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Clinical Trials on Aromatic Amino Acid Decarboxylase Deficiency
Total 554 results
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The People's Hospital of GaozhouRecruitingExploring the Effectiveness and Safety of Amino Acid Peritoneal Dialysis Solution in Improving Nutritional Status of Maintenance Peritoneal Dialysis PatientsChina
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Medical University of GdanskCompletedSepsis | Amino Acid Catabolism DisorderPoland
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University of Novi Sad, Faculty of Sport and Physical...Completed
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Queen Sirikit National Institute of Child HealthChulalongkorn UniversityCompletedObesity | HyperhomocysteinemiaThailand
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Maria Luz Couce PicoFundación Ramón DomínguezWithdrawnLong-chain Fatty Acid Transport DeficiencySpain
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Smt. Kashibai Navale Medical College and General...CompletedType 2 Diabetes | Vitamin B12 Deficiency | HyperhomocysteinemiaIndia
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SEAMEO Regional Centre for Food and NutritionLondon School of Hygiene and Tropical Medicine; University College, London; University... and other collaboratorsRecruitingProtozoan Infections | Birth Weight | Weight Gain | Vitamin A Deficiency | Folate Deficiency | Zinc Deficiency | Child Development | Salmonella Infections | Anemia, Iron Deficiency | Fatty Acid Deficiency | Birth Length | B12 Deficiency Vitamin | Mineral Deficiency | E. Coli Infection | Shigella Infection | Amino Acid Deficiency and other conditionsIndonesia
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London School of Hygiene and Tropical MedicineCompletedHyperhomocysteinemia | Micronutrient DeficienciesGambia
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National Institute of Cardiology, Laranjeiras,...CompletedEndothelial Dysfunction | HyperhomocysteinemiaBrazil
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IRCCS Azienda Ospedaliero-Universitaria di BolognaUniversity of BolognaCompletedInflammation | Mortality | HyperhomocysteinemiaItaly
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National Institute of Neurological Disorders and...CompletedSuccinic Semialdehyde Dehydrogenase Deficiency | SSADH DeficiencyUnited States
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ModernaTX, Inc.RecruitingMethylmalonic AcidemiaUnited States, Spain, Canada, Netherlands, France, Australia, United Kingdom
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LogicBio Therapeutics, IncAlexion Pharmaceuticals, Inc.TerminatedMethylmalonic AcidemiaUnited States
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University of TorontoRecruitingPhysical Inactivity | Resistance Exercise | Amino Acids | Dietary ProteinCanada
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University of LimerickMarigot Ltd.; Enterprise IrelandCompletedBioavailability of Amino Acids Following Oral Ingestion of Plant-Based Proteins in Young, Healthy MenIreland
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Arcturus Therapeutics, Inc.RecruitingOTC Deficiency | Ornithine Transcarbamylase Deficiency | OTCDSpain, Belgium, United Kingdom, Sweden
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ModernaTX, Inc.RecruitingPropionic AcidemiaUnited States, Canada, United Kingdom
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Azienda di Servizi alla Persona di PaviaCompletedObesity | Body Weight Changes | Skin Manifestations | Postmenopausal Disorder | Amino AcidItaly
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CENTOGENE GmbH RostockWithdrawnMetabolic Disorders | Tyrosinosis | Hepatorenal Tyrosinemia | Fumarylacetoacetase Deficiency | Fah DeficiencyGermany, Sri Lanka, India
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Oklahoma State University Center for Health SciencesActive, not recruiting
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Indonesia UniversityUnited States Agency for International Development (USAID); Ministry of Research...Completed
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Harvard UniversityCompleted
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HemoShear TherapeuticsPrometrika, LLC; AllStripes Research Inc.; Genome MedicalTerminatedPropionic Acidemia | Methylmalonic AcidemiaUnited States, Canada, United Kingdom
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S.LAB (SOLOWAYS)Center of New Medical Technologies; Triangel ScientificCompletedHyperlipoproteinemias | HyperhomocysteinemiaRussian Federation
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Aeglea BiotherapeuticsTerminatedArginase I Deficiency | HyperargininemiaCanada
