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- US Clinical Trials Registry
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Search clinical trials for: Urea Cycle Defects
Total 5079 results
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National Human Genome Research Institute (NHGRI)TerminatedCitrullinemia | Argininosuccinic Aciduria | Hyperargininemia | Ornithine Carbamoyltransferase Deficiency | Carbamoyl-Phosphate Synthase I Deficiency | N-Acetylglutamate Synthase DeficiencyUnited States
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Translate Bio, Inc.WithdrawnOrnithine Transcarbamylase Deficiency
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Aeglea BiotherapeuticsCompletedArginase I Deficiency | HyperargininemiaUnited States, Canada, United Kingdom, Portugal
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Centre Hospitalier Universitaire de BesanconUnknownBiomarkers | Enteral Nutrition | Intensive Care Unit
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Promethera TherapeuticsCompletedUrea Cycle Disorders | Crigler Najjar SyndromeBelgium
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Horizon Therapeutics, LLCCompletedUrea Cycle DisorderUnited States, Canada
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Horizon Therapeutics, LLCCompletedUrea Cycle DisordersUnited States, Canada
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University of South FloridaNational Institutes of Health (NIH)CompletedUrea Cycle DisordersUnited States
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Brendan LeeEunice Kennedy Shriver National Institute of Child Health and Human Development... and other collaboratorsCompletedAmino Acid Metabolism, Inborn Errors | Urea Cycle Disorders | Argininosuccinic AciduriaUnited States
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Baylor College of MedicineCompletedUrea Cycle Disorders, InbornUnited States
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Texas Woman's UniversityCompleted
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Luca RonfaniUniversity of TriesteCompletedUrea Cycle Disorders, Inborn | Other Metabolic DiseasesItaly
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Horizon Pharma Ireland, Ltd., Dublin IrelandCompletedUrea Cycle DisordersUnited States
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Horizon Pharma Ireland, Ltd., Dublin IrelandCompletedUrea Cycle DisordersUnited States, Canada
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Horizon Pharma Ireland, Ltd., Dublin IrelandCompletedUrea Cycle DisordersUnited States, Canada
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Horizon Pharma Ireland, Ltd., Dublin IrelandUcyclyd Pharma, Inc.CompletedHepatic Encephalopathy | Urea Cycle DisordersUkraine
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Horizon Pharma Ireland, Ltd., Dublin IrelandCompletedUrea Cycle DisordersUnited States
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Horizon Pharma Ireland, Ltd., Dublin IrelandCompletedUrea Cycle DisordersUnited States, Canada
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Vanderbilt UniversityCompleted
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Cytonet GmbH & Co. KGCompletedOrnithine Transcarbamylase Deficiency | Urea Cycle Disorders | Citrullinemia | Carbamoylphosphate Synthetase I DeficiencyGermany
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Cytonet GmbH & Co. KGTerminatedUrea Cycle DisordersUnited States, Canada
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Mark BatshawEunice Kennedy Shriver National Institute of Child Health and Human Development... and other collaboratorsTerminatedUrea Cycle DisordersUnited States, Canada
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Andrea GropmanNational Center for Research Resources (NCRR); Rare Diseases Clinical Research... and other collaboratorsCompletedBrain Diseases, Metabolic, Inborn | Ornithine Transcarbamylase Deficiency | Urea Cycle DisorderUnited States
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Uta Lichter-KoneckiMedical College of Wisconsin; Children's National Research InstituteCompletedUrea Cycle Disorders | Organic AcidemiasUnited States
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University of PennsylvaniaTerminatedOrnithine Transcarbamylase Deficiency Disease
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Baylor College of MedicineCompletedCitrullinemiaUnited States
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Children's Hospital of PhiladelphiaEunice Kennedy Shriver National Institute of Child Health and Human Development...WithdrawnUrea Cycle Disorders, Inborn | Inborn Errors of Metabolism | Propionic Acidemia | Methylmalonic Acidemia | Carbamyl Phosphate Synthetase Deficiency
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Cliniques universitaires Saint-Luc- Université...UnknownDisorder of the Urea CycleBelgium
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University of North Carolina, Chapel HillNational Center for Complementary and Integrative Health (NCCIH)CompletedAsthma | Allergy | Asthmatic | AllergicUnited States
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Icahn School of Medicine at Mount SinaiTerminatedCongenital Heart DiseaseUnited States
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Akron Children's HospitalCompletedHypoalbuminemiaUnited States
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University Hospital, Clermont-FerrandUnknown
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Cytonet GmbH & Co. KGCompletedUrea Cycle DisordersGermany
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Altitude Physiology ExpeditionsUniversity of EdinburghCompletedAcute Mountain SicknessUnited Kingdom
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Eunice Kennedy Shriver National Institute of Child...Children's National Research InstituteTerminatedPhase I Pilot Study of Liver-Directed Gene Therapy for Partial Ornithine Transcarbamylase DeficiencyOrnithine Transcarbamylase Deficiency Disease
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National Center for Research Resources (NCRR)Baylor College of MedicineUnknownAmino Acid Metabolism, Inborn ErrorsUnited States
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National Center for Research Resources (NCRR)Johns Hopkins UniversityCompletedAmino Acid Metabolism, Inborn Errors
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Istanbul UniversityNot yet recruitingMolar Incisor Hypomineralization | Intraosseous AnesthesiaTurkey
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Riphah International UniversityRecruitingPost-cardiac SurgeryPakistan
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Riphah International UniversityNot yet recruiting
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Riphah International UniversityRecruitingAbdominal SurgeryPakistan
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Bruce CreeKyverna TherapeuticsRecruitingProgressive Multiple SclerosisUnited States
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City of Hope Medical CenterNational Cancer Institute (NCI)RecruitingRecurrent Acute Lymphoblastic Leukemia | Refractory Acute Lymphoblastic LeukemiaUnited States
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University Hospital, RouenNot yet recruiting
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Institute of Hematology & Blood Diseases Hospital...RecruitingRelapse Acute Myeloid LeukemiaChina
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Fresenius Medical Care Deutschland GmbHWinicker Norimed GmbHNot yet recruitingChronic Kidney Diseases | Renal Failure
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Istituto Clinico HumanitasNot yet recruitingSuturing Through-the-scope System Used for Prophylactic Closure of Colonic Post-ESD Defects (STITCH)Precancerous Lesion of Colon
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Mayo ClinicNot yet recruitingWHO Grade 3 Glioma | WHO Grade 2 Glioma | WHO Grade 4 GliomaUnited States
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Nantes University HospitalUniversity of Angers - Pays de la Loire psychology laboratoryNot yet recruitingCongenital Heart Defects | Neurodevelopmental DisorderFrance
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Ruijin HospitalNot yet recruitingDiffuse Large B-Cell Lymphoma