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Clinical Trials on Metachromatic Leukodystrophy (MLD) in United Kingdom
Total 1322 results
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ShireTakeda Development Center Americas, Inc.Active, not recruitingMetachromatic Leukodystrophy (MLD)United States, Canada, Belgium, Israel, Netherlands, United Kingdom, Germany, Spain, Japan, Brazil, Argentina, France, Greece, Italy
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ShireTerminatedMetabolic Diseases | Brain Diseases | Central Nervous System Diseases | Nervous System Diseases | Demyelinating Diseases | Genetic Diseases, Inborn | Metabolism, Inborn Errors | Lysosomal Storage Diseases | Lipid Metabolism Disorders | Sphingolipidoses | Hereditary Central Nervous System Demyelinating Diseases and other conditionsUnited States, Denmark, France, Argentina, Belgium, Brazil, Canada, Germany, Japan, Turkey
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The Cooper Health SystemCompletedMetachromatic LeukodystrophyUnited States
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Talaris Therapeutics Inc.Duke UniversityNo longer availableMetachromatic LeukodystrophyUnited States
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National Organization for Rare DisordersFood and Drug Administration (FDA)Active, not recruitingMetachromatic LeukodystrophyUnited States
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University of PittsburghActive, not recruitingMetachromatic LeukodystrophyUnited States
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Masonic Cancer Center, University of MinnesotaCompletedMucopolysaccharidosis | Hurler Syndrome | Sphingolipidoses | Peroxisomal Disorders | Krabbe Disease | Adrenoleukodystrophy (ALD) | Hunter Syndrome | Sly Syndrome | Fucosidosis | Aspartylglucosaminuria | Alpha Mannosidosis | Metachromatic Leukodystrophy (MLD) | Maroteaux-Lamy SyndromeUnited States
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Talaris Therapeutics Inc.Duke UniversityNo longer availableMetachromatic LeukodystrophyUnited States
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Talaris Therapeutics Inc.Duke UniversityTerminatedNiemann-Pick Disease | Alpha-mannosidosis | Tay Sachs Disease | Sandhoff Disease | Metachromatic Leukodystrophy (MLD) | Hurler-Scheie Syndrome | Hurler Syndrome (MPS I) | Hunter Syndrome (MPS II) | Sanfilippo Syndrome (MPS III) | Krabbe Disease (Globoid Leukodystrophy) | Adrenoleukodystrophy (ALD and AMN) | Pelizaeus...United States
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Bellicum PharmaceuticalsNo longer availableHurler Syndrome | Inborn Errors of Metabolism | Metachromatic Leukodystrophy | Inherited Metabolic Disorder | Lysosomal Storage DisorderUnited States
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Masonic Cancer Center, University of MinnesotaCompletedNiemann-Pick Disease | Wolman Disease | Adrenoleukodystrophy | Batten Disease | Metachromatic Leukodystrophy | GM1 Gangliosidosis | Fucosidosis | Globoid Cell Leukodystrophy | Gaucher's Disease | Tay Sachs Disease | Sandhoff DiseaseUnited States
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Masonic Cancer Center, University of MinnesotaCompletedWolman Disease | Adrenoleukodystrophy | Metachromatic Leukodystrophy | Sanfilippo Syndrome | GM1 Gangliosidosis | Globoid Cell Leukodystrophy | Tay Sachs Disease | Sandhoffs Disease | I-Cell DiseaseUnited States
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National Center for Research Resources (NCRR)University of California, Los AngelesCompletedThrombocytopenia | Inborn Errors of Metabolism | Metachromatic Leukodystrophy | Fanconi's Anemia | Thalassemia Major | Pure Red-Cell AplasiaUnited States
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Washington University School of MedicineCompletedVasculopathy, Retinal, With Cerebral Leukodystrophy | Cerebroretinal Vasculopathy, HereditaryUnited States
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Baylor Research InstituteCompleted
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Fairview University Medical CenterUnknownMucopolysaccharidosis I | Niemann-Pick Disease | Mucopolysaccharidosis VI | Wolman Disease | Adrenoleukodystrophy | Metachromatic Leukodystrophy | Pulmonary Complications | Fucosidosis | Globoid Cell Leukodystrophy | Gaucher's Disease | Mannosidosis | I Cell DiseaseUnited States
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University of UtahRecruiting
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Children's Hospital of PhiladelphiaEli Lilly and Company; University of Pennsylvania; Takeda; National Institute of... and other collaboratorsRecruitingMucopolysaccharidoses | Leukoencephalopathies | Leukodystrophy | Adrenoleukodystrophy | Adrenomyeloneuropathy | X-linked Adrenoleukodystrophy | Gangliosidoses | Metachromatic Leukodystrophy | Krabbe Disease | Refsum Disease | Cadasil | Sjogren-Larsson Syndrome | Allan-Herndon-Dudley Syndrome | White Matter Disease | GM2... and other conditionsUnited States
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Passage Bio, Inc.SuspendedLeukodystrophy, Globoid CellUnited States, Brazil, Netherlands, United Kingdom, Canada, Israel
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Zymenex A/SCompletedInfantile Globoid Cell LeukodystrophyUnited States
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Masonic Cancer Center, University of MinnesotaRecruitingHurler Syndrome | Sphingolipidoses | Peroxisomal Disorders | Metachromatic Leukodystrophy | Alpha-Mannosidosis | Hunter Syndrome | Mucopolysaccharidosis Disorders | Maroteaux Lamy Syndrome | Sly Syndrome | Fucosidosis | Aspartylglucosaminuria | Glycoprotein Metabolic Disorders | Recessive Leukodystrophies | Globoid... and other conditionsUnited States
