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The Study of Brave-LC LDN Treatment Trial

Brave-LC: A Phase 3 Randomized Double-blind, Placebo-controlled Trial to Evaluate the Efficacy of a 16-week Course of Low-dose Naltrexone to Reduce Fatigue Severity in Persons Aged 6 Through 25 Years With Long COVID

This is a randomized, double-blind, placebo-controlled Phase 3 trial evaluating the efficacy and safety of a 16-week course of low-dose naltrexone (LDN) in approximately 1,300 participants aged 6 to 25 years with fatigue associated with Long COVID. Participants will be enrolled across three age cohorts (6-11, 12-17, and 18-25 years) and randomized 1:1 to receive LDN capsules or matching placebo capsules. LDN will be initiated at 1.5 mg daily and titrated weekly to a maximum tolerated dose of up to 4.5 mg daily. Randomization will be stratified by age cohort, and participants will also be randomized to a pharmacokinetic (PK) sampling window. Primary objective is to compare the change in fatigue severity from baseline to 16 weeks between participants aged 6 to 25 years with Long COVID randomized to a 16-week course of LDN or placebo.

Panoramica dello studio

Stato

Non ancora reclutamento

Condizioni

Intervento / Trattamento

Descrizione dettagliata

This is a randomized, double-blind, placebo-controlled Phase 3 trial evaluating the efficacy and safety of a 16-week course of low-dose naltrexone (LDN) in approximately 1,300 participants aged 6 to 25 years with fatigue associated with Long COVID. Participants will be enrolled across three age cohorts (6-11, 12-17, and 18-25 years) and randomized 1:1 to receive LDN capsules or matching placebo capsules. LDN will be initiated at 1.5 mg daily and titrated weekly to a maximum tolerated dose of up to 4.5 mg daily. Randomization will be stratified by age cohort, and participants will also be randomized to a pharmacokinetic (PK) sampling window. Primary objective is to compare the change in fatigue severity from baseline to 16 weeks between participants aged 6 to 25 years with Long COVID randomized to a 16-week course of LDN or placebo. Secondary objectives: To compare the change in fatigue severity from baseline to 16 weeks between participants with Long COVID in age groups: 6 to 11 years, 12 to 17 years and 18-25 years. Each participant will be randomized to a 16-week course of LDN or placebo.

Tipo di studio

Interventistico

Iscrizione (Stimato)

1300

Fase

  • Fase 3

Contatti e Sedi

Questa sezione fornisce i recapiti di coloro che conducono lo studio e informazioni su dove viene condotto lo studio.

Contatto studio

Luoghi di studio

    • Alabama
      • Birmingham, Alabama, Stati Uniti, 35233-0011
        • Children's of Alabama Child Health Research Unit (CHRU)
    • California
      • Chula Vista, California, Stati Uniti, 91910
        • Exalt Clinical Research Inc.
    • Colorado
      • Denver, Colorado, Stati Uniti, 80204-4506
        • Denver Health
    • Florida
      • Gainesville, Florida, Stati Uniti, 32610
        • University of Florida Health
    • Illinois
      • Chicago, Illinois, Stati Uniti, 60612
        • Rush University Medical Center
    • Maryland
      • Baltimore, Maryland, Stati Uniti, 21205
        • Kennedy Krieger Institute
    • Massachusetts
      • Boston, Massachusetts, Stati Uniti, 02115-6110
        • Brigham and Women's Hospital
      • Worcester, Massachusetts, Stati Uniti, 01655
        • University of Massachusetts Chan Medical School
    • New Hampshire
      • Lebanon, New Hampshire, Stati Uniti, 03756-1000
        • Dartmouth Health
    • New Jersey
      • New Brunswick, New Jersey, Stati Uniti, 08901-1935
        • Rutgers Robert Wood Johnson Medical School
    • New York
      • Brooklyn, New York, Stati Uniti, 11220
        • NYU Langone Hospital - Brooklyn
      • New York, New York, Stati Uniti, 10032
        • Columbia University
    • Texas
      • Houston, Texas, Stati Uniti, 77030
        • Baylor College of Medicine

Criteri di partecipazione

I ricercatori cercano persone che corrispondano a una certa descrizione, chiamata criteri di ammissibilità. Alcuni esempi di questi criteri sono le condizioni generali di salute di una persona o trattamenti precedenti.

