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- US Clinical Trials Registry
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Clinical Trials on Hurler-Scheie Syndrome
Total 33916 results
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Fujifilm Pharmaceuticals U.S.A., Inc.WithdrawnMyelodysplastic Syndrome (MDS)
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National Heart, Lung, and Blood Institute (NHLBI)Completed
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TelikTerminatedMyelodysplastic Syndrome (MDS)United States
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Oncology Specialties, AlabamaTerminatedMyelodysplastic Syndrome (MDS)United States
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zhang shoulongChanghai Hospital; Jinan Military General HospitalRecruitingImmune Effector Cell Associated Neurotoxicity SyndromeChina
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AbbVieGenentech, Inc.Active, not recruitingMyelodysplastic Syndrome (MDS)United States, Australia, Austria, Belgium, Brazil, Canada, China, Czechia, France, Germany, Hungary, Israel, Italy, Japan, Korea, Republic of, Netherlands, Poland, Puerto Rico, Russian Federation, Spain, Taiwan, Turkey, United Kingdom
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Amphivena Therapeutics, Inc.CompletedMyelodysplastic Syndrome (MDS)United States
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CelgeneCompletedMyelodysplastic Syndrome (MDS)China
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Novartis PharmaceuticalsTerminatedMyelodysplastic Syndrome (MDS)Germany
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TelikCompletedMyelodysplastic Syndrome (MDS)United States
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Thomas Jefferson UniversityAbbVieRecruitingMyelodysplastic Syndrome | Recurrent Myelodysplastic Syndrome | Refractory Myelodysplastic SyndromeUnited States
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Masonic Cancer Center, University of MinnesotaTerminatedSphingolipidoses | Niemann-Pick Disease, Type C | Krabbe Disease | Sly Syndrome | Fucosidosis | Aspartylglucosaminuria | Alpha Mannosidosis | Hurler's Syndrome | Maroteaux-Lamy Syndrome | Wolman's Disease | Niemann-Pick Disease Type BUnited States
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Scripps HealthJ. Craig Venter InstituteCompletedLi-Fraumeni Syndrome | Hereditary Cancer Syndromes | TP53 Gene Germline Mutation CarrierUnited States
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University of Wisconsin, MadisonTerminatedCompartment Syndrome of LegUnited States
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TakedaCompletedDravet Syndrome (DS)China, Canada, France, Hungary, Poland, United States, Spain, Greece, Australia, Brazil, Serbia, Germany, Italy, Japan, Latvia, Netherlands, Ukraine, Russian Federation
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Jasper Therapeutics, Inc.Recruiting
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University Health Network, TorontoZogenix, Inc.Not yet recruiting
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University of Texas Southwestern Medical CenterChildren's Hospital of PhiladelphiaEnrolling by invitationShort Gut SyndromeUnited States
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Erasmus Medical CenterEnrolling by invitationComplex Regional Pain Syndromes | CRPS (Complex Regional Pain Syndromes)Netherlands
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Institut fuer anwendungsorientierte Forschung und...University Medical Center GoettingenCompletedMyelodysplastic Syndromes (MDS) | Chromosmal Aberrations | Karyotype Evolution | Rare Abnormalities | Cytogenetic MonitoringGermany
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Larissa University HospitalRecruitingDumping Syndrome | Gastric SurgeryGreece
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Children's Hospital of PhiladelphiaUniversity of PennsylvaniaRecruiting
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M.D. Anderson Cancer CenterNational Cancer Institute (NCI)Active, not recruitingHigh Risk Myelodysplastic SyndromeUnited States
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M.D. Anderson Cancer CenterNational Cancer Institute (NCI)Active, not recruitingLeukemia | Myelodysplastic Syndrome | Recurrent Myelodysplastic SyndromeUnited States
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Uma BorateRecruitingTherapy-Related Myelodysplastic Syndrome | Secondary Myelodysplastic SyndromeUnited States
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University Hospital, BrestRecruitingMyelodysplastic Syndromes | Myelodysplastic Syndrome With Isolated Del(5Q) | Myelodysplastic Syndrome With Del(5Q)France
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Cyclacel Pharmaceuticals, Inc.SuspendedLeukemia | Myelodysplastic Syndrome(MDS)United States
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Northwestern UniversityCompletedIrritable Bowel Syndrome | SIBO | Bacterial Overgrowth SyndromeUnited States
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U.S. Army Medical Research and Development CommandUnknownAnterior Tibial Compartment SyndromeUnited States
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Sequenom, Inc.CompletedTurner Syndrome | Down Syndrome (Trisomy 21) | Patau Syndrome (Trisomy 13) | Edwards Syndrome (Trisomy 18)United States
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Progenity, Inc.UnknownDown Syndrome | DiGeorge Syndrome | Turner Syndrome | Klinefelter Syndrome | Edwards Syndrome | Patau Syndrome | Perinatal InfectionsUnited States
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Peter L GreenbergAmgenCompletedMyelodysplastic Syndromes | Myelodysplastic Syndromes (MDS) | Blood CancerUnited States
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Vern C. Juel, M.D.No longer available
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Ricardo MaselliCatalyst Pharmaceuticals, Inc.No longer availableCongenital Myasthenic SyndromeUnited States
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Santa Casa da Misericordia do Rio de Janeiro HospitalUnknownFibromyalgia | Myofascial Pain Syndrome, Diffuse | Diffuse Myofascial Pain Syndrome | Fibromyalgia-Fibromyositis Syndrome | Fibromyositis-Fibromyalgia SyndromeBrazil
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University of Colorado, DenverCompletedMarfan Syndrome | Turner Syndrome | Loeys-Dietz Syndrome | Thoracic Aortic Aneurysm and Dissection Syndromes | Ehlers-Danlos Type IV SyndromeUnited States
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Major Extremity Trauma Research ConsortiumNot yet recruiting
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TakedaRecruitingShort Bowel Syndrome (SBS)Canada
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GlyPharma TherapeuticsVectivBio AGCompletedSBS - Short Bowel SyndromeDenmark
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Groupe Francophone des MyelodysplasiesCompletedHigh Grade Myelodysplastic Syndrome LesionsFrance, Tunisia
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Maastricht University Medical CenterMyrovlytis TrustCompleted
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McGill University Health Centre/Research Institute...United States Department of Defense; Vanderbilt University Medical Center; Hennepin...RecruitingAcute Compartment SyndromeUnited States
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Central Hospital, Nancy, FranceBeaujon Hospital; Société Francophone Nutrition Clinique et MétabolismeUnknownSBS - Short Bowel SyndromeFrance
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Major Extremity Trauma Research ConsortiumCompleted
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J&M ShulerUnited States Department of Defense; Nonin MedicalUnknownAcute Compartment SyndromeUnited States
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J&M ShulerUnited States Department of Defense; Somanetics CorporationCompletedAcute Compartment SyndromeGermany
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RTI InternationalUniversity of North Carolina, Chapel HillEnrolling by invitationTuberous Sclerosis | Down Syndrome | Duchenne Muscular Dystrophy | Prader-Willi Syndrome | Fragile X Syndrome | Rett Syndrome | Turner Syndrome | Williams Syndrome | Angelman Syndrome | Chromosome 22q11.2 Deletion Syndrome | Klinefelter Syndrome | Phelan-McDermid Syndrome | Dup15Q Syndrome | Smith Magenis SyndromeUnited States
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Sinaloa Pediatric HospitalCompleted
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Hospital for Special Surgery, New YorkRecruitingCRPS (Complex Regional Pain Syndromes)United States