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Clinical Trials on Optic Nerve Hypoplasia and Abnormalities of the Central Nervous System in Australia
Total 737 results
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Murdoch Childrens Research InstituteRoyal Children's Hospital; Monash HealthRecruitingSnoring | Tonsillar Hypertrophy | Sleep Disorder; Breathing-Related | Obstructive Sleep Apnea of Child | Sleep Disorders in Children | Adenoidal DisorderAustralia
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Amicus TherapeuticsApproved for marketingPhysician Initiated Expanded Access Request for Migalastat in Individual Patients With Fabry DiseaseFabry DiseaseUnited States, Australia
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Children's Oncology GroupNational Cancer Institute (NCI)CompletedBrain Tumors | Central Nervous System TumorsUnited States, Canada, Netherlands, Puerto Rico, Switzerland, Australia
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Amicus TherapeuticsActive, not recruitingPompe DiseaseUnited States, Netherlands, United Kingdom, Australia, Germany, New Zealand
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Novartis PharmaceuticalsCompletedLong-term Safety of TIPItaly, Spain, Germany, United States, Australia, Canada, Hungary, Mexico, Argentina
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PfizerCompletedTransthyretin Amyloidosis Cardiomyopathy (ATTR-CM)Italy, Romania, France, Australia, Austria, Portugal, Slovakia, Slovenia, Spain, United Kingdom
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Incyte CorporationActive, not recruitingSquamous Cell Carcinoma of the Anal CanalUnited States, Italy, Spain, United Kingdom, Australia, France, Germany, Sweden, Japan, Norway, Belgium, Denmark, Puerto Rico
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CHDI Foundation, Inc.Monash UniversityCompletedHuntington's DiseaseUnited States, Australia, United Kingdom, Canada
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Novo Nordisk A/SCompletedGrowth Hormone Disorder | Adult Growth Hormone DeficiencySweden, Austria, Spain, Switzerland, Germany, France, Australia, Poland, United Kingdom, Norway, Belgium, Hungary
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PfizerCompletedGaucher DiseaseUnited Kingdom, Canada, Israel, United States, Australia, Spain
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Xenova BiomedixWithdrawnGlioblastoma MultiformeUnited States, Australia
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Children's Oncology GroupNational Cancer Institute (NCI)CompletedBrain Tumor | Central Nervous System TumorUnited States, Canada, Puerto Rico, Australia, Netherlands, Switzerland
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Wave Life Sciences Ltd.RecruitingHuntington DiseaseCanada, Spain, Australia, Denmark, Netherlands, Poland, United Kingdom, France, Germany, Italy
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AbbVieTerminatedProgressive Supranuclear Palsy (PSP)United States, Australia, Canada, Italy, Japan
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Sage TherapeuticsRecruitingHuntington's DiseaseUnited States, Australia, Canada, United Kingdom
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Santhera PharmaceuticalsCompletedFreidreich's AtaxiaGermany, Netherlands, France, Austria, Belgium
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Zynerba Pharmaceuticals, Inc.CompletedFragile X SyndromeUnited States, New Zealand, Australia
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University Hospital Birmingham NHS Foundation TrustNorthern Care Alliance NHS Foundation Trust; Cambridge University Hospitals... and other collaboratorsActive, not recruitingArrhythmia Burden, Risk of Sudden Cardiac Death and Stroke in Patients With Fabry Disease (RaILRoAD)Fabry DiseaseUnited Kingdom, Australia
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PrileniaTerminatedHuntington's DiseaseUnited States, Australia, Austria, Canada, France, Germany, Italy, Netherlands, Poland, Russian Federation, United Kingdom