Criteri di ammissibilità

Età idonea allo studio

Da 6 anni a 25 anni (Bambino, Adulto)

Accetta volontari sani

No

Sessi ammissibili allo studio

Tutto

Descrizione

Inclusion Criteria:

  1. Aged 6 to 25 years, inclusive, at the time of randomization.

  2. Fluent in English and/or Spanish.

  3. History of SARS CoV 2 infection shown by (1) a positive nucleic acid amplification test (NAAT) or antigen test, OR (2) meeting clinical criteria* AND an epidemiologic link** to a confirmed case.

    *Clinical criteria is defined as either (1) acute onset of fever AND cough; OR (2) acute altered/loss of taste or smell + one additional symptom including: fever, cough, general weakness/fatigue, headache, myalgia, sore throat, coryza, dyspnea, nausea, diarrhea, or anorexia; OR (3) three or more symptoms, including fever, cough, general weakness/fatigue, headache, myalgia, sore throat, coryza, dyspnea, nausea, diarrhea, or anorexia.

    • Epidemiologic link is defined as having contact (within 6 feet for at least 15 minutes) with someone sick with SARS CoV 2 test-positive COVID 19 illness.
  4. Clinical evidence of Long COVID* and Long COVID symptoms that cannot be attributed to another cause upon investigator review of medical history and workup participant received prior to study entry.

    *Participants must meet the 2024 National Academies of Sciences, Engineering, and Medicine definition for Long COVID.

  5. Has new fatigue*, ** that began either during or in the six months following the onset of the qualifying SARS CoV 2 infection or COVID 19 illness (see inclusion Criterion #3):

    *New fatigue symptoms can fluctuate but the total duration of fatigue must be at least 3 months at time of randomization and fatigue must be present for more days than not in the 30 days prior to randomization.

    **For this trial, fatigue is defined as having physical fatigue and/or cognitive fatigue (e.g., has trouble with memory, focus/attention, or decision-making, or is slow to process information, and is sometimes referred to as having "brain fog"). Fatigue is a persistent state of physical and/or cognitive exhaustion that is not substantially alleviated by sleep or rest, and that interferes with normal functioning, is often profound, and is not the result of ongoing or unusual excessive exertion.

  6. Has at least one new or worsening symptom*, ** that began either during or in the six months following the onset of the qualifying SARS CoV 2 infection or COVID 19 illness:

    *List of qualifying symptoms include: systemic symptoms (chills, Post-Exertional Malaise [PEM]); neurological symptoms (headache, dysautonomia/ Postural Orthostatic Tachycardia Syndrome [POTS], dizziness, unsteadiness, or neuropathy); sleep disturbance resulting in unrefreshing sleep; cardiopulmonary symptoms (chest pain, palpitations, shortness of breath, cough, fainting spells); musculoskeletal symptoms (muscle pain/aches, neck pain, back pain, joint pain); or gastrointestinal symptoms (nausea, diarrhea).

    **While the qualifying symptom(s) may fluctuate, the total duration of at least one qualifying symptom must be at least 3 months at time of randomization. In addition, that symptom must be present for more days than not in the 30 days prior to randomization.

  7. Participant scores <70 on the Pediatric Quality of Life Multidimensional Fatigue Scale (PedsQL-MFS) at Visit 01A.

  8. Willing and able to provide informed consent and assent (as applicable) before initiation of any study procedures.

  9. Able to understand and agree to comply with all planned study procedures and be available for all study visits.

    *Participants still may enroll if they decline genetic testing or if they are unable or unwilling to complete blood draw(s) for biomarkers. An initial blood draw for baseline clinical laboratory assessments is required to be completed prior to randomization.

