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- US Clinical Trials Registry
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Clinical Trials on Sialic Acid Storage Disease
Total 8544 results
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National Taiwan University HospitalRecruiting
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Amicus TherapeuticsActive, not recruitingPompe DiseaseUnited States, Netherlands, United Kingdom, Australia, Germany, New Zealand
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University of FloridaEunice Kennedy Shriver National Institute of Child Health and Human Development...Completed
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Asklepios Biopharmaceutical, Inc.Active, not recruiting
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University of FloridaLacerta TherapeuticsCompletedPompe DiseaseUnited States
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University of FloridaBioMarin PharmaceuticalCompleted
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LMU KlinikumGenzyme, a Sanofi CompanyCompletedPompe DiseaseGermany, Taiwan, Italy
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Amicus TherapeuticsCompleted
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National Taiwan University HospitalCompleted
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National Taiwan University HospitalUnknown
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Genzyme, a Sanofi CompanyCompletedGlycogen Storage Disease Type IIUnited States, France, Germany, Israel, Italy, Netherlands, Taiwan
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Fundació Institut de Recerca de l'Hospital de la...Genzyme, a Sanofi CompanyUnknown
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National Taiwan University HospitalCompleted
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Amicus TherapeuticsCompletedGlycogen Storage Disease Type II | Pompe DiseaseUnited States
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Southeast University, ChinaZhongda Hospital; Chinese Nutrition SocietyActive, not recruitingMetabolic Diseases | Dyslipidemias | Oxidative Stress | Immune System Disorder | Fatty Acid Metabolism DisorderChina
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University of AarhusActive, not recruitingHeart Failure | Ketosis | KetonemiaDenmark
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Nanfang Hospital of Southern Medical UniversityUnknownNeuralgia, SciaticChina
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University of FloridaPrometheus LaboratoriesCompletedInflammatory Bowel Disease | Glycogen Storage Disease Type IaUnited States
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University of FloridaWithdrawnKetosis | Gastrointestinal Infections
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Medical University of GrazCompletedHealthy | Oxidative Stress | Vitamin B 12 Deficiency | Polyphenols | Thiamine and Niacin Deficiency States | Pyridoxine Deficiency | Folic Acid Deficiency Anemia, Dietary | Peroxidase; Defect | Homocystine; Metabolic DisorderAustria
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Huashan HospitalNot yet recruitingPompe Disease (Late-onset)China
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Rambam Health Care CampusRecruitingPompe Disease Infantile-OnsetIsrael
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Astellas Gene TherapiesRecruitingPompe Disease (Late-onset)United States, United Kingdom
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Amicus TherapeuticsRecruitingPompe Disease (Late-onset)United States, Taiwan, Japan, Australia, Canada
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Genzyme, a Sanofi CompanyRecruitingGlycogen Storage Disease Type II | Pompe DiseaseHungary, Croatia, Serbia, United States, Argentina, Australia, Belgium, Brazil, Bulgaria, Canada, Chile, China, Colombia, Denmark, France, Germany, Greece, Hong Kong, India, Indonesia, Israel, Italy, Japan, Jordan, Korea, Republic of, Kuwait and more
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Amicus TherapeuticsActive, not recruitingPompe Disease (Late-onset)United States, Germany, Taiwan, Belgium, Australia, Slovenia, Spain, Netherlands, Hungary, Japan, Austria, United Kingdom, France, Argentina, Canada, Sweden, Denmark, New Zealand, Greece, Korea, Republic of, Bosnia and Herzegovina, Ita... and more
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Duke UniversityGenzyme, a Sanofi CompanyActive, not recruitingPompe Disease (Late-onset) | Pompe Disease | GAA DeficiencyUnited States
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Amicus TherapeuticsAvailablePompe Disease Infantile-OnsetTaiwan, United States, Italy
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BioMarin PharmaceuticalTerminatedLate-onset Pompe DiseaseUnited States, United Kingdom
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Duke UniversityWithdrawnPompe Disease (Late-onset)United States
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Rambam Health Care CampusCompletedEnzyme Replacement Therapy in Pompe Disease
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Genzyme, a Sanofi CompanyCompletedGlycogen Storage Disease Type II | Pompe Disease Infantile-OnsetUnited States, France, South Africa
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Thomas KanderCompletedBleeding | Trauma | Hypothermia | AcidosisSweden
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Ai PengUnknown
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Duke UniversityWithdrawnHypoxia | Lactic AcidosisUnited States
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Meir Medical CenterCompletedFolic Acid Deficiency | Vitamin B12 DeficiencyIsrael
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Makerere UniversityCompletedCompare Blood Age for TransfusionUganda
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Boston Children's HospitalUNICEF; Ministry of Health, Liberia; Liberia Institute of Statistics and Geo-Information...WithdrawnNutritional Anemia | Knowledge, Attitudes, Practice | Food Habits | Iron Deficiency Anemia Treatment | Nutritional Deficiency | Adolescent Development | Folic Acid Deficiency Anemia, Dietary
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University of CincinnatiWithdrawnCardiovascular Disease | Morbid Obesity | Fatty Acid LevelsUnited States
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Universidade do Vale do SapucaiCompletedRespiration Disorders | Acid-Base ImbalanceBrazil
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Fresenius KabiNot yet recruitingMalnutrition | Pediatric ALL | Essential Fatty Acid Deficiency | Parenteral Nutrition Associated Liver Disease (PNALD)
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DeNova ResearchCompletedSubjects Requesting and Requiring Facial Rejuvenation With Neurotoxins and/or Hyaluronic Acid FillersUnited States
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GeneCradle IncRecruitingPompe Disease Infantile-OnsetChina
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Seventh Medical Center of PLA General HospitalGeneCradle Therapeutics, IncRecruiting
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Fundació Institut de Recerca de l'Hospital de la...Genzyme, a Sanofi CompanyUnknownPompe Disease | Late Onset Pompe DiseaseSpain
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Astellas Gene TherapiesRecruitingPompe Disease (Late-onset)United States, Taiwan, France, Spain
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Amicus TherapeuticsCompletedPompe Disease (Late-onset)United States, Australia, Korea, Republic of, Japan, Taiwan, Belgium, Slovenia, New Zealand, United Kingdom, France, Argentina, Canada, Spain, Bosnia and Herzegovina, Germany, Sweden, Hungary, Austria, Bulgaria, Denmark, Greece, I... and more
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Duke UniversityCompleted
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Amicus TherapeuticsTerminatedLate-onset Pompe DiseaseUnited States, Canada, Australia, Belgium