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Search clinical trials for: Mitochondrial depletion syndrome
Total 38153 results
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Jesús González de la Aleja TejeraCompleted
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Aadi Bioscience, Inc.Withdrawn
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Edison Pharmaceuticals IncWithdrawn
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Comenius UniversitySanatórium of Dr. Guhr, n.o.; Kaneka Pharma Europe N.V.CompletedCOVID-19 Respiratory InfectionSlovakia
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Jerry Vockley, MD, PhDUltragenyx Pharmaceutical IncNo longer availableBarth Syndrome | Mitochondrial Trifunctional Protein Deficiency | Very Long-chain acylCoA Dehydrogenase (VLCAD) Deficiency | Carnitine Palmitoyltransferase Deficiencies (CPT1, CPT2) | Long-chain Hydroxyacyl-CoA Dehydrogenase Deficiency | Glycogen Storage Disorders | Pyruvate Carboxylase Deficiency... and other conditionsUnited States
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National Heart, Lung, and Blood Institute (NHLBI)CompletedMitochondrial Disorders | Li-Fraumeni Syndrome | Carriers of p53 MutationUnited States
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Medical College of WisconsinChildren's Hospital of PhiladelphiaCompletedMalignant Diseases (ie, Leukemia, MDS, Lymphoma) | Non-malignant Diseases (ie, Bone Marrow Failure Syndromes)United States
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Abliva ABCompletedMitochondrial Diseases | Mitochondrial Myopathies | MELAS Syndrome | Mitochondrial Respiratory Chain DeficienciesUnited Kingdom
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Khondrion BVDrug Research Unit Ghent, BelgiumCompletedMitochondrial Disease | MELAS | Leigh Syndrome | LHON | Mitochondrial DNA tRNALeu(UUR) m.3243A<G MutationBelgium
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Massachusetts General HospitalCompletedFabry Disease | Mitochondrial Disease | Small Fiber Neuropathy | Ehlers Danlos SyndromeUnited States
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Minovia Therapeutics Ltd.CompletedMitochondrial Diseases | Pearson SyndromeIsrael
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University of Maryland, BaltimoreWithdrawnHiv | Frailty Syndrome
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University of ArkansasSt. Christopher's Hospital for ChildrenCompleted
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Medical College of WisconsinCompletedDyspepsia | Irritable Bowel Syndrome | Functional Gastrointestinal Disorders | Functional Abdominal Pain SyndromeUnited States
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Haukeland University HospitalOslo University Hospital; University Hospital of North Norway; The Research Council... and other collaboratorsCompletedChronic Fatigue Syndrome/ Myalgic Encephalitis (CFS/ME)Norway
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Haukeland University HospitalCompleted
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Federal Research Institute of Pediatric Hematology...CompletedPrimary Immune Deficiency Disorder | Hematopoietic Stem Cell TransplantationRussian Federation
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Kala Pharmaceuticals, Inc.CompletedDry Eye Syndromes | Keratoconjunctivitis SiccaUnited States
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National Heart, Lung, and Blood Institute (NHLBI)CompletedCancer | Muscle Weakness | Skin FibroblastsUnited States
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Edison Pharmaceuticals IncTerminated
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PTC TherapeuticsAxio Research. LLCCompleted
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The Cleveland ClinicNational Institutes of Health (NIH)CompletedPearson Syndrome
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Fred Hutchinson Cancer CenterNational Cancer Institute (NCI)TerminatedMyelodysplastic Syndromes | Leukemia | Graft Versus Host DiseaseUnited States
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Centre Hospitalier Universitaire DijonCompleted
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Center for Rare Neurological Diseases, Norcross...Ultragenyx Pharmaceutical Inc; Rett Syndrome Research TrustUnknownRett SyndromeUnited States
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St. Jude Children's Research HospitalCompletedHodgkin Lymphoma | Myelodysplastic Syndrome (MDS) | Leukemia, Acute Lymphocytic (ALL) | Juvenile Myelomonocytic Leukemia (JMML) | Leukemia, Myeloid, Acute(AML) | Leukemia, Myeloid, Chronic(CML) | Hemoglobinuria, Paroxysmal Nocturnal (PNH) | Lymphoma, Non-Hodgkin (NHL)United States