  10. Participants of childbearing potential* must agree to use highly effective contraception** or practice true abstinence*** throughout the study (Visit 08).

    *Persons of childbearing potential is defined as post-menarchal biological females who have not reached menopause or undergone surgical sterilization. Menopause is defined as having no menses for at least 12 months without an alternative medical cause for amenorrhea.

    **Highly effective contraception includes hormonal contraception (oral, implant, injection, transdermal patch, vaginal ring), intrauterine device (IUD), bilateral tubal ligation, or partner vasectomy.

    ***True abstinence is defined as no heterosexual vaginal/penile intercourse at any time during the study

  11. Participants capable of fathering a child* and having sex with women of childbearing potential must agree to use contraception (i.e., condoms) throughout the study (Visit 08).

    *Persons capable of fathering a child are biological males who are post-pubertal and not permanently sterile by bilateral orchidectomy or vasectomy

  12. Agrees to utilize electronic data capture for the e-Memory Aid and electronic PROs and have access to a device connected to the internet for completion.

  13. Agrees to adhere to all lifestyle considerations.

Exclusion Criteria:

  1. Known acute SARS CoV 2 infection </= 30 days before randomization.

  2. Current or recent opioid use in the 7 days before randomization, as reported by the participant or their parent/legal guardian.

  3. Plans to have elective surgery or procedure which may involve use of opioid medication during the study intervention.

  4. Known allergy/sensitivity/hypersensitivity to naltrexone or its components.

  5. Current or recent use of naltrexone in the 14 days before randomization.

  6. History of use of LDN for >/= 30 days duration to treat Long COVID in the 6 months before randomization.

  7. Enrolled at the time of consent/assent or planned enrollment in another interventional clinical trial during the trial.

  8. Plans to become pregnant or to father a child during the trial or is pregnant or breastfeeding at randomization.

  9. Has a positive pregnancy test at Visit 01A.* *All participants of childbearing potential will have a urine pregnancy test at Visit 01A, with results confirmed as negative before randomization.

  10. Has known active acute hepatitis or a history of chronic liver disease (known Child-Pugh Class B or C) or known severe chronic kidney disease and/or kidney failure (Estimated Glomerular Filtration Rate [eGFR] < 30 ml/min/1.73 m^2).

  11. Has known active Hepatitis B (HBV) infection, active Hepatitis C (HCV) infection, or unstable Human Immunodeficiency Virus (HIV) (i.e., not on antiretroviral therapy (ART) or on ART but has detectable viral load).

  12. Has recent active malignancy (received chemotherapy or radiotherapy in the 12 months prior to randomization) or active malignancy at randomization*.

    • Long COVID patients with non-melanoma skin carcinoma (basal cell or squamous cell skin cancer), or low-grade cervical squamous intraepithelial lesions, which are considered cured and not requiring ongoing therapy, may be enrolled at the discretion of the investigator.
  13. Began taking a new medication*, supplement, or vitamin or changed doses of a medication, supplement, or vitamin the 14 days prior to randomization.

    *Topical and intranasal (non-opioid) medications are not exclusionary.

  14. Diagnosed in the 3 months prior to randomization with a new medical condition*, other than Long COVID, causing new or worsening fatigue that is unresolved at time of randomization.

    *Medical conditions that could cause new or worsening fatigue include but are not limited to iron deficiency with or without severe anemia, hypothyroidism, infectious mononucleosis (Epstein-Barr Virus or cytomegalovirus infection), celiac disease, type 1 diabetes mellitus, acute leukemia or hematologic malignancy, adrenal insufficiency, cardiac disease (e.g. myocarditis, arrythmia, or cardiomyopathy), metabolic disease, renal disease, or a primary sleep disorders (e.g. obstructive sleep apnea, restless legs syndrome, narcolepsy, or parasomnia).

