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Kliniske forsøg sponsoreret af Boston Children's Hospital - Children's Rare Disease Cohorts Initiative
I alt 8 resultater
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Boston Children's HospitalBoston Children's Hospital - Children's Rare Disease Cohorts InitiativeRekrutteringBevægelsesforstyrrelser | Neurodegenerative sygdomme | Motor neuron sygdom | Spasticitet, muskel | Pædiatrisk lidelse | Arvelig spastisk paraplegiForenede Stater
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University of California, San DiegoBaylor College of Medicine; Boston Children's Hospital; Rare Diseases Clinical... og andre samarbejdspartnereAfsluttetSygdomme i nervesystemet | Angelman syndromForenede Stater
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Soul, Janet , M.D.National Institute of Neurological Disorders and Stroke (NINDS); Charles... og andre samarbejdspartnereAfsluttet
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University of Alabama at BirminghamUniversity of Colorado, Denver; Eunice Kennedy Shriver National Institute... og andre samarbejdspartnereAfsluttetRett syndrom | MECP2 duplikationsforstyrrelse | Rett-relateret lidelseForenede Stater
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Boston Children's HospitalEunice Kennedy Shriver National Institute of Child Health and Human Development... og andre samarbejdspartnereRekrutteringAutisme | ASD | Makrocefali | PTEN | PTEN Hamartoma Tumor SyndromForenede Stater
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Boston Children's HospitalEunice Kennedy Shriver National Institute of Child Health and Human Development... og andre samarbejdspartnereRekrutteringIntellektuel handicap | Tuberøs sklerose | Autisme lidelseForenede Stater
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Boston Children's HospitalEunice Kennedy Shriver National Institute of Child Health and Human Development... og andre samarbejdspartnereAfsluttetPTEN-genmutation | PTEN Hamartoma Tumor SyndromForenede Stater
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Boston Children's HospitalEunice Kennedy Shriver National Institute of Child Health and Human Development... og andre samarbejdspartnereRekrutteringIntellektuel handicap | Autismespektrumforstyrrelse | Phelan-McDermid syndromForenede Stater