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Clinical Trials on Genetics/Birth Defects in Canada
Total 2421 results
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Auspex Pharmaceuticals, Inc.CompletedChorea Associated With Huntington DiseaseUnited States, Australia, Canada
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Novartis PharmaceuticalsWithdrawnBasal Cell CarcinomaGreece, Switzerland, Germany, United Kingdom, Belgium, Canada, Czechia, Finland, Italy, Spain
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Fundación Pública Andaluza Progreso y SaludCompletedArteriovenous Fistula Renal Dialysis Devices ObstructionSpain
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Pharnext SACompletedPhase III Trial Assessing the Efficacy and Safety of PXT3003 in CMT1A Patients (PLEO-CMT) (PLEO-CMT)Charcot-Marie-Tooth Disease Type 1AUnited States, United Kingdom, Belgium, Canada, France, Netherlands, Spain, Germany
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Hoffmann-La RocheRecruitingHuntington DiseaseUnited States, Australia, Argentina, Canada, Germany, Italy, France, United Kingdom, Spain, Portugal, New Zealand, Austria, Poland, Switzerland, Denmark
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Canadian Cancer Trials GroupQueen's University, Belfast; Survivorship Research GroupActive, not recruitingDepression | Fatigue | Colorectal Cancer | Sleep Disorders | Cognitive/Functional Effects | Anxiety Disorder | Psychosocial Effects of Cancer and Its Treatment | ExcerciseCanada, United States, Australia, France, Korea, Republic of, United Kingdom
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POINT BiopharmaActive, not recruitingSoft Tissue Sarcoma | Colorectal Cancer | Esophageal Cancer | Cholangiocarcinoma | Head and Neck Squamous Cell Carcinoma | Pancreatic Ductal Adenocarcinoma | Melanoma (Skin)United States, Canada
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ShireTakeda Development Center Americas, Inc.Active, not recruitingMetachromatic Leukodystrophy (MLD)United States, Canada, Belgium, Israel, Netherlands, United Kingdom, Germany, Spain, Japan, Brazil, Argentina, France, Greece, Italy
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KalVista Pharmaceuticals, Ltd.CompletedHereditary AngioedemaUnited States, Australia, Bulgaria, Canada, France, Germany, Greece, Hungary, Israel, Italy, Japan, Netherlands, New Zealand, North Macedonia, Poland, Portugal, Puerto Rico, Romania, Slovakia, Spain, United Kingdom
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Cook Research IncorporatedCompletedDigestive System Abnormalities | Esophageal Atresia | Esophageal Disorders CongenitalUnited States, Canada
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McMaster UniversityCanadian Institutes of Health Research (CIHR); Hamilton Health Sciences Corporation and other collaboratorsRecruitingSingle Dose of Antenatal Corticosteroids for Pregnancies at Risk of Preterm Delivery (SNACS) (SNACS)Premature Birth | Pregnancy Complications | Preterm Birth | Obstetric Labor, Premature | Complication of PrematurityCanada, Australia
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Novartis PharmaceuticalsCompletedOsteoporosisAustralia, Canada, Russian Federation, Hungary, South Africa, United Kingdom
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Canadian Critical Care Trials GroupCanadian Institutes of Health Research (CIHR); McMaster University; University...CompletedAcute Respiratory Distress SyndromeCanada, Saudi Arabia
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Horizon Health NetworkMcGill University; University of Michigan; Carilion Clinic; Lawson Health Research... and other collaboratorsCompleted
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National Tuberous Sclerosis AssociationRecruitingTuberous Sclerosis | LymphangioleiomyomatosisUnited States, Canada
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Rhythm Pharmaceuticals, Inc.Active, not recruitingGenetic ObesityUnited States, Spain, Netherlands, Germany, United Kingdom, Canada, Israel, Greece
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KalVista Pharmaceuticals, Ltd.RecruitingHereditary AngioedemaUnited States, Bulgaria, France, Greece, Hungary, Israel, Italy, Netherlands, New Zealand, North Macedonia, Poland, Spain, United Kingdom, Australia, Germany, South Africa, Austria, Portugal, Slovakia, Romania, Canada, Saudi Arabia, Japa...