  15. Has a clinically significant mental health condition defined by history of one or more of the following:

    a. History of prior suicide attempt. b. Hospitalized in the 6 months prior to randomization for mental health symptoms or worsening of a known mental health condition.

    c. Has moderate-risk or high-risk score on C SSRS at Visit 01A, as applicable. d. Has a diagnosis of severe conduct disorder*that, in the site investigator's judgment, may pose a safety risk or interfere with the ability to adequately assess clinical trial endpoints.

    *The American Psychiatric Association defines conduct disorder as a repetitive and persistent pattern of behavior in which the basic rights of others or major age-appropriate societal norms or rules are violated (e.g., history of recurrent aggressive behavior toward people or animals, and/or serious violations of rules or laws like running away, possessing or using weapons, vandalism). If the site Investigator is unsure if a participant has a diagnosis of severe conduct disorder, they may refer to the DSM-5-TR criteria.

  16. Has any medical condition*, ** that, in the site investigator's judgment, pose a safety risk or interfere with the ability to adequately assess clinical trial endpoints.

    • Medical conditions include but are not limited to severe esophagitis or a condition that precludes participant from taking study product; an active unstable or progressive major psychiatric or neurologic condition, including severe developmental disabilities, new or untreated psychosis or schizophrenia, new or untreated bipolar I disorder; and acute opioid withdrawal disorder to include participants maintained on opiate agonists (methadone) or partial agonists (buprenorphine) and those who has failed a naloxone challenge test.

      • Of note, an abnormal vital sign alone is not exclusionary at baseline. However, the abnormal vital sign may be indicative of an exclusionary medical condition as described above.

Piano di studio

Questa sezione fornisce i dettagli del piano di studio, compreso il modo in cui lo studio è progettato e ciò che lo studio sta misurando.

Come è strutturato lo studio?

Dettagli di progettazione

  • Scopo principale: Trattamento
  • Assegnazione: Randomizzato
  • Modello interventistico: Assegnazione parallela
  • Mascheramento: Quadruplicare

Armi e interventi

Gruppo di partecipanti / Arm
Intervento / Trattamento
Sperimentale: Low-Dose Naltrexone

Participants will receive a low-dose naltrexone (LDN) capsule that will be administered orally once daily for 16 weeks. LDN will be initiated at 1.5 mg daily and titrated weekly to a maximum tolerated dose of up to 4.5 mg daily. N=650

Opioid receptor antagonist used to treat opioid and alcohol use disorders in adults. Formulated as naltrexone hydrochloride, a white, crystalline compound freely soluble in water.

Comparatore placebo: Placebo

Participants will receive a matching placebo capsule that will be administered orally once daily for 16 weeks. The placebo arm will follow the same dosing schedule and titration scheme as the LDN arm. N=650

Matching placebo capsule that is visually identical to the active study product and is administered orally once daily according to the same dosing schedule and titration scheme for 16 weeks.

Cosa sta misurando lo studio?

Misure di risultato primarie

Misura del risultato
Misura Descrizione
Lasso di tempo
Change from baseline in Pediatric Quality of Life - Multidimensional Fatigue Scale (PedsQL-MFS) total score.
Lasso di tempo: Baseline to 16 weeks after randomization

The Pediatric Quality of Life - Multidimensional Fatigue Scale (PedsQL-MFS) contains 18 Likert-type items and is scored from 0 to 100; higher scores represent lower levels of fatigue.

Baseline to 16 weeks after randomization

Misure di risultato secondarie

Misura del risultato
Misura Descrizione
Lasso di tempo
Change from baseline Delis-Kaplan Executive Function System (D-KEFS) Category Fluency t-score
Lasso di tempo: Baseline to 16 weeks after randomization

The D-KEFS Verbal Fluency Category Fluency condition measures verbal fluency and executive function.

Participants generate as many words as possible beginning with a specified letter within a fixed time.

Performance score is scored by the number of correct words and interpreted using age-appropriate normative data.

This outcome applies to English-speaking participants aged 8 to 25 years.

