Tato stránka byla automaticky přeložena a přesnost překladu není zaručena. Podívejte se prosím na anglická verze pro zdrojový text.

BCMA/GPRC5D Dual-Target CAR-T Cell Immunotherapy for Relapsed/Refractory Multiple Myeloma

4. listopadu 2026 aktualizováno: Liping Dou

A Clinical Study on the Safety of BCMA/GPRC5D Dual-Target Autologous CAR-T Cell Immunotherapy for Relapsed/Refractory Multiple Myeloma

This is a single-center, open-label, single-arm, investigator-initiated clinical study to evaluate the safety, tolerability, and preliminary efficacy of SL4903, a BCMA/GPRC5D dual-target autologous CAR-T cell injection, in patients with relapsed or refractory multiple myeloma (R/R MM) whose clonal plasma cells are positive for BCMA and/or GPRC5D. After leukapheresis, participants receive lymphodepleting conditioning (fludarabine 30 mg/m^2/day plus cyclophosphamide 500 mg/m^2/day on Days -5 to -3), followed by a single intravenous infusion of SL4903 at a dose of 1×10^6 CAR-positive cells/kg; bridging therapy (e.g., immunomodulatory drugs or anti-CD38 monoclonal antibody) is permitted between leukapheresis and conditioning at the investigator's discretion. Treatment-emergent adverse events, including cytokine release syndrome (CRS), neurotoxicity, hematologic toxicity, and organ toxicity, will be assessed within 3 months after infusion. Preliminary antitumor activity will be evaluated according to the 2016 International Myeloma Working Group (IMWG) criteria, including objective response rate (ORR), complete response rate (CRR), time to response (TTR), duration of response (DOR), progression-free survival (PFS), overall survival (OS), and measurable residual disease (MRD) negativity rate. Pharmacokinetics (Cmax, Tmax, persistence, and AUCd0-28 of CAR-T cells in peripheral blood by flow cytometry and qPCR) and pharmacodynamics (peripheral blood plasma cell proportion and cytokine levels) will also be evaluated. Participants will be followed for safety and efficacy for up to 2 years after cell therapy.

Přehled studie

Postavení

Zatím nenabíráme

Podmínky

Intervence / Léčba

Detailní popis

This is a single-center, single-arm, open-label, investigator-initiated clinical study of SL4903 autologous T-cell injection in adults with R/R MM. SL4903 is an autologous CAR-T cell product in which the CAR comprises, in order, a GPRC5D-targeting nanobody (VHH1), a BCMA-targeting nanobody (VHH2), a CD8 hinge region, a CD8 transmembrane domain, a 4-1BB costimulatory domain, and a CD3-zeta signaling domain; autologous peripheral blood mononuclear cells are collected by leukapheresis (approximately 80-120 mL), transduced ex vivo with a lentiviral vector, and expanded over a manufacturing period of approximately 7-8 days. Participants receive lymphodepleting conditioning with fludarabine (30 mg/m^2/day) and cyclophosphamide (500 mg/m^2/day) on Days -5 to -3, which may be adjusted at the investigator's discretion, followed by a single intravenous infusion of SL4903 at 1×10^6 CAR-positive cells/kg on Day 0. Planned enrollment is 20 participants; enrollment accounts for potential CAR-T manufacturing failure or rapid disease progression that may preclude infusion. Safety assessments include adverse events and serious adverse events graded per NCI CTCAE v5.0, with CRS and immune effector cell-associated neurotoxicity syndrome (ICANS) graded per the ASTCT consensus criteria; infection, hematologic toxicity, organ toxicity, hemophagocytic lymphohistiocytosis/macrophage activation syndrome (HLH/MAS), and tumor lysis syndrome (TLS) are also monitored. Disease response is assessed per the 2016 IMWG criteria at baseline, Day 28, and Months 2, 3, 6, 12, 18, and 24, including serum/urine M-protein studies, serum free light chains, bone marrow examination with flow cytometry/MRD, and imaging (preferably PET-CT) for extramedullary disease. Pharmacokinetic assessments include CAR-T cell expansion in peripheral blood by flow cytometry and qPCR (Cmax, Tmax, in vivo persistence, and AUCd0-28); pharmacodynamic assessments include peripheral blood plasma cell proportion/count and cytokine quantification (at least IL-6, IL-2, IL-10, IFN-gamma, and TNF-alpha).