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Alnylam PharmaceuticalsCompletedAmyloid Neuropathies | Amyloid Neuropathies, Familial | TTR-mediated Amyloidosis | Amyloidosis, Hereditary | Amyloidosis, Hereditary, Transthyretin-Related | Familial Amyloid PolyneuropathiesUnited States, Canada, Argentina, Australia, Bulgaria, Cyprus, Italy, Japan, Malaysia, Mexico, Netherlands, Portugal, Spain, Sweden, Germany, France, Brazil, Turkey, Korea, Republic of, Taiwan, United Kingdom
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Emalex Biosciences Inc.CompletedTourette Syndrome in Children | Tourette Syndrome in AdolescenceUnited States, Poland, France, Canada, Germany
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KalVista Pharmaceuticals, Ltd.TerminatedAngioedema, Hereditary, Types I and IIUnited States, Czechia, Germany, Hungary, Italy, North Macedonia, United Kingdom, Australia, Bulgaria, Canada, France, New Zealand, Puerto Rico
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Radiation Therapy Oncology GroupNational Cancer Institute (NCI); NRG OncologyCompletedSexual Dysfunction | Prostate Cancer | Radiation Toxicity | Psychosocial Effects of Cancer and Its TreatmentUnited States, Canada
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Kyowa Kirin Pharmaceutical Development LtdCompletedX-Linked HypophosphatemiaFrance, United Kingdom, Spain, Germany, Netherlands
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University of MinnesotaUniversity of Manitoba; University of Alberta; McGill University Health Centre...CompletedCoronavirus Infections | Acute Respiratory Distress Syndrome | Corona Virus Infection | SARS-CoV Infection | CoronavirusUnited States, Canada
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University College CorkInstitut National de la Santé Et de la Recherche Médicale, France; KU Leuven; University of Alberta and other collaboratorsTerminatedHypotension | Low Blood Pressure | Intraventricular Hemorrhage of PrematurityCanada, Ireland, Belgium, Czechia, United Kingdom
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Children's Oncology GroupNational Cancer Institute (NCI)CompletedKidney CancerUnited States, Canada, Puerto Rico, Australia, Netherlands, Switzerland, New Zealand
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GlaxoSmithKlineTerminatedTelangiectasia, Hereditary HemorrhagicUnited States, Canada
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Children's Oncology GroupNational Cancer Institute (NCI)CompletedKidney CancerUnited States, Canada, Puerto Rico, Australia, Netherlands, New Zealand, Switzerland
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Alnylam PharmaceuticalsActive, not recruitingTransthyretin Amyloidosis (ATTR) With CardiomyopathyUnited States, Poland, Argentina, Australia, Belgium, France, Germany, Japan, Netherlands, Portugal, Spain, Sweden, United Kingdom, Canada, Czechia, Denmark, Hungary, Ireland, Norway, Korea, Republic of, Austria, Croatia, Israel, Latvia, Lithuan... and more
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Ardea Biosciences, Inc.CompletedHyperuricemiaPoland, United States, Canada, Bulgaria, Germany, Georgia, Czech Republic
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National Cancer Institute (NCI)WithdrawnHematopoietic and Lymphoid Cell Neoplasm | Lynch Syndrome | Refractory Lymphoma | Refractory Malignant Solid Neoplasm | Recurrent Lymphoma | Recurrent Malignant Solid Neoplasm | Recurrent Neuroblastoma | Refractory Neuroblastoma | Recurrent Primary Central Nervous System Neoplasm | Refractory Primary Central... and other conditionsUnited States, Canada
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Marinus PharmaceuticalsEnrolling by invitationTuberous Sclerosis ComplexUnited States, Spain, United Kingdom, China, Italy, France, Israel, Germany, Canada, Australia
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Ravindra MehtaInternational Serious Adverse Event ConsortiumCompletedAcute Kidney Injury | Kidney Failure | Acute Kidney Failure | Kidney Disease | Adverse Drug ReactionUnited States, United Kingdom, Chile, Bolivia, Canada, India
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International Spine Study Group FoundationMedtronic; Globus Medical Inc; SI-BONE, Inc.RecruitingScoliosis | Kyphosis | Adult Spinal Deformity | Sagittal ImbalanceUnited States, Canada
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University Hospital, GasthuisbergThe University of Texas Health Science Center, Houston; Hospital Clinic of... and other collaboratorsCompletedCongenital Diseases | Pulmonary Hypoplasia | Diaphragmatic HerniaUnited Kingdom, Canada, United States, Belgium, Italy, Germany, France, Japan, Australia, Poland, Spain
