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Kliniske studier på Esferocitose Hereditária
Totalt 5 resultater
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Alnylam PharmaceuticalsFullførtPolynevropati | Hereditær Transthyretin-mediert (ATTRv) amyloidoseForente stater
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National Human Genome Research Institute (NHGRI)National Center for Advancing Translational Sciences (NCATS); Therapeutics...FullførtGNE Myopati | Hereditary Inclusion Body Myopati (HIBM)Forente stater
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Ultragenyx Pharmaceutical IncFullførtHereditary Inclusion Body Myopati (HIBM)Forente stater
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Ultragenyx Pharmaceutical IncFullførtGNE Myopati | Hereditary Inclusion Body Myopati (HIBM)Forente stater, Israel
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NobelpharmaFullførtGNE Myopati | Nonaka sykdom | Distal myopati med kantvakuoler (DMRV) | Hereditary Inclusion Body Myopati (hIBM)Japan