Typ studie

Intervenční

Zápis (Odhadovaný)

20

Fáze

  • Fáze 1

Kontakty a umístění

Tato část poskytuje kontaktní údaje pro ty, kteří studii provádějí, a informace o tom, kde se tato studie provádí.

Studijní kontakt

Studijní místa

    • Beijing Municipality
      • Beijing, Beijing Municipality, Čína, 100853
        • Chinese PLA General Hospital
        • Kontakt:

Kritéria účasti

Výzkumníci hledají lidi, kteří odpovídají určitému popisu, kterému se říká kritéria způsobilosti. Některé příklady těchto kritérií jsou celkový zdravotní stav osoby nebo předchozí léčba.

Kritéria způsobilosti

Věk způsobilý ke studiu

18 let až 75 let (Dospělý, Starší dospělý)

Přijímá zdravé dobrovolníky

Ne

Pohlaví způsobilá ke studiu

Všechno

Popis

Inclusion Criteria:

  • Voluntarily agrees to participate in the study (signed informed consent form by the participant or a legally authorized representative), and is willing and able to comply with scheduled visits, study treatment, laboratory tests, and other study procedures.
  • Clinically diagnosed relapsed/refractory multiple myeloma, meeting both of the following:

Clonal plasma cells positive for BCMA and/or GPRC5D by flow cytometry or immunohistochemistry.

Prior treatment with at least 3 drug classes (proteasome inhibitors [PIs], immunomodulatory drugs [IMiDs], and an anti-CD38 monoclonal antibody), with best response less than partial response (PR) or disease progression after achieving PR or better.

  • Male or female participants aged 18 to 75 years, inclusive.
  • Eastern Cooperative Oncology Group (ECOG) performance status of 0-2.
  • Estimated life expectancy of more than 3 months from the date of signing the informed consent form.
  • Adequate renal, hepatic, cardiac, and pulmonary function, defined as follows:

Creatinine clearance (estimated by the Cockcroft-Gault formula) ≥60 mL/min or serum creatinine ≤1.5 × the upper limit of normal (ULN); Serum alanine aminotransferase (ALT) and aspartate aminotransferase (AST)≤2.5×upper limit of normal (ULN), total bilirubin≤1.5×ULN; Cardiac ejection fraction≥50%, no pericardial effusion on echocardiography, and no significant abnormalities on electrocardiogram (ECG); No clinically significant pleural effusion, and oxygen saturation >92% on room air at baseline.

  • Participants of reproductive potential must agree to use highly effective contraception before enrollment and for at least 12 months after CAR-T cell infusion. A negative serum pregnancy test is required for women of childbearing potential at screening. Participants must immediately notify the investigator if pregnancy occurs or is suspected.

Exclusion Criteria:

  • The patient has severe cardiac dysfunction, or left ventricular ejection fraction (LVEF) <50%, or a history within the 12 months prior to enrollment of myocardial infarction, coronary angioplasty or coronary stent implantation, unstable angina, clinically significant arrhythmia, or other severe cardiovascular diseases.
  • A history of severe pulmonary disease with impaired lung function.
  • Concurrent progressive malignancy other than multiple myeloma.
  • Severe active infection that cannot be effectively controlled.
  • Severe autoimmune disease or congenital immunodeficiency.
  • Active hepatitis, defined as hepatitis B virus DNA (HBV-DNA) or hepatitis C virus RNA (HCV-RNA) levels above the lower limit of detection, or human immunodeficiency virus (HIV) infection, known acquired immunodeficiency syndrome (AIDS), or syphilis infection.
  • A history of severe allergic reactions to biological products, including antibiotics.
  • The patient has severe autoimmune disease, congenital immunodeficiency or active autoimmune disease requiring ongoing systemic immunosuppressive treatment, or is currently within the washout period after having received medications that may affect CAR-T cell immunotherapy, or is anticipated to require medications during the study period that may affect CAR-T cell immunotherapy treatment.
  • The investigator judges that the patient is unlikely to complete all visits and procedures required by the study protocol (including medium- and long-term follow-up visits), such as insufficient willingness of the patient and their family members to participate in the study, refusal to participate, inability of the patient to fully cooperate with the study arrangements, or inadequate compliance on the part of the patient and their family members.
  • Any other severe physical or psychiatric disorder or clinically significant laboratory abnormality that may increase the risk associated with study participation, interfere with the interpretation of study results, or, in the investigator's judgment, make the participant unsuitable for participation in the study.
  • Female participants of childbearing potential who are pregnant or breastfeeding.

