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Clinical Trials on Spinal Muscular Atrophy Type III Non Ambulant in France
Total 202 results
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Hoffmann-La RocheAssociation Française contre les Myopathies (AFM), ParisCompletedSpinal Muscular Atrophy Type II | Spinal Muscular Atrophy Type III Non AmbulantGermany, Italy, France, Belgium, Poland, Netherlands, United Kingdom
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Institut de Myologie, FranceRoche Pharma AGNot yet recruitingMuscular Atrophy, Spinal, Type II | Muscular Atrophy, Spinal, Type IIIFrance
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Novartis Gene TherapiesActive, not recruitingSMA | Spinal Muscular Atrophy Type II | Spinal Muscular Atrophy Type I | Spinal Muscular Atrophy Type IIIUnited States, Belgium, France, Japan, United Kingdom, Italy, Taiwan, Australia, Canada
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Assistance Publique Hopitaux De MarseilleRecruitingSpinal Muscular AtrophyFrance
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Assistance Publique - Hôpitaux de ParisCompleted
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Institut de Myologie, FranceInstitut RocheCompletedType 2 Spinal Muscular Atrophy | Type 3 Spinal Muscular AtrophyBelgium, France, Germany
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Assistance Publique - Hôpitaux de ParisCompletedInfantile Spinal Muscular Atrophy of Type 2 or 3France
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Scholar Rock, Inc.Active, not recruitingNeuromuscular Diseases | Neuromuscular Manifestations | Atrophy | Muscular Atrophy | Spinal Muscular Atrophy | Muscular Atrophy, Spinal | Spinal Muscular Atrophy Type 3 | SMA | Anti-myostatin | Spinal Muscular Atrophy Type IIUnited States, Spain, Belgium, Germany, Netherlands, Poland, Italy, France, United Kingdom
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Assistance Publique - Hôpitaux de ParisRecruitingSpinal Muscular AtrophyFrance
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Assistance Publique - Hôpitaux de ParisRecruiting
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Assistance Publique - Hôpitaux de ParisCompleted
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Assistance Publique - Hôpitaux de ParisNot yet recruiting
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University Hospital, RouenSociety GENOMIC VISIONTerminatedSpinal Muscular AtrophyFrance
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Centre Hospitalier Universitaire de NiceActive, not recruitingSpinal Muscular AtrophyFrance
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Scholar Rock, Inc.Active, not recruitingNeuromuscular Diseases | Neuromuscular Manifestations | Atrophy | Muscular Atrophy | Spinal Muscular Atrophy | Muscular Atrophy, Spinal | Spinal Muscular Atrophy Type 3 | SMA | Spinal Muscular Atrophy Type 2 | Anti-myostatinUnited States, Germany, Belgium, Spain, United Kingdom, Netherlands, France, Italy, Poland
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Centre d'Investigation Clinique et Technologique...CompletedSpinal Muscular Atrophy | Assessment, SelfFrance
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BiogenRecruitingSpinal Muscular Atrophy (SMA)France
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Alcyone Therapeutics, IncBiogenRecruitingScoliosis | Spinal Muscular Atrophy | Spine DeformityUnited States
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Assistance Publique - Hôpitaux de ParisCompletedDuchenne Muscular Dystrophy | Spinal Muscular AtrophyFrance
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CHU de ReimsRecruitingSpinal Muscular AtrophyFrance
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Centre Hospitalier Universitaire, AmiensRecruitingSpinal Muscular Atrophy | Non Invasive Ventilation | Respiratory Bacterial InfectionFrance
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Hospices Civils de LyonNot yet recruitingSpinal Muscular AtrophyFrance
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Institut de Myologie, FranceCompletedSpinal Muscular AtrophyFrance
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Hospices Civils de LyonRecruitingSpinal Muscular AtrophyFrance
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Assistance Publique - Hôpitaux de ParisCompleted
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Hospices Civils de LyonUnknownResponsiveness and Validation Study of MFM-20 in SMA Patients Treated With Nusinersen (RetroNusiMFM)Spinal Muscular AtrophyFrance
