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Clinical Trials on Ullrich Congenital Muscular Dystrophy
Total 2150 results
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University of Texas Southwestern Medical CenterRecruitingDuchenne Muscular Dystrophy | Becker Muscular Dystrophy | Dilated Cardiomyopathy | Cardiomyopathy, Hypertrophic | Heart Failure With Reduced Ejection Fraction | Cardiac Sarcoidosis | Heart Failure With Preserved Ejection FractionUnited States
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McMaster UniversityNot yet recruiting
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Centre Hospitalier Universitaire de NiceWithdrawn
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AMO Pharma LimitedCompletedMyotonic Dystrophy 1United Kingdom
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Coordinación de Investigación en Salud, MexicoInstituto Nacional de RehabilitacionCompletedMuscular Dystrophy, DuchenneMexico
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Assistance Publique - Hôpitaux de ParisCompletedDuchenne Muscular Dystrophy | Spinal Muscular AtrophyFrance
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Manhattan Eye, Ear & Throat HospitalGenentech, Inc.CompletedPolypoidal Choroidal Vasculopathy | Pseudoxanthoma Elasticum | Pathological Myopia | Retinal Angiomatous Proliferation | Coats' Disease | Idiopathic Retinal Telangiectasia | Multi-focal Choroiditis | Rubeosis Iridis | Von Hippel Lindau Disease | BEST VITELLIFORM MACULAR DYSTROPHY, MULTIFOCAL (Disorder)United States
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Ionis Pharmaceuticals, Inc.CompletedMyotonic Dystrophy Type 1United States
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Newcastle-upon-Tyne Hospitals NHS TrustCompletedMyotonic Dystrophy Type 1United Kingdom
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University of RochesterCompletedMyotonic DystrophyUnited States
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University of RochesterNational Institute of Neurological Disorders and Stroke (NINDS); University... and other collaboratorsCompletedMyotonic Dystrophy Type 1United States
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Stanford UniversityUnknownMyotonic Dystrophy Type 1United States
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University of RochesterNational Institute of Neurological Disorders and Stroke (NINDS); Imsmed IncorporatedCompleted
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Universität Duisburg-EssenWeinmann Geräte für Medizin GmbH + Co. KGCompletedDuchenne Muscular Dystrophy | Spinal Muscular Atrophy | Chronic Respiratory InsufficiencyGermany
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Radboud University Medical CenterUnknownMyotonic Dystrophy Type 2 | McArdle Disease | Nemaline Myopathy Type 6
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University Hospital, GrenobleCompletedPediatric ALL | Arthrogryposis Multiplex Congenita | AMC-Arthrogryposis Multiplex CongenitaFrance
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Institut de Myologie, FranceEnrolling by invitationMyotonic Dystrophy Type 1France
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Insmed IncorporatedMuscular Dystrophy AssociationCompleted
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Prof. Dr. Benedikt SchoserCompleted
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Massachusetts General HospitalRecruiting
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Centre d'Investigation Clinique et Technologique...Recruiting
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Johns Hopkins UniversityNational Heart, Lung, and Blood Institute (NHLBI)Enrolling by invitationHypertrophic Cardiomyopathy (HCM) | Long QT Syndrome (LQTS) | Catecholaminergic Polymorphic Ventricular Tachycardia (CPVT) | Inherited Cardiac Arrythmias | Brugada Syndrome (BrS) | Early Repolarization Syndrome (ERS) | Arrhythmogenic Cardiomyopathy (AC, ARVD/C) | Dilated Cardiomyopathy (DCM) | Muscular... and other conditionsUnited States
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Harmony Biosciences, LLCActive, not recruitingMyotonic Dystrophy 1 | Excessive Daytime SleepinessUnited States, Canada
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Assistance Publique - Hôpitaux de ParisTerminatedNeuromuscular Diseases | Amyotrophic Lateral Sclerosis | Duchenne Muscular DystrophyFrance
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University of LiverpoolBournemouth University; Robert Jones and Agnes Hunt Orthopaedic and District... and other collaboratorsRecruitingNeuromuscular Diseases | Shoulder Injuries | Shoulder Pain | Upper Extremity Problem | Facio-Scapulo-Humeral DystrophyUnited Kingdom
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ResMedClinical Trial Center North Hamburg Germany; CRI-The Clinical Research Institute...TerminatedPulmonary Disease, Chronic Obstructive | Amyotrophic Lateral Sclerosis | Muscular Dystrophies | Duchenne Muscular Dystrophy | Myotonic Dystrophy | Spinal Cord Injury | Obesity Hypoventilation Syndrome | Kyphoscoliosis | Congenital Central Hypoventilation Syndrome | MyopathiesGermany