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Albert Einstein College of MedicineEunice Kennedy Shriver National Institute of Child Health and Human Development... and other collaboratorsEnrolling by invitationMucopolysaccharidosis II | Fabry Disease | Niemann-Pick Disease, Type C | Mucopolysaccharidosis VI | Lysosomal Acid Lipase Deficiency | Metachromatic Leukodystrophy | Gaucher Disease | Cerebrotendinous Xanthomatosis | Mucopolysaccharidosis IV A | GM1 Gangliosidosis | Mucopolysaccharidosis VII | Acid Sphingomyelinase... and other conditionsUnited States
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National Human Genome Research Institute (NHGRI)CompletedLeukodystrophy | LeukoencephalopathyUnited States
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Children's Hospital of PhiladelphiaIllumina, Inc.Active, not recruitingMucopolysaccharidoses | Leukodystrophy | Adrenoleukodystrophy | Adrenomyeloneuropathy | X-linked Adrenoleukodystrophy | Gangliosidoses | Metachromatic Leukodystrophy | Krabbe Disease | Refsum Disease | Cadasil | Sjogren-Larsson Syndrome | Allan-Herndon-Dudley Syndrome | White Matter Disease | GM2 Gangliosidosis | Zellweger... and other conditionsUnited States
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Royal College of MusicCompletedIndividuals Experiencing Mild or Moderate Mental Health IssuesUnited Kingdom
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Bausch Health Americas, Inc.CompletedMid Facial Contour DeficienciesUnited Kingdom
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AccexibleCornwall Partnership NHS Foundation TrustRecruitingMild Cognitive Impairment and DementiaUnited Kingdom
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Unilever SEACCompletedAllergy to MoldUnited Kingdom
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University of NottinghamAjinomoto Co., Inc.Unknown
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New York Medical CollegeCompletedMucopolysaccharidosis I | Myelodysplastic Syndrome | Acute Lymphocytic Leukemia | Acute Myelogenous Leukemia | Niemann-Pick Disease | Mucopolysaccharidosis VI | Wolman Disease | Adrenoleukodystrophy | Batten Disease | Metachromatic Leukodystrophy | Diamond-Blackfan Anemia | Severe Aplastic Anemia | Fucosidosis | Gaucher... and other conditionsUnited States
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Joanne Kurtzberg, MDThe Marcus FoundationRecruitingMucopolysaccharidosis II | Brain Diseases, Metabolic, Inborn | Adrenoleukodystrophy | Batten Disease | Leukodystrophy, Metachromatic | Leukodystrophy, Globoid Cell | Alpha-Mannosidosis | Tay-Sachs Disease | Pelizaeus-Merzbacher Disease | Sandhoff Disease | Neimann Pick Disease | Sanfilippo MucopolysaccharidosesUnited States
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Sheffield Teaching Hospitals NHS Foundation TrustSheffield Hallam UniversityCompleted
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Chiesi Farmaceutici S.p.A.CompletedMild Persistent AsthmaUnited Kingdom
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University of NottinghamUnknownOld Age (Focus; Not a Recognized Condition)United Kingdom
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University of DerbyRecruitingOld Age; Debility | Stability | Balance; DistortedUnited Kingdom
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Queen's University, BelfastWellcome TrustCompletedMild Cognitive ImpairmentUnited Kingdom
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UCB CelltechCompletedMild to Moderate PsoriasisUnited Kingdom
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King's College LondonUnknown
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University of SurreyDr. Willmar Schwabe GmbH & Co. KGCompletedMild Stress/AnxietyUnited Kingdom
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University of DerbyCompletedAcute Effects of Elastic Band Resistance on Postural Stability and Physical Function in Older AdultsOld Age; Debility | Stability | Balance | PosturographyUnited Kingdom
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University of ReadingFondazione Edmund Mach di San Michele all'AdigeCompletedMild HypercholesterolemiaUnited Kingdom
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Novoic LimitedTerminatedCognitive Impairment | Mild Cognitive ImpairmentUnited Kingdom
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Anglia Ruskin UniversityCambridgeshire and Peterborough NHS Foundation TrustCompleted
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University of NottinghamMars, Inc.Completed
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University of East AngliaCompletedDepression in Old AgeUnited Kingdom
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South London and Maudsley NHS Foundation TrustEnrolling by invitationMild Cognitive Impairment | Mild Cognitive Impairment Due to Alzheimer's DiseaseUnited Kingdom
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Dr Thomas DannhauserUniversity College, LondonCompletedMild Cognitive ImpairmentUnited Kingdom
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University of BrightonNord University; Brighton & Hove Digital Health Living LabNot yet recruitingHealthy Aging | Old Age; Debility | Dignity | Digital TechnologyUnited Kingdom
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Arxx TherapeuticsRecruitingHealthy Volunteers | Mild to Moderate PsoriasisUnited Kingdom
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University of UlsterQueen Margaret University, Nutrition and Biological Sciences, Musselburgh... and other collaboratorsRecruitingMusculoskeletal Diseases | Vitamin D Deficiency | Cognitive Delay, MildUnited Kingdom