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Clinical Trials on Leber Congenital Amaurosis in Australia
Total 255 results
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Medical University of ViennaEnrolling by invitationGlaucoma | Cataract | Meibomian Gland Dysfunction | Aniridia | Corneal Transplantation | Acanthamoeba Keratitis | Demodicosis | Conjunctival PathologiesAustria
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BioCeryxUniversity of British Columbia; University College London Hospitals; Brugmann... and other collaboratorsUnknownTrisomy 21 and Other Fetal AneuploidyAustralia, United Kingdom, Spain, Canada, Belgium, Portugal
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C. R. BardWithdrawnDysfunctional AV Graft | Dysfunctional AV FistulaAustria, Germany
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Medical University of ViennaMedical Scientific Fund of the Mayor of ViennaRecruitingCerebral Arteriovenous MalformationAustria
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MedImmune LLCCompletedCongenital Heart DiseaseUnited States, Spain, United Kingdom, Canada, Belgium, Germany, Israel, Austria, Poland, Russian Federation, Sweden, Lebanon, France, Czech Republic, Hungary, Denmark, Bulgaria
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Mayne Pharma International Pty LtdTerminatedLamellar IchthyosisUnited States, Spain, Canada, Germany, France, Australia, Israel, Ukraine, United Kingdom
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Hoffmann-La RocheRecruitingAngelman SyndromeAustralia, United States, Spain, Italy, France, Germany
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Stryker CraniomaxillofacialQmed Consulting A/SEnrolling by invitationCraniofacial Abnormalities | Cranioplasty | Craniofacial InjuriesGermany, Spain, United States, Austria, France, United Kingdom
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AbbottCompletedSevere Respiratory Syncytial Virus InfectionAustria, Belgium, France, Germany, Italy, Norway, Poland, Slovenia, Spain, United Kingdom
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Medical University of ViennaUnknownPolycystic Kidney, Type 1 Autosomal Dominant Disease | Polycystic Kidney, Type 2 Autosomal Dominant DiseaseAustria
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Novartis PharmaceuticalsRecruitingLymphatic MalformationsSpain, France, Germany, Australia, United States
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Castle Creek Pharmaceuticals, LLCTerminatedEpidermolysis Bullosa SimplexUnited States, Israel, Australia, Austria, France, Germany, Netherlands, United Kingdom
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Ascend Biopharmaceuticals LtdCompletedBasal Cell Nevus Syndrome | Skin Neoplasm | Nodular Basal Cell Carcinoma of SkinAustralia
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ArQule, Inc. (a wholly owned subsidiary of Merck...Worldwide Clinical TrialsTerminatedPIK3CA-Related Overgrowth Spectrum (PROS)/Proteus SyndromeUnited States, Australia, Italy, Spain
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Medical University of ViennaCompletedEpistaxis | HHT | Morbus OslerAustria
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Sydney Children's Hospitals NetworkJohns Hopkins University; Children's Hospital of Philadelphia; University of... and other collaboratorsUnknownCharcot-Marie-Tooth DiseaseUnited States, Australia, Italy
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SanofiTerminatedCongenital Cystic Kidney DiseaseGermany, Spain, United States, Australia, Belgium, Japan, Korea, Republic of, Netherlands
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Advanced Osteotomy Tools (AOT) AGClinical Trial Unit, University Hospital Basel, SwitzerlandCompletedAbnormalities, Jaw | Malocclusion, Angle Class IIIGermany, Austria, Switzerland
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Merck Sharp & Dohme LLCActive, not recruitingPIK3CA-Related Overgrowth Spectrum (PROS)/Proteus Syndrome (PS)United States, Australia, Brazil, Italy, United Kingdom
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DePuy InternationalTerminatedOsteoarthritis | Rheumatoid Arthritis | Avascular Necrosis | Post-traumatic Arthritis | Congenital Hip Dysplasia | Slipped Capital Femoral Epiphysis | Collagen Disorders | Nonunion of Femoral FracturesAustria, Czech Republic, Finland, Germany, Norway, Portugal, Switzerland, United Kingdom
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Sanford HealthNational Ataxia Foundation; Beyond Batten Disease Foundation; Pitt Hopkins Research... and other collaboratorsRecruitingMitochondrial Diseases | Retinitis Pigmentosa | Myasthenia Gravis | Eosinophilic Gastroenteritis | Multiple System Atrophy | Leiomyosarcoma | Leukodystrophy | Anal Fistula | Spinocerebellar Ataxia Type 3 | Friedreich Ataxia | Kennedy Disease | Lyme Disease | Hemophagocytic Lymphohistiocytosis | Spinocerebellar Ataxia... and other conditionsUnited States, Australia
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SCAD AlliancePERFUSE Study GroupRecruitingSpontaneous Coronary Artery DissectionUnited States, Australia
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University of UlmUniversity of Pisa; IRCCS Azienda Ospedaliero-Universitaria di Bologna; Medical... and other collaboratorsRecruitingLipodystrophy Acquired | Lipodystrophy CongenitalAustria, France, Germany, Hungary, Italy, Portugal, Spain, Netherlands, Russian Federation, Slovenia, Switzerland, Turkey, United Kingdom
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Boehringer IngelheimRecruitingNetherton SyndromeBelgium, United Kingdom, Australia, Germany, China, Malaysia, United States, Japan, France, Israel, Bulgaria, Italy, Switzerland, Netherlands, Portugal
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Rhythm Pharmaceuticals, Inc.CompletedBardet-Biedl Syndrome | POMC Deficiency Obesity | PCSK1 Deficiency Obesity | LEPR Deficiency ObesityUnited States, Australia, Spain, United Kingdom