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Myogem Health Company, S.L.CompletedMyotonic Dystrophy 1Spain
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Assistance Publique - Hôpitaux de ParisNot yet recruitingMyotonic Dystrophy 1 | Steinert's Disease | MetforminFrance
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Radboud University Medical CenterAssistance Publique - Hôpitaux de Paris; Ludwig-Maximilians - University of... and other collaboratorsCompletedMyotonic Dystrophy Type 1Netherlands, France, Germany, United Kingdom
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Eye Hospital Pristina KosovoEnrolling by invitationMacular Corneal DystrophyKosovo
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Lokman Hekim ÜniversitesiHacettepe UniversityCompletedQuality of Life | Lower Urinary Tract Symptoms | Muscle Weakness | Duchenne Muscular Dystrophy | Pelvic Floor Muscle Weakness | Posture Disorders in Children | Lumbar LordosisTurkey
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Wake Forest University Health SciencesNational Institute of Neurological Disorders and Stroke (NINDS)RecruitingMyotonic Dystrophy Type 2United States
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Stanford UniversityBiogenActive, not recruitingMyotonic Dystrophy 1United States
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Turkish Society of Pediatric Gastroenterology,...CompletedDuchenne Muscular Dystrophy | Pompe Disease (Late-onset)Turkey
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University of Campania "Luigi Vanvitelli"RecruitingSudden Cardiac Death | Myotonic Dystrophy 1Italy
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Nemours Children's ClinicCompletedMuscular Dystrophy | Spinal Muscular Atrophy | Arthrogryposis
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Gillette Children's Specialty HealthcareUniversity of MinnesotaCompletedSpinal Muscular Dystrophy | Neuromuscular DisabilityUnited States
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University College, LondonNational Institute for Health Research, United Kingdom; Myotonic Dystrophy... and other collaboratorsRecruitingMyotonic Dystrophy 1 | Dysphagia, OropharyngealUnited Kingdom
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Institut de Myologie, FranceRecruitingMuscular Dystrophies | Mitochondrial Myopathies | Glycogen Storage Disease | Idiopathic Inflammatory Myopathies | Congenital MyopathyFrance
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Institut de Myologie, FranceRecruitingMuscular Dystrophies | Mitochondrial Myopathies | Glycogen Storage Disease | Idiopathic Inflammatory Myopathies | Congenital MyopathyFrance
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McGill UniversityCanadian Institutes of Health Research (CIHR); McGill University Health Centre... and other collaboratorsCompletedCerebral Palsy | Muscular Dystrophies | Spina Bifida | Musculoskeletal DisorderCanada
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National Institute of Respiratory Diseases, MexicoUnknownMyotonic Dystrophy 1 | Steinert DiseaseMexico
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The Methodist Hospital Research InstituteRecruitingMeningocele | Myelomeningocele | Spina Bifida | Bladder Exstrophy | Genitourinary Congenital Anomalies | Cloacal ExstrophyUnited States
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Barcelona Macula FoundationRecruitingRetinitis Pigmentosa | Choroideremia | Stargardt Disease 1 | Best Disease | Pattern Dystrophy of MaculaSpain
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National Heart, Lung, and Blood Institute (NHLBI)CompletedCardiomyopathy, Hypertrophic | Muscular Dystrophy, OculopharyngealUnited States
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Wake Forest University Health SciencesTerminatedFuchs Dystrophy | Cystoid Macular EdemaUnited States
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Spark Therapeutics, Inc.Children's Hospital of Philadelphia; University of IowaActive, not recruitingLeber Congenital Amaurosis | Inherited Retinal Dystrophy Due to RPE65 MutationsUnited States
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ProQR TherapeuticsRecruitingEye Diseases | Neurologic Manifestations | Retinal Degeneration | Retinal Dystrophies | Sensation Disorders | Vision Disorders | Blindness | Leber Congenital Amaurosis | Leber Congenital Amaurosis 10 | Retinal Disease | Eye Disorders CongenitalBelgium, Brazil, Canada, Germany, Italy, Netherlands, United Kingdom
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Fondazione Policlinico Universitario Agostino Gemelli...RecruitingRetinal Detachment | Epiretinal Membrane | Macular Holes | Macular DystrophiesItaly
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GlaxoSmithKlineCompleted