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Clinical Trials on X-linked Adrenoleukodystrophy in United Kingdom
Total 1262 results
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Washington University School of MedicineNational Heart, Lung, and Blood Institute (NHLBI)CompletedHypertension | Overweight | Dyslipidemias | Prediabetic State | Metabolic Syndrome XUnited States
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National Heart, Lung, and Blood Institute (NHLBI)CompletedMyocardial Ischemia | Coronary Disease | Healthy | Cardiomyopathy, Hypertrophic | Syndrome XUnited States
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Veterans Medical Research FoundationNational Institute of Mental Health (NIMH); PfizerCompletedSchizophrenia | Insulin Resistance | Metabolic Syndrome XUnited States
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Northeastern Ohio Universities College of MedicineMercy Medical Center; Aultman Health Foundation; Akron General Medical Center; Forum... and other collaboratorsSuspendedDiabetes Mellitus, Type 2 | Metabolic Syndrome XUnited States
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Krystal Biotech, Inc.RecruitingWrinkle | Skin Roughness | Fine Lines | Skin ThicknessUnited States
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Stanford UniversityCompletedPsychotic Disorders | Mood Disorders | Insulin Resistance | Metabolic Syndrome X | Schizophrenia and Disorders With Psychotic FeaturesUnited States
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New Mexico VA Healthcare SystemBristol-Myers SquibbCompletedSchizophrenia | Schizoaffective Disorder | Bipolar Disorder | Metabolic Syndrome XUnited States
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Khondrion BVJulius Clinical; ProPharma Group; CertaraCompletedMitochondrial Diseases | Mitochondrial DNA tRNALeu(UUR) m.3243A<G Mutation | Maternally Inherited Diabetes and Deafness (MIDD) | Mitochondrial Encephalomyopathy, Lactic Acidosis and Stroke Like Episodes (MELAS) | Chronic Progressive External Ophthalmoplegia (CPEO)Netherlands, Denmark, United Kingdom, Germany
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AllerganCompleted
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AbbVieRecruiting
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Boston Children's HospitalSterileCare Inc.Enrolling by invitationCentral Line Complication | Central Line-associated Bloodstream Infection (CLABSI)United States
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O & O Alpan LLCUnknownFabry Disease | Niemann-Pick Disease | Gaucher Disease | Pompe Disease | Lysosomal Storage DisordersUnited States
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SwanBio Therapeutics, Inc.Active, not recruitingAMN | AMN Gene Mutation | X-ALDUnited States, Netherlands, Germany
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Boston Children's HospitalCompletedAML | ALL | Biphenotypic Leukemia | Refractory Anemia | Refractory Cytopenia With Multilineage Dysplasia | Refractory Anemia With Ringed Sideroblasts | Undifferentiated Leukemia | Ref. Cytopenia w Multilineage Dysplasia & Ringed Sideroblasts | Refractory Anemia With Excess Blasts-1 (5-10% Blasts) | Refractory... and other conditionsUnited States
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Christine HunterMerz North America, Inc.Completed
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Milton S. Hershey Medical CenterCompletedCentral Venous Catheter | Central Line | PICC | Neuro ICU | Neuroscience ICU | CVCUnited States
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Wright State UniversityRecruitingAging | UVB Phototherapy Burn | Insulin-like Growth Factor 1United States
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University of VirginiaUnknownCentral Line-associated Bloodstream Infection (CLABSI) | Line Insertion SiteUnited States
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Revision SkincareValidated Claim SupportCompletedWrinkle | Periorbital Edema | Fine Lines | Periorbital HyperpigmentationUnited States
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University of VirginiaUnknownCentral Lines in ICU PatientsUnited States