Studijní plán

Tato část poskytuje podrobnosti o studijním plánu, včetně toho, jak je studie navržena a co studie měří.

Jak je studie koncipována?

Detaily designu

  • Primární účel: Léčba
  • Přidělení: N/A
  • Intervenční model: Přiřazení jedné skupiny
  • Maskování: Žádné (otevřený štítek)

Zbraně a zásahy

Skupina účastníků / Arm
Intervence / Léčba
Experimentální: The experimental group

SL4903 Treatment Group - after leukapheresis and lymphodepleting conditioning (fludarabine 30 mg/m^2/day plus cyclophosphamide 500 mg/m^2/day on Days -5 to -3), participants receive a single intravenous infusion of SL4903 autologous T-cell injection at a dose of 1 x 10^6 CAR-positive cells/kg. Bridging therapy (e.g., immunomodulatory drugs or anti-CD38 monoclonal antibody) may be given between leukapheresis and conditioning at the investigator's discretion.

SL4903 is an investigational autologous dual-target CAR T-cell therapy (lentiviral vector-based) directed against BCMA and GPRC5D, for patients with relapsed or refractory multiple myeloma whose clonal plasma cells are positive for BCMA and/or GPRC5D. The CAR comprises a GPRC5D-targeting nanobody (VHH1), a BCMA-targeting nanobody (VHH2), a CD8 hinge region, a CD8 transmembrane domain, a 4-1BB costimulatory domain, and a CD3-zeta signaling domain. After leukapheresis and lymphodepleting conditioning (fludarabine plus cyclophosphamide), participants receive a single intravenous infusion of SL4903 at 1×10^6 CAR-positive cells/kg.

Ostatní jména:
  • SL4903; BCMA-GPRC5D CAR-T injection

Co je měření studie?

Primární výstupní opatření

Měření výsledku
Popis opatření
Časové okno
Adverse Events
Časové okno: From SL4903 infusion through 3 months after infusion; long-term safety follow-up continues through 12 months

AEs are graded per NCI CTCAE v5.0

From SL4903 infusion through 3 months after infusion; long-term safety follow-up continues through 12 months
Cytokine Release Syndrome
Časové okno: From SL4903 infusion through 3 months after infusion; long-term safety follow-up continues through 12 months

Cytokine release syndrome (CRS) is graded according to the ASTCT consensus criteria.

From SL4903 infusion through 3 months after infusion; long-term safety follow-up continues through 12 months
Immune Effector Cell-associated Neurotoxicity Syndrome
Časové okno: From SL4903 infusion through 3 months after infusion; long-term safety follow-up continues through 12 months

Immune effector cell-associated neurotoxicity syndrome (ICANS) is graded according to the ASTCT consensus criteria.

From SL4903 infusion through 3 months after infusion; long-term safety follow-up continues through 12 months

Sekundární výstupní opatření

Měření výsledku
Popis opatření
Časové okno
Objective Response Rate
Časové okno: At Day 28 and Months 2, 3, 6, 12, 18, and 24 after SL4903 infusion

The proportion of participants achieving a partial response or better (ORR), assessed by the investigator according to the 2016 International Myeloma Working Group (IMWG) criteria.

At Day 28 and Months 2, 3, 6, 12, 18, and 24 after SL4903 infusion
Complete Response Rate
Časové okno: At Day 28 and Months 2, 3, 6, 12, 18, and 24 after SL4903 infusion

The proportion of participants achieving a complete response (CR) or stringent complete response (sCR), per the 2016 IMWG criteria.

At Day 28 and Months 2, 3, 6, 12, 18, and 24 after SL4903 infusion
Time to Response and Duration of Response
Časové okno: From SL4903 infusion through 24 months after treatment

Time to response (TTR), defined as the time from SL4903 infusion to first documented response, and duration of response (DOR), defined as the time from first documented response to disease progression or death, per the 2016 IMWG criteria.

From SL4903 infusion through 24 months after treatment
Progression-Free Survival
Časové okno: From SL4903 infusion through 24 months after treatment

Progression-free survival (PFS), defined as the time from SL4903 infusion to disease progression or death from any cause, whichever occurs first, per the 2016 IMWG criteria; PFS rates at 6, 9, 12, 18, and 24 months will also be estimated.