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Scioderm, Inc.Amicus TherapeuticsTerminatedEpidermolysis BullosaPoland, Spain, Serbia, Netherlands, United States, Austria, Australia, Israel, Germany, France, United Kingdom, Lithuania
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ReCode TherapeuticsRecruitingPrimary Ciliary DyskinesiaUnited Kingdom, United States, Australia, New Zealand
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Insel Gruppe AG, University Hospital BernSwiss National Science Foundation; Mach Gaensslen Foundation; Baxalta Innovations...RecruitingThrombotic Thrombocytopenic Purpura | Congenital Thrombotic Thrombocytopenic Purpura | Familial Thrombotic Thrombocytopenic Purpura | Thrombotic Thrombocytopenic Purpura, Congenital | Upshaw-Schulman SyndromeUnited States, Austria, Czechia, Germany, Japan, Norway, Switzerland
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Spruce BiosciencesActive, not recruitingCongenital Adrenal HyperplasiaUnited States, Australia, Brazil, Canada, Denmark, Estonia, Germany, Ireland, Italy, Korea, Republic of, Latvia, Lithuania, Netherlands, Poland, Romania, Spain, Sweden, Switzerland, Turkey, United Kingdom
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Ionis Pharmaceuticals, Inc.BiogenActive, not recruitingAngelman SyndromeUnited States, Israel, Italy, France, Australia, United Kingdom
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Medical University of GrazCompletedSkin Cancer | Basal Cell Nevus Syndrome | Xeroderma PigmentosumAustria
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BioMarin PharmaceuticalRecruitingHypochondroplasiaUnited States, Spain, Canada, France, Japan, Australia, Italy, Argentina, Brazil, Germany, United Kingdom
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AlbireoEnrolling by invitationBiliary AtresiaSpain, United States, Netherlands, Malaysia, Canada, Germany, Turkey, Italy, France, Australia, Poland, New Zealand
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Scioderm, Inc.Amicus TherapeuticsCompletedEpidermolysis BullosaItaly, Spain, Serbia, United States, Australia, Netherlands, Austria, Germany, Israel, Lithuania, France, United Kingdom, Poland
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Healx LimitedWithdrawnFragile X SyndromeUnited States, Australia
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C. R. BardCompletedPeripheral Vascular Disease | Venous Disease | May-Thurner Syndrome | Iliofemoral Occlusive DiseaseUnited States, Australia, Germany, Ireland, Netherlands, Spain, United Kingdom
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Novartis PharmaceuticalsCompletedTumors Characterized by Genetic Abnormalities of ALKAustralia, Belgium, Germany, Netherlands, Spain, Italy, Singapore, Korea, Republic of, United Kingdom, United States, Canada
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Novartis PharmaceuticalsCompletedTreatment for Basal Cell Carcinomas (BCCs) in Gorlin Syndrome PatientsAustria, Switzerland
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University of RegensburgRecruitingSickle Cell Disease | Sickle Cell Anemia | Sickle Cell Disorders | HbS Disease | Hemoglobin S Disease | Sickling Disorder Due to Hemoglobin SGermany, Austria
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Novo Nordisk A/SCompletedCongenital Bleeding Disorder | Congenital FXIII DeficiencyUnited States, Israel, Austria, Spain, Switzerland, Germany, Canada, France, United Kingdom, Italy, Finland
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bluebird bioActive, not recruitingTransfusion-dependent Beta-ThalassemiaUnited States, France, United Kingdom, Australia, Thailand, Italy, Germany, Greece
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RHEACELL GmbH & Co. KGFGK Clinical Research GmbH; Ticeba GmbH; Granzer Regulatory Consulting & ServicesCompletedRecessive Dystrophic Epidermolysis BullosaUnited States, Austria, France, Germany, United Kingdom
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University of Alabama at BirminghamMedtronic; The Children's Tumor FoundationTerminatedNF1 | Congenital Pseudarthrosis of TibiaUnited States, Australia
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Novo Nordisk A/STerminatedHealthy | Congenital Bleeding Disorder | Haemophilia AAustria, Spain, United Kingdom, France, Germany
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CelgeneAcceleron Pharma Inc. (a wholly owned subsidiary of Merck Sharp and Dohme...CompletedBeta-Thalassemia | Erythrocyte TransfusionUnited States, Israel, Australia, Turkey, Taiwan, Malaysia, United Kingdom, Canada, Thailand, France, Lebanon, Italy, Bulgaria, Greece, Tunisia
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CSL BehringCompletedCongenital Hemophilia AUnited States, Austria, Germany, Malaysia, Netherlands, Philippines, Ukraine, Romania, Spain, Australia, France, Georgia, Italy, Lebanon, Poland, Portugal, Switzerland, Thailand, Turkey
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Amryt Research LimitedCompletedEpidermolysis BullosaUnited States, Spain, Israel, Australia, France, Denmark, Switzerland, Italy, Hong Kong, Argentina, Austria, Brazil, Chile, Colombia, Czechia, Georgia, Germany, Greece, Hungary, Ireland, Romania, Russian Federation, Serbia, Singapore, U... and more
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Optimed Medizinische Instrumente GmbHCompletedPost-thrombotic Syndrome | Iliac Vein Compression SyndromeSwitzerland, Austria, Germany, Netherlands
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University College, LondonUniversity of LiverpoolTerminatedCortical DysplasiaUnited Kingdom, France, Austria, United States, Czechia, Germany, Italy, Switzerland
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Zynerba Pharmaceuticals, Inc.RecruitingFragile X SyndromeUnited States, Australia, United Kingdom, Ireland