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Amicus TherapeuticsRecruitingPompe Disease (Late-onset)United States, Taiwan, Japan, Australia, Canada
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University of California, San FranciscoNational Institute of Neurological Disorders and Stroke (NINDS); The Chad-Tough... and other collaboratorsRecruitingDiffuse Intrinsic Pontine Glioma | Diffuse Midline Glioma, H3 K27M-Mutant | Recurrent Diffuse Intrinsic Pontine Glioma | Recurrent Diffuse Midline Glioma, H3 K27M-Mutant | Recurrent WHO Grade III Glioma | WHO Grade III GliomaUnited States, Netherlands, Israel, Australia, New Zealand, Switzerland
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Aeglea BiotherapeuticsTerminatedHomocystinuria Due to Cystathionine Beta-Synthase DeficiencyUnited States, United Kingdom, Australia
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Ataxia Study GroupRecruitingSpinocerebellar AtaxiaAustria, Belgium, France, Germany, Hungary, Italy, Netherlands, Poland, Spain, United Kingdom
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Santhera PharmaceuticalsCompletedFriedreich's AtaxiaNetherlands, Austria, United Kingdom, Belgium, France, Germany
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PfizerCompletedGaucher DiseaseChile, United Kingdom, Canada, Spain, Israel, United States, Australia, South Africa
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Salzburger LandesklinikenCompletedNeonatology | Perinatal Distress SyndromeAustria
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PTC TherapeuticsEnrolling by invitationFriedreich AtaxiaUnited States, Australia, Brazil, Canada, France, Germany, Italy, New Zealand, Spain
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PTC TherapeuticsCompletedFriedreich AtaxiaUnited States, Australia, Brazil, Canada, France, Germany, Italy, New Zealand, Spain
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Novartis PharmaceuticalsCompletedMelanoma and Brain MetastasesCanada, United States, Australia, France, Germany, Italy, Spain
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Massachusetts General HospitalNational Center for Complementary and Integrative Health (NCCIH); University...TerminatedHuntington's DiseaseUnited States, Canada, New Zealand, Australia
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HP Therapeutics FoundationHuntington Study GroupUnknownHuntington DiseaseUnited States, Canada, Australia
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Rigel PharmaceuticalsNationwide Children's HospitalNot yet recruitingAstrocytoma | High Grade Glioma | Oligodendroglioma | Diffuse Intrinsic Pontine Glioma | Diffuse Midline Glioma, H3 K27M-Mutant | WHO Grade III Glioma | Metastatic Brain Tumor | Spinal Tumor | Astrocytoma, Grade III | Astrocytoma, Grade IV | IDH1 Mutation | WHO Grade IV Glioma | Thalamus Tumor | IDH1 R132 | IDH1 R132C | IDH1 R132H and other conditionsUnited States, Australia, United Kingdom, Canada, Germany, Netherlands
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Universitätsklinikum Hamburg-EppendorfDeutsche KinderkrebsstiftungActive, not recruitingBrain TumorsGermany, Denmark, United Kingdom, Belgium, Poland, Ireland, Austria, Italy, Czechia, France, Netherlands, Norway, Portugal, Spain, Sweden, Switzerland
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Children's Oncology GroupNational Cancer Institute (NCI)CompletedSarcoma | Brain and Central Nervous System Tumors | NeuroblastomaUnited States, Canada, Puerto Rico, Netherlands, Australia, New Zealand, Switzerland
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Alliance for Clinical Trials in OncologyNational Cancer Institute (NCI); Canadian Cancer Trials Group; European Organisation...RecruitingBrain and Central Nervous System TumorsUnited States, Canada, France, Netherlands, Austria, Belgium
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GlaxoSmithKlineTerminatedNarcolepsySpain, Germany, Netherlands, Austria, Finland, United Kingdom