Baseline to 16 weeks after randomization
Change from baseline Delis-Kaplan Executive Function System (D-KEFS) Letter Fluency t-score
Lasso di tempo: Baseline to 16 weeks after randomization

The D-KEFS Verbal Fluency Letter Fluency condition measures verbal fluency and executive function.

Participants generate as many words as possible beginning with a specified letter within a fixed time.

Performance score is scored by the number of correct words and interpreted using age-appropriate normative data.

This outcome applies to English-speaking participants aged 8 to 25 years.

Baseline to 16 weeks after randomization
Change from baseline in Behavior Rating Inventory of Executive Function-Second Edition (BRIEF-2) Global Executive Composite t-score
Lasso di tempo: Baseline to 16 weeks after randomization

The BRIEF-2 is a standardized questionnaire assessing executive function and self-regulation in participants aged 6 to 17 years.

Scores are interpreted using age- and sex-appropriate normative data. Higher scores indicate greater impairment in executive functioning.

Baseline to 16 weeks after randomization
Change from baseline in Behavior Rating Inventory of Executive Function-Second Edition (BRIEF-2A) Global Executive Composite t-score
Lasso di tempo: Baseline to 16 weeks after randomization

The BRIEF-2A is a standardized 75-item self-report assessment of executive functioning in participants aged 18 years and older.

Scores are interpreted using age- and sex-appropriate normative data. Higher scores indicate greater impairment in executive functioning.

Baseline to 16 weeks after randomization
Change from baseline in Conners Continuous Performance Test-Third Edition (CPT-3) Detectability t-score.
Lasso di tempo: Baseline to 16 weeks after randomization

The CPT-3 is a computerized assessment of sustained attention and response control for participants aged 8 years and older.

Performance is automatically recorded and interpreted using age-appropriate normative data.

Baseline to 16 weeks after randomization
Change from baseline in Conners Continuous Performance Test-Third Edition (CPT-3) Hit Reaction Time t-score
Lasso di tempo: Baseline to 16 weeks after randomization

The CPT-3 is a computerized assessment of sustained attention and response control for participants aged 8 years and older.

Performance is automatically recorded and interpreted using age-appropriate normative data.

Baseline to 16 weeks after randomization
Change from baseline in Connors Kiddie Continuous Performance Test (K-CPT-2) Detectability t-score.
Lasso di tempo: Baseline to 16 weeks after randomization

The K-CPT-2 Computerized assessment of sustained attention and response control for participants aged 6 to 7 years. Performance is automatically recorded and interpreted using age-appropriate normative data.

Baseline to 16 weeks after randomization
Change from baseline in Connors Kiddie Continuous Performance Test (K-CPT-2) Hit Reaction Time t-score
Lasso di tempo: Baseline to 16 weeks after randomization

The K-CPT-2 Computerized assessment of sustained attention and response control for participants aged 6 to 7 years. Performance is automatically recorded and interpreted using age-appropriate normative data.

Baseline to 16 weeks after randomization
Change from baseline in Developmental Neuropsychological Assessment (NEPSY-II) Semantic Word Generation Scaled score.
Lasso di tempo: Baseline to 16 weeks after randomization

The NEPSY-II Word Generation subtest measures verbal fluency and executive function. Participants generate words within semantic category during 60-second time limit.

Performance is scored by the number of correct words[TS3.1] and interpreted using age-appropriate normative data.

This outcome applies to English-speaking participants aged 6 to 7 years.

Baseline to 16 weeks after randomization
Change from baseline in Digit Span-Wechsler Intelligence Scale for Children-Fifth Edition (WISC-V) t-score.
Lasso di tempo: Baseline to 16 weeks after randomization

The WISC-V Digit Span subtest assesses attention and working memory in participants aged 6 to 15 years.

Raw scores are based on Digit Span Forward, Backward, and Sequencing tasks and are interpreted using age-appropriate normative data.

