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Clinical Trials on Hereditary Pulmonary Alveolar Proteinosis
Total 59 results
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Children's Hospital Medical Center, CincinnatiNational Heart, Lung, and Blood Institute (NHLBI); University of South FloridaRecruiting
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Children's Hospital Medical Center, CincinnatiGenzyme, a Sanofi Company; Virginia Commonwealth UniversityCompletedHereditary Pulmonary Alveolar ProteinosisUnited States
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Jiuzhitang Maker (Beijing) Cell Technology Co.,Ltd...The First Affiliated Hospital of Guangzhou Medical UniversityNot yet recruitingAutoimmune Pulmonary Alveolar Proteinosis
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Assistance Publique - Hôpitaux de ParisRecruitingGenetic Mutation | Pulmonary Alveolar Proteinosis (PAP) | MARSFrance
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Guangzhou Institute of Respiratory DiseaseActive, not recruitingPulmonary Alveolar Proteinosis(PAP)China
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Niigata University Medical & Dental HospitalCompletedPulmonary Alveolar Proteinosis, AutoimmuneJapan
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Children's Hospital Medical Center, CincinnatiNational Heart, Lung, and Blood Institute (NHLBI); Rare Diseases Clinical Research...CompletedAutoimmune Pulmonary Alveolar ProteinosisUnited States
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Children's Hospital Medical Center, CincinnatiCompletedAutoimmune Pulmonary Alveolar ProteinosisUnited States
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IRCCS Policlinico S. MatteoAgenzia Italiana del FarmacoCompleted
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Savara Inc.CompletedAutoimmune Pulmonary Alveolar ProteinosisNetherlands, Denmark, France, Germany, Greece, Israel, Italy, Russian Federation, Turkey, United Kingdom
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Niigata University Medical & Dental HospitalCompletedPulmonary Alveolar Proteinosis, AutoimmuneJapan
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Dai HuapingUnknownTreatment | Pulmonary Alveolar ProteinosisChina
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Savara Inc.Active, not recruitingAutoimmune Pulmonary Alveolar ProteinosisUnited States, Korea, Republic of, United Kingdom, Netherlands, Australia, Romania, Japan, Portugal, Canada, Greece, Spain, Italy, Poland, Belgium, France, Germany, Ireland, Turkey
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Savara Inc.CompletedAutoimmune Pulmonary Alveolar ProteinosisUnited States, United Kingdom, Denmark, Switzerland, Australia, Portugal, Italy, Greece, Netherlands, Japan, Germany, France, Israel, Korea, Republic of, Russian Federation, Slovakia, Spain, Turkey
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Children's Hospital Medical Center, CincinnatiRare Diseases Clinical Research Network; National Center for Advancing Translational...CompletedAutoimmune Pulmonary Alveolar ProteinosisUnited States
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Peking Union Medical College HospitalThe Affiliated Nanjing Drum Tower Hospital of Nanjing University Medical...UnknownAutoimmune Pulmonary Alveolar ProteinosisChina
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Shanghai Pulmonary Hospital, Shanghai, ChinaCompletedPulmonary Alveolar ProteinosisChina
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Children's Hospital Medical Center, CincinnatiCompletedPulmonary Alveolar ProteinosisUnited States
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Children's Hospital Medical Center, CincinnatiNational Heart, Lung, and Blood Institute (NHLBI); Rare Diseases Clinical Research... and other collaboratorsRecruiting
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Shanghai Pulmonary Hospital, Shanghai, ChinaUnknownPulmonary Alveolar ProteinosisChina
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The Cleveland ClinicTerminated
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East Carolina UniversityGenentech, Inc.CompletedPulmonary Alveolar Proteinosis | Primary DiseaseUnited States
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Children's Hospital Medical Center, CincinnatiNational Center for Research Resources (NCRR); Rare Diseases Clinical Research...CompletedPulmonary Alveolar ProteinosisUnited States, Germany, Italy, Japan
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National Institute of Allergy and Infectious Diseases...CompletedPulmonary Alveolar Proteinosis (PAP) | Severe Mucocutaneous CandidiasisUnited States
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Assistance Publique - Hôpitaux de ParisCompletedPulmonary Alveolar Proteinosis | Mutation Ala393Thr of the MARS Gene | mutationSer567Leu of the MARS GeneFrance
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TRPHARMEnrolling by invitationPulmonary Alveolar ProteinosisTurkey
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Matthias GrieseRecruitingChild | Pulmonary Fibrosis | Lung Diseases, Interstitial | Pulmonary Eosinophilia | Respiratory Distress Syndrome, Newborn | Pulmonary Alveolar ProteinosisGermany, Turkey, United Kingdom
