- ICH GCP
- US Clinical Trials Registry
- Search trials
Search clinical trials for: miglustat
Total 33 results
-
Amicus TherapeuticsRecruitingPompe DiseaseUnited States
-
Amicus TherapeuticsRecruitingGlycogen Storage Disease Type II Infantile OnsetTaiwan, United States, France, Germany, Italy, United Kingdom
-
Amicus TherapeuticsRecruitingPompe Disease (Late-onset)United States, Taiwan, Japan, Australia, Canada
-
Tehran University of Medical SciencesMashhad University of Medical Sciences; Kashan University of Medical SciencesRecruitingEffects of Miglustat Therapy on Infantile Type of Sandhoff and Taysachs Diseases (EMTISTD) (EMTISTD)Supportive Care | GM2 GangliosidosisIran, Islamic Republic of
-
Beyond Batten Disease FoundationTheranexusActive, not recruitingBatten DiseaseUnited States
-
Amicus TherapeuticsActive, not recruitingPompe DiseaseUnited States, Netherlands, United Kingdom, Australia, Germany, New Zealand
-
Amicus TherapeuticsActive, not recruitingPompe Disease (Late-onset)United States, Germany, Taiwan, Belgium, Australia, Slovenia, Spain, Netherlands, Hungary, Japan, Austria, United Kingdom, France, Argentina, Canada, Sweden, Denmark, New Zealand, Greece, Korea, Republic of, Bosnia and Herzegovina, Ita... and more
-
University of SurreyThe Whiteley ClinicCompletedVaricose VeinsUnited Kingdom
-
Amicus TherapeuticsCompletedPompe Disease (Late-onset)United States, Australia, Korea, Republic of, Japan, Taiwan, Belgium, Slovenia, New Zealand, United Kingdom, France, Argentina, Canada, Spain, Bosnia and Herzegovina, Germany, Sweden, Hungary, Austria, Bulgaria, Denmark, Greece, I... and more
-
ActelionCompleted
-
IRCCS Fondazione Stella MarisCompletedHereditary Spastic ParaparesisItaly
-
University of MinnesotaNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK); National... and other collaboratorsTerminatedTay-Sachs Disease | Sandhoff Disease | GM1 Gangliosidoses | GM2 GangliosidosesUnited States
-
National Taiwan University HospitalActelionUnknown
-
University of FloridaAmicus TherapeuticsTerminatedPompe Disease | Hypersensitivity Reaction
-
ActelionCompletedGaucher Disease Type 1United States, Taiwan, Canada, Spain, Australia, France, Brazil, Hungary, Czechia, Germany, Italy, Netherlands, United Kingdom
-
University of New MexicoUniversity of Pittsburgh; Dialysis Clinic, Inc.TerminatedHypertension | Proteinuria | Type II DiabetesUnited States
-
Assistance Publique - Hôpitaux de ParisActelion; CRCM (Centres de Ressources et de Compétences de la Mucoviscidose)Completed
-
University of FloridaCompletedPompe DiseaseUnited States
-
National Institute of Neurological Disorders and...CompletedGaucher DiseaseUnited States, United Kingdom
-
National Eye Institute (NEI)CompletedNiemann Pick DiseasesUnited States, United Kingdom
-
The Hospital for Sick ChildrenActelionCompletedGangliosidoses GM2Canada
-
Laboratorio Pablo Cassará S.R.L.National Council of Scientific and Technical Research, Argentina; Fundacion... and other collaboratorsUnknownCutaneous MelanomaArgentina
-
National Taiwan University HospitalCompleted
-
Cliniques universitaires Saint-Luc- Université...Completed
-
ActelionCompleted
-
University of WashingtonEunice Kennedy Shriver National Institute of Child Health and Human Development...CompletedContraceptionUnited States
-
Children's National Research InstituteActelionCompletedSandhoff Disease | GM2 Gangliosidoses | Tay-SachsUnited States
-
G D SearleCompleted
-
G D SearleNational Institute of Allergy and Infectious Diseases (NIAID)Completed