Baseline to 16 weeks after randomization
Change from baseline in Digit Span-Wechsler Intelligence Scale for Children-Fourth Edition (WISC-IV) t-score.
Lasso di tempo: Baseline to 16 weeks after randomization

The WISC-IV Digit Span subtest assesses attention and working memory in participants aged 16 years and older.

Raw scores are based on Digit Span Forward, Backward, and Sequencing tasks and are interpreted using age-appropriate normative data.

Baseline to 16 weeks after randomization
Change from baseline in Functional Disability Inventory (FDI) total score.
Lasso di tempo: Baseline to 16 weeks after randomization

The Functional Disability Inventory (FDI) contains 15 items rated from 0 ('no trouble') to 4 ('impossible').

Total scores range from 0 to 60. Higher scores represent greater functional disability and more impairment in daily functioning.

Baseline to 16 weeks after randomization
Change from baseline in Patient Global Impression of Severity (PGI-S)
Lasso di tempo: Baseline to 16 weeks after randomization

The Patient Global Impression of Severity (PGI-S) is a single-item questionnaire rated on a 5-point Likert scale from 1 ('None') to 5 ('Very severe').

Higher scores reflect greater perceived illness or symptom severity.

Baseline to 16 weeks after randomization
Change from baseline in Patient-Reported Outcomes Measurement Information System (PROMIS) Adult Pain Intensity Scale t-score in participants aged 18 to 25 years.
Lasso di tempo: Baseline to 16 weeks after randomization

The Patient-Reported Outcomes Measurement Information System (PROMIS) Pain Intensity Scale asks about pain over the past 7 days.

Items are rated on a 5-point scale from 1 ('not at all') to 5 ('very much'). Results are reported as T-scores. Higher scores representing greater pain intensity.

Baseline to 16 weeks after randomization
Change from baseline in Patient-Reported Outcomes Measurement Information System (PROMIS) Adult Pain Interference Scale t-score in participants aged 18 to 25 years.
Lasso di tempo: Baseline to 16 weeks after randomization

The Patient-Reported Outcomes Measurement Information System (PROMIS) Pain Intensity Scale asks how pain affects activities, mood, and social participation over the past 7 days.

Items are rated on a 5-point scale from 1 ('not at all') to 5 ('very much'). Results are reported as T-scores. Higher scores representing greater pain interference.

Baseline to 16 weeks after randomization
Change from baseline in Patient-Reported Outcomes Measurement Information System (PROMIS) Parent-Proxy Pain Intensity Scale t-score in participants aged 6 to 7 years.
Lasso di tempo: Baseline to 16 weeks after randomization

The Patient-Reported Outcomes Measurement Information System (PROMIS) Pain Intensity scale asks about pain over the past 7 days.

Items are rated on a 5-point scale from 1 ('not at all') to 5 ('very much'). Results are reported as T-scores, with higher scores representing greater pain intensity.

Baseline to 16 weeks after randomization
Change from baseline in Patient-Reported Outcomes Measurement Information System (PROMIS) Parent-Proxy Pain Interference Scale t-score in participants aged 6 to 7 years.
Lasso di tempo: Baseline to 16 weeks after randomization

The Patient-Reported Outcomes Measurement Information System (PROMIS) Parent-Proxy Pain Interference Scale asks how pain affects activities, mood, and social participation over the past 7 days.

Items are rated on a 5-point scale from 1('not at all') to 5('very much'). Results are reported as T-scores. Higher scores representing greater pain interference.

Baseline to 16 weeks after randomization
Change from baseline in Patient-Reported Outcomes Measurement Information System (PROMIS) Pediatric Pain Intensity Scale t-score in participants aged 8 to 17 years.
Lasso di tempo: Baseline to 16 weeks after randomization

The Patient-Reported Outcomes Measurement Information System (PROMIS) Pediatric Pain Intensity Scale asks about pain over the past 7 days.

Items are rated on a 5-point scale from 1 ('not at all') to 5 ('very much'). Results are reported as T-scores. Higher scores representing greater pain intensity.

