- ICH GCP
- US Clinical Trials Registry
- Klinisk forsøg NCT07602205
Efficacy and Safety of Daily Home-based Hyperthermic Baths for Reducing Epileptic Seizures in CDKL5 Deficiency Disorder: A PROBE Clinical Trial
15. maj 2026 opdateret af: Liankun_Ren, Xuanwu Hospital, Beijing
Efficacy and Safety of Daily Home-based Hyperthermic Baths for Reducing Epileptic Seizures in CDKL5 Deficiency Disorder: A Prospective, Randomized, Parallel-Controlled, Open-Label, Blinded Endpoint (PROBE) Clinical Trial
The primary objective of this research is to study the efficacy and safety of daily, home-based hyperthermic baths for reducing epileptic seizures in CDKL5 Deficiency Disorder.
Studieoversigt
Status
Ikke rekrutterer endnu
Betingelser
Intervention / Behandling
Detaljeret beskrivelse
This is a prospective, randomized, open-label, blinded-endpoint study designed to evaluate the efficacy and safety of daily home-based hyperthermic bathing in participants with CDKL5 deficiency disorder.
Eligible participants will be randomized in a 1:1 ratio to receive either hyperthermic baths in addition to usual antiseizure care or usual antiseizure care alone without hyperthermic baths.
Efficacy will be assessed primarily by changes in epileptic seizure burden, and safety will be evaluated throughout the study period.
Undersøgelsestype
Interventionel
Tilmelding (Anslået)
34
Fase
- Ikke anvendelig
Kontakter og lokationer
Dette afsnit indeholder kontaktoplysninger for dem, der udfører undersøgelsen, og oplysninger om, hvor denne undersøgelse udføres.
Studiekontakt
- Navn: Liankun Ren, MD, PhD
- Telefonnummer: +86 13681576621
- E-mail: renlk2022@outlook.com
Deltagelseskriterier
Forskere leder efter personer, der passer til en bestemt beskrivelse, kaldet berettigelseskriterier. Nogle eksempler på disse kriterier er en persons generelle helbredstilstand eller tidligere behandlinger.
Berettigelseskriterier
Aldre berettiget til at studere
- Barn
Tager imod sunde frivillige
Ingen
Beskrivelse
Inclusion Criteria:
- A diagnosis of CDKL5 deficiency disorder, including molecular confirmation of a pathogenic CDKL5 variant and exhibiting epileptic seizures.
- Male or female participants aged 6 months to 14 years, inclusive.
- Patients presenting with drug-resistant epilepsy that seizures were uncontrolled despite the appropriate trial of at least two antiseizure medications (ASMs).
- At least 8 motor seizures during each 4 weeks in the 8-week historical seizure records preceding screening.
- Treatment regimens of 0-4 ASMs were required to be stable for at least 4 weeks before screening and throughout the intervention. Ongoing ketogenic diets were allowed if remain unchanged during screening and treatment.
Subjects who have undergone surgical implantation of vagus nerve stimulation (VNS) will be eligible for inclusion in the study, provided they meet all of the following criteria:
- The VNS device has been in place for at least one year prior to the screening visit;
- The stimulation parameters remain unchanged throughout the duration of the trial.
- Parents or caregivers must be able and willing to maintain an accurate and comprehensive daily electronic seizure diary throughout the duration of the study.
- Participants' legal guardians willing to provide written informed consent.
Exclusion Criteria:
- Patients who had any history of previous brain disease (including trauma, encephalitis, etc.) that were likely to precipitate seizures; defined by MRI outcomes.
- Participants with skin ulceration or dermatologic conditions that make bathing unsuitable.
- Parents or guardians who, based on past experiences, determine that the child has an intolerance to thermal baths.
- A history of seizures induced by thermal baths, or an increase in seizure frequency after thermal baths.
- Patients who presented any clinical condition that in the opinion of the principal investigator made the patient not suitable to participate in the survey.
Studieplan
Dette afsnit indeholder detaljer om studieplanen, herunder hvordan undersøgelsen er designet, og hvad undersøgelsen måler.
Hvordan er undersøgelsen tilrettelagt?
Design detaljer
- Primært formål: Behandling
- Tildeling: Randomiseret
- Interventionel model: Parallel tildeling
- Maskning: Enkelt
Våben og indgreb
Deltagergruppe / Arm |
Intervention / Behandling |
|---|---|
|
Eksperimentel: Home-based hyperthermic baths group
Patients with CDKL5 deficiency disorder assigned to the daily home-based hyperthermic bathing group will undergo immersion in a 40-42°C water bath for 20 minutes per session under continuous parental supervision.
|
A 12-week daily home-based hyperthermic bathing intervention consisting of immersion in a 40-42°C water bath for 20 minutes per session under continuous parental supervision.
The intervention will be administered according to the study protocol.
|
|
Ingen indgriben: Control Group
Participants assigned to the control group will not receive hyperthermic baths during the study period and will continue their usual care, including their existing antiseizure treatment regimen.
Seizure frequency and safety outcomes will be assessed according to the study protocol.
|
Hvad måler undersøgelsen?
Primære resultatmål
Resultatmål |
Foranstaltningsbeskrivelse |
Tidsramme |
|---|---|---|
|
Seizure Responder Rate
Tidsramme: Baseline to week 12 at home-based hyperthermic baths phase
|
The proportion of participants achieving at least a 50% reduction in seizure frequency from baseline during the 12-week home-based hyperthermic baths period.
|
Baseline to week 12 at home-based hyperthermic baths phase
|
Sekundære resultatmål
Resultatmål |
Foranstaltningsbeskrivelse |
Tidsramme |
|---|---|---|
|
Change in Seizure Frequency
Tidsramme: Baseline to week 12 at home-based hyperthermic baths phase
|
Change in the frequency of epileptic seizures from baseline to the 12-week home-based hyperthermic baths period.
|
Baseline to week 12 at home-based hyperthermic baths phase
|
|
Seizure-free Days
Tidsramme: Baseline to week 12 at home-based hyperthermic baths phase
|
Number of days without epileptic seizures during the 12-week treatment period.
|
Baseline to week 12 at home-based hyperthermic baths phase
|
Samarbejdspartnere og efterforskere
Det er her, du vil finde personer og organisationer, der er involveret i denne undersøgelse.
Sponsor
Efterforskere
- Ledende efterforsker: Liankun Ren, MD, PhD, Xuanwu Hospital, Beijing
Datoer for undersøgelser
Disse datoer sporer fremskridtene for indsendelser af undersøgelsesrekord og resumeresultater til ClinicalTrials.gov. Studieregistreringer og rapporterede resultater gennemgås af National Library of Medicine (NLM) for at sikre, at de opfylder specifikke kvalitetskontrolstandarder, før de offentliggøres på den offentlige hjemmeside.
Studer store datoer
Studiestart (Anslået)
1. august 2026
Primær færdiggørelse (Anslået)
31. december 2027
Studieafslutning (Anslået)
31. december 2027
Datoer for studieregistrering
Først indsendt
15. maj 2026
Først indsendt, der opfyldte QC-kriterier
15. maj 2026
Først opslået (Faktiske)
22. maj 2026
Opdateringer af undersøgelsesjournaler
Sidste opdatering sendt (Faktiske)
22. maj 2026
Sidste opdatering indsendt, der opfyldte kvalitetskontrolkriterier
15. maj 2026
Sidst verificeret
1. maj 2026
Mere information
Begreber relateret til denne undersøgelse
Yderligere relevante MeSH-vilkår
Andre undersøgelses-id-numre
- 2026-161-001
Plan for individuelle deltagerdata (IPD)
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