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Hospices Civils de LyonCompletedSpinal Muscular AtrophyFrance
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Novartis Gene TherapiesCompletedSMAFrance, United Kingdom, Italy, Belgium
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Novartis PharmaceuticalsRecruitingSpinal Muscular Atrophy (SMA)Spain, Canada, Taiwan, Belgium, Malaysia, China, Japan, Italy, Singapore, United Kingdom, France, Australia, Thailand, Denmark, United States
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Hoffmann-La RocheActive, not recruitingSpinal Muscular AtrophyBelgium, United States, United Kingdom, France, Poland, Italy, Switzerland, Netherlands, Germany
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Hoffmann-La RocheCompletedMuscular Atrophy, SpinalBelgium, United Kingdom, Germany, France, Italy, Netherlands, Poland
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Hoffmann-La RocheTerminatedMuscular Atrophy, SpinalFrance, Turkey, Canada, United States, Italy, Netherlands, Sweden, Switzerland, United Kingdom
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Hoffmann-La RocheCompletedMuscular Atrophy, SpinalBelgium, United States, China, Spain, Japan, Canada, France, Poland, Brazil, Croatia, Italy, Russian Federation, Turkey, Germany, Serbia, United Kingdom
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BiogenCompletedSpinal Muscular AtrophyUnited States, Germany, Spain, Canada, France, Hong Kong, Italy, Japan, Korea, Republic of, Sweden
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CytokineticsAstellas Pharma Global Development, Inc.CompletedSpinal Muscular AtrophyUnited States, Canada
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Hoffmann-La RocheCompletedMuscular Atrophy, SpinalBelgium, United States, China, Spain, Japan, France, Brazil, Croatia, Italy, Russian Federation, Saudi Arabia, Serbia, Switzerland, Turkey, Ukraine, Poland
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BiogenCompletedSpinal Muscular AtrophyUnited States, Spain, Germany, United Kingdom, Australia, Japan, Canada, Belgium, France, Hong Kong, Italy, Korea, Republic of, Sweden, Turkey
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BiogenActive, not recruitingMuscular Atrophy, SpinalChina, United States, Netherlands, Spain, Korea, Republic of, Taiwan, Australia, Canada, Chile, Saudi Arabia, Poland, Israel, Brazil, Russian Federation, Hungary, Japan, United Kingdom, Italy, Germany, Estonia, Greece, Mexico, Colombia and more
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University Hospital, Strasbourg, FranceRecruitingFeasibility of Neonatal Screening for Spinal AmyotrophyFrance
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BiogenTerminatedSpinal Muscular AtrophyKorea, Republic of, United States, Spain, Canada, Germany, Australia, Japan, Sweden, Belgium, France, Italy, Turkey, United Kingdom
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Genentech, Inc.RecruitingSpinal Muscular AtrophyUnited States, Puerto Rico
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Novartis PharmaceuticalsCompletedSpinal and Bulbar Muscular AtrophyUnited States, Germany, Italy, Denmark
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Novartis PharmaceuticalsCompletedSpinal Muscular AtrophyTaiwan, Belgium, Canada, United States, Australia, France, Italy, Portugal, United Kingdom
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Novartis PharmaceuticalsActive, not recruitingSpinal Muscular AtrophyJapan, Belgium, Spain, Canada, United States, Australia, Italy, France, Netherlands
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AnnJi Pharmaceutical Co., Ltd.Active, not recruitingSpinal and Bulbar Muscular Atrophy | Kennedy's DiseaseUnited States
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BiogenRecruitingHealthy Volunteer | Muscular Atrophy, SpinalKorea, Republic of, Germany, Belgium, Netherlands, France, Italy, Poland, Canada, United Kingdom, Israel
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Centre Henri BecquerelCompletedDiffuse Large B Cell Lymphoma | Grade IIIB Follicular LymphomaFrance
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Hospices Civils de LyonCompletedSarcopenia | SpondylarthropathyFrance
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Assistance Publique - Hôpitaux de ParisInstitut National de la Santé Et de la Recherche Médicale, France; Association...RecruitingAmyotrophic Lateral Sclerosis | Kennedy DiseaseFrance
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University Hospital, Strasbourg, FranceUnknown