- ICH GCP
- US Clinical Trials Registry
- Klinisk forsøg NCT07601295
Tiprelestat Versus Placebo When Added to Standard of Care for the Treatment of Pulmonary Arterial Hypertension (PAH) (ATHENA)
15. maj 2026 opdateret af: Roham T. Zamanian, Stanford University
A Phase II, Randomized, Double-Blind, Safety and Efficacy Study of Tiprelestat Versus Placebo When Added to Standard of Care for the Treatment of Pulmonary Arterial Hypertension (PAH)
The primary objective of this study is to compare the efficacy, safety, and tolerability of tiprelestat plus Standard of Care (SOC) compared with placebo plus SOC in patients with World Health Organization (WHO) functional class II-IV pulmonary arterial hypertension (PAH).
Studieoversigt
Status
Ikke rekrutterer endnu
Betingelser
Intervention / Behandling
Undersøgelsestype
Interventionel
Tilmelding (Anslået)
90
Fase
- Fase 2
Kontakter og lokationer
Dette afsnit indeholder kontaktoplysninger for dem, der udfører undersøgelsen, og oplysninger om, hvor denne undersøgelse udføres.
Studiesteder
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Arizona
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Tucson, Arizona, Forenede Stater, 85719
- The University of Arizona / Banner University Medical Center
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California
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San Francisco, California, Forenede Stater, 94143
- University of California, San Francisco
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Stanford, California, Forenede Stater, 94305
- Stanford University
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Colorado
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Aurora, Colorado, Forenede Stater, 80045
- University of Colorado (UCD) Anschutz
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Massachusetts
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Boston, Massachusetts, Forenede Stater, 02138
- Harvard University / Brigham and Women's Hospital
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North Carolina
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Durham, North Carolina, Forenede Stater, 27710
- Duke University
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Pennsylvania
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Philadelphia, Pennsylvania, Forenede Stater, 19104
- University of Pennsylvania
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Rhode Island
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Providence, Rhode Island, Forenede Stater, 02904
- Brown University/Rhode Island Hospital
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Texas
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Dallas, Texas, Forenede Stater, 75390
- University of Texas Southwestern
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Washington
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Seattle, Washington, Forenede Stater, 98195
- University of Washington
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Deltagelseskriterier
Forskere leder efter personer, der passer til en bestemt beskrivelse, kaldet berettigelseskriterier. Nogle eksempler på disse kriterier er en persons generelle helbredstilstand eller tidligere behandlinger.
Berettigelseskriterier
Aldre berettiget til at studere
- Voksen
- Ældre voksen
Tager imod sunde frivillige
Ingen
Beskrivelse
Inclusion Criteria:
- Adults age 18 to 75 years.
- Willingness to give written informed consent prior to any study-related procedures being performed and to be able to adhere to the study restrictions and examination schedule.
- Diagnosis of WHO Group I PAH.
- WHO functional class II - IV despite optimized treatment SOC, with 1 or more modalities including phosphodiesterase 5 (PDE5) inhibitor, soluble guanylate cyclase stimulator (sGCS), endothelin receptor antagonist (ERA), and/or a prostacyclin analogue or receptor agonist (SC/inhaled/PO) (see #5), as well as Sotatercept (see #6).
- On stable doses of PDE5 inhibitor, ERA, sGCS, or prostacyclin analogue/receptor agonist for at least 90 days prior to screening; for infusion prostacyclins, dose adjustment within 10% of baseline dose during the duration of the study is allowed per medical practice.
- On stable doses of Sotatercept therapy for at least 6 months prior to screening, and intended to be continued during the duration of the study.
- Screening right heart catheterization mean pulmonary arterial pressure (mPAP) ≥ 25 mmHg at rest; pulmonary wedge pressure (PAWP) ≤ 15 mmHg or left ventricular end diastolic pressure (LVEDP) ≤ 15 mmHg; AND pulmonary vascular resistance (PVR) ≥ 400 dynes•sec/cm5 (5 Wood Units).
- If participant is of childbearing potential, willing to use adequate methods of contraception throughout the course of the study. If participant is of childbearing potential (a participant < 55 years of age who has not been postmenopausal for ≥ 5 years or who has not had a bilateral salpingectomy, hysterectomy and/or oophorectomy), need to employ two reliable means of contraception which may include surgical sterilization, barrier methods, spermicidals, intrauterine devices, and/or hormonal contraception, unless the participant chooses abstinence (to avoid heterosexual intercourse completely). If a participant chooses abstinence, then a second reliable means of contraception is not needed.
