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Search clinical trials for: Wolman Disease (early onset LAL Deficiency)
Total 379856 results
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Clinique Dentaire et d'implantologie Dr.Vinh NguyenGoethe UniversityUnknown
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Cairo UniversityUnknown
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Cairo UniversityUnknownSoft Tissue Augmentation | Ridge Deficency
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Laval UniversityCompleted
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McGill University Health Centre/Research Institute...Merck Sharp & Dohme LLCWithdrawn
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University of PennsylvaniaInternational Foundation for CDKL5 Research; Loulou Foundation; CDKL5 AllianceRecruiting
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Damascus UniversityCompletedSkeletal Maxillary Transverse DeficiencySyrian Arab Republic
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Cairo UniversityActive, not recruitingTransverse Maxillary DeficiencyEgypt
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Cairo UniversityActive, not recruitingTransverse Maxillary DeficiencyEgypt
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TC Erciyes UniversityCompletedTransverse Maxillary DeficiencyTurkey
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TC Erciyes UniversityCompletedTransverse Maxillary DeficiencyTurkey
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Assistance Publique - Hôpitaux de ParisCompletedIntellectual Deficiency | Cerebral AbnormalityFrance
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University of Turin, ItalyCompletedMaxillary Transverse Deficiency (MTD)Italy
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Population Health Research InstituteCanadian Institutes of Health Research (CIHR)RecruitingCalcium Release Deficiency Syndrome (CRDS)United States, Israel, Canada, Belgium, Denmark, France, United Kingdom
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Mendel TuchmanChildren's Hospital of Philadelphia; University of California, Los Angeles; Icahn... and other collaboratorsCompletedMethylmalonic Acidemia | Carbamoyl-Phosphate Synthase I Deficiency Disease | Propionic Acidemia, Type I and/or Type II | Ornithine Carbamoyltransferase DeficiencyUnited States
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Cairo UniversityNot yet recruitingSocket Preservation, Alveolar Ridge Deficiency, Alveolar Ridge Preservation
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Lei LiUnknownEpithelial Ovarian Cancer | Homologous Recombination Deficiency | Prognosis | BRCA Mutation | Loss of Heterozygosity | Platinum ResistanceChina
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Memorial Sloan Kettering Cancer CenterMerck Sharp & Dohme LLCRecruitingMetastatic Pancreatic Ductal Adenocarcinoma | Homologous Recombination Deficiency (HRD)United States
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Istanbul Medeniyet UniversityCompletedEpilepsy | Ischemic Stroke | Hyperhomocysteinemia, Thrombotic, Cbs-RelatedTurkey
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Peking University Third HospitalChina Academy of Chinese Medical Sciences; Beijing University of Chinese Medicine and other collaboratorsRecruitingYin Deficiency SyndromeChina
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Lei LiCompletedEpithelial Ovarian Cancer | BRCA1 Mutation | BRCA2 Mutation | Homologous Recombination Deficiency | Prognosis | Chinese | Homologous Recombination GenesChina
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University Hospital, CaenCompleted
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GCS Ramsay Santé pour l'Enseignement et la RechercheRecruitingACL - Anterior Cruciate Ligament DeficiencyFrance
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Hospital of South West JutlandCompletedQuality of Life | Fatigue | Iron-deficiency | Cognitive Impairment | Colorectal Cancer | Iron Deficiency AnemiaDenmark
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First Affiliated Hospital Xi'an Jiaotong UniversitySimcere CompanyRecruitingCerebral Infarction | G6PD DeficiencyChina
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HaEmek Medical Center, IsraelCompleted
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Fudan UniversityNot yet recruitingHomologous Recombination Deficiency Alterations Metastatic Colorectal CancerChina
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Hospital Universitario Pedro ErnestoCompletedMalocclusion | Transverse Maxillary Deficiency | Maxillar HypoplasiaBrazil
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Spital ZollikerbergViollier Inc.CompletedFunctional Iron DeficiencySwitzerland
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VIFORFRANCEUnknown
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University of Alabama at BirminghamActive, not recruitingDental Implant | Ridge Deficency | Bone Graft; Complications, Infection or InflammationUnited States
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AlexionCompletedWolman Disease | Lysosomal Acid Lipase DeficiencyUnited States, Canada, United Kingdom, Italy, France
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PATHBill and Melinda Gates Foundation; Centre National de Greffe de Moelle Osseuse and other collaboratorsNot yet recruitingPrimary Immunodeficiency DiseasesTunisia
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The Hospital for Sick ChildrenBristol-Myers SquibbTerminatedRefractory or Recurrent Hypermutated Malignancies | Biallelic Mismatch Repair Deficiency (bMMRD) Positive PatientsUnited States, France, Canada, Australia, Israel
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University Hospital, Clermont-FerrandUnknownIron Deficiency AnemiaFrance
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Hospital Universitario de CanariasUnknownColorectal CancerSpain
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University of AlbertaGeistlich Pharma AGWithdrawnThin Gingiva | Transverse Maxillary Deficiency | Cross BiteCanada
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Alexion PharmaceuticalsCompletedLysosomal Acid Lipase Deficiency | Cholesterol Ester Storage Disease(CESD)United States, United Kingdom, France, Canada, Czech Republic, Italy, Poland, Switzerland
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Alexion PharmaceuticalsCompletedLysosomal Acid Lipase Deficiency | LAL-Deficiency | Cholesterol Ester Storage Disease (CESD)France, United Kingdom, United States, Canada, Czechia
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Baxter Healthcare CorporationCompletedEssential Fatty Acid Deficiency (EFAD)United States
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Baxter Healthcare CorporationTerminatedEssential Fatty Acid Deficiency (EFAD)United States
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University Hospital, CaenInstitut National de la Santé Et de la Recherche Médicale, FranceUnknownACL Tear | ACL - Anterior Cruciate Ligament DeficiencyFrance
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The University of Hong KongNot yet recruitingCOVID19 | Herbal MedicineHong Kong
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Fujian Cancer HospitalFujian Provincial HospitalNot yet recruiting
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Casa Sollievo della Sofferenza IRCCSUniversity of Bari; University of FoggiaActive, not recruitingAnemia | Bleeding | Placenta Diseases | Pregnancy Anemia | Transfusion-dependent Anemia | Pregnancy Bleeding | Transfusion; Embolism, ThrombusItaly
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GCS Ramsay Santé pour l'Enseignement et la RechercheRecruitingACL - Anterior Cruciate Ligament DeficiencyFrance
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AstraZenecaActive, not recruitingSolid TumorsBelgium, United Kingdom, Switzerland, Australia
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Beijing University of Chinese MedicineDongzhimen Hospital, Beijing; Hubei Hospital of Traditional Chinese Medicine; Wuhan Hospital of Traditional Chinese Medicine and other collaboratorsCompleted
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Alexion PharmaceuticalsCompletedLysosomal Acid Lipase Deficiency | Cholesterol Ester Storage Disease(CESD) | LAL-DeficiencyFrance, United States, United Kingdom, Czechia
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Federico II UniversityCompletedHeart Failure | Ischemic Heart Disease | Growth Hormone Deficiency | CardiomyopathyItaly