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Avila HerbalsUnknownFlu-like SymptomsUnited States
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National Cancer Institute (NCI)RecruitingFanconi Anemia | Dyskeratosis Congenita | Diamond Blackfan Anemia | Shwachman Diamond Syndrome | Inherited Bone Marrow Failure Syndrome, Aplastic AnemiaUnited States
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University of Missouri-ColumbiaTerminatedDiastasis Recti and Weakness of the Linea AlbaUnited States
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Ethicon, Inc.CompletedBariatric - Sleeve Gastrectomy Staple Line Reinforcement | Gynecology - Vaginal Cuff ClosureItaly, United States, Germany
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Johns Hopkins UniversityNational Institute of Neurological Disorders and Stroke (NINDS)RecruitingAmyotrophic Lateral Sclerosis | Tetraplegia | Locked-in Syndrome | Brainstem StrokeUnited States
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LeMaitre VascularAvaniaRecruitingGreat Vessel Reconstruction | Peripheral Vessel Reconstruction | Suture Line ButtressingUnited States, Italy
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BiositeCompletedStroke | Stroke Mimic(Conditions Presenting With Stroke-like Conditions)United States, Canada, Germany, Switzerland, United Kingdom
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Hospital for Special Surgery, New YorkRecruitingGlucagon-like Peptide 1 | Gastric Ultrasound | Point of Care UltrasoundUnited States, Canada
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Revision SkincareCompletedHyperpigmentation | Wrinkle | Photodamaged Skin | Fine LinesUnited States
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National Institute on Aging (NIA)University of PittsburghUnknownObstructive Sleep Apnea | Metabolic Syndrome XUnited States
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National Cancer Institute (NCI)CompletedUnspecified Childhood Solid Tumor, Protocol Specific | Childhood Myelodysplastic Syndromes | Previously Treated Myelodysplastic Syndromes | Secondary Myelodysplastic Syndromes | de Novo Myelodysplastic Syndromes | Refractory Anemia | Refractory Anemia With Excess Blasts | Refractory Cytopenia With... and other conditionsUnited States
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RTI InternationalEunice Kennedy Shriver National Institute of Child Health and Human Development... and other collaboratorsEnrolling by invitationPrimary Hyperoxaluria Type 3 | Diabetes Mellitus | Hemophilia A | Hemophilia B | Hereditary Fructose Intolerance | Cystic Fibrosis | Factor VII Deficiency | Phenylketonurias | Sickle Cell Disease | Dravet Syndrome | Duchenne Muscular Dystrophy | Prader-Willi Syndrome | Fragile X Syndrome | Chronic Granulomatous Disease and other conditionsUnited States
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William Beaumont HospitalsWithdrawnDeep Vein Thrombosis | Vascular Access Complication | Central Line Complication | Superficial Vein Thrombosis | Central Line-Associated InfectionUnited States
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Columbia UniversityCompletedCentral Line Complication | Neonatal DiseaseUnited States
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Leigh R. Hochberg, MD, PhD.National Institute of Neurological Disorders and Stroke (NINDS); US Department... and other collaboratorsRecruitingAmyotrophic Lateral Sclerosis | Muscular Dystrophy | Spinal Cord Injuries | Tetraplegia | Brain Stem Infarctions | Locked in SyndromeUnited States
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M.D. Anderson Cancer CenterNot yet recruitingMesonephric-like AdenocarcinomaUnited States
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University of Texas Southwestern Medical CenterDonald W. Reynolds FoundationCompletedMyocardial Infarction | Hypertension | Obesity | Diabetes Mellitus | Atherosclerosis | Congestive Heart Failure | Metabolic Syndrome X | Left Ventricular HypertrophyUnited States