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Black Tie Medical, Inc.Robert W. Alexander, MDEnrolling by invitationCoronavirus Infection | Idiopathic Pulmonary Fibrosis | Interstitial Lung Disease | COPD | Pulmonary Alveolar Proteinosis | Viral PneumoniaUnited States
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Tanta UniversityNot yet recruitingBariatric Surgery | Atelectasis | Alveolar Recruitment ManeuversEgypt
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Sixth Affiliated Hospital, Sun Yat-sen UniversityCompletedPostoperative Pulmonary Complications | Mechanical Power | Protective Ventilation | Alveolar Recruitment ManeuversChina
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Savara Inc.CelerionCompletedBronchiectasis | Cystic Fibrosis | Acute Respiratory Distress Syndrome | Pulmonary Alveolar ProteinosisUnited Kingdom
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University of MilanCompletedChronic Obstructive Pulmonary Disease | Salmeterol Effect Against an Acute Alveolar Fluid Clearance Challenge Secondary to Lung Fluid Overload in COPD Patients | Bronchodilator Agents | SalmeterolItaly
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University of PennsylvaniaCompletedHereditary Hemorrhagic Telangiectasia (HHT)United States
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IRCCS Azienda Ospedaliera Universitaria San Martino...CompletedLong COVID | Breathlessness | Exercise Intolerance | Pulmonary Gas Exchange | Alveolar Lung DiseaseItaly
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Hospices Civils de LyonCompletedPulmonary Arteriovenous Malformations (PAVMs) in Hereditary Haemorrhagic Telangiectasia (HHT) (PAVM)Pulmonary Arteriovenous Malformation | Hereditary Haemorrhagic Telangiectasia | Cerebral Disorder
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Heidelberg UniversityTerminatedHereditary Emphysema (Alpha 1-antitrypsin Deficiency)Germany
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Imperial College LondonThe Margaret Hayton HHT FundRecruitingTelangiectasia, Hereditary HemorrhagicUnited Kingdom
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Imperial College LondonCompletedHereditary Hemorrhagic Telangiectasia | Pulmonary Arteriovenous MalformationsUnited Kingdom
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Imperial College LondonUnknownAsthma | COPD | Hereditary Hemorrhagic Telangiectasia | Pulmonary Arteriovenous Malformations
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Hospices Civils de LyonCompletedTelangiectasia, Hereditary Hemorrhagic | Rendu Osler DiseaseFrance
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National Heart, Lung, and Blood Institute (NHLBI)Suburban HospitalRecruitingAsthma | Pulmonary Fibrosis | Tuberous Sclerosis | Cystic Fibrosis | Pulmonary SarcoidosisUnited States
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Lassen Therapeutics 1 PTY LTDRecruitingThyroid Eye Disease | Pulmonary FibrosisAustralia, Hong Kong, New Zealand
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Children's Oncology GroupNational Cancer Institute (NCI)CompletedSarcoma | Kidney Cancer | Brain and Central Nervous System Tumors | Neuroblastoma | Liver Cancer | Pleuropulmonary Blastoma | Hereditary Wilms Tumor
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National Cancer Institute (NCI)Active, not recruitingSoft Tissue Sarcoma | Renal Cell Carcinoma | Hepatocellular Carcinoma | Osteosarcoma | Ewing Sarcoma | Recurrent Renal Cell Carcinoma | Refractory Malignant Solid Neoplasm | Rhabdomyosarcoma | Recurrent Ewing Sarcoma | Recurrent Hepatoblastoma | Recurrent Malignant Solid Neoplasm | Recurrent Osteosarcoma | Recurrent... and other conditionsUnited States
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Vanderbilt UniversityNational Heart, Lung, and Blood Institute (NHLBI); University of South Florida and other collaboratorsCompletedHermansky Pudlak SyndromeUnited States
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National Human Genome Research Institute (NHGRI)TerminatedPulmonary Fibrosis | Metabolic Disease | Oculocutaneous Albinism | Hermansky-Pudlak Syndrome (HPS) | Platelet Storage Pool DeficiencyUnited States
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National Human Genome Research Institute (NHGRI)RecruitingPulmonary Fibrosis | Healthy Volunteers | Hermansky-Pudlak Syndrome (HPS)United States
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William Gahl, M.D.National Human Genome Research Institute (NHGRI)CompletedPulmonary Fibrosis | Inborn Errors of Metabolism | Albinism | Oculocutaneous Albinism | Platelet Storage Pool DeficiencyUnited States
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National Cancer Institute (NCI)CompletedRecurrent Neuroblastoma | Recurrent Osteosarcoma | Recurrent Childhood Rhabdomyosarcoma | Recurrent Adult Soft Tissue Sarcoma | Recurrent Wilms Tumor and Other Childhood Kidney Tumors | Previously Treated Childhood Rhabdomyosarcoma | Recurrent Childhood Soft Tissue Sarcoma | Recurrent Ewing Sarcoma... and other conditionsUnited States
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National Human Genome Research Institute (NHGRI)CompletedCancer | Myelofibrosis | Pulmonary Fibrosis | Gaucher Disease | Hermansky-Pudlak Syndrome (HPS)United States