- 6MWD ≥100 and ≤500 meters at screening.
- Willing to adhere to study restrictions and examination schedule.
Exclusion Criteria:
- Diagnosis of WHO Group 2 - 5 Pulmonary Hypertension.
- Participation in another clinical trial, or experimental use, involving a PAH investigational drug or device within the last 3 months.
- Total lung capacity (TLC) < 60% predicted; if TLC is ≥ 60% and < 70% predicted, high resolution computed tomography (HRCT) must be available to exclude significant interstitial lung disease.
- FEV1 / FVC < 70% predicted and FEV1 < 60% predicted.
Significant left-sided heart disease (based on screening Echocardiogram):
- Moderate or severe aortic or mitral valve disease
- Diastolic dysfunction ≥ Grade II
- LV systolic function < 45%
- Pericardial constriction
- Restrictive cardiomyopathy
- Significant coronary disease with demonstrable ischemia
- Chronic renal insufficiency defined as an estimated creatinine clearance < 30 ml/min.
- Current atrial arrhythmias not under optimal control.
- Uncontrolled systemic hypertension: SBP > 160 mmHg or DBP > 100mmHg.
- Severe hypotension: SBP < 80 mmHg.
- Pregnant or breast-feeding.
- Psychiatric, addictive, or other disorders that compromise the patient's ability to provide informed consent, to follow study protocol, and adhere to treatment instructions.
- Known allergy or hypersensitivity to tiprelestat.
- Moderate to severe hepatic dysfunction with a Child Pugh score >10.
- Hyperkalemia defined as Potassium > 5.1 mEq/L at screening.
- Initiation of an exercise program for cardiopulmonary rehabilitation within 90 days prior to screening or planned during the study. Subjects who are already stable in the maintenance phase of an exercise program which will continue for the duration of the study are eligible.
- Known active infection requiring antibiotic, antifungal, or antiviral therapies. Patients may be rescreened at physician discretion after the resolution of infection and discontinuation of antibiotic, antifungal, or antiviral therapies.
- Co-morbid conditions that would impair a patient's exercise performance and ability to assess WHO functional class, including but not limited to chronic low-back pain or peripheral musculoskeletal problems, other comorbidities expected to alter the patient's clinical course (i.e. active cancer; >3 comorbidities e.g., obesity, systemic HTN, diabetes).
Studieplan
Dette afsnit indeholder detaljer om studieplanen, herunder hvordan undersøgelsen er designet, og hvad undersøgelsen måler.
Hvordan er undersøgelsen tilrettelagt?
Design detaljer
- Primært formål: Behandling
- Tildeling: Randomiseret
- Interventionel model: Parallel tildeling
- Maskning: Tredobbelt
Våben og indgreb
Deltagergruppe / Arm |
Intervention / Behandling |
|---|---|
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Eksperimentel: Tiprelestat (5 mg)
Participants receive tiprelestat injection daily for 168 days.
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5 mg of tiprelestat in 1 mL saline administered as a daily subcutaneous injection for 168 days.
Andre navne:
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Eksperimentel: Tiprelestat (10 mg)
Participants receive tiprelestat injection daily for 168 days.
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10 mg of tiprelestat in 1 mL saline administered as a daily subcutaneous injection for 168 days.
Andre navne:
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Placebo komparator: Placebo (1 mL 0.9% saline solution)
Participants receive placebo injection (matching tiprelestat) daily for 168 days.
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Matching 1 mL 0.9% saline solution administered as a daily subcutaneous injection for 168 days.
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Hvad måler undersøgelsen?
Primære resultatmål
Resultatmål |
Foranstaltningsbeskrivelse |
Tidsramme |
|---|---|---|
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Change in Pulmonary Vascular Resistance (PVR)
Tidsramme: Baseline to week 24
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PVR is calculated based on direct measurements during the right heart catheterization (RHC) procedure.
PVR = (mPAP - PAWP) / CO, where mPAP is the mean pulmonary artery pressure, PAWP is the pulmonary wedge arterial pressure, and CO is the cardiac output.
These cardiac measures are also obtained from right heart catheterization.
