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Søg i kliniske forsøg efter: AAVrh.10CUhCLN2 vektor 9,0x10^11 genom kopier
I alt 3 resultater
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Weill Medical College of Cornell UniversityNational Institutes of Health (NIH)AfsluttetBattens sygdom | Sen-infantil neuronal ceroid lipofuscinoseForenede Stater
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Weill Medical College of Cornell UniversityNational Heart, Lung, and Blood Institute (NHLBI)RekrutteringMyokardiefibrose | Kardiomyopatier | Friedreich Ataxia | HjertehypertrofiForenede Stater
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Radboud University Medical CenterUMC Utrecht; Prothya BiosolutionsAfsluttetSepsis | Betændelse | Endotoksæmi | Medfødt immunresponsHolland