Baseline to 16 weeks after randomization
Change from baseline in Patient-Reported Outcomes Measurement Information System (PROMIS) Pediatric Pain Interference Scale t-score in participants aged 8 to 17 years.
Lasso di tempo: Baseline to 16 weeks after randomization

The Patient-Reported Outcomes Measurement Information System (PROMIS) Pediatric Pain Interference scale asks how pain affects activities, mood, and social participation over the past 7 days.

Items are rated on a 5-point scale from 1 ('not at all') to 5 ('very much'). Results are reported as T-scores. Higher scores representing greater pain interference.

Baseline to 16 weeks after randomization
Change from baseline in Pediatric Quality of Life (PedsQL) Generic Core Scales Short Form 15 total score.
Lasso di tempo: Baseline to 16 weeks after randomization

The PedsQL Generic Core Scales Short Form 15 contains 15 Likert-type items across physical, emotional, social, and school functioning and is scored from 0 to 100.

Higher scores represent better quality of life.

Baseline to 16 weeks after randomization
Change from baseline in Pediatric Quality of Life - Multidimensional Fatigue Scale (PedsQL-MFS) subscale scores.
Lasso di tempo: Baseline to 16 weeks after randomization

The Pediatric Quality of Life - Multidimensional Fatigue Scale (PedsQL-MFS) contains 18 Likert-type items and includes general fatigue, sleep/rest fatigue, and cognitive fatigue subscales. Scores are reported on a 0 to 100 scale.

Higher scores represent lower levels of fatigue.

Baseline to 16 weeks after randomization
Change from baseline in Pediatric Quality of Life - Multidimensional Fatigue Scale (PedsQL-MFS) total score in participants aged 12 to 17 years.
Lasso di tempo: Baseline to 16 weeks after randomization

The Pediatric Quality of Life - Multidimensional Fatigue Scale (PedsQL-MFS) contains 18 Likert-type items and is scored from 0 to 100; higher scores represent lower levels of fatigue.

Baseline to 16 weeks after randomization
Change from baseline in Pediatric Quality of Life - Multidimensional Fatigue Scale (PedsQL-MFS) total score in participants aged 18 to 25 years.
Lasso di tempo: Baseline to 16 weeks after randomization

The Pediatric Quality of Life - Multidimensional Fatigue Scale (PedsQL-MFS) contains 18 Likert-type items and is scored from 0 to 100; higher scores represent lower levels of fatigue.

Baseline to 16 weeks after randomization
Change from baseline in Pediatric Quality of Life - Multidimensional Fatigue Scale (PedsQL-MFS) total score in participants aged 6 to 11 years.
Lasso di tempo: Baseline to 16 weeks after randomization

The Pediatric Quality of Life - Multidimensional Fatigue Scale (PedsQL-MFS) contains 18 Likert-type items and is scored from 0 to 100; higher scores represent lower levels of fatigue.

Baseline to 16 weeks after randomization
Change in Pediatric Quality of Life Multidimensional Fatigue Scale (PedsQL-MFS) total score from 16 to 26 weeks after randomization.
Lasso di tempo: 16 to 26 weeks after randomization

The Pediatric Quality of Life Multidimensional Fatigue Scale (PedsQL-MFS) contains 18 Likert-type items and is scored from 0 to 100.

Higher scores represent lower levels of fatigue.

16 to 26 weeks after randomization
Incidence of new infections.
Lasso di tempo: First administration of study product through 6 months after randomization

New infections will be summarized by frequency, percentage, and incidence rate. Severity and relatedness will also be summarized as applicable.

First administration of study product through 6 months after randomization
Incidence of new-onset chronic medical conditions (NOCMCs).
Lasso di tempo: First administration of study product through 6 months after randomization

NOCMCs will be assessed by number, severity, and relatedness and summarized by frequency, percentage, and incidence rate.