PVR is measured in Wood units (WU) or dynes (dynes*sec/cm5), and higher values are associated with more severe disease.
Normal range for PVR is 1-3 WU (80-240 dynes*sec/cm5) and can be as high as 30 WU (2,400 80-240 dynes*sec/cm5) in disease.
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Baseline to week 24
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Samarbejdspartnere og efterforskere
Det er her, du vil finde personer og organisationer, der er involveret i denne undersøgelse.
Sponsor
Efterforskere
- Ledende efterforsker: Roham T Zamanian, MD, Stanford University
Datoer for undersøgelser
Disse datoer sporer fremskridtene for indsendelser af undersøgelsesrekord og resumeresultater til ClinicalTrials.gov. Studieregistreringer og rapporterede resultater gennemgås af National Library of Medicine (NLM) for at sikre, at de opfylder specifikke kvalitetskontrolstandarder, før de offentliggøres på den offentlige hjemmeside.
Studer store datoer
Studiestart (Anslået)
1. juli 2026
Primær færdiggørelse (Anslået)
1. februar 2030
Studieafslutning (Anslået)
1. marts 2030
Datoer for studieregistrering
Først indsendt
15. maj 2026
Først indsendt, der opfyldte QC-kriterier
15. maj 2026
Først opslået (Faktiske)
22. maj 2026
Opdateringer af undersøgelsesjournaler
Sidste opdatering sendt (Faktiske)
22. maj 2026
Sidste opdatering indsendt, der opfyldte kvalitetskontrolkriterier
15. maj 2026
Sidst verificeret
1. maj 2026
Mere information
Begreber relateret til denne undersøgelse
Yderligere relevante MeSH-vilkår
Andre undersøgelses-id-numre
- 84755
- UG3HL180990 (U.S. NIH-bevilling/kontrakt)
- U24HL180994 (U.S. NIH-bevilling/kontrakt)
Plan for individuelle deltagerdata (IPD)
Planlægger du at dele individuelle deltagerdata (IPD)?
INGEN
Lægemiddel- og udstyrsoplysninger, undersøgelsesdokumenter
Studerer et amerikansk FDA-reguleret lægemiddelprodukt
Ja
Studerer et amerikansk FDA-reguleret enhedsprodukt
Ingen
Disse oplysninger blev hentet direkte fra webstedet clinicaltrials.gov uden ændringer. Hvis du har nogen anmodninger om at ændre, fjerne eller opdatere dine undersøgelsesoplysninger, bedes du kontakte register@clinicaltrials.gov. Så snart en ændring er implementeret på clinicaltrials.gov, vil denne også blive opdateret automatisk på vores hjemmeside .
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VIVUS LLCIkke rekrutterer endnuPulmonal arteriel hypertension | Pulmonal arteriel hypertension (PAH) (WHO Group 1 PH) | Pulmonal arteriel hypertension (PAH) | Pulmonal arteriel hypertension WHO gruppe I | Pulmonal arteriel hypertension PAH
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ImmuneCare Biopharmaceuticals (Shanghai) Co., Ltd.RekrutteringPulmonal arteriel hypertension PAHKina
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Ege UniversityAfsluttetPulmonal arteriel hypertension (PAH) (WHO Group 1 PH)Tyrkiet (Türkiye)
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Chinese Pulmonary Vascular Disease Research GroupIkke rekrutterer endnuLivskvalitet | Patienter rapporterede resultater | Pulmonal arteriel hypertension (PAH)
Kliniske forsøg med Tiprelestat (5 mg)
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Eisai Co., Ltd.Afsluttet
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PfizerAfsluttetSund og raskForenede Stater
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Hanmi Pharmaceutical Company LimitedAfsluttetBenign prostatahyperplasi
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Roham T. ZamanianNational Heart, Lung, and Blood Institute (NHLBI); Duke University; SRI InternationalAfsluttet
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Laboratorios Andromaco S.A.Afsluttet
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GlaxoSmithKlineAfsluttet
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EstetraAfsluttetOvergangsalderen | SvangerskabsforebyggelseBulgarien
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Suzhou Kintor Pharmaceutical Inc,Afsluttet
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Proteimax Biotechnology Israel LTDAfsluttet
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Shandong Suncadia Medicine Co., Ltd.Ikke rekrutterer endnu