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Clinical Trials on Storage Disease in Australia
Total 13394 results
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Medical University of ViennaRecruitingPompe Disease | McArdle DiseaseAustria
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BioMarin PharmaceuticalTerminatedPompe DiseaseUnited States, United Kingdom, Australia, France, Germany, New Zealand
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ISU Abxis Co., Ltd.CompletedGaucher DiseaseAustralia
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Evopoint Biosciences Inc.Completed
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Amicus TherapeuticsActive, not recruitingPompe DiseaseUnited States, Netherlands, United Kingdom, Australia, Germany, New Zealand
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Amicus TherapeuticsRecruitingPompe Disease (Late-onset)United States, Taiwan, Japan, Australia, Canada
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PathWest Laboratory Medicine WACompletedEnd Stage Renal Failure on DialysisAustralia
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Nacuity Pharmaceuticals, Inc.Recruiting
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The Canberra HospitalCompletedColonic DiseasesAustralia
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BioMarin PharmaceuticalTerminatedLate-onset Pompe Patients Untreated or Treated With rhGAASpain, Slovenia, Serbia, Korea, Republic of, Greece, Australia, Singapore, Brazil, Canada, Taiwan, Ireland, Poland, Romania
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4D Molecular TherapeuticsActive, not recruiting
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Amicus TherapeuticsCompletedFabry DiseaseAustralia, Brazil
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Amicus TherapeuticsCompleted
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Immutep Australia Pty. Ltd.CompletedStage IV Melanoma | Stage III MelanomaAustralia
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BioMarin PharmaceuticalCompletedPompe DiseaseUnited States, United Kingdom, France, Australia, Germany
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Sir Charles Gairdner HospitalCompletedEnd Stage Kidney DiseaseAustralia
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Olivia Newton-John Cancer Research InstituteBristol-Myers Squibb; Barwon Health; Austin Health; Eastern Health; Fiona Stanley... and other collaboratorsRecruitingFollicular Lymphoma Stage II | Follicular Lymphoma Stage III | Follicular Lymphoma Stage IVAustralia
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University College, LondonUniversity of Sydney; University Hospital BirminghamUnknownFabry DiseaseUnited Kingdom, Australia
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The Netherlands Cancer InstituteBristol-Myers SquibbActive, not recruitingMalignant Melanoma Stage IIIAustria, Netherlands, Australia, Sweden
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Genzyme, a Sanofi CompanyCompletedGlycogen Storage Disease Type II (GSD-II) | Pompe Disease | Glycogenesis 2 Acid Maltase DeficiencyUnited States, Canada, Australia
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Royal Perth HospitalReCor Medical, Inc.RecruitingHeart Failure | Chronic Kidney Diseases | End Stage Renal DiseaseAustralia
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KDL Inc.UnknownEnd Stage Renal Disease | HyperphosphatemiaAustralia
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Melbourne HealthSanofiWithdrawnLysosomal Storage Diseases | Fabry Disease | Niemann-Pick Disease, Type C | Gaucher DiseaseAustralia
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Evaxion Biotech A/SNovotech (Australia) Pty LimitedTerminatedMelanoma Stage IV | Melanoma Stage IIIAustralia
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Evaxion Biotech A/SMerck Sharp & Dohme LLCRecruitingMelanoma Stage IV | Melanoma Stage IIIAustralia
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Ultragenyx Pharmaceutical IncAbeona Therapeutics, IncEnrolling by invitationMucopolysaccharidosis III-AUnited States, Australia, Spain
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Baker Heart and Diabetes InstituteCompletedHypertension | End-stage Renal DiseaseAustralia
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Amicus TherapeuticsCompletedFabry DiseaseFrance, Austria, United States, Belgium, Japan, United Kingdom, Denmark, Brazil, Australia, Italy
