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Search clinical trials for: Infantile Spinal Muscular Atrophy
Total 30373 results
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Assistance Publique - Hôpitaux de ParisNot yet recruiting
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Hoffmann-La RocheRecruitingSpinal Muscular Atrophy (SMA)Belgium, United States, Croatia, Japan, Netherlands, Spain, Canada, Poland, United Kingdom, Portugal, Italy, Australia
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Sanford HealthNational Ataxia Foundation; Beyond Batten Disease Foundation; Pitt Hopkins Research... and other collaboratorsRecruitingMitochondrial Diseases | Retinitis Pigmentosa | Myasthenia Gravis | Eosinophilic Gastroenteritis | Multiple System Atrophy | Leiomyosarcoma | Leukodystrophy | Anal Fistula | Spinocerebellar Ataxia Type 3 | Friedreich Ataxia | Kennedy Disease | Lyme Disease | Hemophagocytic Lymphohistiocytosis | Spinocerebellar Ataxia... and other conditionsUnited States, Australia
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Hoffmann-La RocheCompletedMuscular Atrophy, SpinalBelgium, United States, China, Spain, Japan, Canada, France, Poland, Brazil, Croatia, Italy, Russian Federation, Turkey, Germany, Serbia, United Kingdom
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Hoffmann-La RocheActive, not recruitingSpinal Muscular AtrophyBelgium, United States, United Kingdom, France, Poland, Italy, Switzerland, Netherlands, Germany
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Hoffmann-La RocheCompletedMuscular Atrophy, SpinalBelgium, United States, China, Spain, Japan, France, Brazil, Croatia, Italy, Russian Federation, Saudi Arabia, Serbia, Switzerland, Turkey, Ukraine, Poland
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Assistance Publique - Hôpitaux de ParisCompleted
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Institut de Myologie, FranceCompletedSpinal Muscular AtrophyFrance
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Assistance Publique - Hôpitaux de ParisCompletedInfantile Spinal Muscular Atrophy of Type 2 or 3France
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BiogenNo longer availableInfantile-onset Spinal Muscular AtrophyNew Zealand, Colombia, Turkey
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BiogenCompletedSpinal Muscular AtrophyUnited States, Germany, Spain, Canada, France, Hong Kong, Italy, Japan, Korea, Republic of, Sweden
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Hoffmann-La RocheCompletedMuscular Atrophy, SpinalBelgium, United Kingdom, Germany, France, Italy, Netherlands, Poland
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Institut de Myologie, FranceInstitut RocheCompletedType 2 Spinal Muscular Atrophy | Type 3 Spinal Muscular AtrophyBelgium, France, Germany
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Hoffmann-La RocheTerminatedMuscular Atrophy, SpinalFrance, Turkey, Canada, United States, Italy, Netherlands, Sweden, Switzerland, United Kingdom
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Tehran University of Medical SciencesUnknownInfantile Spinal Muscular Atrophy, Type I [Werdnig- Hoffman]Iran, Islamic Republic of
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GeneCradle IncRecruitingSpinal Muscular Atrophy Type 3China
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University of OxfordOxford Brookes University; Oxford University Hospitals NHS Trust; Scholar Rock... and other collaboratorsNot yet recruiting
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Nido Biosciences, Inc.RecruitingSpinal and Bulbar Muscular Atrophy | Kennedy's DiseaseKorea, Republic of, Denmark, Italy, United Kingdom
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McGill University Health Centre/Research Institute...Not yet recruiting
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Rigshospitalet, DenmarkRecruitingSpinal Muscular AtrophyDenmark
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Wiktor Dega University Orthopedic and Rehabilitation...Recruiting
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University of Dublin, Trinity CollegeMotor Neurone Disease Association, UK; Irish Research Council, IE; Thierry Latran... and other collaboratorsRecruitingMultiple Sclerosis | Primary Lateral Sclerosis | Postpoliomyelitis Syndrome | Motor Neuron Disease, Amyotrophic Lateral Sclerosis | Motor Neuron Disease Progressive Spinal Muscle AtrophyIreland
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Hospices Civils de LyonNot yet recruitingSpinal Muscular AtrophyFrance
