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Search clinical trials for: Brain Diseases, Metabolic, Inborn
Total 48136 results
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Hospices Civils de LyonNot yet recruitingWilson DiseaseFrance
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TakedaRecruitingDravet Syndrome (DS) | Lennox-Gastaut Syndrome (LGS)United Kingdom, Denmark
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Leiden University Medical CenterThe Dutch Brain Foundation (funding)Not yet recruitingCerebral Amyloid Angiopathy
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Poitiers University HospitalRecruiting
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Johns Hopkins UniversityNational Center for Complementary and Integrative Health (NCCIH); Bowdoin CollegeRecruitingTourette Syndrome | Tic Disorders | Tourette's Disorder | Persistent Tic Disorder | Chronic Motor Tic Disorder | Chronic Vocal Tic Disorder | Persistent Motor Tic Disorder | Persistent Vocal Tic DisorderUnited States
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Tisento TherapeuticsNot yet recruitingMitochondrial Encephalopathy, Lactic Acidosis and Stroke-Like Episodes (MELAS Syndrome)United States, Australia, Italy, Germany, Canada, United Kingdom
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TakedaNot yet recruitingDravet Syndrome (DS) | Lennox-Gastaut Syndrome (LGS)
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Steminent US, Inc.Not yet recruitingSpinocerebellar Ataxias
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Alnylam PharmaceuticalsRecruitingCerebral Amyloid AngiopathyCanada
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GeneCradle IncRecruitingPompe Disease (Late-onset)China
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University College, LondonLondon School of Hygiene and Tropical Medicine; King's College London; University... and other collaboratorsRecruitingTourette Syndrome | Deep Brain StimulationUnited Kingdom
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University of UtahRecruitingClinical Characteristics and Temporal Properties of Individual Tics in Persistent Tic Disorder (PTD)Tourette Syndrome | Tic Disorders | Tics | Tourette Syndrome in Children | Tourette Syndrome in Adolescence | Vocal Tic | Motor Tic | Tics/TremorUnited States
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The First Affiliated Hospital of Zhejiang Chinese...RecruitingInflammatory Response | Tourette Syndrome in Children | Food IntoleranceChina
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IRCCS Eugenio MedeaRecruiting
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Chang Gung UniversityRecruiting
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Xuanwu Hospital, BeijingNot yet recruiting
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IRCCS Eugenio MedeaRecruitingEpilepsy | Angelman Syndrome | Dup15q SyndromeItaly
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Huntington Study GroupRoche Products LimitedRecruitingHuntington DiseaseUnited States
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Jirair Krikor BedoyanUltragenyx Pharmaceutical IncRecruitingPyruvate Dehydrogenase Complex DeficiencyUnited States
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Rigshospitalet, DenmarkNot yet recruitingBrain Diseases | Genetic Diseases, Inborn | Metabolism, Inborn Errors | Brain Diseases, Metabolic | Phenylketonurias | Brain Diseases, Metabolic, Inborn | Amino Acid Metabolism, Inborn Errors | Metabolic DiseaseDenmark
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NGGT (Suzhou) Biotechnology Co., Ltd.Not yet recruitingPhenylketonurias
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Chiesi Farmaceutici S.p.A.ICON plcNot yet recruiting
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Caroline Michaela KistorpSanofiNot yet recruitingChronic Kidney Diseases | Fabry DiseaseDenmark
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The University of QueenslandNot yet recruitingAtaxia TelangiectasiaAustralia
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National Taiwan University HospitalRecruiting
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Noema Pharma AGNot yet recruiting
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Forge Biologics, IncNot yet recruitingKrabbe DiseaseUnited States
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BioMarin PharmaceuticalRecruitingPhenylketonuria (PKU)United States
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PTC TherapeuticsRecruitingPhenylketonuriaUnited States
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metaX Institut fuer Diatetik GmbHGreat Ormond Street Hospital for Children NHS Foundation Trust; Birmingham...Not yet recruitingAlkaptonuria | Homocystine; Metabolic Disorder | Tyrosinemia, Type I | Tyrosinemia, Type II | Tyrosinemia, Type III | MSUD (Maple Syrup Urine Disease)
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IRCCS Fondazione Stella MarisRecruitingFragile X SyndromeItaly
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Assistance Publique - Hôpitaux de ParisNot yet recruiting
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Specila hospital for cerebral palsy and developmental...FRAXA Research FoundationRecruitingFragile X SyndromeSerbia
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Meyer Children's Hospital IRCCSRecruiting
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Xinhua Hospital, Shanghai Jiao Tong University...Shanghai Vitalgen BioPharma Co., Ltd.RecruitingType II Gaucher DiseaseChina
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Karolinska InstitutetRecruitingTourette Syndrome | Chronic Tic DisorderSweden
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UniQure Biopharma B.V.RecruitingFabry DiseaseUnited States
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Central Hospital, Nancy, FranceRecruiting
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Université du Québec à ChicoutimiMcGill University; Université de Sherbrooke; University of Alberta; University... and other collaboratorsRecruitingAutosomal Recessive Spastic Ataxia of Charlevoix-Saguenay | Spastic Paraplegia 7Canada
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Université de SherbrookeCanadian Institutes of Health Research (CIHR); Centre de recherche du Centre... and other collaboratorsNot yet recruitingFragile X Syndrome
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Brunel UniversityRoyal Free Hospital NHS Foundation TrustRecruiting
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Chung-Hsing WangSanofiNot yet recruiting
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iECURE, Inc.RecruitingUrea Cycle Disorders, Inborn | Ornithine Transcarbamylase Deficiency | Ornithine Transcarbamylase Deficiency Disease | Ornithine Carbamoyltransferase Deficiency (Disorder)United Kingdom
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PTC TherapeuticsRecruitingHuntington DiseaseAustralia, France, Germany, Netherlands, United Kingdom, Spain, Austria, Canada, Italy, New Zealand
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Travere Therapeutics, Inc.Recruiting
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Rolfs Consulting und Verwaltungs-GmbH (RCV)Rhythm Pharmaceuticals, Inc.RecruitingCognitive Impairment | Hyperphagia | Obesity, Childhood | Bardet-Biedl Syndrome | Polydactyly | Retinopathy | Syndactyly | POMC DeficiencyGermany
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Children's Hospital Medical Center, CincinnatiEunice Kennedy Shriver National Institute of Child Health and Human Development...RecruitingAutism Spectrum Disorder | Autistic Disorder | Fragile X Syndrome | Asperger SyndromeUnited States
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Swedish Orphan BiovitrumRecruitingHereditary Tyrosinemia, Type IChina
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University of CambridgeSanofiRecruiting
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bluebird bioCenter for International Blood and Marrow Transplant ResearchRecruitingCerebral Adrenoleukodystrophy (CALD)United States