From SL4903 infusion through 24 months after treatment
Overall Survival
Časové okno: From SL4903 infusion through 24 months after treatment

Overall survival (OS), defined as the time from SL4903 infusion to death from any cause; OS rates at 6, 9, 12, 18, and 24 months will also be estimated. Participants who are alive at the last follow-up will be censored on the date of their last known survival status.

From SL4903 infusion through 24 months after treatment
Measurable Residual Disease (MRD) Negativity Rate
Časové okno: At Day 28 and Months 2, 3, 6, 12, 18, and 24 after SL4903 infusion

The proportion of participants achieving MRD negativity in bone marrow, assessed by flow cytometry, among responding participants.

At Day 28 and Months 2, 3, 6, 12, 18, and 24 after SL4903 infusion
Peak Expansion of SL4903 CAR-T Cells in Peripheral Blood
Časové okno: Through Day 28 for AUCd0-28, Cmax, and Tmax; CAR-T persistence through 24 months after infusion

Peak expansion of SL4903 CAR-T cells in peripheral blood (Cmax, measured by both flow cytometry and qPCR),

Through Day 28 for AUCd0-28, Cmax, and Tmax; CAR-T persistence through 24 months after infusion
Time to Peak Expansion
Časové okno: Through Day 28 for AUCd0-28, Cmax, and Tmax; CAR-T persistence through 24 months after infusion

Time to Peak Expansion

Through Day 28 for AUCd0-28, Cmax, and Tmax; CAR-T persistence through 24 months after infusion
Area Under The Gene-copy Expansion Curve from Day 0 to Day 28
Časové okno: Through Day 28 for AUCd0-28, Cmax, and Tmax; CAR-T persistence through 24 months after infusion

in vivo persistence of CAR-T cells, and the area under the gene-copy expansion curve from Day 0 to Day 28 (AUCd0-28).

Through Day 28 for AUCd0-28, Cmax, and Tmax; CAR-T persistence through 24 months after infusion
Pharmacodynamic Markers (Exploratory)
Časové okno: Through 24 months after SL4903 infusion

Proportion and absolute count of plasma cells in peripheral blood by flow cytometry, and peripheral blood cytokine levels (at least IL-6, IL-2, IL-10, IFN-gamma, and TNF-alpha) at prespecified time points.

Through 24 months after SL4903 infusion

Spolupracovníci a vyšetřovatelé

Zde najdete lidi a organizace zapojené do této studie.

Sponzor

Termíny studijních záznamů

Tato data sledují průběh záznamů studie a předkládání souhrnných výsledků na ClinicalTrials.gov. Záznamy ze studií a hlášené výsledky jsou před zveřejněním na veřejné webové stránce přezkoumány Národní lékařskou knihovnou (NLM), aby se ujistily, že splňují specifické standardy kontroly kvality.

Hlavní termíny studia

Začátek studia (Odhadovaný)

30. listopadu 2026

Primární dokončení (Odhadovaný)

30. listopadu 2028

Dokončení studie (Odhadovaný)

30. listopadu 2029

Termíny zápisu do studia

První předloženo

28. října 2026

První předloženo, které splnilo kritéria kontroly kvality

4. listopadu 2026

První zveřejněno (Aktuální)

10. listopadu 2026

Aktualizace studijních záznamů

Poslední zveřejněná aktualizace (Aktuální)

10. listopadu 2026

Odeslaná poslední aktualizace, která splnila kritéria kontroly kvality

4. listopadu 2026

Naposledy ověřeno

1. listopadu 2026

Více informací

Termíny související s touto studií

Další identifikační čísla studie

  • 2026-750

Plán pro data jednotlivých účastníků (IPD)

Plánujete sdílet data jednotlivých účastníků (IPD)?

NE

Informace o lécích a zařízeních, studijní dokumenty

Studuje lékový produkt regulovaný americkým FDA

Ne

Studuje produkt zařízení regulovaný americkým úřadem FDA

Ne

Tyto informace byly beze změn načteny přímo z webu clinicaltrials.gov. Máte-li jakékoli požadavky na změnu, odstranění nebo aktualizaci podrobností studie, kontaktujte prosím register@clinicaltrials.gov. Jakmile bude změna implementována na clinicaltrials.gov, bude automaticky aktualizována i na našem webu .