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Clinical Trials on Pompe Disease (Late-onset)
Total 985 results
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Haukeland University HospitalUnknownInsulin-dependent Diabetes Mellitus | Maturity-Onset Diabetes of the Young, Type 3 | Maturity Onset Diabetes of the Young, Type 1 | Childhood Diabetes MellitusNorway
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Alnylam PharmaceuticalsRecruitingEarly-Onset Alzheimer DiseaseUnited Kingdom, United States, Netherlands, Canada
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Mayo ClinicRecruitingEarly Onset Alzheimer DiseaseUnited States
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Imperial College LondonUnknownDiabetes | Type 1 Diabetes | Type 2 Diabetes | Maturity Onset Diabetes of the YoungUnited Kingdom
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Rambam Health Care CampusCompletedEnzyme Replacement Therapy in Pompe Disease
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Swedish Orphan BiovitrumCMIC Co, Ltd. JapanRecruitingStill's Disease, Adult-Onset | Still's Disease, Juvenile OnsetJapan
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Apollo Therapeutics LtdTerminatedAdult Onset Still's DiseaseUnited States, Belgium, Poland, Ukraine
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Swedish Orphan BiovitrumTerminatedStill's Disease, Adult-Onset | Still's Disease, Juvenile-OnsetUnited States, Canada
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University of OklahomaNational Center for Research Resources (NCRR)CompletedDiabetes Mellitus, Adult OnsetUnited States
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Assistance Publique - Hôpitaux de ParisCompleted
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University of Illinois at ChicagoGenentech, Inc.WithdrawnGlaucoma | Neovascular Glaucoma | New Onset Glaucoma | New Onset Neovascular Glaucoma
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MX LABS spółka z ograniczoną odpowiedzialnością...CompletedHeart Rate Variability | Heart Rate | Respiratory RatePoland
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University Hospital, Gentofte, CopenhagenUniversity of Copenhagen; Steno Diabetes Center CopenhagenCompletedMaturity-onset Diabetes of the YoungDenmark
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National Institute of Mental Health (NIMH)TerminatedMental Disorders | Schizophrenia | Psychosis | Childhood Onset Psychotic DisordersUnited States
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Tufts Medical CenterHoffmann-La RocheTerminatedArthritis, Juvenile Rheumatoid | Still's Disease, Juvenile OnsetUnited States
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Genzyme, a Sanofi CompanyCompletedGlycogen Storage Disease Type II Pompe DiseaseUnited States, Belgium, Denmark, France, Germany, Netherlands, United Kingdom
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Children's Hospital of Fudan UniversityRecruitingSeizures | Seizure Disorder | Epileptic Encephalopathy | Seizures, Generalized | Seizure Newborn | Epileptic Encephalopathy, Neonatal-onset | Epileptic Encephalopathy, Infant-onset | KCNQ2China
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Swedish Orphan BiovitrumCompletedArthritis, Juvenile | Lymphohistiocytosis, Hemophagocytic | Macrophage Activation Syndrome | Adult Onset Still DiseaseUnited States, Spain, United Kingdom, France, Italy
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EVEREST PESQUISA E DESENVOLVIMENTO LTDANot yet recruiting
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Universitas DiponegoroCompletedObesity Adult OnsetIndonesia
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Vanderbilt UniversityCompletedInsulin Resistance | Type 1 Diabetes Mellitus | Maturity-Onset Diabetes of the Young, Type 2 | MODY2United States
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University Hospital, Gentofte, CopenhagenNovo Nordisk A/S; University of CopenhagenCompletedMaturity-onset Diabetes of the YoungDenmark
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University of North Carolina, Chapel HillMetagenics, Inc.; North Carolina Translational and Clinical Sciences InstituteCompleted
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Oslo University HospitalHologic, Inc.; Cancer Registry of NorwayUnknownRecall Rate | Cancer Detection Rate | False Positive Rate | Positive Predictive ValueNorway
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Jessa HospitalCompletedLatex Hypersensitivity | Latex AllergyBelgium
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California Baptist UniversityCompletedObesity Adult OnsetUnited States
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AO Innovation Translation CenterActive, not recruitingEarly Onset ScoliosisUnited Kingdom, Switzerland
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Professor Lu Neurological ClinicUnknownEarly Onset Parkinson DiseaseTaiwan
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Harran UniversityHasan Kalyoncu UniversityNot yet recruitingNecrotizing Enterocolitis | Breast Milk Expression | Preterm | Late-Onset Neonatal Sepsis
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Institut National de la Santé Et de la Recherche...Active, not recruitingStill's Disease, Adult-Onset | Still Disease | Still Disease, Juvenile OnsetFrance
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OctapharmaActive, not recruitingPediatric Acute-Onset Neuropsychiatric SyndromeUnited States, Italy, Sweden
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Shanghai Jiao Tong University School of MedicineTerminated
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Matias VestedCompletedIntubation Conditions | Onset Time of Cisatracurium | Duration of Action of CisatracuriumDenmark
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Janssen Research & Development, LLCCompletedFocal Onset SeizuresGermany, Korea, Republic of, Belgium, United States, Russian Federation, Poland, Ukraine, Spain
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Novartis PharmaceuticalsCompletedPartial Onset SeizuresGermany, United States, Hungary, Korea, Republic of, Poland, Slovakia
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University of MinnesotaCompletedPANDAS | PANSUnited States
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Novartis PharmaceuticalsCompleted
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National Yang Ming UniversityUnknownEarly Onset Parkinson Disease | Early Stage Parkinson Disease
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prof. dr. Frans B. PlötzDutch Society of Pediatrics; Zorgevaluatie Nederland; Care4Neo; everywhereIMRecruitingEOS | Early-Onset Sepsis, NeonatalNetherlands
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University of MinnesotaNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK); National... and other collaboratorsRecruitingGM2 Gangliosidosis | GM1 Gangliosidosis | Tay-Sachs Disease | Sandhoff Disease | Late Onset Tay-Sachs DiseaseUnited States
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Institut National de la Santé Et de la Recherche...CompletedSystemic-Onset Juvenile Idiopathic ArthritisFrance
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ElMindA LtdUnknownDepression | Aging | Mild Cognitive Impairment | Early Onset Alzheimer DiseaseUnited States
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Shahid Beheshti University of Medical SciencesCompletedLate Postvitrectomy Diabetic Hemorrhage.Iran, Islamic Republic of
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Eisai Inc.CompletedPartial Onset EpilepsyUnited Kingdom
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Eisai Inc.CompletedPartial Onset EpilepsyUnited Kingdom
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United Arab Emirates UniversityNot yet recruitingMaturity-onset Diabetes of the Young | MODY | Monogenic Diabetes
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Eisai Inc.CompletedPartial Onset SeizuresGermany, Sweden, Norway, Austria, Denmark
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University of California, San FranciscoRecruitingMucopolysaccharidosis I | Mucopolysaccharidosis II | Mucopolysaccharidosis VI | Wolman Disease | Pompe Disease Infantile-Onset | Mucopolysaccharidosis IV A | Mucopolysaccharidosis VII | Neuronopathic Gaucher DiseaseUnited States
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ART Fertility Clinics LLCRecruitingInfertility | Live Birth Rate | Clinical Pregnancy Rate | Implantation Rate | FET | BlastocystsUnited Arab Emirates
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Xenon Pharmaceuticals Inc.Worldwide Clinical TrialsRecruitingFocal Onset SeizuresUnited States, Spain, Italy, Croatia, Portugal, Poland, Chile, Argentina, Austria, Czechia