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Clinical Trials on Academic Attainment in Korea, Republic of
Totalt 8 resultater
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National Human Genome Research Institute (NHGRI)RekrutteringMedfødte stoffskiftefeil | Methylmalonic acidemi | Organisk acidemiForente stater
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Recordati Rare DiseasesTarget PharmaSolutions, Inc.RekrutteringPropionsyreacidemi | Methylmalonic acidemi | HyperammonemiForente stater
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Mendel TuchmanUniversity of Colorado, Denver; Children's Hospital of Philadelphia; University... og andre samarbeidspartnereAvsluttetPropionsyreacidemi | Methylmalonic acidemiForente stater
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HemoShear TherapeuticsAvsluttetPropionsyreacidemi | Methylmalonic acidemiForente stater, Saudi-Arabia, Australia
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Mendel TuchmanChildren's Hospital of Philadelphia; University of California, Los Angeles og andre samarbeidspartnereFullførtMethylmalonic acidemi | Karbamoyl-fosfatsyntase I mangelsykdom | Propionsyre, Type I og/eller Type II | Ornithine Carbamoyltransferase mangelForente stater
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Children's National Research InstituteNational Center for Advancing Translational Sciences (NCATS)RekrutteringHypoksisk-iskemisk encefalopati | Urea syklus lidelse | Organisk acidemi | Fettsyreoksidasjonsforstyrrelse | Lønnesirup urinsykdom | Glutarsyre IForente stater
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Uta Lichter-KoneckiMedical College of Wisconsin; Children's National Research InstituteFullførtUreasyklusforstyrrelser | Organiske acidemierForente stater
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ModernaTX, Inc.RekrutteringPropionsyreacidemiForente stater, Spania, Nederland, Frankrike, Storbritannia, Australia, Canada, Italia