bioverativ Therapeutics Inc.Swedish Orphan BiovitrumCompletedSevere Hemophilia AUnited States, Australia, New Zealand
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BayerTerminatedHemophilia A and BAustralia, United Kingdom, Taiwan, Japan, Korea, Republic of, Austria, Bulgaria, Hungary, Italy, France, New Zealand
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OctapharmaCompletedSevere Hemophilia AUnited States, Bulgaria
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PfizerCompletedHemophilia A or BUnited States, Chile, Croatia, Poland, South Africa, Switzerland
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Margaret RagniWithdrawn
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Beijing Children's HospitalUnknownHemophilia A With InhibitorChina
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Hampshire Hospitals NHS Foundation TrustUppsala University; University of Wales Cardiff United Kingdom (UK)CompletedSevere Haemophilia AUnited Kingdom
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National Institute of Allergy and Infectious Diseases...Completed
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Skane University HospitalCompleted
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Tri-Service General HospitalRecruitingSevere Hemophilia A Without InhibitorTaiwan
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Institute of Hematology & Blood Diseases HospitalRecruiting
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Groupe Maladies hémorragiques de BretagneRecruitingDesmopressin | Hemophilia A, Mild | Factor VIIIFrance
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University of WashingtonGenentech, Inc.Recruiting
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Novo Nordisk A/SEnrolling by invitationHaemophilia AAustria, Spain, Bulgaria, Croatia, Estonia, Hungary, Italy, Lithuania, Portugal, Greece, Germany, Czechia, Slovenia, Switzerland, Slovakia
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Chulalongkorn UniversityCompletedSevere Hemophilia A Without InhibitorThailand
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Baxalta now part of ShireNo longer available
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The Hospital for Sick ChildrenUnity Health Toronto; Nationwide Children's Hospital; Canadian Hemophilia SocietyUnknown
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Novo Nordisk A/SRecruitingHaemophilia A With or Without InhibitorsKorea, Republic of, India, China, Canada, Spain, Netherlands, South Africa, United States, Israel, Japan, Poland, United Kingdom, Italy, Lithuania, Portugal, Switzerland, Taiwan
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Zhang Lei, MDHenan Cancer Hospital; Qilu Hospital of Shandong University; Tianjin First Central... and other collaboratorsCompletedAcquired Hemophilia AChina
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Baxalta now part of ShireBaxalta Innovations GmbH, now part of ShireCompletedHemophilia A or B With InhibitorsCroatia, North Macedonia, Ukraine
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AryoGen Pharmed Co.CompletedHemophilia A or B With InhibitorIran, Islamic Republic of, Turkey
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University of ValenciaBaxter Healthcare CorporationCompletedHemophilia A, CongenitalSpain
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Grifols Italia S.p.AThrombinoscopeUnknownSevere Hemophilia A With InhibitorItaly
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UPECLIN HC FM Botucatu UnespCompletedHepatitis, Viral, Non-A, Non-B, Parenterally-TransmittedBrazil
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Novo Nordisk A/SCompletedEpidemiological Study on Haemophilia Care and Orthopaedic Status in Developing Countries (HAEMOcare)Congenital Bleeding Disorder | Haemophilia A With Inhibitors | Haemophilia B With Inhibitors | Haemophilia A | Haemophilia BIndia, Morocco, South Africa, Oman
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Novo Nordisk A/SCompletedCongenital Bleeding Disorder | Haemophilia A With Inhibitors | Haemophilia B With Inhibitors | Haemophilia A | Haemophilia BSpain
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CerbaXpertNot yet recruitingWoman Suffering From a Pathology Frequently Associated With the Presence of These Anti-autoantibodies Type-I Interferons
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Consorci Sanitari de l'Alt Penedès i GarrafInstitut Català de la SalutRecruitingVarious Clinical Conditions Commonly Followed up in a Secondary HospitalSpain
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University of Alabama at BirminghamWithdrawnValidation of a New Noninvasive Method to Obtain the Arterial Input Function (AIF) Directly by PET ImagingUnited States
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Assistance Publique - Hôpitaux de ParisCompletedMinor Patient Treated by One or More Antiretroviral and for Which a Blood Test Has Been PerformedFrance
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University Hospital, BordeauxUniversity of BordeauxCompletedEvaluation of a National Health Information Technology-based Program to Improve Healthcare Coordination and Access to InformationFrance
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Université de SherbrookeFonds de la Recherche en Santé du Québec; BSN Medical IncCompletedAutomobile Driving With an Aircast Walker | Automobile Driving With a Walking CastCanada
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Michigan State UniversityNot yet recruiting
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University Medical Center GroningenAccare; Hanzehogeschool Groningen; GGZ Friesland; WIJ Groningen; Amaryllis LeeuwardenRecruiting
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University of PadovaAzienda Ospedaliero Universitaria, Santa Maria della Misericordia di Udine... and other collaboratorsCompletedPregnant Women in All Gestational Ages Hospitalized for a Problem of Pregnancy
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Institute of Liver and Biliary Sciences, IndiaCompletedMindfulness is a Moment by Moment Awareness to Remain Purposefully and Non Judgmentally Attentive to Their Own ExperienceIndia
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Stefan Gilg, MD, PhDUnknownLiver Failure as A Complication of Care
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Central Hospital, Nancy, FranceCompletedPatients Over 75 Years Old With a Cancer DiscoveryFrance
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University Hospital, BrestBayerCompletedBlood Loss After a Total Hip ReplacementFrance