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Cancer Prevention Pharmaceuticals, Inc.CompletedFamilial Adenomatous PolyposisUnited States, Belgium, Germany, Canada, Netherlands, Spain, United Kingdom
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Amicus TherapeuticsActive, not recruitingPompe Disease (Late-onset)United States, Germany, Taiwan, Belgium, Australia, Slovenia, Spain, Netherlands, Hungary, Japan, Austria, United Kingdom, France, Argentina, Canada, Sweden, Denmark, New Zealand, Greece, Korea, Republic of, Bosnia and Herzegovina, Ita... and more
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Otsuka Pharmaceutical Development & Commercialization...CompletedTic Disorder | Tourette's DisorderUnited States, Germany, Spain, Mexico, Romania, Canada, Hungary, Italy, Sweden
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Hoffmann-La RocheCompletedHuntingtons DiseaseUnited States, United Kingdom, Australia, Canada, Japan, Poland, Netherlands, Germany, Russian Federation, France, Spain, Argentina, New Zealand, Austria, Denmark, Italy, Switzerland, Chile
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ShireCompletedHereditary Angioedema (HAE)United States
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Alexion Pharmaceuticals, Inc.TerminatedWilson DiseaseUnited States, Spain, Taiwan, France, Czechia, Hungary, Turkey, United Kingdom, Austria, Germany, Israel, Serbia, Australia, Japan, Denmark, Korea, Republic of, New Zealand, Canada, Russian Federation, Poland, Singapore, Hong Kong
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Hospital for Special Surgery, New YorkThe Hospital for Sick Children; Boston Children's Hospital; Nicklaus Children... and other collaboratorsWithdrawnCerebral Palsy | Hip DysplasiaUnited States, Canada
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University Hospital, GasthuisbergThe University of Texas Health Science Center, Houston; Baylor College of Medicine and other collaboratorsCompletedCongenital Diaphragmatic Hernia | Pulmonary Hypoplasia | Fetal SurgeryUnited Kingdom, Canada, United States, Belgium, Germany, Italy, France, Australia, Poland, Spain
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Genzyme, a Sanofi CompanyCompletedGlycogen Storage Disease Type II (GSD-II) | Pompe Disease (Late-Onset) | Glycogenesis Type II | Acid Maltase Deficiency (AMD)United States, France, Canada, Netherlands, Australia
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Otsuka Pharmaceutical Development & Commercialization...CompletedPolycystic Kidney, Autosomal DominantBelgium, Germany, Italy, Spain, Sweden, United States, Canada, Australia, Netherlands, Czechia, Poland, Denmark, Israel, Hungary, Russian Federation, South Africa, United Kingdom, Romania, Argentina, Norway
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Pharvaris Netherlands B.V.Active, not recruitingHereditary Angioedema | Hereditary Angioedema Type I | Hereditary Angioedema Type II | Hereditary Angioedema Types I and II | Hereditary Angioedema Attack | Hereditary Angioedema With C1 Esterase Inhibitor Deficiency | Hereditary Angioedema - Type 1 | Hereditary Angioedema - Type 2 | C1 Esterase Inhibitor... and other conditionsUnited States, Poland, Germany, Austria, Bulgaria, Canada, Ireland, Italy, United Kingdom
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Novartis Gene TherapiesActive, not recruitingSMA | Spinal Muscular Atrophy Type II | Spinal Muscular Atrophy Type I | Spinal Muscular Atrophy Type IIIUnited States, Belgium, France, Japan, United Kingdom, Italy, Taiwan, Australia, Canada
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CSL BehringChiltern International Inc.CompletedIncludes: Hereditary AngioedemaUnited States, Denmark, Germany, Switzerland
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University of WashingtonNational Heart, Lung, and Blood Institute (NHLBI); American Thoracic Society; American Society for Parenteral and Enteral Nutrition and other collaboratorsCompletedAcute Respiratory Distress Syndrome | Acute Lung Injury | Respiratory Distress Syndrome, AdultUnited States, Canada
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Ozlem SahinUnknownTuberculosis | SarcoidosisTurkey
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University of British ColumbiaUniversity of Pennsylvania; Wuhan University; Canadian Institutes of Health Research... and other collaboratorsUnknownCOVID-19 | SARS-CoV2Canada