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Bristol-Myers SquibbNektar TherapeuticsTerminatedEwing Sarcoma | Ependymoma | Medulloblastoma | Neuroblastoma | Rhabdomyosarcoma | High-grade Glioma | Leukemia and Lymphoma | Miscellaneous Brain Tumors | Miscellaneous Solid Tumors | Relapsed, Refractory Malignant NeoplasmsUnited States, Australia, France, Germany, Italy, Spain
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Natera, Inc.Children's Hospital of Philadelphia; Montefiore Medical Center; University of... and other collaboratorsCompletedPrader-Willi Syndrome | DiGeorge Syndrome | 22q11 Deletion Syndrome | Angelman Syndrome | Trisomy 21 | Trisomy 18 | Trisomy 13 | Monosomy X | Sex Chromosome Abnormalities | 1p36 Deletion Syndrome | Cri-du-Chat SyndromeUnited States, Australia, Ireland, Spain, Sweden, United Kingdom
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Daiichi Sankyo, Inc.CompletedTenosynovial Giant Cell Tumor | Pigmented Villonodular Synovitis | Giant Cell Tumors of the Tendon SheathUnited States, France, Australia, Denmark, Spain, Netherlands, Germany, Canada, United Kingdom, Hungary, Italy, Poland
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Institut CurieActive, not recruitingNeuroblastoma | Opsoclonus Myoclonus SyndromeFrance, Austria, Italy, Spain, Sweden, Switzerland, United Kingdom
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National Cancer Institute (NCI)CompletedGliosarcoma | Anaplastic Oligoastrocytoma | Anaplastic Astrocytoma | Diffuse Intrinsic Pontine GliomaUnited States, Canada, Australia
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Amicus TherapeuticsCompletedFabry DiseaseUnited States, Australia, France, United Kingdom, Brazil, Canada
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Novartis PharmaceuticalsCompletedGlioblastoma | Astrocytoma | Anaplastic Astrocytoma | Anaplastic Ganglioglioma | Anaplastic Pleomorphic Xanthoastrocytoma | Ganglioglioma | Pleomorphic Xanthoastrocytoma | Diffuse Astrocytoma | Anaplastic Oligodendroglioma | Pilocytic Astrocytoma | Gangliocytoma | Central Neurocytoma | Oligodendroglioma, Childhood and other conditionsUnited States, Italy, Japan, Germany, Spain, France, Canada, Australia, Brazil, Israel, Russian Federation, Argentina, United Kingdom, Finland, Belgium, Denmark, Czechia, Sweden, Switzerland, Netherlands
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PrileniaHuntington Study Group; European Huntington's Disease NetworkCompletedHuntington's DiseaseUnited States, Australia, Austria, Canada, Denmark, France, Germany, Italy, Netherlands, Poland, Russian Federation, United Kingdom
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bluebird bioActive, not recruitingCerebral Adrenoleukodystrophy (CALD) | Adrenoleukodystrophy (ALD) | X-Linked Adrenoleukodystrophy (X-ALD)United States, Argentina, Australia, Brazil, France, Germany, Netherlands, United Kingdom, Italy
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Antiva BiosciencesTerminatedHIV Infection | Anal Cancer | Human Papilloma Virus Infection | HSIL, High-Grade Squamous Intraepithelial Lesions | Anus NeoplasmUnited States, Australia
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Novartis Gene TherapiesActive, not recruitingSMA | Spinal Muscular Atrophy Type II | Spinal Muscular Atrophy Type I | Spinal Muscular Atrophy Type IIIUnited States, Belgium, France, Japan, United Kingdom, Italy, Taiwan, Australia, Canada
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Friedreich's Ataxia Research AllianceChildren's Hospital of Philadelphia; University of RochesterRecruitingFriedreich Ataxia | Neuro-Degenerative DiseaseUnited States, Canada, New Zealand, Australia, India
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University of OxfordAmerican College of Rheumatology; The European League Against Rheumatism (EULAR) and other collaboratorsUnknownGiant Cell Arteritis | Wegener's Granulomatosis | Microscopic Polyangiitis | Polyarteritis Nodosa | Takayasu Arteritis | Churg Strauss SyndromeKorea, Republic of, United States, Germany, Australia, Japan, Ireland, Belgium, Italy, Denmark, Slovenia, Switzerland, Canada, Argentina, Austria, China, Czech Republic, Egypt, Finland, France, Hungary, India, Mexico, Netherlands, New... and more