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Clinical Trials on Type 1 Facioscapulohumeral Muscular Dystrophy
Total 10058 results
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University Hospital, MontpellierTerminatedPrimary Disease Facioscapulohumeral Dystrophy (FSHD)France
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Centre for Human Drug Research, NetherlandsFacio TherapeuticsCompleted
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Centre Hospitalier Universitaire de Saint EtienneAssociation Française contre les Myopathies (AFM), ParisCompletedMuscular Dystrophy, FacioscapulohumeralFrance
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Newcastle-upon-Tyne Hospitals NHS TrustRecruitingBethlem Myopathy | Ullrich Congenital Muscular Dystrophy 1, Digenic, Col6A1/Col6A2 | Ullrich Congenital Muscular Dystrophy 1, Autosomal Recessive | Ullrich Congenital Muscular Dystrophy 1, Autosomal Dominant | Bethlem Myopathy 1, Autosomal Recessive | UCMD | BTHLM1United Kingdom
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Grete Andersen, MDAP Moeller Foundation; The Danish Rheumatism Association; Aase and Ejnar Danielsens... and other collaboratorsCompletedFacioscapulohumeral Muscle DystrophyDenmark
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Radboud University Medical CenterSolve FSHDRecruitingMuscular Dystrophy, FacioscapulohumeralNetherlands
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Centre Hospitalier Universitaire de NiceCompletedMuscular Dystrophy, FacioscapulohumeralFrance
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Centre Hospitalier Universitaire de NiceCompletedMuscular Dystrophy, FacioscapulohumeralFrance
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McMaster UniversityCompletedMuscular Dystrophies | Myotonic Dystrophy 1Canada
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Centre Hospitalier Universitaire de Saint EtienneÖrebro University, Sweden; Association Française contre les Myopathies (AFM)...CompletedMuscular Dystrophy, FacioscapulohumeralFrance
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Lupin Ltd.WithdrawnMyotonic Dystrophy Type 1 and Type 2
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Murdoch Childrens Research InstituteCompletedFacio-Scapulo-Humeral Dystrophy | FSHD2 | FSHD1Australia
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Nationwide Children's HospitalRecruiting
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Istanbul University - Cerrahpasa (IUC)CompletedFacio-Scapulo-Humeral DystrophyTurkey
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Vertex Pharmaceuticals IncorporatedRecruitingMyotonic Dystrophy Type 1 (DM1)United Kingdom, Canada, Australia
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Dyne TherapeuticsRecruitingMyotonic Dystrophy Type 1 (DM1)United Kingdom, France, Netherlands, Italy, Germany, New Zealand
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Ohio State UniversityCompletedMuscular Dystrophy, Facioscapulohumeral
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University of OsloOslo University Hospital; Vikersund Rehabilitation CenterCompletedMyotonic Dystrophy Type 1 (DM1)Norway
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Expansion Therapeutics, Inc.CompletedMyotonic Dystrophy | Myotonic Dystrophy, Type 1 (DM1)United States
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Avidity Biosciences, Inc.Active, not recruitingNervous System Diseases | Genetic Diseases, Inborn | Musculoskeletal Diseases | Muscular Diseases | Neuromuscular Diseases | Neurodegenerative Diseases | Muscular Dystrophies | Muscular Disorders, Atrophic | Heredodegenerative Disorders, Nervous System | Myotonic Dystrophy | Myotonic Disorders | Myotonic Dystrophy... and other conditionsUnited States
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University Hospital, MontpellierRecruitingPrimary Disease Fascioscapulohumeral Dystrophy (FSHD)France
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Université du Québec à ChicoutimiRecruitingMyotonic Dystrophy Type 1 (DM1)Canada
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Virginia Commonwealth UniversityRadboud University Medical Center; University of California, Los Angeles; University... and other collaboratorsRecruitingMyotonic Dystrophy 1United States, Netherlands, United Kingdom, New Zealand, Germany, Italy, Canada, France
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Vrije Universiteit BrusselCompletedMyotonic Dystrophy 1Belgium
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Élise DuchesneFondation du Grand défi Pierre LavoieCompletedMyotonic Dystrophy 1Canada