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Milton S. Hershey Medical CenterBioSensicsNot yet recruitingAmyotrophic Lateral Sclerosis | Primary Lateral Sclerosis | Progressive Muscular Atrophy
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IRCCS Burlo GarofoloRecruiting
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Marco CapogrossoRoche-GenentechNot yet recruitingSpinal Muscular Atrophy | Spinal Muscular Atrophy Type 3 | SMA | Spinal Muscular Atrophy Type II | Spinal Muscular Atrophy 4United States
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Lantu BiopharmaNot yet recruitingSpinal Muscular Atrophy
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Université du Québec à ChicoutimiMcGill University; Université de Sherbrooke; University of Alberta; University... and other collaboratorsRecruitingAutosomal Recessive Spastic Ataxia of Charlevoix-Saguenay | Spastic Paraplegia 7Canada
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Bar-Chama, Natan, M.D.RecruitingFertility IssuesUnited States
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Kun SunRecruitingSpinal Muscular Atrophy 1China
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MarsiBionicsHospital General Universitario Gregorio Marañon; Hospital Infantil Universitario... and other collaboratorsRecruitingCerebral Palsy | Acquired Brain Injury | Spinal Muscular AtrophySpain
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Gianni SoraruMario Negri Institute for Pharmacological ResearchRecruitingSpinal and Bulbar Muscular AtrophyItaly
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Assistance Publique - Hôpitaux de ParisNot yet recruitingHemophilia A | Hemophilia B | Cystic Fibrosis | Sickle Cell Disease | Muscular Dystrophy, Duchenne | Fragile X Syndrome | Huntington Disease | Myotonic Dystrophy | Autosomal Recessive Polycystic Kidney Disease | Neurofibromatosis-Noonan Syndrome | Muscular Dystrophy, Becker | Invasive PreNatal Diagnosis in a... and other conditionsFrance
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Novartis PharmaceuticalsRecruitingSpinal Muscular AtrophiesBrazil
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Robert Jones and Agnes Hunt Orthopaedic and District...University Hospital Birmingham NHS Foundation TrustRecruitingSpinal Muscular AtrophyUnited Kingdom
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Massachusetts General HospitalNorthwestern University; University of Florida; University of Minnesota; Henry... and other collaboratorsRecruitingALS | Kennedy Disease | MND (Motor Neurone DIsease) | PLS | PMA - Progressive Muscular Atrophy | PBP - Progressive Bulbar PalsyUnited States, Italy
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All India Institute of Medical Sciences, New DelhiRecruiting
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National Taiwan University HospitalNot yet recruiting
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GeneCradle IncRecruiting
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University of Sao Paulo General HospitalAgência Brasileira de Desenvolvimento Industrial (Brazilian Agency For Industrial...Not yet recruitingBrain Injuries | Spinal Cord Injuries | Muscle AtrophyBrazil
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Medipol UniversityRecruitingScoliosis | Exercise | Pulmonary Rehabilitation | Spinal Muscular Atrophy Type I | Chest Deformities | Spinal OrthosisTurkey
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Fondazione Policlinico Universitario Agostino Gemelli...IRCCS Eugenio Medea; Azienda Ospedaliera Universitaria Policlinico "G. Martino... and other collaboratorsNot yet recruitingSpinal Muscular Atrophy
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Alcyone Therapeutics, IncBiogenRecruitingScoliosis | Spinal Muscular Atrophy | Spine DeformityUnited States
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Hoffmann-La RocheRecruiting
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Hoffmann-La RocheRecruiting
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Institut de Myologie, FranceRoche Pharma AGNot yet recruitingMuscular Atrophy, Spinal, Type II | Muscular Atrophy, Spinal, Type IIIFrance
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GeneCradle IncRecruitingSpinal Muscular AtrophyChina
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Hoffmann-La RocheRecruitingMuscular Atrophy, SpinalGermany, United States, Belgium
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NMD Pharma A/SRecruitingSpinal Muscular AtrophyUnited States, Spain, Belgium, Denmark, Germany, Netherlands, Italy, Canada
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BiogenRecruitingMuscular Atrophy, SpinalUnited States