First administration of study product through 6 months after randomization
Incidence of solicited adverse events (AEs).
Lasso di tempo: First administration of study product through 8 weeks after randomization

Solicited AEs will be assessed by number, severity, and relatedness according to the DAIDS table for Grading the Severity of Adult and Pediatric Adverse Event, version 2.1.

First administration of study product through 8 weeks after randomization
Incidence of treatment emergent serious adverse events (SAEs).
Lasso di tempo: First administration of study product through 6 months after randomization

Treatment-emergent SAEs will be assessed by number, severity, and relatedness and summarized by frequency, percentage, and incidence rate.

First administration of study product through 6 months after randomization
Incidence of treatment emergent unsolicited adverse events (AEs).
Lasso di tempo: First administration of study product through 16 weeks after randomization

Treatment-emergent unsolicited AEs will be assessed by number, severity, and relatedness according to the DAIDS table for Grading the Severity of Adult and Pediatric Adverse Event, version 2.1.

First administration of study product through 16 weeks after randomization
Incidence of treatment-emergent medically attended adverse events (MAAEs).
Lasso di tempo: First administration of study product through 6 months after randomization

Treatment-emergent MAAEs will be assessed by number, severity, and relatedness and summarized by frequency, percentage, and incidence rate.

First administration of study product through 6 months after randomization
Patient Global Impression of Change (PGI-C) at 16 weeks after randomization
Lasso di tempo: 16 weeks after randomization

The PGI-C is a 7-point self-report scale ranging from 'very much improved'[TS4.1] to 'very much worse'[TS5.1] and measures overall improvement from treatment.

16 weeks after randomization

Collaboratori e investigatori

Qui è dove troverai le persone e le organizzazioni coinvolte in questo studio.

Sponsor

Investigatori

  • Investigatore principale: Laura Malone, MD PhD, Hugo W. Moser Research Institute at Kennedy Krieger, Inc.

Studiare le date dei record

Queste date tengono traccia dell'avanzamento della registrazione dello studio e dell'invio dei risultati di sintesi a ClinicalTrials.gov. I record degli studi e i risultati riportati vengono esaminati dalla National Library of Medicine (NLM) per assicurarsi che soddisfino specifici standard di controllo della qualità prima di essere pubblicati sul sito Web pubblico.

Studia le date principali

Inizio studio (Stimato)

16 novembre 2026

Completamento primario (Stimato)

31 dicembre 2028

Completamento dello studio (Stimato)

1 gennaio 2029

Date di iscrizione allo studio

Primo inviato

29 ottobre 2026

Primo inviato che soddisfa i criteri di controllo qualità

29 ottobre 2026

Primo Inserito (Effettivo)

4 novembre 2026

Aggiornamenti dei record di studio

Ultimo aggiornamento pubblicato (Effettivo)

4 novembre 2026

Ultimo aggiornamento inviato che soddisfa i criteri QC

29 ottobre 2026

Ultimo verificato

28 ottobre 2026

Maggiori informazioni

Termini relativi a questo studio

Altri numeri di identificazione dello studio

  • 25-0018
  • 1OT2HL156812 (Sovvenzione/contratto NIH degli Stati Uniti)

Piano per i dati dei singoli partecipanti (IPD)

Hai intenzione di condividere i dati dei singoli partecipanti (IPD)?

NO

Informazioni su farmaci e dispositivi, documenti di studio

Studia un prodotto farmaceutico regolamentato dalla FDA degli Stati Uniti

Sì

Studia un dispositivo regolamentato dalla FDA degli Stati Uniti

No

prodotto fabbricato ed esportato dagli Stati Uniti

No

Queste informazioni sono state recuperate direttamente dal sito web clinicaltrials.gov senza alcuna modifica. In caso di richieste di modifica, rimozione o aggiornamento dei dettagli dello studio, contattare register@clinicaltrials.gov. Non appena verrà implementata una modifica su clinicaltrials.gov, questa verrà aggiornata automaticamente anche sul nostro sito web .