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Azienda Socio Sanitaria Territoriale degli Spedali...CompletedCerebellar Ataxia | Multiple System Atrophy | Spinocerebellar Ataxias | Spinocerebellar Degenerations | Spinocerebellar Ataxia 3 | Friedreich Ataxia | Spinocerebellar Ataxia Type 1 | Spinocerebellar Ataxia Type 2 | Ataxia, Spinocerebellar | Ataxia, Cerebellar | Ataxia With Oculomotor ApraxiaItaly
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Fundación para el Fomento de la Investigación Sanitaria...CompletedPolycystic Ovary SyndromeSpain
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Cairo UniversityCompletedPolycystic Ovary Syndrome | Assisted ReproductionEgypt
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Chiang Mai UniversityCompleted
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Baylor College of MedicineThe Methodist Hospital Research Institute; Center for Cell and Gene Therapy...CompletedAcute Myeloid Leukemia | Acute Lymphoblastic Leukemia | Myelodysplastic Syndrome | Chronic Myelogenous Leukemia | Hemophagocytic Lymphohistiocytosis (HLH) | Non Hodgkins Lymphoma | Familial Hemophagocytic Lymphohistiocytosis (FLH) | Viral-associated Hemophagocytic Syndrome (VAHS) | X-linked Lymphoproliferative...United States
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Medical College of WisconsinChildren's Hospital and Health System Foundation, WisconsinCompletedVomiting | MigrainesUnited States
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Helsinki University Central HospitalGöteborg University; University of Iowa; University of Helsinki; Finnish Institute...Completed
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The University of Texas Health Science Center at...National Institute of Diabetes and Digestive and Kidney Diseases (NIDDK)CompletedInsulin Sensitivity | Multiple Mitochondrial Dysfunctions SyndromeUnited States
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University of Colorado, DenverCompletedMitochondrial Diseases | Human Immunodeficiency Virus (HIV)United States
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First People's Hospital of ChenzhouUnknownIntensive Care UnitChina
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University of California, San DiegoBioMarin PharmaceuticalWithdrawnBehavioral Manifestations of Lesch-Nyhan DiseaseUnited States
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Assistance Publique - Hôpitaux de ParisTerminatedCombined ImmunodeficienciesFrance
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Icahn School of Medicine at Mount SinaiColumbia University; New York Stem Cell Foundation Research InstituteCompletedClinically Isolated Syndrome | Relapsing-Remitting Multiple Sclerosis | Primary Progressive Multiple Sclerosis | Secondary Progressive Multiple SclerosisUnited States
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University Hospital Hradec KraloveUnknown
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University of AarhusUniversity of CopenhagenCompletedIleostomy - Stoma | Short Bowel Syndrome | Nutritional Deficiency | Sodium DepletionDenmark
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Medical University InnsbruckCompletedMyofascial Pain | Myofascial Trigger Point Pain | Pain, Back | Pain, Neck | Mitochondrial Pathology
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Horizon Pharma USA, Inc.Terminated
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Yungjin Pharm. Co., Ltd.CompletedMELAS Syndrome | Mitochondrial Respiratory Chain DeficienciesKorea, Republic of
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Children's Hospital of PhiladelphiaCompletedBone Marrow Failure Syndromes | Immunodeficiencies | Immune Dysregulation SyndromesUnited States
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Massachusetts General HospitalDana-Farber Cancer InstituteTerminatedLymphoma | Leukemia | Multiple Myeloma | Myelodysplastic SyndromeUnited States
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University of ChileFondo Nacional de Desarrollo Científico y Tecnológico, ChileTerminatedMetabolic SyndromeChile
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Masonic Cancer Center, University of MinnesotaTerminatedHematologic Diseases | Hemophagocytic Lymphohistiocytosis | Immunologic Diseases | Chediak-Higashi Syndrome | X-Linked Lymphoproliferative Disorders | Griscelli Syndrome | Langerhans-Cell HistiocytosisUnited States
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Woodinville Psychiatric AssociatesCompletedDiabetes Mellitus, Type 2 | Mitochondrial Diseases | Movement Disorders | FibromyalgiaUnited States