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Aeglea BiotherapeuticsCompletedArginase I Deficiency | HyperargininemiaUnited States, Italy, Canada, France, United Kingdom, Austria, Germany
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National Institute of Neurological Disorders and...CompletedSuccinic Semialdehyde | Dehydrogenase Deficiency | DiseasesUnited States
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Mendel TuchmanChildren's Hospital of Philadelphia; University of California, Los Angeles; Icahn... and other collaboratorsCompletedMethylmalonic Acidemia | Carbamoyl-Phosphate Synthase I Deficiency Disease | Propionic Acidemia, Type I and/or Type II | Ornithine Carbamoyltransferase DeficiencyUnited States
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Hadassah Medical OrganizationUnknown
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National Institute of Health and NutritionCompletedFolate Deficiency
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HemoShear TherapeuticsTerminatedPropionic Acidemia | Methylmalonic AcidemiaUnited States, Saudi Arabia, Australia
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King Abdullah International Medical Research CenterCompletedPropionic Acidemia | Methylmalonic AcidemiaSaudi Arabia
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Mendel TuchmanUniversity of Colorado, Denver; Children's Hospital of Philadelphia; University... and other collaboratorsTerminatedPropionic Acidemia | Methylmalonic AcidemiaUnited States
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Eunice Kennedy Shriver National Institute of Child...Children's National Research InstituteTerminatedPhase I Pilot Study of Liver-Directed Gene Therapy for Partial Ornithine Transcarbamylase DeficiencyOrnithine Transcarbamylase Deficiency Disease
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Mansoura UniversitySwedish University of Agricultural Sciences; The Swedish Research Council for...Completed
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Ultragenyx Pharmaceutical IncRecruitingOTC DeficiencyUnited States, Portugal, Australia, Italy, Spain, United Kingdom, Japan, Canada, Germany, France, Argentina, Netherlands, Brazil
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University College, LondonRecruitingOrnithine Transcarbamylase DeficiencyUnited Kingdom
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Arcturus Therapeutics, Inc.Active, not recruitingOrnithine Transcarbamylase DeficiencyUnited States
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Recordati Rare DiseasesRecruitingPropionic Acidemia | Methylmalonic AcidemiaFrance, Spain, Italy, United Kingdom, Norway, Germany, Sweden
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University of PennsylvaniaTerminatedOrnithine Transcarbamylase Deficiency Disease
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Ultragenyx Pharmaceutical IncActive, not recruitingOrnithine Transcarbamylase (OTC) DeficiencyCanada, United States, France, Spain, United Kingdom
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AlexionRecruitingWolman Disease | Cholesterol Ester Storage Disease | Lysosomal Acid Lipase Deficiency | Acid Cholesteryl Ester Hydrolase Deficiency, Type 2 | Acid Lipase Deficiency | LIPA Deficiency | LAL-DeficiencyFrance, Belgium, United States, Spain, Germany, Greece, Israel, Italy, Slovenia, United Kingdom, Brazil, Canada, Denmark, Australia, Croatia, Czechia, Ireland, Mexico, Netherlands, Poland, Portugal, Saudi Arabia
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Ultragenyx Pharmaceutical IncCompletedOrnithine Transcarbamylase DeficiencyUnited States
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Second Affiliated Hospital of Nanchang UniversityPeking University First HospitalUnknownHypertension | HyperhomocysteinemiaChina
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Shenzhen Ausa Pharmed Co.,LtdPeking University First Hospital; China Medical University, China; Fudan University and other collaboratorsUnknownEssential HypertensionChina
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Radboud University Medical CenterCompletedMild HyperhomocysteinemiaNetherlands
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BioMarin PharmaceuticalQuintiles, Inc.CompletedTetrahydrobiopterin DeficiencyChina
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Meir Medical CenterCompletedFolic Acid Deficiency | Vitamin B12 DeficiencyIsrael
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Arcturus Therapeutics, Inc.CompletedOrnithine Transcarbamylase DeficiencyNew Zealand
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Translate Bio, Inc.WithdrawnOrnithine Transcarbamylase Deficiency