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Amicus TherapeuticsActive, not recruitingPompe Disease (Late-onset)United States, Germany, Taiwan, Belgium, Australia, Slovenia, Spain, Netherlands, Hungary, Japan, Austria, United Kingdom, France, Argentina, Canada, Sweden, Denmark, New Zealand, Greece, Korea, Republic of, Bosnia and Herzegovina, Ita... and more
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University of ManitobaCanadian Institutes of Health Research (CIHR)Recruiting
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BioMarin PharmaceuticalCompletedMucopolysaccharidosis IVA (Morquio A Syndrome)Australia
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Center for Eye Research AustraliaCompleted
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Ultragenyx Pharmaceutical IncAbeona Therapeutics, IncTerminatedMucopolysaccharidosis III | Sanfilippo Syndrome | MPS IIIA | Sanfilippo AUnited States, Spain, Australia
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Medtronic Cardiac Rhythm and Heart FailureTerminated
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Amicus TherapeuticsCompletedPompe Disease (Late-onset)United States, Australia, Korea, Republic of, Japan, Taiwan, Belgium, Slovenia, New Zealand, United Kingdom, France, Argentina, Canada, Spain, Bosnia and Herzegovina, Germany, Sweden, Hungary, Austria, Bulgaria, Denmark, Greece, I... and more
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Amicus TherapeuticsTerminatedLate-onset Pompe DiseaseUnited States, Canada, Australia, Belgium
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Klinikum Wels-GrieskirchenGenzyme, a Sanofi CompanyCompletedFocus of Study: Prevalence of Fabry Disease in CKD PopulationAustria
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Genzyme, a Sanofi CompanyCompletedGlycogen Storage Disease Type II;Pompe's DiseaseCzechia, Taiwan, Belgium, Germany, Korea, Republic of, United States, Argentina, Australia, Austria, Brazil, Canada, Denmark, France, Hungary, Italy, Japan, Mexico, Netherlands, Poland, Portugal, Russian Federation, Spain, Switzerland, Turk... and more
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Oslo University HospitalSt John of God Hospital, Vienna; Nepean Blue Mountains Local Health DistrictCompletedQuality of Life | Pain, Chronic | Deep Endometriosis | Bowel Dysfunction | Endometriosis Related Pain | Endometriosis Rectum | Deep Infiltrating EndometriosisNorway, Australia, Austria
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CSL LimitedCompletedIdiopathic Thrombocytopenic Purpura (ITP)Australia
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AVROBIOTerminatedFabry DiseaseAustralia, Brazil
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Menzies School of Health ResearchThe George Institute; Northern Territory Government of AustraliaCompletedCardiovascular DiseasesAustralia
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Ultragenyx Pharmaceutical IncAbeona Therapeutics, IncActive, not recruitingMucopolysaccharidosis III | Sanfilippo Syndrome | MPS IIIA | Sanfilippo AUnited States, Australia, Spain
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Medical University of ViennaMedical University of GrazUnknownFabry Disease | Left Ventricular HypertrophyAustria
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Genzyme, a Sanofi CompanyCompletedGlycogen Storage Disease Type II (GSD-II) | Pompe Disease (Late-Onset) | Glycogenesis Type II | Acid Maltase Deficiency (AMD)United States, France, Canada, Netherlands, Australia
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Amicus TherapeuticsApproved for marketingPhysician Initiated Expanded Access Request for Migalastat in Individual Patients With Fabry DiseaseFabry DiseaseUnited States, Australia
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Queensland Centre for Gynaecological CancerRoyal Brisbane and Women's HospitalNot yet recruitingUltrasound Therapy; Complications | Lymph Node Metastasis | Groin Node | Vulvar Cancer Stage Ib | Vulvar Cancer Stage IIAustralia
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Medtronic VascularCompletedEnd Stage Renal DiseaseAustralia, Poland
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Melanoma and Skin Cancer Trials LimitedBristol-Myers Squibb; Amgen; Peter MacCallum Cancer Centre, AustraliaActive, not recruitingMelanoma | Melanoma Stage Iv | Melanoma Stage IiiAustralia
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GlaxoSmithKlineCompletedInfluenzaAustralia, Singapore