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University of VirginiaUniversity of TennesseeCompletedInitial Efficacy of Quit Line | Efficacy of Secondary Reengagement InterventionUnited States
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National Human Genome Research Institute (NHGRI)RecruitingMetabolic Disease | Purine-Pyrimidine Metabolism | AICDA, OMIM *605257, Immunodeficiency With Hyper-IgM, Type 2; HIGM2 | UNG, OMIM *191525, Hyper-IgM Syndrome 5 | NT5C3A<TAB>, OMIM *606224, Anemia, Hemolytic, Due to UMPH1 Deficiency | UMPS, OMIM *613891, Orotic Aciduria | DHODH, OMIM *126064,... and other conditionsUnited States
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Leigh R. Hochberg, MD, PhD.National Institute on Deafness and Other Communication Disorders (NIDCD)RecruitingAmyotrophic Lateral Sclerosis | Muscular Dystrophies | Spinal Cord Injuries | Tetraplegia | Dysarthria | Brain Stem Infarctions | Locked in Syndrome | AnarthriaUnited States
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Emory UniversityChildren's Healthcare of AtlantaTerminatedSickle Cell Disease | Fanconi Anemia | Thalassemia | Severe Congenital Neutropenia | Wiskott-Aldrich Syndrome | Diamond-Blackfan Anemia | Severe Aplastic Anemia | Glanzmann Thrombasthenia | Leukocyte Adhesion Deficiency | Dyskeratosis-congenita | Chediak-Higashi Syndrome | Chronic-granulomatous Disease | Schwachman-Diamond...United States
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Bill McGheeAstellas Pharma IncCompletedCentral Line Fungal InfectionsUnited States
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National Eye Institute (NEI)National Cancer Institute (NCI)RecruitingStargardt-Like Macular DystrophyUnited States
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Loulou FoundationActive, not recruitingCyclin-Dependent Kinase-Like 5 Deficiency DisorderUnited States, Spain, Italy, France, Canada, Germany, United Arab Emirates
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Case Comprehensive Cancer CenterCompletedMyelodysplastic Syndromes | Thrombocytopenia | Chronic Myelomonocytic Leukemia | de Novo Myelodysplastic Syndromes | Refractory Anemia | Refractory Anemia With Excess Blasts | Refractory Cytopenia With Multilineage Dysplasia | Refractory Anemia With Ringed SideroblastsUnited States
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National Institute of Diabetes and Digestive and...Vidacare CorporationWithdrawnCatheters, Indwelling | Central Venous Line | Intraosseous NeedleUnited States
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Astellas Pharma Global Development, Inc.RecruitingAcute Myeloid Leukemia (AML) | Acute Myeloid Leukemia With FMS-like Tyrosine Kinase 3 (FLT3) Mutation / Internal Tandem Duplication (ITD)United States, Canada, Germany, Italy, Spain, United Kingdom, France
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National Cancer Institute (NCI)CompletedChronic Myelomonocytic Leukemia | Previously Treated Myelodysplastic Syndromes | Secondary Myelodysplastic Syndromes | de Novo Myelodysplastic Syndromes | Refractory Anemia | Refractory Anemia With Excess Blasts | Refractory Anemia With Excess Blasts in Transformation | Refractory Anemia With Ringed...United States
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Sanford HealthNational Ataxia Foundation; Beyond Batten Disease Foundation; Pitt Hopkins Research... and other collaboratorsRecruitingMitochondrial Diseases | Retinitis Pigmentosa | Myasthenia Gravis | Eosinophilic Gastroenteritis | Multiple System Atrophy | Leiomyosarcoma | Leukodystrophy | Anal Fistula | Spinocerebellar Ataxia Type 3 | Friedreich Ataxia | Kennedy Disease | Lyme Disease | Hemophagocytic Lymphohistiocytosis | Spinocerebellar Ataxia... and other conditionsUnited States, Australia
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Natera, Inc.Children's Hospital of Philadelphia; Montefiore Medical Center; University of... and other collaboratorsCompletedPrader-Willi Syndrome | DiGeorge Syndrome | 22q11 Deletion Syndrome | Angelman Syndrome | Trisomy 21 | Trisomy 18 | Trisomy 13 | Monosomy X | Sex Chromosome Abnormalities | 1p36 Deletion Syndrome | Cri-du-Chat SyndromeUnited States, Australia, Ireland, Spain, Sweden, United Kingdom