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IRCCS Eugenio MedeaRecruiting
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Oslo University HospitalUniversity of Oslo; Haukeland University HospitalRecruitingMyotonic Dystrophy 1Norway
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Université de SherbrookeRare Disease FoundationCompletedMyotonic Dystrophy 1Canada
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LMU KlinikumCompleted
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Cynthia GagnonFondation du Grand défi Pierre LavoieCompletedEffects of a Multiple Component Training Program on Muscles in Adults With Myotonic Dystrophy Type 1Myotonic Dystrophy 1Canada
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Acceleron Pharma Inc. (a wholly owned subsidiary...TerminatedCharcot-Marie-Tooth Disease | Facioscapulohumeral Muscular DystrophyUnited States, Spain, Canada
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PepGen IncRecruitingMyotonic Dystrophy 1United States, Canada
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Norwegian School of Sport SciencesUniversity of Oslo; Oslo University Hospital; University of Copenhagen; University... and other collaboratorsCompleted
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CHU de ReimsCompletedMyotonic Dystrophy Type 1 (DM1)France
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IRCCS San Camillo, Venezia, ItalyCompletedMyotonic Dystrophy Type 1 (DM1)
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Centre Hospitalier Universitaire de Saint EtienneMinistry of Health, France; Association Française contre les Myopathies (AFM)...CompletedMuscular Dystrophy | FacioscapulohumeralFrance
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Laval UniversityCompleted
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Swiss Federal Institute of TechnologyCompletedMuscle Weakness | Muscular Dystrophies | Muscular Dystrophy | Muscular Dystrophy, Facioscapulohumeral | Scapular Dyskinesis | Muscular WeaknessGermany, Switzerland
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University of Kansas Medical CenterHoffmann-La Roche; Seattle Children's Hospital; University of Rochester; University... and other collaboratorsRecruitingFSHDUnited States, Canada, United Kingdom
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Centre Hospitalier Universitaire de NiceActive, not recruitingMuscular Dystrophy | FacioscapulohumeralFrance
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Fondazione Policlinico Universitario Agostino Gemelli...Recruiting
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Ohio State UniversityGilead SciencesCompletedMyotonic Dystrophy 1 | Myotonia Congenita | Paramyotonia CongenitaUnited States
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Assistance Publique - Hôpitaux de ParisRecherche Clinique Paris Descartes Necker Cochin Sainte Anne; AFM-Téléthon...Recruiting
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University Hospital of North NorwayUniversity of Tromso; Norwegian Muscle Disease Association (FFM); Norwegian National... and other collaboratorsActive, not recruitingMuscular Dystrophies | Limb Girdle Muscular Dystrophy | Limb Girdle Muscular Dystrophy, Type 2I | Limb Girdle Muscular Dystrophy R9 FKRP-relatedNorway
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University of LiverpoolBournemouth University; Robert Jones and Agnes Hunt Orthopaedic and District... and other collaboratorsRecruitingNeuromuscular Diseases | Shoulder Injuries | Shoulder Pain | Upper Extremity Problem | Facio-Scapulo-Humeral DystrophyUnited Kingdom
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University Hospital, MontpellierUnknownDuchenne Muscular Distrophy (DMD)France
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ML Bio Solutions, Inc.RecruitingLimb-Girdle Muscular Dystrophy Type 2I (LGMD2I)United States, Netherlands, United Kingdom, Denmark, Australia, Italy, Norway
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Linda Pax LowesRecruitingLimb-Girdle Muscular Dystrophy Type 2A | Limb-Girdle Muscular Dystrophy, Type 2EUnited States
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Cooperative International Neuromuscular Research...Carolinas Medical Center lead study siteCompletedBecker Muscular Dystrophy | Limb-Girdle Muscular Dystrophy, Type 2A (Calpain-3 Deficiency) | Limb-Girdle Muscular Dystrophy, Type 2B (Miyoshi Myopathy, Dysferlin Deficiency) | Limb-Girdle Muscular Dystrophy, Type 2I (FKRP-deficiency)United States
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Rigshospitalet, DenmarkCompletedBecker Muscular Dystrophy | Limb-Girdle Muscular Dystrophy Type 2IDenmark